Muscular Dystrophies clinical trials
The registry lists 224 studies for Muscular Dystrophies across more than 10 countries. 48 are recruiting or about to start. 59 of them are mainly about Muscular Dystrophies (how this is decided). Per ClinicalTrials.gov, last updated 2026-11-13. Counting its 4 narrower conditions too, such as Muscular Dystrophy, Duchenne: 794 studies, 189 open.
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Who runs them
Cooperative International Neuromuscular Research Group (8) · GlaxoSmithKline (7) · Rigshospitalet, Denmark (5) · Avidity Biosciences, Inc. (5) · National Institute of Neurological Disorders and Stroke (NINDS) (5) · Wake Forest University Health Sciences (4) · IRCCS Eugenio Medea (4) · Fulcrum Therapeutics (4)
What is being tested here
Drugs under test in Muscular Dystrophies studies, those with the most open studies first. Medicines only given beside them are not counted. How drugs are counted
| Drug | Open | Phase 3 | All |
|---|---|---|---|
| Tadalafil | 1 | 0 | 4 |
| Tegacorat | 1 | 0 | 1 |
| Delpacibart zotadirsen | 1 | 1 | 1 |
| Prednisolone | 1 | 0 | 1 |
| PRO051 | 0 | 4 | 7 |
| Losmapimod | 0 | 1 | 4 |
| Prednisone | 0 | 4 | 4 |
| Deramiocel | 0 | 1 | 3 |
| Ataluren | 0 | 3 | 3 |
| Edasalonexent | 0 | 2 | 3 |
Drug classes tested here PDE5 inhibitors 1 open · Corticosteroids 1 open
Coming up
Studies recruiting or running, from their records. “Main data collection” ends at the primary completion date, the sponsor’s own estimate, which often moves.
The 10 nearest
- Nov 2026Vasodilator and Exercise Study for DMD (VASO-REx) · University of Florida
- Nov 2026Self-Efficacy Enhancement Among Online Support Group of Primary Caregivers of Children With Neuro Muscular Dystrophy · Aga Khan University
- Dec 2026VirtualPark_Pediatric · Istituto di Sistemi e Tecnologie Industriali Intelligenti per il Manifatturiero Avanzato
- Dec 2026Observational Study to Observe Variations of Gait Parameters in Patients With Neuromuscular Diseases · IRCCS Eugenio Medea
- Dec 2026Assessment of a Portable Digital Device for Quantified Analysis of Markerless Walking in Volunteers With Neuromuscular Diseases or Asymptomatic Volunteers · Institut de Myologie, France
- Feb 2027A Phase 1/2 Study of VX-670 in Adult Participants With Myotonic Dystrophy 1 (DM1) · Vertex Pharmaceuticals Incorporated
- Mar 2027Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients · Satellos Bioscience, Inc.
- Jun 2027Brain Structure and Clinical Endpoints in Myotonic Dystrophy Type 2 · Wake Forest University Health Sciences
- Jun 2027Muscle Health Measurements Using Electrical Impedance Myography · Beth Israel Deaconess Medical Center
- Jun 2027iBCI Optimization for Veterans With Paralysis · VA Office of Research and Development
Who these studies take
Of the 38 Muscular Dystrophies studies recruiting now, 14 (37%) set no upper age limit and 15 (39%) stop at 75 or younger. 24 (63%) take children under 18. 0 (0%) are for women only and 8 (21%) for men only; 7 (18%) take healthy volunteers.
| Age | Women | Men |
|---|---|---|
| 10 | 15 (39%) | 21 (55%) |
| 18 | 28 (74%) | 33 (87%) |
| 30 | 27 (71%) | 30 (79%) |
| 40 | 27 (71%) | 30 (79%) |
| 50 | 27 (71%) | 30 (79%) |
| 65 | 25 (66%) | 28 (74%) |
| 75 | 21 (55%) | 24 (63%) |
| 85 | 16 (42%) | 19 (50%) |
Across all 224 studies, recruiting or not: 51% stop at 75 or younger and 43% at 65; 59% take children; 0% are for women only and 29% for men only; 20% take healthy volunteers. From each study’s registry entry; the criteria on its page decide.
How long Muscular Dystrophies studies take
Of 48 interventional studies with no phase under Muscular Dystrophies, half reached primary completion within 33 months of starting, counting those still running.
| Start to primary completion | Every sponsor | Industry | Non-industry |
|---|---|---|---|
| Interventional, no phase | 33 mo11–59 · 48 studies | — | 35 mo10–59 · 46 studies |
| Observational | 113 mo38–… · 37 studies | — | — |
Each figure is the month by which half the studies had reached primary completion, with the range in which the middle half did. Studies still running count until their last registry update; studies that stopped early are left out. Phase 1 includes early phase 1; observational means prospective or not stated, as retrospective and cross-sectional studies date a window of data rather than a study. How these figures are worked out
What changed recently
From the registry's own updates since Oct 15, 2026.
Newly registered2
Studies
Recruiting first, then most recently updated. Showing 50 of 224. Browse all 224 → or search them.
- A Phase 3 Study to Evaluate the Safety and Efficacy of AOC 1044 (Also Referred to as Delpacibart Zotadirsen) in Participants With DMD With Gene Mutations Amenable to Exon 44 SkippingRecruitingNCT07587242Phase 310 countries
- Personalized Disease Modeling for Rare Genetic MyopathiesEnrolling by invitationNCT079140491 country
- A Phase 2 Trial to Investigate the Efficacy, Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Tegacorat in Male Participants 4 to <7 Years of Age With Duchenne Muscular DystrophyNot yet recruitingNCT07911995Phase 2
- Assessment of a Portable Digital Device for Quantified Analysis of Markerless Walking in Volunteers With Neuromuscular Diseases or Asymptomatic VolunteersRecruitingNCT07321977Not applicable1 country
- Duchenne Electronic Health Record StudyRecruitingNCT076093941 country
- Study of Inherited Neurological DisordersRecruitingNCT000045682 countries
- Evaluating Long-term Use of a Pediatric Robotic Exoskeleton (P.REX/Agilik) to Improve Gait in Children With Movement DisordersRecruitingNCT05726591Not applicable1 country
- PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)RecruitingNCT07429240Phase 1/21 country
- Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) ExtensionRecruitingNCT077002251 country
- A Study of Long-term Safety and Efficacy of VX-670 in Participants With Myotonic Dystrophy Type IEnrolling by invitationNCT06926621Phase 28 countries
- Interfacing With NeuroTechnology to Expand Neural Throughput (INTENT)RecruitingNCT07521930Not applicable1 country
- Registry for Duchenne and Becker Muscular DystrophyRecruitingNCT074021222 countries
- Managed Access Program for Del-zota in Participants With DMD Mutations Amenable to Exon 44 SkippingAvailableNCT072507371 country
- Evaluating VM100 Nutritional Supplement for Improving Quality of Life in Duchenne Muscular Dystrophy PatientsRecruitingNCT07766980Phase 21 country
- Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMITRecruitingNCT065649742 countries
- Investigational Use of Neuromuscular UltrasoundRecruitingNCT052379731 country
- Sodium/Glucose Cotransporter-2 Inhibitors (SGLT2i) Therapy in Duchenne CardiomyopathyRecruitingNCT07172971Phase 11 country
- The United Kingdom Facioscapulohumeral Muscular Dystrophy Patient RegistryRecruitingNCT040015821 country
- Once Weekly Infant Corticosteroid Trial for DMDRecruitingNCT05412394Phase 41 country
- VirtualPark_PediatricRecruitingNCT07580365Not applicable1 country
- iBCI Optimization for Veterans With ParalysisNot yet recruitingNCT05470478Not applicable1 country
- Toward Ubiquitous Lower Limb Exoskeleton Use in Children and Young AdultsRecruitingNCT069981341 country
- Brain Structure and Clinical Endpoints in Myotonic Dystrophy Type 2Enrolling by invitationNCT058544331 country
- A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular DystrophyRecruitingNCT071279781 country
- Feasibility of the BrainGate2 Neural Interface System in Persons With TetraplegiaRecruitingNCT05724173Not applicable1 country
- BrainGate2: Feasibility Study of an Intracortical Neural Interface System for Persons With TetraplegiaRecruitingNCT00912041Not applicable1 country
- Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)RecruitingNCT07608432Phase 31 country
- Vasodilator and Exercise Study for DMD (VASO-REx)RecruitingNCT06290713Phase 21 country
- Nomad P-KAFO StudyRecruitingNCT05644522Not applicable1 country
- The Duchenne RegistryRecruitingNCT020697561 country
- ECoG BMI for Motor and Speech ControlRecruitingNCT03698149Not applicable1 country
- Amino Acids and Exercise in FSHDRecruitingNCT07543016Not applicable1 country
- A Multicenter Cohort Study of Duchenne and Becker Muscular Dystrophy in Western Chinese ChildrenNot yet recruitingNCT075119201 country
- Muscle Health Measurements Using Electrical Impedance MyographyRecruitingNCT075029891 country
- Modifying Factors in Striated Muscle LaminopathiesRecruitingNCT05394506Not applicable1 country
- Development of Quantitative Muscle Imaging as a Biomarker of Disease Endpoints in Myotonic DystrophyRecruitingNCT073628751 country
- Observational Study to Observe Variations of Gait Parameters in Patients With Neuromuscular DiseasesRecruitingNCT066668161 country
- Derivation of Human Induced Pluripotent Stem (iPS) Cells to Heritable Cardiac ArrhythmiasEnrolling by invitationNCT024134501 country
- Feasibility of the BrainGate2 Neural Interface System in Persons With Tetraplegia (BG-Speech-02)RecruitingNCT06094205Not applicable1 country
- Long-Term Development of Muscular Dystrophy Outcome AssessmentsRecruitingNCT059896201 country
- Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy RegistryRecruitingNCT000821081 country
- Genetics of Cardiovascular and Neuromuscular DiseaseRecruitingNCT001389311 country
- Fear of Falling in Muscular DystrophyRecruitingNCT07129954Not applicable1 country
- Clinical Trial Readiness for the DystroglycanopathiesRecruitingNCT003136771 country
- Follow-up Study on Female Carriers With DMD Gene VariantsEnrolling by invitationNCT057159571 country
- Spanish Natural History Study for LAMA2 Muscular DystrophyRecruitingNCT069241251 country
- Effectiveness of 5-week Digital Respiratory Practice in Children With Duchenne and Becker Muscular Dystrophies.Enrolling by invitationNCT06363526Not applicable1 country
- Rehabilitation in Muscular Dystrophies From the Hospital Facility to the Home: Pilot Project [RIMUDI]RecruitingNCT06378203Not applicable1 country
- Open-label Extension of the HOPE-2 TrialActive, not recruitingNCT04428476Phase 21 country
- A Study of Deramiocel (CAP-1002) in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular DystrophyActive, not recruitingNCT05126758Phase 31 country