CClinicalTrials.gg
Status unknownNCT03414918MAPAUpdated Jan 30, 2018

Macrolides for KCNJ5 - Mutated Aldosterone-Producing Adenoma (MAPA)

An interventional study of Clarithromycin in Hyperaldosteronism, sponsored by University Hospital Padova. Status unknown at 1 site in Italy. Open to participants aged 18 Years to 75 Years, including healthy volunteers. Per ClinicalTrials.gov, last updated 2018-01-30.

Sponsored by University Hospital Padova · Not applicable, Interventional, and Diagnostic

The sponsor has not verified this record recently (last verified Jan 2018), so the status shown — last known as Not yet recruiting — may be out of date.
Phase
Not applicable
Study type
Interventional
Enrollment
342
Allocation
Not applicable
Ages
18 Years to 75 Years
Sex
All
01

Study summary

This study evaluates if :

1 ) the plasma aldosterone concentration and blood pressure change in response to roxithromycin could be useful for the screening of PA patients carrying a KCNJ5-mutated APA; 2) the change of PAC in response to mutated KCNJ5 channel is truly occurring in KCNJ5-mutated APA.

Read the detailed description

Aldosterone-producing adenoma (APA) cause primary aldosteronism (PA), the main curable cause of endocrine hypertension, is in up to 66% of all cases investigated with adrenal vein sampling (AVS). Mutations in the KCNJ5 potassium channel involve up to 70% of APA and cause the most florid PA phenotypes. The recent finding that macrolide antibiotics specifically inhibit in vitro the altered function of mutated KCNJ5 channels has opened new horizons for the diagnosis and treatment of APA with KCNJ5 mutations in that it can allow identification and target treatment of PA patients harbouring a mutated APA. Thus, the aim of the present study was to investigate if clarithromycin and roxithromycin, two macrolides that potently blunt mutated Kir3.4 channel function in vitro, affect plasma aldosterone concentration in adrenal vein blood during AVS and in peripheral blood, respectively, in PA patients with a mutated APA.

The investigators designed two proof of concept studies. In study A: consecutive patients with an unambiguous biochemical evidence of PA will be exposed to a single dose of 250 mg clarithromycin during AVS, to assess its effect on the relative aldosterone secretion index (RASI) in adrenal vein blood from the gland with and without APA. In study B: consecutive hypertensive patients submitted to the work-up for hypertension will receive a single oral dose of 150 mg roxithromycin. The experimental endpoints will be the change induced by roxithromycin of plasma aldosterone concentration (PAC) and other steroids, direct active renin concentration (DRC), serum K+, systolic and diastolic blood pressure.

The investigators expect to prove that: i) clarithromycin allows identification of mutated APA before adrenalectomy and sequencing of tumour DNA; ii) the acute changes of PAC, DRC, and blood pressure in peripheral venous blood after roxithromycin can be a proxy for the presence of an APA with somatic mutations.

02

Conditions studied

  • Hyperaldosteronism

Keywords

  • Macrolides, KCNJ5 potassium channel, aldosteronism
03

Who can participate

Ages eligible
18 Years to 75 Years
Sexes eligible
All
Accepts healthy volunteers
Yes

Inclusion criteria

  • A signed and dated informed consent form
  • A diagnosis of hypertension defined either as:

Use of antihypertensive drug (s) Arterial hypertension: in untreated patients this must be confirmed by daytime ambulatory blood pressure monitoring (ABPM), or home blood pressure monitoring, with blood pressure higher or equal to 135 mmHg for systolic blood pressure and/or higher or equal to 85 mmHg for diastolic blood pressure.

Normal observation of ECG QT interval.

Exclusion criteria

Exclusion Criteria:

  • History of allergy/intolerance to any macrolides;
  • Refusal of the patient to undergo dynamic testing;
  • Refusal of the patient to undergo AVS and/or contraindications to the general anesthesia that is required for laparoscopic adrenalectomy (for objective 2);
  • Suspicion of cortisol-aldosterone co-secreting adenoma
  • Pregnancy
  • Family history of sudden death
  • Family history of syncope
  • Family history of Long QT syndrome and or torsade de point
  • Congenital or drug-induced Long QT syndrome
04

Study design

Phase
Not applicable
Primary purpose
Diagnostic
Allocation
Not applicable
Intervention model
Single group
Masking
None (open label)
Enrollment
342 participants (estimated)

Study arms

  • Experimental
    Clarithromycin

    250 mg clarithromycin diluted in 250 ml saline will be administered as a slow infusion (45 min) in a peripheral vein during AVS. This dose of clarithromycin should yield peak plasma concentrations of 2.78 mcg/mL (on average)13, which are higher than the IC50 measured in vitro (0.53-1.29 mcg/mL).

    Drug: Clarithromycin

Interventions

  • DrugClarithromycin

    Hypertensive patients will be exposed to a single oral dose of 150 mg of roxithromycin. A 150-mg oral dose of roxithromycin should yield peak plasma concentrations of 5-12 mcg/mL14, which are higher than the IC50 measured in vitro (0.18-0.53 mcg/mL).

    Also known as: roxithromycin

05

What researchers measure

Primary outcomes

  1. Study 1: Change in Relative Aldosterone Secretion Index (RASI).

    Within-patient change from baseline of the RASI in adrenal vein blood draining the gland with and without the APA.

    Time frame: Baseline and after 45min clarithromycin infusion.

  2. Study 2: Change in plasma aldosterone concentration (PAC).

    Within-patient change from baseline of PAC in peripheral venous blood in patients undergoing screening for PA.

    Time frame: Baseline and after 60 and 120 minutes roxitromycin administration

06

Study locations

1 site
  • Department of Medicine - DIMED, University of Padova, Italy
    Padova, Italy
    • Gian Paolo Rossi, MD · Principal investigator
07

References and documents

Publications

  • Rossi GP, Belfiore A, Bernini G, Desideri G, Fabris B, Ferri C, Giacchetti G, Letizia C, Maccario M, Mallamaci F, Mannelli M, Montemurro D, Palumbo G, Rizzoni D, Rossi E, Semplicini A, Agabiti-Rosei E, Pessina AC, Mantero F; PAPY Study Investigators. Prospective evaluation of the saline infusion test for excluding primary aldosteronism due to aldosterone-producing adenoma. J Hypertens. 2007 Jul;25(7):1433-42. doi: 10.1097/HJH.0b013e328126856e. PubMed 17563566 ↗
  • Choi M, Scholl UI, Yue P, Bjorklund P, Zhao B, Nelson-Williams C, Ji W, Cho Y, Patel A, Men CJ, Lolis E, Wisgerhof MV, Geller DS, Mane S, Hellman P, Westin G, Akerstrom G, Wang W, Carling T, Lifton RP. K+ channel mutations in adrenal aldosterone-producing adenomas and hereditary hypertension. Science. 2011 Feb 11;331(6018):768-72. doi: 10.1126/science.1198785. PubMed 21311022 ↗
  • Scholl UI, Abriola L, Zhang C, Reimer EN, Plummer M, Kazmierczak BI, Zhang J, Hoyer D, Merkel JS, Wang W, Lifton RP. Macrolides selectively inhibit mutant KCNJ5 potassium channels that cause aldosterone-producing adenoma. J Clin Invest. 2017 Jun 30;127(7):2739-2750. doi: 10.1172/JCI91733. Epub 2017 Jun 12. PubMed 28604387 ↗
  • Caroccia B, Prisco S, Seccia TM, Piazza M, Maiolino G, Rossi GP. Macrolides Blunt Aldosterone Biosynthesis: A Proof-of-Concept Study in KCNJ5 Mutated Adenoma Cells Ex Vivo. Hypertension. 2017 Dec;70(6):1238-1242. doi: 10.1161/HYPERTENSIONAHA.117.10226. Epub 2017 Oct 9. PubMed 28993452 ↗
  • Rossitto G, Battistel M, Barbiero G, Bisogni V, Maiolino G, Diego M, Seccia TM, Rossi GP. The subtyping of primary aldosteronism by adrenal vein sampling: sequential blood sampling causes factitious lateralization. J Hypertens. 2018 Feb;36(2):335-343. doi: 10.1097/HJH.0000000000001564. PubMed 28957852 ↗

Individual participant data

Plan to share: Undecided — The decision to share the data will be taken upon completion of the study and publication of the results.

08

Registry details

Key details

Study ID
NCT03414918
Lead sponsor
University Hospital Padova
Collaborators
DMG Paris Descartes
Responsible party
Gian Paolo Rossi, MD, FAHA, FACC (Director of Arterial Hypertension Unit - DIMED, University Hospital Padova) — Principal investigator
First posted
Jan 30, 2018
Start date
Mar 2018 (estimated)
Primary completion
Jan 2019 (estimated)
Completion
Jan 2020 (estimated)
Last update
Jan 30, 2018

Study contacts

Gian Paolo Rossi, MD
Contact
gianpaolo.rossi@unipd.it
+39-049-8212263
Gian Paolo Rossi, MD
principal investigator · University of Padova

Oversight

Data monitoring committee
No
FDA-regulated drug
No
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

Not currently enrolling

This study is status unknown, as verified in Jan 2018. You cannot join it, but the record below documents what was studied.

Follow this study

Get an email when the registry record changes — status, dates, results — or when someone posts here.

Sign in to follow

Discussion

Questions and observations about this study, from anyone following it. Not medical advice, and not a channel to the study team — their contact details are on the registry record.

Sign in to join the discussion. Reading takes no account; posting does. You choose a display name, and a pseudonym is the default.

Nothing here yet. If you are running this trial, taking part in it, or weighing whether to, this is the place to say so.

Start the discussion