Pancytopenia clinical trials
The registry lists 63 studies for Pancytopenia across more than 10 countries. 11 are recruiting or about to start. Per ClinicalTrials.gov, last updated 2026-09-16.
Status
- Completed
- 30
- Status unknown
- 9
- Recruiting
- 7
- Terminated
- 6
- Not yet recruiting
- 3
- Active, not recruiting
- 3
Phase
- Phase 2
- 29
- Phase 1
- 16
- Phase 3
- 5
- Early Phase 1
- 2
- Phase 4
- 1
Where
- United States
- 35
- China
- 7
- Australia
- 3
- Korea, Republic of
- 2
- Israel
- 1
- Canada
- 1
Who runs them
National Heart, Lung, and Blood Institute (NHLBI) (10) · Assiut University (3) · Institute of Hematology & Blood Diseases Hospital, China (2) · Children's Hospital of Philadelphia (2) · Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins (2) · Peter MacCallum Cancer Centre, Australia (2) · Columbia University (2) · Emory University (2)
Studies
Recruiting first, then most recently updated. Showing 50 of 63 — search for more.
- Clinical, Hematological and Pathological Profile of PancytopeniaNot yet recruitingNCT07785726
- A Phase 1/2 Study to Evaluate the Safety and Efficacy of Dibotatug (DR-01) in Adults With Bone Marrow Failure SyndromesNot yet recruitingNCT07712562Phase 1/21 country
- Shwachman-Diamond Syndrome Global Patient Survey and Partnering PlatformRecruitingNCT069999541 country
- CD7 CAR-T Cell Sequential Allo-HSCT for Non-malignant Blood and Immune System DiseasesRecruitingNCT06787560Early Phase 11 country
- Avatrombopag for Platelet Recovery Post-UCBT in Patients With Bone Marrow Failure DiseaseRecruitingNCT058233761 country
- Diagnosis and Phenotype Characterisation Using Genomics in Patients With Inherited Bone Marrow Failure (IBMDx Study)RecruitingNCT051967891 country
- REscuing Bone Marrow Function in Patients with AplaStic AnaEmia and Bone Marrow FaiLure Post AllogEneiC Transplantation 2Not yet recruitingNCT06607367Phase 1/21 country
- Rollover Study From EXG-US-01Enrolling by invitationNCT05868499Phase 11 country
- European Rare Blood Disorders Platform (ENROL)RecruitingNCT062505951 country
- Clinical Study of UCB Combined With UC-MSCs in the Treatment of Bone Marrow Failure DisordersRecruitingNCT05794425Phase 1/21 country
- Mutations and Phenotypes of Unclassifiable Inherited Bone Marrow Failure SyndromesRecruitingNCT054365871 country
- Eltrombopag for Fanconi AnemiaActive, not recruitingNCT03206086Phase 21 country
- Eltrombopag With Standard Immunosuppression for Severe Aplastic AnemiaActive, not recruitingNCT01623167Phase 1/21 country
- Severe Immune Cytopenia Registry Www.Sic-reg.OrgCompletedNCT035767421 country
- A Clinical Trial of CK0801 (a New Drug) in Patients With Bone Marrow Failure Syndrome (BMF)Active, not recruitingNCT03773393Phase 11 country
- Observational of PNH Type Cells in Korean Patients With Bone Marrow Failure Syndrome and Having Hemolytic PNHCompletedNCT03460301
- Risk-Adapted Allogeneic Stem Cell Transplantation For Mixed Donor Chimerism In Patients With Non-Malignant DiseasesCompletedNCT01019876Phase 2/31 country
- TPO-Mimetic Use in Children for Hematopoietic FailureCompletedNCT04478227Early Phase 11 country
- Trial of Haploidentical Stem Cell Transplantation for Haematological CancersCompletedNCT01597219Phase 21 country
- Response to SARS-CoV-2 Vaccine in Stem Cell Transplant and Cellular Therapy PatientsCompletedNCT047237061 country
- Safety Study of Gene Modified Donor T Cell Infusion After Stem Cell Transplant for Non-Malignant DiseasesTerminatedNCT02231710Phase 11 country
- Conditioning Regimen for Allogeneic Hematopoietic Stem-Cell TransplantationCompletedNCT03513328Phase 1/21 country
- Nandrolone Decanoate in the Treatment of TelomeropathiesCompletedNCT02055456Phase 1/21 country
- Transplantation of Partially Mismatched Related or Matched Unrelated Bone Marrow for Patients With Refractory Severe Aplastic AnemiaCompletedNCT02224872Phase 21 country
- Phase I/II Pilot Study of Mixed Chimerism to Treat HemoglobinopathiesWithdrawnNCT01419704Phase 1/21 country
- MNCs for Bone Marrow Failure After Malignant Diseases Children ChemotherapyStatus unknownNCT05628272Not applicable1 country
- Spectrum of Hematological Disorders in PediatricsStatus unknownNCT05473650
- NMA Haplo or MUD BMT for Newly Diagnosed Severe Aplastic AnemiaCompletedNCT02833805Phase 21 country
- T-cell Depleted Alternative Donor TransplantationTerminatedNCT00968864Phase 21 country
- Peripheral Blood Stem Cell Transplantation Using the CliniMACS DeviceCompletedNCT01071226Not applicable1 country
- Pancytopenia Related to PARP Inhibitors (PancytoRIB)CompletedNCT047746271 country
- The Evaluating Multidisciplinary Bone Marrow Failure Care in Bone Marrow Failure and Related Disorders.Status unknownNCT048196071 country
- A Pilot Study of Fludarabine Plus Cyclophosphamide in Refractory Severe Aplastic AnemiaCompletedNCT01187017Phase 1/21 country
- Expanded Access Protocol (EAP) Using the CliniMACS® Device for Pediatric Haplocompatible Donor Stem Cell TransplantNo longer availableNCT012000171 country
- Cytokine Gene Polymorphisms in Bone Marrow FailureCompletedNCT000856701 country
- Collection of Blood From Patients With PancytopeniaCompletedNCT000012141 country
- Pilot Trial of Clofarabine Added to Standard Busulfan and Fludarabine for Conditioning Prior to Allogeneic Hematopoietic Cell TransplantationTerminatedNCT01596699Phase 21 country
- Identification of Autoantibodies and Autoantigens in the Cerebrospinal Fluid of Patients With Spinal Cord TraumaWithdrawnNCT03249129
- CD34+ Stem Cell Infusion to Augment Graft FunctionTerminatedNCT01856582Phase 21 country
- Sirolimus for Autoimmune Disease of Blood CellsCompletedNCT00392951Phase 1/21 country
- CD34+Selection for Partially Matched Family or Matched Unrelated Adult Donor TransplantCompletedNCT01049854Phase 21 country
- Patient-Driven Transfusion Thresholds in Hematological Disorders: A Pilot StudyWithdrawnNCT03086252Not applicable1 country
- Management of Childhood PancytopeniaStatus unknownNCT03521947
- Reduced Intensity Conditioning Using CD3+/CD19+ Depletion for Non Malignant Transplantable DiseasesCompletedNCT02277639Phase 21 country
- Umbilical Cord Blood Transplantation As Treatment Of Adult Patients With Hematologic DisordersCompletedNCT00897260Not applicable1 country
- Stem Cell Transplant for Bone Marrow Failure SyndromesCompletedNCT00176878Phase 2/31 country
- G-CSF PMRD: Granulocyte Colony Stimulating Factor (G-CSF) Stimulated Bone Marrow and In Vivo T-Cell Depletion in Patients With Hematologic Malignancies or Bone Marrow Failure SyndromeTerminatedNCT00228813Not applicable1 country
- Gene Therapy for the Treatment of Fanconi's Anemia Type CCompletedNCT00001399Phase 11 country
- Three Immunosuppressive Treatment Regimens for Severe Aplastic AnemiaCompletedNCT00260689Phase 21 country
- Cyclophosphamide Plus Cyclosporine in Treatment-Naive Severe Aplastic AnemiaCompletedNCT01193283Phase 1/21 country