Muscular Dystrophy, Duchenne: all 480 studies

Page 3 of 5. Open to participants first (109), then studies with results posted, then the rest; newest registration first within each.

• Safety Study of Transvenous Limb Perfusion in Human Muscular DystrophyCompletedNCT00873782Phase 1Results posted
• Phase 2B Extension Study of Ataluren (PTC124) in Duchenne/Becker Muscular Dystrophy (DMD/BMD)TerminatedNCT00847379Phase 2Results posted
• Dose-Ranging Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy (DMD) PatientsCompletedNCT00844597Phase 1/2Results posted
• Phase 2a Extension Study of Ataluren (PTC124) in Duchenne Muscular Dystrophy (DMD)TerminatedNCT00759876Phase 2Results posted
• Efficacy and Tolerability of Idebenone in Boys With Cardiac Dysfunction Associated With Duchenne Muscular DystrophyCompletedNCT00654784Phase 2Results posted
• Phase 2B Study of PTC124 (Ataluren) in Duchenne/Becker Muscular Dystrophy (DMD/BMD)CompletedNCT00592553Phase 2Results posted
• CoQ10 and Prednisone in Non-Ambulatory DMDTerminatedNCT00308113Phase 3Results posted
• Safety and Efficacy Study of Antisense Oligonucleotides in Duchenne Muscular DystrophyCompletedNCT00159250Phase 1/2Results posted
• Relation Between Muscle Architecture and Functional Ability in Children With Duchenne Muscular DystrophyCompletedNCT07437378
• Self-Efficacy Enhancement Among Online Support Group of Primary Caregivers of Children With Neuro Muscular DystrophyActive, not recruitingNCT07356063Not applicable
• A Trial to Investigate the Safety and Pharmacokinetics of GRT6019 in Healthy Male ParticipantsCompletedNCT07347548Phase 1
• Virtual Reality and Whole Body Vibration on Muscle Strength and Balance in Children With DMDCompletedNCT07338812Not applicable
• A Trial to Investigate Safety and Pharmacokinetics of GRT6019, Including Food Effect, in Healthy Male ParticipantsCompletedNCT07317063Phase 1
• Phase 2 Study of SAT-3247 in Pediatric Ambulatory PatientsActive, not recruitingNCT07287189Phase 2
• A Study to Evaluate the Safety and Tolerability of RAG-18 in Pediatric Patients With Duchenne Muscular DystrophyActive, not recruitingNCT07282652Early Phase 1
• Gut Peptides and Bone Remodeling in Children With Neuromuscular DisordersTerminatedNCT07254988Not applicable
• Investigation of the Effects of Functional Inspiratory Muscle Training Applied With Tele-Rehabilitation on Respiratory and Functional Parameters and Quality of Life in Children With Duchenne Muscular Dystrophy: Randomized Controlled StudyCompletedNCT07172737Not applicable
• Estimation of Non-Reimbursable Costs for Patients With Duchenne Muscular Dystrophy in FranceCompletedNCT06861270
• A Study of PGN-EDO51 or Placebo in People With Duchenne Muscular Dystrophy Amenable to Exon 51-Skipping TreatmentWithdrawnNCT06833931Phase 2
• A Study to Investigate the Safety and Biodistribution of a Single Intrathecal (IT) Injection of INS1201 in Ambulatory Males With Duchenne Muscular Dystrophy (DMD)Active, not recruitingNCT06817382Phase 1
• A Study on Safety and Effectiveness of Long-term Treatment With Vamorolone in Boys With Duchenne Muscular DystrophyActive, not recruitingNCT06713135Phase 4
• Nutritional Status and Therapy in DMD PatientsCompletedNCT06682585Not applicable
• A Gene Transfer Therapy to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) Following Therapeutic Plasma Exchange (Plasmapheresis) in Participants With Duchenne Muscular Dystrophy (DMD) and Pre-existing Antibodies to AAVrh74TerminatedNCT06597656Phase 1
• An Open-label, Multidose Dose-escalation Study to Understand the Safety of CRISPR Gene-editing Therapy and Its Long-Lasting Effects in DMD Patients (MUSCLE)Active, not recruitingNCT06594094Early Phase 1
• Study of UC-MSC in DMD PatientsActive, not recruitingNCT06579352Phase 2
• First in Human SAD/MAD Safety and PK Study With Adult DMD Safety and PK CohortCompletedNCT06565208Early Phase 1
• A Study to Assess the Efficacy and Safety of Satralizumab in Duchenne Muscular Dystrophy (DMD)Active, not recruitingNCT06450639Phase 2
• Hydrotherapy in Duchenne Muscular Dystrophy (DMD)Active, not recruitingNCT06445985Not applicable
• A Study to Evaluate the Safety and Tolerability of GEN6050X in Duchenne Muscular Dystrophy.Active, not recruitingNCT06392724Early Phase 1
• Upper Extremity Muscle Strength, Balance and Functional Skills in DMDCompletedNCT06379906
• The Effect of a Muscle-mimicking, Fabric-type Shoulder Orthosis on Functional Movements of the Upper Limb in Patients With Neuromuscular DisorderCompletedNCT06363357Not applicable
• Tele-assessment of Functional Performance and Quality of Life in Patients With Duchenne Muscular Dystrophy: Validity and Reliability StudyCompletedNCT06295718
• A Phase 1/2 Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of BMN 351 in Participants With Duchenne Muscular DystrophyActive, not recruitingNCT06280209Phase 1/2
• DMD- Interactive Virtual Reality StudyCompletedNCT06274983Not applicable
• Ph2 Open-label Study of AOC 1044 in Duchenne Muscular Dystrophy Participants With Mutations Amenable to Exon44 SkippingActive, not recruitingNCT06244082Phase 2
• A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) Following Imlifidase Infusion in Participants With Duchenne Muscular Dystrophy (DMD) Determined to Have Pre-existing Antibodies to Recombinant Adeno-Associated Virus Serotype (rAAVrh74)TerminatedNCT06241950Phase 1
• Effectiveness of Aquatic Therapy in Children With Duchenne and Becker Muscular DystrophyCompletedNCT06186310Not applicable
• Validity and Reliability of the 6 Minute Pegboard Ring TestCompletedNCT06174025
• A Gene Delivery Study to Evaluate the Safety and Expression of Delandistrogene Moxeparvovec in Participants Under the Age of Four With Duchenne Muscular Dystrophy (DMD)Active, not recruitingNCT06128564Phase 2
• A Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of Single Intravenous Infusion of JWK007 in Patients With Duchenne Muscular Dystrophy (DMD)Active, not recruitingNCT06114056Phase 1
• Remote Physiotherapy to Protect Physical Health in Duchenne Muscular DystrophyCompletedNCT06103006Not applicable
• Phase 2 Study of EDG-5506 in Children and Adolescents With Duchenne Muscular Dystrophy Previously Treated With Gene TherapyActive, not recruitingNCT06100887Phase 2
• A Study Of PGN-EDO51 In Participants With Duchenne Muscular Dystrophy Amenable To Exon 51-Skipping TreatmentTerminatedNCT06079736Phase 2
• NSAA NON-Interventional Study ProtocolCompletedNCT06054971
• NS-050/NCNP-03 in Boys With DMD (Meteor50)Active, not recruitingNCT06053814Phase 1/2
• NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD)Active, not recruitingNCT05996003Phase 2
• Peabody Developmental Motor Scaling In Children With Period Duchenne Muscular DystrophyCompletedNCT05990608
• A Study of ATL1102 or Placebo in Participants with Non-ambulatory Duchenne Muscular DystrophyTerminatedNCT05938023Phase 2
• A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Non-Ambulatory and Ambulatory Participants With Duchenne Muscular Dystrophy (DMD)Active, not recruitingNCT05881408Phase 3
• Bicycle Training on Ventilatory Functions in Duchenne Muscular DystrophyStatus unknownNCT05849688Not applicable
• Study of Genotype and Phenotype Characterization in Duchenne Muscular Dystrophy With Small MutationsCompletedNCT05833633
• Duchenne Muscular Dystrophy Video Assessment RegistryCompletedNCT05712447
• AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD)Active, not recruitingNCT05693142Phase 2/3
• A Study to Understand the Long-term Safety and Effects of an Experimental Gene Therapy for Duchenne Muscular Dystrophy.TerminatedNCT05689164Phase 3
• Trunk Oriented Exercises Versus Whole-body Vibration for Duchenne Muscular DystrophyCompletedNCT05688072Not applicable
• AFFINITY BEYOND: Anti-AAV8 Antibody Assessment Study of Males With DMDActive, not recruitingNCT05683379
• Study of AOC 1044 in Healthy Adult Volunteers and Participants With Duchenne Muscular Dystrophy (DMD) Mutations Amenable to Exon 44 SkippingCompletedNCT05670730Phase 1/2
• Neuropsychological Profiles of Children With Duchenne Muscular Dystrophy and Its Effects on Motor FunctionsStatus unknownNCT05661071
• Evaluation of Home Based Assessments on Participants With DMDCompletedNCT05657938
• Physical Activity Level and Cognitive Functions in Children With Duchenne Muscular DystrophyStatus unknownNCT05641805
• Dual Task in Duchenne Muscular DystrophyCompletedNCT05575648Not applicable
• Quality and Independence of Gait Classification Scale for DMD (QIGS-DMD)CompletedNCT05564962
• Motor Imagery in Duchenne Muscular DystrophyCompletedNCT05559710
• Natural History of Duchenne Muscular Dystrophy Cardiomyopathy (DMD-CMP)WithdrawnNCT05558813Not applicable
• Cultural Adaptation, Validity, and Reliability of the Turkish Version of North Star Ambulatory AssessmentCompletedNCT05549999
• A Study of EDG-5506 in Children With Duchenne Muscular Dystrophy (LYNX)Active, not recruitingNCT05540860Phase 2
• Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-251 in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51 SkippingActive, not recruitingNCT05524883Phase 1/2
• E-monitoring of PULMonary Function in Patients With Duchenne Muscular Dystrophy at Home"Status unknownNCT05516745Not applicable
• Treatment of a Single Patient With CRD-TMH-001CompletedNCT05514249Phase 1
• Examination of Lower Urinary System Symptoms With Duchenne Muscular DystrophyCompletedNCT05464446
• Postural and Anthropometric Properties of Foot and Ankle of Patients With DMDCompletedNCT05436210
• Study of Fordadistrogene Movaparvovec in Early Stage Duchenne Muscular DystrophyTerminatedNCT05429372Phase 2
• Schulze Muscular Dystrophy Ability Clinical StudyStatus unknownNCT05409079Not applicable
• Determine the Safety and Dose of EN001 in Patients With Duchenne Muscular Dystrophy(DMD)CompletedNCT05338099Phase 1
• Bicycle Ergometer Training in Duchenne Muscular DystrophyCompletedNCT05330195Not applicable
• Physical Therapy Treatment on Children and Adolescents With Neurological PathologiesCompletedNCT05313295Not applicable
• Telerehabilitation in Duchenne Muscular DystrophyCompletedNCT05305976Not applicable
• Phase 2 Study of EDG-5506 in Becker Muscular Dystrophy (GRAND CANYON)CompletedNCT05291091Phase 2
• Effects of Low-level Mechanical Vibration on Bone Density in Ambulant Children Affected by Duchenne Muscular DystrophyCompletedNCT05281120Not applicable
• Assessment of Neurodevelopmental Needs in Duchenne Muscular DystrophyCompletedNCT05280730
• Reliability and Validity of the Turkish Version of the Upper Limb Short Questionnaire in Duchenne Muscular DystrophyCompletedNCT05274555
• Defining Endpoints in Becker Muscular DystrophyActive, not recruitingNCT05257473
• Development of a New Instrument to Evaluate Gait Characteristics of Individuals With Duchenne Muscular DystrophyCompletedNCT05244395Not applicable
• Effects of Parental Influence on Physical Activity Level and Participation in Children With Duchenne Muscular DystrophyCompletedNCT05209087
• Tadalafil as Adjuvant Therapy for DMDActive, not recruitingNCT05195775Phase 2/3
• Extension Study of NS-089/NCNP-02 in DMDActive, not recruitingNCT05135663Phase 2
• A Study of Deramiocel (CAP-1002) in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular DystrophyActive, not recruitingNCT05126758Phase 3
• Public AttitudesTowards SMA and DMD Awareness, Newborn and Carrier Screening and Physiotherapy PracticesStatus unknownNCT05110885
• Comprehensive Study of Duchenne Muscular Dystrophy at Sohag University HospitalStatus unknownNCT05029232Not applicable
• CureDuchenne Link®: A Resource for ResearchCompletedNCT04972604
• Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53)Active, not recruitingNCT04906460Phase 1/2
• The Effect of Telerehabilitation of Patients With Duchenne Muscular DystrophyStatus unknownNCT04782440Not applicable
• Study to Assess the Safety and Efficacy of Viltolarsen in Ambulant Boys With DMD (RACER53-X)Active, not recruitingNCT04768062Phase 3
• Heart Rate Variability in Individuals With Duchenne Muscular DystrophyCompletedNCT04740554
• An Open-Label Study of Golodirsen in Non-Ambulant Patients With Duchenne Muscular DystrophyTerminatedNCT04708314Phase 4
• Long-term Use of Viltolarsen in Boys With Duchenne Muscular Dystrophy in Clinical Practice (VILT-502)Active, not recruitingNCT04687020Phase 4
• The Effects of Trunk Exercises on Upper Extremity and Respiratory Functions in DMDCompletedNCT04669847Not applicable
• Brain Involvement in Dystrophinopathies Part 2CompletedNCT04668716
• Heart Rate Variability in Duchenne Muscular Dystrophy During Computer TaskCompletedNCT04607824
• A Phase 3 Study of TAS-205 in Patients With Duchenne Muscular Dystrophy（REACH-DMD）CompletedNCT04587908Phase 3

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