Muscular Dystrophy, Duchenne: all 480 studies

Page 2 of 5. Open to participants first (109), then studies with results posted, then the rest; newest registration first within each.

• A Registered Cohort Study on Duchenne Muscular DystrophyRecruitingNCT04012671
• Natural History of Duchenne Muscular DystrophyRecruitingNCT03882827
• Expanded Access Protocol for Boys With Duchenne Muscular DystrophyAvailableNCT03863119
• Parent and Infant Inter(X)Action Intervention (PIXI)Enrolling by invitationNCT03836300Not applicable
• Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability StudyRecruitingNCT03373968Phase 2/3
• Derivation of Human Induced Pluripotent Stem (iPS) Cells to Heritable Cardiac ArrhythmiasEnrolling by invitationNCT02413450
• The Duchenne RegistryRecruitingNCT02069756
• Magnetic Resonance Imaging and Biomarkers for Muscular DystrophyRecruitingNCT01484678
• Molecular Analysis of Patients With Neuromuscular DiseaseRecruitingNCT00390104
• Halt cardiomyOPathy progrEssion in Duchenne (HOPE-OLE)CompletedNCT06304064Phase 2Results posted
• A Study to Assess Vamorolone in Boys Ages 2 to <4 Years and 7 to <18 Years With Duchenne Muscular Dystrophy (DMD)CompletedNCT05185622Phase 2Results posted
• A Study to Assess Vamorolone in Becker Muscular Dystrophy (BMD)CompletedNCT05166109Phase 2Results posted
• A Study of EDG-5506 in Adult Males With Becker Muscular DystrophyCompletedNCT05160415Phase 1Results posted
• A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD)CompletedNCT05096221Phase 3Results posted
• Study to Assess the Safety, Tolerability, and Efficacy of Viltolarsen in Ambulant and Non-Ambulant Boys With DMD (Galactic53)CompletedNCT04956289Phase 2Results posted
• Placebo-Corrected Effects of Therapeutic Dose (100 mg) and Supratherapeutic Dose (300 mg) of ITF2357 (Givinostat) and Moxifloxacin on QT/QTC IntervalCompletedNCT04821063Phase 1Results posted
• Phase 3 Trial of Pamrevlumab or Placebo in Combination With Systemic Corticosteroids in Participants With Ambulatory DMDTerminatedNCT04632940Phase 3Results posted
• Open-label Extension of the HOPE-2 TrialActive, not recruitingNCT04428476Phase 2Results posted
• Phase 3 Trial of Pamrevlumab or Placebo With Systemic Corticosteroids in Participants With Non-ambulatory Duchenne Muscular Dystrophy (DMD)TerminatedNCT04371666Phase 3Results posted
• A Study to Evaluate the Safety and Pharmacokinetics of Ataluren in Participants From ≥6 Months to <2 Years of Age With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)CompletedNCT04336826Phase 2Results posted
• Twice Weekly Steroids and Exercise as Therapy for DMDCompletedNCT04322357Phase 2Results posted
• Study to Evaluate the Safety and Efficacy of PF-06939926 for the Treatment of Duchenne Muscular DystrophyActive, not recruitingNCT04281485Phase 3Results posted
• AAV9 U7snRNA Gene Therapy to Treat Boys With DMD Exon 2 Duplications.CompletedNCT04240314Phase 1/2Results posted
• A 48-Week, Open Label, Study to Evaluate the Efficacy and Safety of AMONDYS 45, EXONDYS 51, VYONDYS 53 in Subjects With DuchenneMuscular Dystrophy Carrying Eligible DMD Duplications.CompletedNCT04179409Phase 2Results posted
• Study to Assess the Efficacy and Safety of Viltolarsen in Ambulant Boys With DMD (RACER53)CompletedNCT04060199Phase 3Results posted
• Weekly Steroids in Muscular DystrophyCompletedNCT04054375Phase 2Results posted
• A Study to Evaluate Safety, Tolerability, and Efficacy of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) Who Have Completed Study 4658-102 (NCT03218995)TerminatedNCT03985878Phase 2Results posted
• Efficacy and Safety Study of WVE-210201 (Suvodirsen) With Open-label Extension in Ambulatory Patients With Duchenne Muscular DystrophyTerminatedNCT03907072Phase 2/3Results posted
• A Study to Assess Dystrophin Levels in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) Who Have Been Treated With AtalurenCompletedNCT03796637Phase 2Results posted
• Spironolactone Versus Prednisolone in DMDTerminatedNCT03777319Phase 1Results posted
• A Randomized, Double-blind, Placebo-controlled Study of Delandistrogene Moxeparvovec (SRP-9001) for Duchenne Muscular Dystrophy (DMD)CompletedNCT03769116Phase 1/2Results posted
• A Natural History Study In Chinese Male Patients With Duchenne Muscular DystrophyCompletedNCT03760029Not applicableResults posted
• Phase III Study of Edasalonexent in Boys With Duchenne Muscular DystrophyCompletedNCT03703882Phase 3Results posted
• An Open-Label Extension Study for Patients With Duchenne Muscular Dystrophy Who Participated in Studies of SRP-5051 (Vesleteplirsen)TerminatedNCT03675126Phase 1/2Results posted
• A Study to Assess Dystrophin Levels in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)CompletedNCT03648827Phase 2Results posted
• An Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular DystrophyTerminatedNCT03532542Phase 3Results posted
• Use of Dynamic Arm Supports to Promote Activities of Daily Living in Individuals With DMDTerminatedNCT03531788Not applicableResults posted
• A Study to Assess the Efficacy and Safety of Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)CompletedNCT03439670Phase 2Results posted
• A Study of CAP-1002 in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular DystrophyCompletedNCT03406780Phase 2Results posted
• A Study to Assess the Efficacy and Safety of MNK-1411 in Duchenne Muscular DystrophyTerminatedNCT03400852Phase 2Results posted
• A Gene Transfer Therapy Study to Evaluate the Safety of Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD)CompletedNCT03375164Phase 1/2Results posted
• A Study to Evaluate the Safety and Tolerability of PF-06939926 Gene Therapy in Duchenne Muscular DystrophyTerminatedNCT03362502Phase 1Results posted
• Gene Transfer Clinical Trial to Deliver rAAVrh74.MCK.GALGT2 for Duchenne Muscular DystrophyCompletedNCT03333590Phase 1/2Results posted
• Clinical Study to Evaluate the Efficacy and Safety of Givinostat in Ambulant Patients With Becker Muscular DystrophyCompletedNCT03238235Phase 2Results posted
• (-)- Epicatechin Becker Muscular DystrophyCompletedNCT03236662Phase 2Results posted
• Study of Eteplirsen in Young Participants With Duchenne Muscular Dystrophy (DMD) Amenable to Exon 51 SkippingCompletedNCT03218995Phase 2Results posted
• Long-Term Outcomes of Ataluren in Duchenne Muscular DystrophyCompletedNCT03179631Phase 3Results posted
• Extension Study of NS-065/NCNP-01 in Boys With Duchenne Muscular Dystrophy (DMD)CompletedNCT03167255Phase 2Results posted
• Clinical Trial to Evaluate the Efficacy, Safety, and Tolerability of RO7239361 in Ambulatory Boys With Duchenne Muscular DystrophyCompletedNCT03039686Phase 2/3Results posted
• Long-term Extension Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)CompletedNCT03038399Phase 2Results posted
• Plus Epicatechin Duchenne Muscular Dystrophy in Non-ambulatory AdolescentsCompletedNCT02964377Phase 1/2Results posted
• An Open-label Extension Study To Evaluate Safety Of PF-06252616 In Boys With Duchenne Muscular DystrophyTerminatedNCT02907619Phase 2Results posted
• Proof of Concept Study to Assess Activity and Safety of SMT C1100 (Ezutromid) in Boys With Duchenne Muscular Dystrophy (DMD)TerminatedNCT02858362Phase 2Results posted
• Clinical Study to Evaluate the Efficacy and Safety of Givinostat in Ambulant Patients With Duchenne Muscular DystrophyCompletedNCT02851797Phase 3Results posted
• Study of Ataluren in ≥2 to <5 Year-Old Male Participants With Duchenne Muscular DystrophyCompletedNCT02819557Phase 2Results posted
• An Extension Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)CompletedNCT02760277Phase 2Results posted
• A Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)CompletedNCT02760264Phase 2Results posted
• A Phase IIa Study of TAS-205 for Duchenne Muscular DystrophyCompletedNCT02752048Phase 2Results posted
• Safety and Dose Finding Study of NS-065/NCNP-01 in Boys With Duchenne Muscular Dystrophy (DMD)CompletedNCT02740972Phase 2Results posted
• Rimeporide in Patients With Duchenne Muscular DystrophyCompletedNCT02710591Phase 1Results posted
• Study of DS-5141b in Patients With Duchenne Muscular DystrophyCompletedNCT02667483Phase 1/2Results posted
• Trial of Pamrevlumab (FG-3019), in Non-Ambulatory Participants With Duchenne Muscular Dystrophy (DMD)TerminatedNCT02606136Phase 2Results posted
• Dose-Titration and Open-label Extension Study of SRP-4045 in Advanced Stage Duchenne Muscular Dystrophy (DMD) PatientsCompletedNCT02530905Phase 1Results posted
• HOPE-Duchenne (Halt cardiomyOPathy progrEssion in Duchenne)CompletedNCT02485938Phase 2Results posted
• Phase 1/2 Study in Boys With Duchenne Muscular DystrophyCompletedNCT02439216Phase 1/2Results posted
• Safety Study of Eteplirsen to Treat Early Stage Duchenne Muscular DystrophyCompletedNCT02420379Phase 2Results posted
• Clinical Intramuscular Gene Transfer of rAAV1.CMV.huFollistatin344 Trial to Patients With Duchenne Muscular DystrophyCompletedNCT02354781Phase 1/2Results posted
• Therapeutic Potential for Aldosterone Inhibition in Duchenne Muscular DystrophyCompletedNCT02354352Phase 3Results posted
• Phase I/II Study of SRP-4053 in DMD PatientsCompletedNCT02310906Phase 1/2Results posted
• A Phase 2 Study to Evaluate the Safety, Efficacy, Pharmacokinetics and Pharmacodynamics of PF-06252616 in Duchenne Muscular DystrophyTerminatedNCT02310763Phase 2Results posted
• Safety Study of Eteplirsen to Treat Advanced Stage Duchenne Muscular DystrophyCompletedNCT02286947Phase 2Results posted
• Study of Eteplirsen in DMD PatientsCompletedNCT02255552Phase 3Results posted
• A Study of TAS-205 for Duchenne Muscular DystrophyCompletedNCT02246478Phase 1Results posted
• Historically Controlled Trial of Corticosteroids in Young Boys With Duchenne Muscular DystrophyCompletedNCT02167217Phase 2Results posted
• An Extension Study of Ataluren (PTC124) in Participants With Nonsense Mutation DystrophinopathyTerminatedNCT02090959Phase 3Results posted
• Stacking Exercises Aid the Decline in FVC and Sick TimeCompletedNCT01999075Phase 4Results posted
• Cardiomyopathy in DMD: Lisinopril vs. LosartanCompletedNCT01982695Not applicableResults posted
• Duchenne Muscular Dystrophy Clinical TrialCompletedNCT01874275Not applicableResults posted
• A Study of Tadalafil for Duchenne Muscular DystrophyTerminatedNCT01865084Phase 3Results posted
• Use of (-)-Epicatechin in the Treatment of Becker Muscular Dystrophy (Pilot Study)CompletedNCT01856868Phase 1/2Results posted
• Phase 3 Study of Ataluren in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)CompletedNCT01826487Phase 3Results posted
• Effect of EPA and DHA in the Inflammation and Metabolic Disorders in DMD/DMB PatientsCompletedNCT01826422Not applicableResults posted
• A Study to Assess Safety/Tolerability, pk, Effects on Histology, Clinical Parameters of Givinostat in Children With DMDCompletedNCT01761292Phase 1/2Results posted
• Sedation During Muscle Biopsy in Patients With Duchenne Muscular DystrophyCompletedNCT01645098Not applicableResults posted
• Finding the Optimum Regimen for Duchenne Muscular DystrophyCompletedNCT01603407Phase 3Results posted
• Study of Ataluren for Previously Treated Participants With Nonsense Mutation Duchenne/Becker Muscular Dystrophy (nmDBMD) in Europe, Israel, Australia, and CanadaCompletedNCT01557400Phase 3Results posted
• Efficacy, Safety, and Tolerability Rollover Study of Eteplirsen in Subjects With Duchenne Muscular DystrophyCompletedNCT01540409Phase 2Results posted
• DART Electrical Impedance Myography (EIM) Trial in Duchenne Muscular Dystrophy (DMD) and Healthy ControlsCompletedNCT01523964Not applicableResults posted
• Eplerenone for Subclinical Cardiomyopathy in Duchenne Muscular DystrophyCompletedNCT01521546Not applicableResults posted
• A Clinical Study to Assess Two Doses of GSK2402968 in Subjects With Duchenne Muscular Dystrophy (DMD)CompletedNCT01462292Phase 2Results posted
• Flu Vaccine Study in Neuromuscular Patients 2011CompletedNCT01422200Phase 4Results posted
• Efficacy Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy PatientsCompletedNCT01396239Phase 2Results posted
• A Clinical Study to Assess the Efficacy and Safety of GSK2402968 in Subjects With Duchenne Muscular DystrophyCompletedNCT01254019Phase 3Results posted
• Study of Ataluren in Previously Treated Participants With Nonsense Mutation Dystrophinopathy (nmDBMD)TerminatedNCT01247207Phase 3Results posted
• Safety and Efficacy Study of IGF-1 in Duchenne Muscular DystrophyCompletedNCT01207908Phase 1/2Results posted
• Revatio for Heart Disease in Duchenne Muscular Dystrophy and Becker Muscular DystrophyTerminatedNCT01168908Phase 2Results posted
• Study of ACE-031 in Subjects With Duchenne Muscular DystrophyTerminatedNCT01099761Phase 2Results posted
• Phase I/II Study of PRO044 in Duchenne Muscular Dystrophy (DMD)CompletedNCT01037309Phase 1/2Results posted
• Phase III Study of Idebenone in Duchenne Muscular Dystrophy (DMD)CompletedNCT01027884Phase 3Results posted
• Study of Ataluren (PTC124) in Nonambulatory Participants With Nonsense-Mutation-Mediated Duchenne/Becker Muscular Dystrophy (nmDMD/BMD)TerminatedNCT01009294Phase 2Results posted

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