Muscular Dystrophy, Duchenne: all 480 studies

Page 1 of 5. Open to participants first (109), then studies with results posted, then the rest; newest registration first within each.

• Does Chronic Pain Change Over Time in Children With Duchenne Muscular Dystrophy?RecruitingNCT07892196
• Bone Health in Adults With Duchenne Muscular Dystrophy: A Survey on Osteoporosis, Fractures and Treatment.RecruitingNCT07890883
• Respiratory Progression in Adults With Duchenne Muscular Dystrophy.RecruitingNCT07879989
• Urotherapy Education for Families of Children With Duchenne Muscular DystrophyNot yet recruitingNCT07821125Not applicable
• Intermittent vs Alternate Daily Regimen of Prednisolone in Ambulatory Boys With Duchenne Muscular DystrophyNot yet recruitingNCT07787689Not applicable
• Evaluating VM100 Nutritional Supplement for Improving Quality of Life in Duchenne Muscular Dystrophy PatientsRecruitingNCT07766980Phase 2
• Multimodal Study About Absence of Dp140 in Becker Muscular Dystrophy: Brain-muscle Imaging, Cognition and Muscle FunctionNot yet recruitingNCT07740057
• Safety and Efficacy of KER-065 in Participants With Duchenne Muscular DystrophyRecruitingNCT07704099Phase 2
• Long-Term Extension Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon Skipping to Evaluate the Safety and Efficacy of Endosomal Escape Vehicle Phosphorodiamidate Morpholino Oligomer Platform Products (ELEVATE-LTE)Not yet recruitingNCT07682129Phase 2
• Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug TrialsRecruitingNCT07674758
• A Study to Evaluate the Tolerability, Safety and Efficacy of GNR-097 Gene Therapy in Pediatric Patients With Duchenne Muscular DystrophyRecruitingNCT07673809Phase 1/2
• Digital Monitoring of Upper Limb Function in Non-Ambulant DMDNot yet recruitingNCT07664124Not applicable
• Glucagon-Like Peptide-1 Receptor Agonists to Attenuate Metabolic Risk in Individuals With Duchenne Muscular DystrophyNot yet recruitingNCT07642635Phase 1/2
• Duchenne Electronic Health Record StudyRecruitingNCT07609394
• Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)RecruitingNCT07608432Phase 3
• A Phase 3 Study to Evaluate the Safety and Efficacy of AOC 1044 (Also Referred to as Delpacibart Zotadirsen) in Participants With DMD With Gene Mutations Amenable to Exon 44 SkippingRecruitingNCT07587242Phase 3
• An Open-Label Extension Study to Evaluate the Long-term Safety and Efficacy of BMN 351 in Participants With Duchenne Muscular DystrophyEnrolling by invitationNCT07573631Phase 2
• Usability and User Experience of a Virtual Reality Rehabilitation Game Platform in Individuals With Duchenne Muscular DystrophyEnrolling by invitationNCT07565272
• Can External Vagus Nerve Stimulation Reduce Systemic Levels of Inflammatory Mediators in Duchenne Muscular Dystrophy Patients?Enrolling by invitationNCT07543302Not applicable
• Study to Evaluate the Safety and Effectiveness of ELEVIDYS in Participants With Duchenne Muscular Dystrophy Treated in a Post-Marketing SettingRecruitingNCT07542314Phase 4
• DMD Gene Variants and Cardiac Dysfunction in Young Males With DystrophinopathiesRecruitingNCT07515235
• A Multicenter Cohort Study of Duchenne and Becker Muscular Dystrophy in Western Chinese ChildrenNot yet recruitingNCT07511920
• A Study to Evaluate the Safety and Tolerability of Rituxan in Duchenne Muscular DystrophyNot yet recruitingNCT07475754Not applicable
• Invasive Home Ventilation in DenmarkRecruitingNCT07467187
• Duchenne Muscular Dystrophy and the Viscoelastic Properties of Upper Limb MusclesEnrolling by invitationNCT07435116
• PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)RecruitingNCT07429240Phase 1/2
• A Remote Study Using Technology to Assess Outcomes in DMDRecruitingNCT07423026
• Evaluation of the Role of miR-1 in the Pathogenesis and as a Biomarker in Muscular Dystrophies and Congenital MyopathiesRecruitingNCT07415837Not applicable
• Registry for Duchenne and Becker Muscular DystrophyRecruitingNCT07402122
• Multiparametric Ultrafast Ultrasound Biomarkers for Duchenne and Becker Muscular DystrophiesRecruitingNCT07378553
• Factors Influencing Physical Activity Levels in Children With Duchenne Muscular Dystrophy: An ICF-CY-Based StudyNot yet recruitingNCT07369609
• DMD and Gamified PhysiotherapyNot yet recruitingNCT07368400Not applicable
• Urinary Titin Biomarker in DMDRecruitingNCT07332013Not applicable
• Active NBS Study: Decentralised Monitoring Motor Development in Children With Duchenne Muscular Dystrophy or Spinal Muscular Atrophy Identified by Newborn ScreeningRecruitingNCT07286565Not applicable
• Managed Access Program for Del-zota in Participants With DMD Mutations Amenable to Exon 44 SkippingAvailableNCT07250737
• Open-Label Extension Study of WVE-N531 in Patients With Duchenne Muscular DystrophyEnrolling by invitationNCT07209332Phase 2
• Safety and Dystrophin Expression of SPOT-03 in Duchenne Muscular Dystrophy (DMD) PatientsRecruitingNCT07188012Early Phase 1
• Sodium/Glucose Cotransporter-2 Inhibitors (SGLT2i) Therapy in Duchenne CardiomyopathyRecruitingNCT07172971Phase 1
• A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)RecruitingNCT07160634Phase 3
• Fear of Falling in Muscular DystrophyRecruitingNCT07129954Not applicable
• A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular DystrophyRecruitingNCT07127978
• Transition to Adulthood in People With Muscular DystrophyNot yet recruitingNCT07101185Not applicable
• The Baby Duchenne Study: Characterizing Developmental and Clinical Outcomes in the First Three Years in Children With Duchenne Muscular DystrophyRecruitingNCT07092540
• The Effect of Virtual Reality Applications on Upper Extremity Functions in Patients With Duchenne Muscular DystrophyRecruitingNCT07039799Not applicable
• A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 45 Skipping to Evaluate the Safety and Efficacy of ENTR-601-45RecruitingNCT07038824Phase 1/2
• A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 44 Skipping to Evaluate the Safety and Efficacy of ENTR-601-44RecruitingNCT07037862Phase 1/2
• DMD Voice: Qualitative Interviews With Patients and CaregiversRecruitingNCT06925269
• Muscle MRI Outlining of Neuromuscular Diseases Using Artificial IntelligenceNot yet recruitingNCT06917430
• Evaluation of the Safety, Tolerability, and Efficacy of LE051 in Patients With Duchenne Muscular DystrophyRecruitingNCT06900049Early Phase 1
• The Effect of Dual-tasking Program on Cognitive and Physical Functions and Independence in Activities of Daily Living in Children With Duchenne Muscular Dystrophy: A Single-blind Randomized Controlled TrialEnrolling by invitationNCT06887491Not applicable
• Social Cognition in Dystrophinopathies and Neurodevelopmental DisordersNot yet recruitingNCT06874166
• Investigation of the Relationship Between Executive Functions and Occupational Performance of Children With Duchenne Muscular DystrophyEnrolling by invitationNCT06868784
• An Open-label Long-term Follow-up Study of SAT-3247 for Participants With Duchenne Muscular Dystrophy Including Those Who Participated in SAT-3247-CL-101Enrolling by invitationNCT06867107Phase 2
• Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular DisordersRecruitingNCT06839469
• Transcriptomic Analysis to Put an End to Misdiagnosis in Patients With Rare Muscle DiseasesRecruitingNCT06833489Not applicable
• Follow-up of NIV At Home in Patients with Duchenne Muscular DystrophyRecruitingNCT06773988
• Pharmacokinetics and Safety of Givinostat in DMD Patients Ages From at Least 2 Years to Less Then 6 Years OldRecruitingNCT06769633Phase 2
• Respiratory Functions, Thoracoabdominal Movements and Exercise Capacity in Neuromuscular DiseasesRecruitingNCT06756633
• Research on the Relationship Between Scoliosis, Pain, Quality of Life, and Trunk Muscle Compensation Patterns Among Patients with Duchenne Muscular Dystrophy.RecruitingNCT06755138
• Evaluation of Brain Dysfunction in Patients with Duchene Muscular DystrophyNot yet recruitingNCT06732011
• The U.K. NorthStar Clinical NetworkNot yet recruitingNCT06711692
• Trial of Cell Based Therapy for DMDRecruitingNCT06692426Phase 1
• Effects of Lumbopelvic Stabilization-based Physiotherapy and Rehabilitation Training in Duchenne Muscular DystrophyNot yet recruitingNCT06643923Not applicable
• Evaluation of the Safety and Efficacy of BBM-D101 to Treat Patients with Duchenne Muscular DystrophyRecruitingNCT06641895Early Phase 1
• A Long-term Observational Study Evaluating Eteplirsen, Golodirsen, or Casimersen in Routine Clinical PracticeEnrolling by invitationNCT06606340
• Development of a Registry to Assess Natural History in Duchenne Muscular DystrophyNot yet recruitingNCT06579859
• Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMITRecruitingNCT06564974
• Applying the Pathways and Resources for Engagement and Participation Protocol Among People With Muscles DystrophiesNot yet recruitingNCT06540365Not applicable
• FLOWER: Following Longitudinal Outcomes With Epidemiology for Rare DiseasesRecruitingNCT06539169
• Long Term Follow-up for RGX-202Enrolling by invitationNCT06491927
• Psychoeducation Program for Parents of Children with Duchenne Muscular DystrophyEnrolling by invitationNCT06412328Not applicable
• Gamified Occupational Therapy for Adolescents With Duchenne Muscular DystrophyRecruitingNCT06402942Not applicable
• Rehabilitation in Muscular Dystrophies From the Hospital Facility to the Home: Pilot Project [RIMUDI]RecruitingNCT06378203Not applicable
• phenotypeS in Non Ambulant Duchenne Muscular DystrophyRecruitingNCT06366815
• Effectiveness of 5-week Digital Respiratory Practice in Children With Duchenne and Becker Muscular Dystrophies.Enrolling by invitationNCT06363526Not applicable
• Characterization of DupEx2 Duchenne Muscular DystrophyRecruitingNCT06337669
• Evaluate the Efficacy and Safety of EN001 in Patients With Duchenne Muscular DystrophyNot yet recruitingNCT06328725Phase 1/2
• Vasodilator and Exercise Study for DMD (VASO-REx)RecruitingNCT06290713Phase 2
• An Observational Study Comparing Delandistrogene Moxeparvovec (ELEVIDYS) With Standard of Care in Participants With Duchenne Muscular DystrophyEnrolling by invitationNCT06270719
• Modulation of SERCA2a of Intra-Myocytic Calcium Trafficking in Cardiomyopathy Secondary to Duchenne Muscular DystrophyRecruitingNCT06224660Phase 1
• Development of Non-Invasive Prenatal Diagnosis for Single Gene DisordersRecruitingNCT06147414
• A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)RecruitingNCT06138639Phase 1/2
• Wearable Technology to Evaluate Hyperglycemia and HRV in DMDRecruitingNCT06124196
• Telerehabilitation-based Motor Imagery Training in Children With Duchenne Muscular DystrophyNot yet recruitingNCT06109103Not applicable
• Wearable Technology to Evaluate Hyperglycemia and HRV in DMD - Longitudinal AimRecruitingNCT06093100
• Open-Label Extension of EDG-5506 in Participants With Becker Muscular DystrophyEnrolling by invitationNCT06066580Phase 2
• Assessments in Patients With Muscular Pathology and in Control Subjects : The ActiLiège Next StudyRecruitingNCT05982119Not applicable
• Effect of Kinesiology Taping on Head and Trunk Control in Children With Duchenne Muscular DystrophyRecruitingNCT05967793Not applicable
• A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical StudyEnrolling by invitationNCT05967351Phase 3
• Efficacy, Safety and Tolerability of Givinostat in Non-ambulant Patients With Duchenne Muscular DystrophyRecruitingNCT05933057Phase 3
• Phase 1/2a for Safety, PK and PD of SQY51 in Paediatric and Adult Patients Duchenne Muscular DystrophyRecruitingNCT05753462Phase 1/2
• Follow-up Study on Female Carriers With DMD Gene VariantsEnrolling by invitationNCT05715957
• Motor Imagery on Children With DMD on Gait and Balance FunctionsRecruitingNCT05601986Not applicable
• Once Weekly Infant Corticosteroid Trial for DMDRecruitingNCT05412394Phase 4
• Correlation Between Functional Capacity and Functional Capability in Duchenne Muscular DystrophyRecruitingNCT05249361
• The Efficacy and Safety of Metoprolol as add-on Treatment to Standard of Care in Preventing Cardiomyopathy in Patients With DMDRecruitingNCT05066633Phase 3
• Biomarker Development for Muscular DystrophiesRecruitingNCT05019625
• Extracellular RNA Biomarkers of Duchenne Muscular DystrophyRecruitingNCT05016908
• A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory CohortRecruitingNCT04626674Phase 1
• CRT-P or CRT-D in Dilated CardiomyopathyNot yet recruitingNCT04139460Not applicable

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