Muscular Dystrophy, Duchenne: all 480 studies

Page 4 of 5. Open to participants first (109), then studies with results posted, then the rest; newest registration first within each.

• A Study to Assess Safety, Tolerability, and PK of EDG-5506 in Healthy Volunteers and Becker Muscular Dystrophy AdultsCompletedNCT04585464Phase 1
• Brain Involvement in Dystrophinopathies Part 1CompletedNCT04583917
• Sleep Intervention in Young Boys with Duchenne Muscular DystrophyCompletedNCT04529707Not applicable
• Long-term, Extension Study of DS-5141b in Patients With Duchenne Muscular DystrophyActive, not recruitingNCT04433234Phase 2
• Safety and Biomarker Response to (+)-Epicatechin in Becker Muscular DystrophyCompletedNCT04386304Phase 1
• Digestive Events in Duchenne Muscular Dystrophy PatientsCompletedNCT04384354
• Examination of the Relationship Between Foot - Body Posture and Balance and Gait in Duchenne Muscular DystrophyCompletedNCT04353167
• Fast Troponin as a Biomarker to Assess Exercise-induced Muscle Damage in Muscle DiseasesCompletedNCT04349566
• The Expanded Access Use of Viltolarsen in Duchenne Muscular Dystrophy With Confirmed Exon 53 Amenable MutationApproved for marketingNCT04337112
• Characterization of the Postural Habits of Wheelchair Users Analysis of the Acceptability of International Recommendations in the Prevention of Pressure Sores Risk by Using a Connected Textile SensorCompletedNCT04335942Not applicable
• The Evaluation of Muscle Activation in Climbing up Stairs Activity in Children With Duchenne Muscular DystrophyStatus unknownNCT04287582
• A Low Interventional Study to Monitor Activity Using Wearable Sensors in Duchenne Muscular DystrophyTerminatedNCT04254172
• Wearable Technology to Assess Gait Function in SMA and DMDCompletedNCT04193085
• A Study to Assess the Safety, Tolerability and Preliminary Efficacy of ASP0367 (MA-0211) in Pediatric Male Participants With Duchenne Muscular Dystrophy (DMD)TerminatedNCT04184882Phase 1
• Aerobic Exercise in Duchenne Muscular DystrophyCompletedNCT04173234Not applicable
• Exploratory Study of NS-089/NCNP-02 in DMDCompletedNCT04129294Phase 1/2
• Study Determining the Frequency of Duchenne Muscular Dystrophy and Late-onset Pompe DiseaseCompletedNCT04120168
• Two-Part Study for Dose Determination of Vesleteplirsen (SRP-5051) (Part A), Then Dose Expansion (Part B) in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51-Skipping TreatmentTerminatedNCT04004065Phase 2
• A Study to Compare Safety and Efficacy of High Doses of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) (MIS51ON)Active, not recruitingNCT03992430Phase 3
• Regular Physical Exercise in Duchenne Muscular DystrophyCompletedNCT03963453
• The Burden of Access in Duchenne Muscular Dystrophy in the USCompletedNCT03951675
• Physical Activity Level of Norwegian Boys with Duchenne Muscular DystrophyCompletedNCT03947112
• Single Escalating Dose Pilot Trial of Canakinumab (ILARIS®) in Duchenne Muscular DystrophyActive, not recruitingNCT03936894Phase 1/2
• An Open-Label Extension Study of Edasalonexent in Boys With Duchenne Muscular DystrophyTerminatedNCT03917719Phase 3
• Effectiveness of a Multimodal Physiotherapy Program With Virtual Reality Glasses in Duchenne and Becker.CompletedNCT03879304Not applicable
• Safety Study of BLS-M22 in Healthy VolunteersCompletedNCT03789734Phase 1
• Quantitative Muscle Ultrasound as a Marker of Progression in Children With Muscular DiseasesCompletedNCT03786913
• Bisoprolol in DMD Early CardiomyopathyStatus unknownNCT03779646Phase 2/3
• Feasibility of Virtual Reality in Children With Neuromuscular Disease, Effectiveness of Virtual Reality and BiofeedbackCompletedNCT03689660Not applicable
• Your Voice; Impact of Duchenne Muscular Dystrophy (DMD) on the Lives of FamiliesCompletedNCT03680365
• Early Check: Expanded Screening in NewbornsActive, not recruitingNCT03655223
• A Study of Deflazacort (Emflaza®) in Participants With Duchenne Muscular Dystrophy (DMD)WithdrawnNCT03642145Phase 3
• Prevention of Scoliosis in Patients With Duchenne Muscular Dystrophy Using Portable Seat DeviceStatus unknownNCT03611244Not applicable
• Phase III Study With Idebenone in Patients With Duchenne Muscular Dystrophy (SIDEROS-E)TerminatedNCT03603288Phase 3
• Regression of Hamstring Flexibility and Performance in Children With Duchenne Muscular DystrophyCompletedNCT03589612
• Effect of Muscle Strength on Hamstring Flexibility in Children With Duchenne Muscular DystrophyCompletedNCT03589573
• Safety and Efficacy of P-188 NF in DMD PatientsTerminatedNCT03558958Phase 2
• Pulmonary and Upper Limb Functions in Duchenne Muscular DystrophyCompletedNCT03552874
• The Effect of Kinesiology Taping on Balance in Duchenne Muscular DystrophyCompletedNCT03541070Not applicable
• Lower Limb Flexibility in Duchenne Muscular Dystrophy: Effects on Functional PerformanceCompletedNCT03534349
• Kinesiology Taping in Duchenne Muscular Dystrophy: Effects on Performance, Gait Characteristics, and Energy ConsumptionCompletedNCT03529240Not applicable
• Investigation Of Factors Affecting Hand Functions in Nonambulatory Patients With Duchenne Muscular DystrophyCompletedNCT03521271
• The Validation Process for Confirmation of the French Version of the Pediatric Quality of Life Inventory :PedsQLTM.Status unknownNCT03513367
• Safety and Tolerability of WVE-210201 in Patients With Duchenne Muscular DystrophyCompletedNCT03508947Phase 1
• Effects of Fear of Falling on Physical Performance and Quality of Life in Children With Duchenne Muscular DystrophyStatus unknownNCT03507530
• Non-invasive Imaging of Muscle Structure in Duchenne Muscular Dystrophy Using Multispectral Optoacoustic TomographyCompletedNCT03490214Not applicable
• Duchenne Muscular Dystrophy Heart StudyStatus unknownNCT03443115
• Expanded Access Program for Idebenone in Participants With Duchenne Muscular Dystrophy (DMD)No longer availableNCT03433807
• A Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of a Single Dose of SRP-5051 (Vesleteplirsen) in Patients With Duchenne Muscular Dystrophy (DMD)CompletedNCT03375255Phase 1
• Prognostic Factors Affecting Duchenne Muscular DystrophyStatus unknownNCT03372655
• Microdystrophin Gene Transfer Study in Adolescents and Children With DMDActive, not recruitingNCT03368742Phase 1/2
• Tamoxifen in Duchenne Muscular DystrophyCompletedNCT03354039Phase 3
• Relationship Between PFTs and Pdi in DMDWithdrawnNCT03335384Not applicable
• Aerobic Exercise in Boys With Duchenne Muscular Dystrophy (DMD)CompletedNCT03319030
• User-centred Assistive System for Arm Functions in Neuromuscular SubjectsCompletedNCT03127241Not applicable
• Bone Marrow-Derived Autologous Stem Cells for the Treatment of Duchenne Muscular DystrophyStatus unknownNCT03067831Phase 1/2
• UTSW HP [13-C] Pyruvate Injection in HCMCompletedNCT03057002
• Virtual Reality in Individuals With Duchenne Muscular DystrophyCompletedNCT03002298Not applicable
• Biomarker for Duchenne Muscular DystrophyCompletedNCT02994030
• Characterization of Clinical Skeletal and Cardiac Impairment in Carriers of DMD and BMDActive, not recruitingNCT02972580
• Extension Study of BMN 044 in Duchenne Muscular Dystrophy (DMD)TerminatedNCT02958202Phase 2
• Analysis of a Virtual Reality Task in Patients With Duchenne Muscular DystrophyCompletedNCT02891434Not applicable
• Sodium Nitrate to Improve Blood FlowCompletedNCT02847975Phase 1
• Treatment Effect of Tamoxifen on Patients With DMDCompletedNCT02835079Phase 1
• Validating Cardiac MRI Biomarkers and Genotype-Phenotype Correlations for DMDCompletedNCT02834650Not applicable
• A Phase III Double-blind Study With Idebenone in Patients With Duchenne Muscular Dystrophy (DMD) Taking Glucocorticoid SteroidsTerminatedNCT02814019Phase 3
• Acceptance and Commitment Therapy for Muscle DiseaseCompletedNCT02810028Not applicable
• Muscle Oxygenation in Effort in Neuromuscular DiseasesCompletedNCT02789059Not applicable
• Outcome Measures in Duchenne Muscular Dystrophy: A Natural History StudyCompletedNCT02780492
• Gene Transfer Clinical Trial for Duchenne Muscular Dystrophy Using rAAVrh74.MCK.GALGT2WithdrawnNCT02704325Phase 1/2
• The Study of Skeletal Muscle Blood Flow in Becker Muscular DystrophyTerminatedNCT02653833Early Phase 1
• Extension Study of Drisapersen in DMD SubjectsNo longer availableNCT02636686
• The Safety, Efficacy and Tolerability of Remote Ischemic Preconditioning as a Therapy to DMDStatus unknownNCT02614820Not applicable
• Deflazacort Expanded Access Program for Children, Adolescents and Adults With Duchenne Muscular DystrophyApproved for marketingNCT02592941
• Testosterone Therapy for Pubertal Delay in Duchenne Muscular DystrophyCompletedNCT02571205
• HT-100 Long-term Study in DMD Patients Who Completed HALO-DMD-02TerminatedNCT02525302Phase 2
• Improved Muscle Function in Duchenne Muscular Dystrophy Through L-Arginine and MetforminCompletedNCT02516085Phase 1
• Study of SRP-4045 (Casimersen) and SRP-4053 (Golodirsen) in Participants With Duchenne Muscular Dystrophy (DMD)CompletedNCT02500381Phase 3
• Efficacy of Stem Cell Therapy in Ambulatory and Non-ambulatory Children With Duchenne Muscular Dystrophy - Phase 1-2Status unknownNCT02484560Phase 1
• Biomechanical and Morphological Changes in Dystrophic MuscleStatus unknownNCT02472990Not applicable
• Cardiac Involvement in Patients With Duchenne/Becker Muscular DystrophyCompletedNCT02470962
• Upper Limb Assessment in Duchenne Muscular DystrophyStatus unknownNCT02436720
• Sodium Nitrate for Muscular DystrophyCompletedNCT02434627Phase 1
• Myocardial Fibrosis Progression in Duchenne and Becker Muscular Dystrophy - ACE Inhibitor Therapy TrialCompletedNCT02432885Phase 3
• Strength Training in Duchenne Muscular DystrophyCompletedNCT02421523Not applicable
• 2D Strain Evaluation: Children With Duchenne Muscular Dystrophy Versus Healthy ChildrenCompletedNCT02418338Not applicable
• Modified Diet Trial: A Study of SMT C1100 in Paediatric Patients With DMD Who Follow a Balanced DietCompletedNCT02383511Phase 1
• Clinical Intramuscular Gene Transfer Trial of rAAVrh74.MCK.Micro-Dystrophin to Patients With Duchenne Muscular DystrophyCompletedNCT02376816Phase 1
• Registry of Translarna (Ataluren) in Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)CompletedNCT02369731
• A Device for Rapid, Painless, Bedside Muscle Evaluation of ChildrenCompletedNCT02340923
• Open Label, Extension Study of PRO044 in Duchenne Muscular Dystrophy (DMD)TerminatedNCT02329769Phase 2
• European Home Mechanical Ventilation RegistryTerminatedNCT02315339
• An Open-Label, Long-Term Extension Study to Evaluate the Safety and Tolerability DeflazacortCompletedNCT02295748Phase 1
• Efficacy of Umbilical Cord Mesenchymal Stem Cells in Duchenne Muscular DystrophyStatus unknownNCT02285673Phase 1/2
• A Pharmacokinetic Study of Oral Deflazacort in Children and Adolescent Subjects With Duchenne Muscular DystrophyCompletedNCT02251600Phase 1
• Stem Cell Therapy in Duchenne Muscular DystrophyWithdrawnNCT02241434Phase 1
• Allogeneic Human Umbilical Cord Mesenchymal Stem Cells for a Single Male Patient With Duchenne Muscular Dystrophy (DMD)CompletedNCT02235844Phase 1
• Transplantation of Myoblasts to Duchenne Muscular Dystrophy (DMD) PatientsStatus unknownNCT02196467Phase 1/2
• Assessment of Cardiopulmonary Function in Duchenne Muscular DystrophyCompletedNCT02195999
• Where Does Hope Fit In? The Relationship Between Hope, Uncertainty, and Coping Efficacy in Mothers of Children With Duchenne/Becker Muscular DystrophyCompletedNCT02194725

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