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TerminatedNCT03703908Updated Mar 17, 2025Results posted

A Study of CCX140-B in Subjects With Primary FSGS and Nephrotic Syndrome

A Phase 2 interventional study of CCX140-B in Focal Segmental Glomerulosclerosis, sponsored by Amgen. Terminated at 5 sites in United States. Open to participants aged 18 Years and older. Per ClinicalTrials.gov, last updated 2025-03-17.

Sponsored by Amgen · Phase 2, Interventional, and Treatment

Why this study was terminated
Program not advancing
Phase
Phase 2
Study type
Interventional
Enrollment
5
Allocation
Not applicable
Ages
18 Years and older
Sex
All
01

Study summary

An Open Label, Intra-Subject Dose Escalation Study of CCX140 B in Subjects with Primary FSGS and Nephrotic Syndrome

Read the detailed description

An Open Label, Intra-Subject Dose Escalation Study of CCX140 B in Subjects with Primary Focal Segmental Glomerulosclerosis (FSGS) and Nephrotic Syndrome. The aim of this study is to explore the effect of CCX140-B, a selective antagonist of C-C chemokine receptor type 2, on proteinuria in subjects with FSGS.

Study acquired by Amgen and all disclosures were done by previous sponsor ChemoCentryx.

02

Conditions studied

  • Focal Segmental Glomerulosclerosis

Keywords

  • FSGS
  • Glomerulosclerosis
  • Proteinuria
03

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  1. Male or female subjects aged 18 years and older
  2. Primary FSGS based on renal biopsy findings consistent with FSGS and based on presentation of histopathology, medical history and clinical course OR subjects with genetic risk factors with presentations that are otherwise consistent with primary FSGS
  3. Urinary total protein:creatinine ratio (UPCR) ≥ 3.5 g protein/g creatinine at screening

Exclusion criteria

Exclusion Criteria:

  1. Pregnant or nursing
  2. History of organ transplantation, including renal transplantation
  3. Currently on an organ transplant waiting list or there's a reasonable possibility of getting an organ transplant within 6 months of screening
  4. Histological FSGS subtype of collapsing variant
  5. Subjects who initiated, discontinued or changed dose of anti-CD20 monoclonal antibodies within 16 weeks (4 months) prior to screening are excluded. Subjects who initiated treatment with anti-CD20 monoclonal antibodies >16 weeks (4 months) prior to screening are permitted if deemed safe by the investigator and only if they intend to remain on continued, unchanged therapy at a dosing interval that has been documented to achieve continuous B cell depletion for the given patient.
  6. Subjects who discontinued Rituximab or other anti-CD20 monoclonal antibodies >16 weeks (4 months) prior to screening without confirmed recovery of CD20+ B cell population to within normal range are excluded. Subjects who discontinued rituximab or other anti-CD20 monoclonal antibodies >16 weeks (4 months) prior to screening with confirmed recovery of CD20+ B cell population to within normal range are permitted in the study. UPCR and other urine protein assessments up to 1 year prior to screening (if available) that were performed in these patients as part of the clinical routine should be recorded in the medical history.
  7. Body Mass Index (BMI) ≥ 40
04

Study design

Phase
Phase 2
Primary purpose
Treatment
Allocation
Not applicable
Intervention model
Sequential assignment
Masking
None (open label)
Enrollment
5 participants (actual)

Study arms

  • Experimental
    Sequential

    All enrolled subjects will initially be treated with the active study medication CCX140-B at a dose of 5 mg twice daily. Dose will increase in a step-wise fashion up to 15 mg twice daily.

    Drug: CCX140-B

Interventions

  • DrugCCX140-B

    Orally administered tablet

05

What researchers measure

Primary outcomes

  1. The Number of Subjects With a Reduction in Urine Protein to Creatinine Ratio (UPCR) of at Least 20%

    Number of subjects with a reduction in Urine Protein to Creatinine Ratio (UPCR) of at least 20% , i.e., ≥20%, by Week 12.

    Time frame: Baseline to week 12

Secondary outcomes

  1. Achievement of Partial or Complete Remission of UPCR Through Week 12 and Through the End of Treatment

    Partial and complete remission were defined as follows: Partial remission (included all of the following): * Reduction from baseline by ≥50% in urine protein:creatinine ratio (UPCR) * Reduction in UPCR to a level that was \<3.5 g/g * Subject could not have been a treatment failure Complete remission (included all of the following): * Reduction in UPCR to \<0.3 g/g * Serum albumin within normal range * For subjects with abnormal serum creatinine levels at baseline, return to normal levels * For subjects with normal serum creatinine levels at baseline, final value within 20% of baseline levels * Subject could not have been a treatment failure

    Time frame: Baseline to week 12

  2. Proportion of Subjects With Achievement of Complete Remission During the Treatment Period

    Complete remission is defined as reduction in urine protein:creatinine ratio (UPCR) to \<0.3 g/g, normal serum albumin, and normal serum creatinine levels or within 20% of baseline levels.

    Time frame: Baseline to week 52

  3. Time Taken of Subjects to Achieve Complete Remission During the Treatment Period

    Complete remission is defined as reduction in urine protein:creatinine ratio (UPCR) to \<0.3 g/g, normal serum albumin, and normal serum creatinine levels or within 20% of baseline levels.

    Time frame: Baseline to week 52

  4. Change From Baseline in Urine Protein:Creatinine Ratio (UPCR) Over Time

    Mean change from baseline in urinary protein:creatinine ratio (UPCR) over time.

    Time frame: Baseline to week 12 and week 52

  5. Assessment of Time to and Proportion of Subjects With Achievement of Partial Remission During the Treatment Period

    Partial remission is defined as reduction from baseline by ≥50% in UPCR, reduction in UPCR to a level that was \<3.5 g/g.

    Time frame: Baseline to week 52

  6. Time to Rescue Therapy

    Based on Investigator or physician initiation of glucocorticoids or new immunosuppressive agents or new major treatment modalities (e.g. plasmapheresis, dialysis)

    Time frame: Baseline to week 52

  7. Mean Change From Baseline for eGFR Using the CKD-EPI Cystatin C Equation Over Time

    eGFR-Estimated Glomerular Filtration Rate;CKD-EPI=Chronic Kidney Disease Epidemiology Collaboration

    Time frame: Baseline to Week 12 and Week 52

  8. Mean Change From Baseline for the eGFR CKD-EPI Creatinine Equation Over Time

    CKD-EPI = Chronic Kidney Disease Epidemiology Collaboration; eGFR = estimated glomerular filtration rate

    Time frame: Baseline to Week 12 and Week 52

  9. Mean Change From Baseline for eGFR CKD-EPI Creatinine-Cystatin C Equation Over Time

    CKD-EPI = Chronic Kidney Disease Epidemiology Collaboration; eGFR = estimated glomerular filtration rate;

    Time frame: Baseline to Week 12 and Week 52

  10. Mean Change From Baseline for the MDRD Creatinine Equation Over Time

    MDRD = Modification of Diet in Renal Disease. The mean eGFR (using the MDRD Creatinine equation) change from baseline to Week 12 and Week 52

    Time frame: Baseline to Week 12 and Week 52

  11. Effect of CCX140-B Treatment on Quality of Life Endpoint SF-36V2

    Summary of the Effect of CCX140-B Treatment on Quality of Life Endpoints SF-36V2 for the overall trial SF-36v2: Medical Outcomes Survey Short Form-36 version 2. SF-36v2 measures each of the following eight health domains: Physical Functioning, Role-Physical, Bodily Pain, General Health, Vitality, Social Functioning, Role-Emotional, and Mental Health. Scores on each item are summed and averaged. The SF-36v2 component domain scores range from 0 (worst health) to 100 (best health).

    Time frame: Baseline to Week 52

  12. Effect of CCX140-B Treatment on Quality of Life Endpoint EQ-5D-5L for the Overall Trial

    Summary of the Effect of CCX140-B Treatment on Quality of Life Endpoint EQ-5D-5L for the overall trial EQ-5D-5L: EuroQuality of Life-5 Domains-5 Levels. The EQ-5D-5L consists of : the EQ-5D descriptive system. The descriptive system comprises five dimensions: mobility, self-care, usual activities, pain/discomfort and anxiety/depression. Each dimension has 5 levels: no problems, slight problems, moderate problems, severe problems and extreme problems. The scale is numbered from 0 to 100. 100 means the best health you can imagine. 0 means the worst health you can imagine.

    Time frame: Baseline to Week 12 and Week 52

  13. Changes to Laboratory Parameters Related to Renal Function Including Serum Albumin, Creatinine, Cystatin C, Urinary Albumin:Creatinine Ratio, Total 24-hour Protein Excretion During the Trial

    Changes to laboratory parameters related to renal function including serum albumin, creatinine, cystatin C, urinary albumin:creatinine ratio, total 24-hour protein excretion during the trial

    Time frame: Baseline to Day 57

06

Results

Posted Feb 6, 2024
Limitations and caveats
The CL012_140 study was terminated early due to lack of efficacy in another study, CL011_140, investigating the use of CCX140-B.

Participant flow

Participant flow — Overall Study
MilestoneCCX140-B
Started5
Completed2
Not completed3

Outcome measures

PrimaryThe Number of Subjects With a Reduction in Urine Protein to Creatinine Ratio (UPCR) of at Least 20%

Number of subjects with a reduction in Urine Protein to Creatinine Ratio (UPCR) of at least 20% , i.e., ≥20%, by Week 12.

Time frame:
Baseline to week 12
Reported as:
Count of participants · Participants
The Number of Subjects With a Reduction in Urine Protein to Creatinine Ratio (UPCR) of at Least 20%
ParticipantsCCX140-B
The Number of Subjects With a Reduction in Urine Protein to Creatinine Ratio (UPCR) of at Least 20%2
SecondaryAchievement of Partial or Complete Remission of UPCR Through Week 12 and Through the End of Treatment

Partial and complete remission were defined as follows: Partial remission (included all of the following): * Reduction from baseline by ≥50% in urine protein:creatinine ratio (UPCR) * Reduction in UPCR to a level that was \<3.5 g/g * Subject could not have been a treatment failure Complete remission (included all of the following): * Reduction in UPCR to \<0.3 g/g * Serum albumin within normal range * For subjects with abnormal serum creatinine levels at baseline, return to normal levels * For subjects with normal serum creatinine levels at baseline, final value within 20% of baseline levels * Subject could not have been a treatment failure

Time frame:
Baseline to week 12
Reported as:
Count of participants · Participants
Achievement of Partial or Complete Remission of UPCR Through Week 12 and Through the End of Treatment
ParticipantsCCX140-B
No Complete or Partial remission at week 12/ end of treatment4
Partial remission at Week 121
SecondaryProportion of Subjects With Achievement of Complete Remission During the Treatment Period

Complete remission is defined as reduction in urine protein:creatinine ratio (UPCR) to \<0.3 g/g, normal serum albumin, and normal serum creatinine levels or within 20% of baseline levels.

Time frame:
Baseline to week 52
Reported as:
Count of participants · Participants
Proportion of Subjects With Achievement of Complete Remission During the Treatment Period
ParticipantsCCX140-B
Achieved complete remission0
Did not achieve complete remission5
SecondaryTime Taken of Subjects to Achieve Complete Remission During the Treatment Period

Complete remission is defined as reduction in urine protein:creatinine ratio (UPCR) to \<0.3 g/g, normal serum albumin, and normal serum creatinine levels or within 20% of baseline levels.

Time frame:
Baseline to week 52
Reported as:
Number · days
Time Taken of Subjects to Achieve Complete Remission During the Treatment Period
daysCCX140-B
Time Taken of Subjects to Achieve Complete Remission During the Treatment PeriodNA
SecondaryChange From Baseline in Urine Protein:Creatinine Ratio (UPCR) Over Time

Mean change from baseline in urinary protein:creatinine ratio (UPCR) over time.

Time frame:
Baseline to week 12 and week 52
Reported as:
Mean · g protein/g creatinine
Change From Baseline in Urine Protein:Creatinine Ratio (UPCR) Over Time
g protein/g creatinineCCX140-B
Week 12-1.3100 ± 3.76247
Week 52-0.4985 ± 3.37926
SecondaryAssessment of Time to and Proportion of Subjects With Achievement of Partial Remission During the Treatment Period

Partial remission is defined as reduction from baseline by ≥50% in UPCR, reduction in UPCR to a level that was \<3.5 g/g.

Time frame:
Baseline to week 52
Reported as:
Count of participants · Participants
Assessment of Time to and Proportion of Subjects With Achievement of Partial Remission During the Treatment Period
ParticipantsCCX140-B
Partial remission at Week 121
Did not achieve partial remission4
SecondaryTime to Rescue Therapy

Based on Investigator or physician initiation of glucocorticoids or new immunosuppressive agents or new major treatment modalities (e.g. plasmapheresis, dialysis)

Time frame:
Baseline to week 52

No measurements were reported for this outcome.

SecondaryMean Change From Baseline for eGFR Using the CKD-EPI Cystatin C Equation Over Time

eGFR-Estimated Glomerular Filtration Rate;CKD-EPI=Chronic Kidney Disease Epidemiology Collaboration

Time frame:
Baseline to Week 12 and Week 52
Reported as:
Mean · mL/min/1.73m²
Mean Change From Baseline for eGFR Using the CKD-EPI Cystatin C Equation Over Time
mL/min/1.73m²CCX140-B
Week 127.50 (-11.0 to 37.0)
Week 52-2.00 (-2.0 to -2.0)
SecondaryMean Change From Baseline for the eGFR CKD-EPI Creatinine Equation Over Time

CKD-EPI = Chronic Kidney Disease Epidemiology Collaboration; eGFR = estimated glomerular filtration rate

Time frame:
Baseline to Week 12 and Week 52
Reported as:
Mean · ml/min/1.73 m²
Mean Change From Baseline for the eGFR CKD-EPI Creatinine Equation Over Time
ml/min/1.73 m²CCX140-B
Week 12-14.50 (-27.0 to -6.0)
Week 52-15.0 (-15.0 to -15.0)
SecondaryMean Change From Baseline for eGFR CKD-EPI Creatinine-Cystatin C Equation Over Time

CKD-EPI = Chronic Kidney Disease Epidemiology Collaboration; eGFR = estimated glomerular filtration rate;

Time frame:
Baseline to Week 12 and Week 52
Reported as:
Mean · ml/min/1.73 m²
Mean Change From Baseline for eGFR CKD-EPI Creatinine-Cystatin C Equation Over Time
ml/min/1.73 m²CCX140-B
Week 12-2.25 (-18.0 to 13.0)
Week 52-8.0 (-8.0 to -8.0)
SecondaryMean Change From Baseline for the MDRD Creatinine Equation Over Time

MDRD = Modification of Diet in Renal Disease. The mean eGFR (using the MDRD Creatinine equation) change from baseline to Week 12 and Week 52

Time frame:
Baseline to Week 12 and Week 52
Reported as:
Mean · ml/min/1.73 m²
Mean Change From Baseline for the MDRD Creatinine Equation Over Time
ml/min/1.73 m²CCX140-B
Week 12-12.75 (-24.0 to -5.0)
Week 52-13.00 (-13.00 to -13.00)
SecondaryEffect of CCX140-B Treatment on Quality of Life Endpoint SF-36V2

Summary of the Effect of CCX140-B Treatment on Quality of Life Endpoints SF-36V2 for the overall trial SF-36v2: Medical Outcomes Survey Short Form-36 version 2. SF-36v2 measures each of the following eight health domains: Physical Functioning, Role-Physical, Bodily Pain, General Health, Vitality, Social Functioning, Role-Emotional, and Mental Health. Scores on each item are summed and averaged. The SF-36v2 component domain scores range from 0 (worst health) to 100 (best health).

Time frame:
Baseline to Week 52

No measurements were reported for this outcome.

SecondaryEffect of CCX140-B Treatment on Quality of Life Endpoint EQ-5D-5L for the Overall Trial

Summary of the Effect of CCX140-B Treatment on Quality of Life Endpoint EQ-5D-5L for the overall trial EQ-5D-5L: EuroQuality of Life-5 Domains-5 Levels. The EQ-5D-5L consists of : the EQ-5D descriptive system. The descriptive system comprises five dimensions: mobility, self-care, usual activities, pain/discomfort and anxiety/depression. Each dimension has 5 levels: no problems, slight problems, moderate problems, severe problems and extreme problems. The scale is numbered from 0 to 100. 100 means the best health you can imagine. 0 means the worst health you can imagine.

Time frame:
Baseline to Week 12 and Week 52
Reported as:
Mean · score on a scale
Effect of CCX140-B Treatment on Quality of Life Endpoint EQ-5D-5L for the Overall Trial
score on a scaleCCX140-B
Week 1266.3 ± 31.98
Week 5285 ± 0
SecondaryChanges to Laboratory Parameters Related to Renal Function Including Serum Albumin, Creatinine, Cystatin C, Urinary Albumin:Creatinine Ratio, Total 24-hour Protein Excretion During the Trial

Changes to laboratory parameters related to renal function including serum albumin, creatinine, cystatin C, urinary albumin:creatinine ratio, total 24-hour protein excretion during the trial

Time frame:
Baseline to Day 57

No measurements were reported for this outcome.

Adverse events

Collected over 52 weeks. Non-serious events are listed at a 0% frequency threshold.

Adverse event summary by group
GroupDeathsSeriousOther
CCX140-B0/5 (0%)0/5 (0%)4/5 (80%)
Most frequent other events
Showing 10 of 28
Most frequent other events
EventCCX140-B
Amylase increasedInvestigations1/5
Blood creatine phosphokinase increasedInvestigations1/5
Blood potassium increasedInvestigations1/5
Lipase increasedInvestigations1/5
FatigueGeneral disorders1/5
Oedema peripheralGeneral disorders1/5
PyrexiaGeneral disorders1/5
Upper respiratory tract infectionInfections and infestations1/5
NasopharyngitisInfections and infestations1/5
Pulpitis dentalInfections and infestations1/5

Baseline characteristics

Age, Continuous
Age, Continuous(years)CCX140-B
Mean37.6 ± 18.65
Sex: Female, Male
Sex: Female, Male(Participants)CCX140-B
Female1
Male4
Ethnicity (NIH/OMB)
Ethnicity (NIH/OMB)(Participants)CCX140-B
Hispanic or Latino2
Not Hispanic or Latino3
Unknown or Not Reported0
Race (NIH/OMB)
Race (NIH/OMB)(Participants)CCX140-B
American Indian or Alaska Native0
Asian0
Native Hawaiian or Other Pacific Islander0
Black or African American0
White4
More than one race0
Unknown or Not Reported1
Region of Enrollment
Region of Enrollment(Participants)CCX140-B
United States4
Poland1
Age at diagnosis of FSGS (years)
Age at diagnosis of FSGS (years)(years)CCX140-B
Mean35.2 ± 19.18
Duration of FSGS (months)
Duration of FSGS (months)(months)CCX140-B
Mean29.4 ± 16.32
Baseline UPCR - morning void
Baseline UPCR - morning void(g protein/ g creatinine)CCX140-B
Mean5.71 ± 1.563

11 further baseline measures are reported on the registry.

07

Study locations

5 sites
  • Los Angeles Biomedical Research Institute
    Torrance, California 90502, United States
  • Northwest Louisiana Nephrology
    Shreveport, Louisiana 71101, United States
  • Massachusetts General Hospital
    Boston, Massachusetts 02114, United States
  • University of Minnesota
    Minneapolis, Minnesota 55414, United States
  • Utah Kidney Research Institute
    Salt Lake City, Utah 84115, United States
08

References and documents

Study documents

  • Study protocol · Apr 17, 2018
  • Statistical analysis plan · Jul 29, 2020

Documents are hosted by the registry — open the source record to download them.

09

Registry details

Key details

Study ID
NCT03703908
Lead sponsor
Amgen
Responsible party
Sponsor
First posted
Oct 12, 2018
Start date
Oct 1, 2018
Primary completion
Jun 24, 2020
Completion
Jun 24, 2020
Results posted
Feb 6, 2024
Last update
Mar 17, 2025

Study contacts

MD
study director · Amgen

Oversight

Data monitoring committee
No
FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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