CClinicalTrials.gg
Status unknownNCT03184597Updated Sep 5, 2018

HLA Screening in Reducing the Risk of Antiepileptic Drug-induced Cutaneous Adverse Reactions

An interventional study of HLA screening before commencing aromatic AEDs in Epilepsy, Neuropathy and Psychiatric Illness, sponsored by Second Affiliated Hospital of Guangzhou Medical University. Status unknown at 1 site in China. Per ClinicalTrials.gov, last updated 2018-09-05.

Sponsored by Second Affiliated Hospital of Guangzhou Medical University · Not applicable, Interventional, and Prevention

The sponsor has not verified this record recently (last verified Aug 2018), so the status shown — last known as Recruiting — may be out of date.
Phase
Not applicable
Study type
Interventional
Enrollment
4,000
Allocation
Non-randomized
Sex
All
01

Study summary

Cutaneous adverse drug reactions (cADRs) include mild maculopapular exanthema (MPE) and severe cutaneous reactions such as hypersensitivity syndrome, Stevens-Johnson syndrome (SJS), and toxic epidermal necrolysis (TEN). cADRs are considered as a major public health issue because of their potentially life-threatening morbidity, especially severe cutaneous reactions. The incidence of SJS/TEN is estimated to vary from 1 in 1,000 to 10,000 drug exposures, and its mortality is as high as 35%. Antiepileptic drugs (AEDs), particularly those with aromatic ring structures such as carbamazepine (CBZ), oxcarbazepine (OXC), lamotrigine (LTG), phenobarbital (PB), and phenytoin (PHT), are among the most common causes of severe cutaneous reactions. The incidence of AED-induced SJS was estimated as 0.2% and all cases occurred in individuals receiving aromatic AEDs.

Previous studies have validated that the human leukocyte antigen (HLA) allele HLA-B*15:02 is strongly associated with CBZ-induced SJS/TEN in southern Han Chinese and populations in southeast Asia. Our recent studies indicated that HLA-A*24:02 is a common genetic risk factor for CBZ-, LTG-, and PHT-induced SJS/TEN. It is also associated with MPE. Additionally, another four alleles, including HLA-B*15:01, HLA-B*15:11, HLA-A*02:01,and HLA-DRB1*01:01, were showed to be potential risk factors for aromatic AEDs-induced SJS/TEN. In 2007, the US Food and Drug Administration issued the safety alert that recommended HLA-B*15:02 screening for people with Asian ancestry before starting CBZ, and avoidance of the drug if the test is positive. Subsequent studies from Taiwan, Hong Kong and Thailand demonstrated that HLA-B*15:02 screening before commencing CBZ can significantly reduce the incidence of CBZ-induced SJS/TEN. However, the overall incidence of AEDs-induced SJS/TEN remained unchanged in Hong Kong, as PHT-induced SJS/TEN increased when CBZ-SJS/TEN decreased. Moreover, no study focuses on the incidences of AEDs-induced cADRs with and without HLA screening before commencing aromatic AEDs. Therefore, we are planning to conduct a multicenter prospective study to examine the reduction of AEDs-induced cADRs after the HLA screening prior to the beginning of aromatic AEDs administration.

Read the detailed description

In this prospective study, 4000 or more patients from multicenters in southern China will be recruited. A HLA screening will be conducted before these patients start aromatic AEDs treatments. According to the HLA genotype, these patients will be divided into four groups that are three positive groups with different risk alleles and one negative group with no known risk allele. Aromatic AEDs were avoided or administrated with caution according to the risk level in the three positive groups, while they can be prescribed in the negative group. The effectiveness of HLA screening prior to the beginning of aromatic AEDs administration will be observed by the reduction of overall incidence of AEDs-induced cADRs.

02

Conditions studied

  • Epilepsy
  • Neuropathy
  • Psychiatric Illness
  • Blepharospasm

Keywords

  • HLA screening
  • SJS/TEN
  • MPE
  • AEDs
03

Who can participate

Ages eligible
Child (0–17), Adult (18–64), Older adult (65+)
Sexes eligible
All
Accepts healthy volunteers
Yes

Inclusion criteria

  1. Patients who are going to receive a kind of aromatic AEDs including CBZ, OXC, LTG, PHT, and PB as a new therapy. An AED was deemed newly commenced if there was no record of its prescription in at least the previous 12 months.
  2. Ethnic Han Chinese. None of the biological grandparents of the participants were from other races.

Exclusion criteria

Exclusion Criteria:

  1. individuals who are not of Han Chinese descent.
  2. individuals who had undergone bone marrow transplantation
04

Study design

Phase
Not applicable
Primary purpose
Prevention
Allocation
Non-randomized
Intervention model
Parallel assignment
Masking
None (open label)
Enrollment
4,000 participants (estimated)

Study arms

  • Experimental
    Group with two strong risk factors

    When HLA screening before commencing aromatic AEDs shows positive for both HLA-A\*24:02 and HLA-B\*15:02 in a patient, aromatic AEDs were not administrated for this patient.

    Diagnostic Test: HLA screening before commencing aromatic AEDs

  • Experimental
    Group with one strong risk factors

    When HLA screening before commencing aromatic AEDs shows positive for HLA-B\*15:02, carbamazepine (CBZ) was not administrated, and other aromatic AEDs were prescribed with caution or avoided if alternative non-aromatic AEDs can be prescribed instead. When HLA screening before commencing aromatic AEDs shows positive for HLA-B\*15:01 or HLA-A\*24:02, aromatic AEDs were prescribed with caution or avoided if alternative non-aromatic AEDs can be prescribed instead.

    Diagnostic Test: HLA screening before commencing aromatic AEDs

  • Experimental
    Group with one potential risk factors

    When HLA screening before commencing aromatic AEDs shows positive for any potential risk allele such as HLA-B\*15:11, HLA-A\*02:01and HLA-DRB1\*01:01, aromatic AEDs were prescribed with caution or avoided if alternative non-aromatic AEDs can be prescribed instead.

    Diagnostic Test: HLA screening before commencing aromatic AEDs

  • Experimental
    Group without known risk factors

    When HLA screening before commencing aromatic AEDs shows negative for any known HLA risk allele , aromatic AEDs was administrated to these patients.

    Diagnostic Test: HLA screening before commencing aromatic AEDs

Interventions

  • Diagnostic testHLA screening before commencing aromatic AEDs

    When the risk HLA alleles are tested positive for the patients, aromatic AEDs were avoided or administrated with caution according to the risk level.

05

What researchers measure

Primary outcomes

  1. AEDs-induced cADRs incidence

    the incidence of AEDs-induced cADRs within the first 3 months of commencing an aromatic AED

    Time frame: 3 months

06

Study locations

1 of 1 sites recruiting
  • The Second Affiliated Hospital of Guangzhou Medical Universty
    Guangzhou, Guangdong 510260, China
    • Wei-Ping Liao, M.D., Ph.D. · Contact · wpliao@163.net · +86-20-34152625
    • Na He · Contact · henachilli@163.com · +86-20-34152640
    • Wei-Ping Liao, M.D., Ph.D. · Principal investigator
    Recruiting
07

References and documents

Publications

  • Shi YW, Min FL, Zhou D, Qin B, Wang J, Hu FY, Cheung YK, Zhou JH, Hu XS, Zhou JQ, Zhou LM, Zheng ZZ, Pan J, He N, Liu ZS, Hou YQ, Lim KS, Ou YM, Hui-Ping Khor A, Ng CC, Mao BJ, Liu XR, Li BM, Kuan YY, Yi YH, He XL, Deng XY, Su T, Kwan P, Liao WP. HLA-A*24:02 as a common risk factor for antiepileptic drug-induced cutaneous adverse reactions. Neurology. 2017 Jun 6;88(23):2183-2191. doi: 10.1212/WNL.0000000000004008. Epub 2017 May 5. PubMed 28476759 ↗
  • Shi YW, Min FL, Qin B, Zou X, Liu XR, Gao MM, Wang Q, Zhou JQ, Liao WP. Association between HLA and Stevens-Johnson syndrome induced by carbamazepine in Southern Han Chinese: genetic markers besides B*1502? Basic Clin Pharmacol Toxicol. 2012 Jul;111(1):58-64. doi: 10.1111/j.1742-7843.2012.00868.x. Epub 2012 Mar 17. PubMed 22348435 ↗
  • Shi YW, Min FL, Liu XR, Zan LX, Gao MM, Yu MJ, Liao WP. Hla-B alleles and lamotrigine-induced cutaneous adverse drug reactions in the Han Chinese population. Basic Clin Pharmacol Toxicol. 2011 Jul;109(1):42-6. doi: 10.1111/j.1742-7843.2011.00681.x. Epub 2011 Mar 16. PubMed 21306565 ↗
  • Chen P, Lin JJ, Lu CS, Ong CT, Hsieh PF, Yang CC, Tai CT, Wu SL, Lu CH, Hsu YC, Yu HY, Ro LS, Lu CT, Chu CC, Tsai JJ, Su YH, Lan SH, Sung SF, Lin SY, Chuang HP, Huang LC, Chen YJ, Tsai PJ, Liao HT, Lin YH, Chen CH, Chung WH, Hung SI, Wu JY, Chang CF, Chen L, Chen YT, Shen CY; Taiwan SJS Consortium. Carbamazepine-induced toxic effects and HLA-B*1502 screening in Taiwan. N Engl J Med. 2011 Mar 24;364(12):1126-33. doi: 10.1056/NEJMoa1009717. PubMed 21428768 ↗
  • Chen Z, Liew D, Kwan P. Effects of a HLA-B*15:02 screening policy on antiepileptic drug use and severe skin reactions. Neurology. 2014 Nov 25;83(22):2077-84. doi: 10.1212/WNL.0000000000001034. Epub 2014 Oct 29. PubMed 25355835 ↗
  • Rattanavipapong W, Koopitakkajorn T, Praditsitthikorn N, Mahasirimongkol S, Teerawattananon Y. Economic evaluation of HLA-B*15:02 screening for carbamazepine-induced severe adverse drug reactions in Thailand. Epilepsia. 2013 Sep;54(9):1628-38. doi: 10.1111/epi.12325. Epub 2013 Jul 29. PubMed 23895569 ↗
  • Chen Z, Liew D, Kwan P. Real-world cost-effectiveness of pharmacogenetic screening for epilepsy treatment. Neurology. 2016 Mar 22;86(12):1086-94. doi: 10.1212/WNL.0000000000002484. Epub 2016 Feb 17. PubMed 26888992 ↗

Individual participant data

Plan to share: Yes — The clinical data and HLA genotype of the participant will be shared in the collaborators

Supporting information: Study protocol, Sap, Csr

08

Registry details

Key details

Study ID
NCT03184597
Lead sponsor
Second Affiliated Hospital of Guangzhou Medical University
Collaborators
Guangzhou First People's Hospital, West China Hospital, Guangdong Provincial People's Hospital, First Affiliated Hospital of Jinan University, Guangdong 999 Brain Hospital, First Affiliated Hospital, Sun Yat-Sen University, Wuhan Women and Children's Medical Center, First People's Hospital, Shunde China
Responsible party
Sponsor
First posted
Jun 12, 2017
Start date
Aug 1, 2017
Primary completion
Jun 2021 (estimated)
Completion
Jun 2021 (estimated)
Last update
Sep 5, 2018

Study contacts

Wei-Ping Liao, M.D.,Ph.D.
Contact
wpliao@163.net
+86-20-34152625
Na He, Ph.D.
Contact
henachilli@163.com
+86-20-34152640
Wei-Ping Liao, M.D.,Ph.D.
principal investigator · Second Affiliated Hospital of Guangzhou Medical University

Oversight

Data monitoring committee
Yes
FDA-regulated drug
No
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

Not currently enrolling

This study is status unknown, as verified in Aug 2018. You cannot join it, but the record below documents what was studied.

Follow this study

Get an email when the registry record changes — status, dates, results — or when someone posts here.

Sign in to follow

Discussion

Questions and observations about this study, from anyone following it. Not medical advice, and not a channel to the study team — their contact details are on the registry record.

Sign in to join the discussion. Reading takes no account; posting does. You choose a display name, and a pseudonym is the default.

Nothing here yet. If you are running this trial, taking part in it, or weighing whether to, this is the place to say so.

Start the discussion