Lipidoses clinical trials
The registry lists 16 studies for Lipidoses across more than 10 countries. 3 are recruiting or about to start. 6 of them are mainly about Lipidoses (how this is decided). Per ClinicalTrials.gov, last updated 2026-11-04. Counting its 15 narrower conditions too, such as Fabry Disease: 631 studies, 133 open.
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Who runs them
CENTOGENE GmbH Rostock (2) · University of Toronto (2) · 4D Molecular Therapeutics (2) · Children's Mercy Hospital Kansas City (1) · Duke University (1) · Alexion Pharmaceuticals, Inc. (1) · University of Alicante (1) · Monash University Malaysia (1)
What is being tested here
Drugs under test in Lipidoses studies, those with the most open studies first. Medicines only given beside them are not counted. How drugs are counted
| Drug | Open | Phase 3 | All |
|---|---|---|---|
| Rosuvastatin | 1 | 0 | 1 |
| Sebelipase alfa | 0 | 0 | 1 |
| Ezetimibe | 0 | 0 | 1 |
Coming up
Studies recruiting or running, from their records. “Main data collection” ends at the primary completion date, the sponsor’s own estimate, which often moves.
The study
- Oct 2027Liver Adiposity Effects on Pediatric Statin · Children's Mercy Hospital Kansas City
Who these studies take
Of the 2 Lipidoses studies recruiting now, 0 (0%) set no upper age limit and 2 (100%) stop at 75 or younger. 1 (50%) take children under 18. 0 (0%) are for women only and 0 (0%) for men only; 1 (50%) take healthy volunteers.
| Age | Women | Men |
|---|---|---|
| 10 | 1 (50%) | 1 (50%) |
| 18 | 2 (100%) | 2 (100%) |
| 30 | 1 (50%) | 1 (50%) |
| 40 | 1 (50%) | 1 (50%) |
| 50 | 1 (50%) | 1 (50%) |
| 65 | 1 (50%) | 1 (50%) |
| 75 | 0 (0%) | 0 (0%) |
| 85 | 0 (0%) | 0 (0%) |
Across all 16 studies, recruiting or not: 25% stop at 75 or younger and 25% at 65; 56% take children; 0% are for women only and 0% for men only; 25% take healthy volunteers. From each study’s registry entry; the criteria on its page decide.
Studies
Recruiting first, then most recently updated. Showing 16 of 16. search them.
- Liver Adiposity Effects on Pediatric StatinRecruitingNCT04903223Phase 11 country
- 4D-310 in Adults With Fabry Disease and Cardiac InvolvementRecruitingNCT05629559Phase 1/22 countries
- Daily Living Activities and Exercise Capacity in Lipid Storage DiseasesNot yet recruitingNCT038751051 country
- Gene Transfer Clinical Trial for Infantile and Late Infantile Krabbe Disease Treated Previously With HSCTActive, not recruitingNCT05739643Phase 1/21 country
- An Open-label, Phase 1/2 Trial of Gene Therapy 4D-310 in Adults With Fabry DiseaseActive, not recruitingNCT04519749Phase 1/21 country
- The Effect of Tele-Nursing Based Motivational Interviewing in Individuals With Type 2 Diabetes:RCTCompletedNCT05628259Not applicable1 country
- Assessment of Lifestyle, Blood Pressure, Cholesterol and Glycated Hemoglobin in a Specific PopulationCompletedNCT043738631 country
- Biomarker for Niemann Pick Type C Disease (BioNPC)WithdrawnNCT013066043 countries
- Improvement of Physical and Physiological Parameters Through the Use of a Mobile AppCompletedNCT05093803Not applicable1 country
- Lyso-Gb1 as a Long-term Prognostic Biomarker in Gaucher DiseaseCompletedNCT024166617 countries
- Can Mindful Eating Improve Cholesterol and Glucose LevelStatus unknownNCT04833595Not applicable1 country
- Farber Disease Natural History StudyCompletedNCT032338419 countries
- Safety and Efficacy Study of Sebelipase Alfa in Participants With Lysosomal Acid Lipase DeficiencyCompletedNCT02112994Phase 215 countries
- Umbrella Review of the DASH Dietary Pattern and Cardiometabolic RiskStatus unknownNCT035423701 country
- Meta-analysis of the Portfolio Dietary Pattern and Cardiometabolic RiskStatus unknownNCT035344141 country
- SCH-58235 (Ezetimibe) to Treat Homozygous SitosterolemiaCompletedNCT00045812Phase 21 country