Leukodystrophy, Globoid Cell clinical trials

The registry lists 31 studies for Leukodystrophy, Globoid Cell across more than 10 countries. 8 are recruiting or about to start. 10 of them are mainly about Leukodystrophy, Globoid Cell (how this is decided). Per ClinicalTrials.gov, last updated 2026-11-06.

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Status

Completed: 10
Recruiting: 7
Terminated: 5
Active, not recruiting: 4
Withdrawn: 2
Not yet recruiting: 1

Phase

Phase 2: 11
Phase 1: 5
Phase 3: 2

Where

United States: 27
Canada: 1
India: 1
Israel: 1
Germany: 1
Egypt: 1

Who runs them

Masonic Cancer Center, University of Minnesota (6) · Children's Hospital of Philadelphia (2) · University of Pittsburgh (2) · Magenta Therapeutics, Inc. (2) · Duke University (2) · Paul Szabolcs (2) · Gemma Biotherapeutics (1) · Polaryx Therapeutics, Inc. (1)

What is being tested here

Drugs under test in Leukodystrophy, Globoid Cell studies, those with the most open studies first. Medicines only given beside them are not counted. How drugs are counted

Drug	Open	Phase 3	All
Alemtuzumab	1	0	4
Melphalan	1	0	2
Gemfibrozil	1	0	1
Hydroxyurea	1	0	1
Fludarabine	1	0	1
Thiotepa	1	0	1
Cyclophosphamide	0	1	3
Busulfan	0	1	3
Cyclosporine	0	0	2
Mycophenolic Acid	0	0	2

Drug classes tested here Alkylating agents 1 open

Coming up

0phase 3 studies under way

5studies finish main data collection within a year

Studies recruiting or running, from their records. “Main data collection” ends at the primary completion date, the sponsor’s own estimate, which often moves.

All 5

Nov 2026Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT · Paul Szabolcs
Nov 2026Early Check: Expanded Screening in Newborns · RTI International
Mar 2027Krabbe Disease Global Patient Registry · State University of New York at Buffalo
Apr 2027Diffusion Tensor Imaging (DTI) in Infants With Krabbe Disease · University of Pittsburgh
Oct 2027UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells · Joanne Kurtzberg, MD

Who these studies take

Of the 7 Leukodystrophy, Globoid Cell studies recruiting now, 4 (57%) set no upper age limit and 3 (43%) stop at 75 or younger. 6 (86%) take children under 18. 0 (0%) are for women only and 0 (0%) for men only; 0 (0%) take healthy volunteers.

Recruiting studies that take each age, of 7
Age	Women	Men
10	6 (86%)	6 (86%)
18	7 (100%)	7 (100%)
30	6 (86%)	6 (86%)
40	6 (86%)	6 (86%)
50	6 (86%)	6 (86%)
65	4 (57%)	4 (57%)
75	4 (57%)	4 (57%)
85	4 (57%)	4 (57%)

Across all 31 studies, recruiting or not: 68% stop at 75 or younger and 65% at 65; 97% take children; 0% are for women only and 0% for men only; 6% take healthy volunteers. From each study’s registry entry; the criteria on its page decide.

Studies

Recruiting first, then most recently updated. Showing 31 of 31. search them.