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Gaucher Disease clinical trials

The registry lists 177 studies for Gaucher Disease across more than 10 countries. 41 are recruiting or about to start. 146 of them are mainly about Gaucher Disease (how this is decided). Per ClinicalTrials.gov, last updated 2026-11-10.

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Example · made-up studies

Breast cancer · Recruiting: 2 came in, 3 changed

What changed in your saved searches, Oct 31 – Nov 6:

A study of drug A after surgery for early breast cancer

Came in · now Recruiting

Drug B with hormone therapy in advanced breast cancer

Changed

· Sites: 4 added, including Seoul and Busan

· Enrollment: 300 → 450 participants

Exercise during chemotherapy

Now Active, not recruiting

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Status

Completed
92
Recruiting
26
Status unknown
18
Not yet recruiting
11
Active, not recruiting
10
Withdrawn
7

Phase

Phase 2
34
Phase 1
32
Phase 3
28
Phase 4
11
Early Phase 1
2

Where

United States
92
Israel
33
United Kingdom
24
Spain
21
Canada
17
India
13

Who runs them

Shire (14) · Sanofi (12) · Genzyme, a Sanofi Company (12) · Pfizer (8) · Shaare Zedek Medical Center (7) · Takeda (6) · University of Minnesota (6) · National Institute of Neurological Disorders and Stroke (NINDS) (6)

What is being tested here

Drugs under test in Gaucher Disease studies, those with the most open studies first. Medicines only given beside them are not counted. How drugs are counted

DrugOpenPhase 3All
Nizubaglustat212
Eliglustat1413
Venglustat123
Laronidase101
Hydroxyurea101
Alemtuzumab101
Fludarabine101
Melphalan101
Thiotepa101
Velaglucerase alfa0712

Coming up

5phase 3 studies under way
11studies finish main data collection within a year

Studies recruiting or running, from their records. “Main data collection” ends at the primary completion date, the sponsor’s own estimate, which often moves.

The 10 nearest

Who these studies take

Of the 26 Gaucher Disease studies recruiting now, 11 (42%) set no upper age limit and 11 (42%) stop at 75 or younger. 15 (58%) take children under 18. 1 (4%) are for women only and 0 (0%) for men only; 4 (15%) take healthy volunteers.

Recruiting studies that take each age, of 26
AgeWomenMen
1014 (54%)14 (54%)
1823 (88%)22 (85%)
3022 (85%)21 (81%)
4024 (92%)23 (88%)
5024 (92%)23 (88%)
6518 (69%)18 (69%)
7518 (69%)18 (69%)
8513 (50%)13 (50%)

Across all 177 studies, recruiting or not: 36% stop at 75 or younger and 30% at 65; 56% take children; 1% are for women only and 2% for men only; 20% take healthy volunteers. From each study’s registry entry; the criteria on its page decide.

How long Gaucher Disease studies take

Of 11 phase 3 interventional studies under Gaucher Disease, half reached primary completion within 25 months of starting, counting those still running.

Start to primary completionEvery sponsorIndustryNon-industry
Phase 325 mo15–57 · 11 studies——

Each figure is the month by which half the studies had reached primary completion, with the range in which the middle half did. Studies still running count until their last registry update; studies that stopped early are left out. Phase 1 includes early phase 1; observational means prospective or not stated, as retrospective and cross-sectional studies date a window of data rather than a study. How these figures are worked out

What changed recently

From the registry's own updates since Oct 13, 2026.

Newly registered3

Studies

Recruiting first, then most recently updated. Showing 50 of 177. Browse all 177 → or search them.