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RecruitingNCT05934188GutBrainUpdated Jan 9, 2026

Exploring the Gut-Brain Axis in Ageing and Neurodegeneration

An observational study in Healthy, Prodromal Alzheimer's Disease and Parkinson Disease, sponsored by IRCCS San Camillo, Venezia, Italy. Recruiting at 3 sites in Italy. Open to participants aged 20 Years to 90 Years, including healthy volunteers. Per ClinicalTrials.gov, last updated 2026-01-09.

Sponsored by IRCCS San Camillo, Venezia, Italy · Observational

Study type
Observational
Model
Case-control
Time perspective
Cross-sectional
Enrollment
200
Ages
20 Years to 90 Years
Sex
All
01

Study summary

Neurodegenerative diseases are a major health concern due to their growing societal implications and economic costs. The identification of early markers of pathogenic mechanisms is one of the current main challenges. The gut-brain axis has become a primary target because of its transversal role across the neurodegenerative spectrum and its effect on cognition. However, despite recent progress, how changes in the gut-microbiota composition can affect the human brain is still unclear.

The goal of this observational study is to characterise the gut-microbiota composition associated with alterations in brain structure and function during the ageing process and across neurodegenerative disorders. This is based on recent studies showing that changes in the human brain and in the microbiota composition, can indicate very sensitively and in a predictive way pathological development and, consequently, be used as markers of neurodegenerative diseases.

The main questions it aims to answer are:

  • How variation in the gut-microbiota composition correlates with the normal brain ageing trajectory?
  • How dysregulation in the gut-microbiota correlates with pathological changes in brain regions in specific neurodegenerative disorders?
  • Can the impact of the gut-microbiota on the brain be modulated by blood biomarkers?

The investigators will recruit 40 young healthy participants, 40 old healthy participants, 40 participants with prodromal Alzheimer's Disease, 40 participants with Parkinson's Disease and 40 participants with Multiple Sclerosis.

Participants will undergo the following examinations:

  • Magnetic Resonance Imaging
  • Analysis of a stool sample
  • Analysis of a blood sample
  • Neuropsychological assessment
  • Questionnaires on eating habits
Read the detailed description

Recent studies show that alterations in the microbiota profile has been observed in the ageing process and across neurodegenerative disorders and it has been associated with cognitive decline and disease-specific clinical symptoms.

The objective of this multicenter observational cross-sectional cohort study is to characterise how changes in the gut-microbiota profile may affect brain changes during the physiological ageing processes and across neurodegenerative disorders with different etiopathogenesis.

The investigators will combine novel magnetic resonance imaging and biological techniques to test these hypotheses:

  1. Specific functional and structural changes, which reflect unsuccessful compensatory mechanisms to counteract ageing, are associated with changes in the gut-microbiota composition.
  2. Neurodegenerative disorders (prodromal Alzheimer's Disease, Parkinson's Disease, Multiple Sclerosis) show unique changes in the gut-microbiome profile, associated with specific structural and functional brain changes.
  3. The microbiota profile characterizing the unsuccessful ageing and different neurodegenerative diseases is associated with alterations in blood biomarkers.

For this study the investigators plan to recruit 80 healthy subjects divided into two groups (40 subjects aged 20-50 years and 40 subjects aged 60-90 years) and 120 patients divided into three groups (40 patients with prodromal Alzheimer's Disease, 40 patients with Parkinson's Disease and 40 patients with Multiple Sclerosis).

All participants will undergo a multimodal Magnetic Resonance Imaging protocol to study the brain structure and function and a detailed neuropsychological protocol to assess cognitive functioning. In addition, stool and blood samples will be collected to investigate the gut-microbiota composition and the presence of inflammatory markers, respectively. Participants will also be asked to fill out questionnaires on eating habits.

There are no known risks or long-term side effects related to Magnetic Resonance Imaging. The performance of the examination does not involve physical or mental impairment.

The study does not directly benefit the participant. However, participation in the study will increase knowledge in the area of the relationship between the gut microbiota and the brain, providing potential new knowledge useful for preventing the risk of developing neurodegenerative processes.

The study takes place at San Camillo IRCCS S.r.l. (70 Alberoni street, Lido VE, 30126, Italy IT).

The study started on 01/05/2023 and the end is planned for 30/04/2026. The submitted study is funded by the Ministry of Health through a finalized research call won by Principal Investigator, Dr. Nicola Filippini, and approved by Ethics Committee for Clinical Trials of the Province of Venice and IRCCS San Camillo, Azienda ULSS 3 Serenissima.

02

Conditions studied

  • Healthy
  • Prodromal Alzheimer's Disease
  • Parkinson Disease
  • Multiple Sclerosis

Keywords

  • MRI
  • Microbiota
  • Stool sample
  • Blood sample
  • Neuropsychological assessment
  • Neuroimaging
  • Biomarkers for brain disorders
03

Who can participate

Ages eligible
20 Years to 90 Years
Sexes eligible
All
Accepts healthy volunteers
Yes
Sampling method
Non-probability sample

Study population

The groups will be selected from local community sample, hospital and general practitioners (gp).

Inclusion criteria

Healthy Young and Old Subjects:

  • 20-50 or 60-90 years old
  • Cognitively healthy (Mini-Mental State examination ≥ 26)
  • Absence of significant neurological disorders

Patients with prodromal Alzheimer's Disease:

  • Subjective cognitive complaint (corroborated by the informant)
  • Episodic memory deficit on neuropsychological testing
  • Clinical Dementia Rating = 0.5
  • Mini-Mental State Examination (MMSE) > 23
  • Independently functioning in activities of daily living

Patients with Parkinson's Disease:

  • Recent diagnosis of Parkinson's Disease
  • Mild-moderate score at the Unified Parkinson's Disease Rating Scale (UPDRS)
  • Cognitively healthy (Mini-Mental State examination ≥ 26)
  • In case of taking medications for Parkinson's Disease: stable dosage for at least 6 months

Patients with Multiple Sclerosis:

  • Recent diagnosis of relapsing-remitting Multiple Sclerosis
  • Expanded Disability Status Scale score ≤ 4.0
  • Cognitively healthy (Mini-Mental State examination ≥ 26)
  • In case of taking medications for Multiple Sclerosis: stable dosage for at least 6 months.

Exclusion criteria

EXCLUSION CRITERIA:

For both healthy participants and patients:

  • Contraindications to magnetic resonance imaging (metal implant in body, known claustrophobia, pacemakers)
  • Severe comorbidities
  • Antibiotics treatments over the last 3 months
04

Study design

Observational model
Case-control
Time perspective
Cross-sectional
Enrollment
200 participants (estimated)
Patient registry
No

Groups and cohorts

  • Young Healthy Subjects (N = 40)

    * 20-50 years old * Cognitively healthy (Mini-Mental State examination ≥ 26) * Absence of significant neurological disorders

    Diagnostic Test: Magnetic Resonance Imaging · Behavioral: Neuropsychological protocol · Behavioral: Eating habits · Diagnostic Test: Microbiome analyses · Diagnostic Test: Inflammatory markers

  • Old Healthy Subjects (N = 40)

    * 60-90 years old * Cognitively healthy (Mini-Mental State examination ≥ 26) * Absence of significant neurological disorders

    Diagnostic Test: Magnetic Resonance Imaging · Behavioral: Neuropsychological protocol · Behavioral: Eating habits · Diagnostic Test: Microbiome analyses · Diagnostic Test: Inflammatory markers

  • Patients with prodromal Alzheimer's Disease (N = 40)

    * Subjective cognitive complaint (corroborated by the informant) * Episodic memory deficit on neuropsychological testing * Clinical Dementia Rating = 0.5 * Mini-Mental State Examination (MMSE) \> 23 * Independently functioning in activities of daily living

    Diagnostic Test: Magnetic Resonance Imaging · Behavioral: Neuropsychological protocol · Behavioral: Eating habits · Diagnostic Test: Microbiome analyses · Diagnostic Test: Inflammatory markers · Diagnostic Test: Alzheimer's Disease biomarkers

  • Patients with Parkinson's Disease (N = 40)

    * Recent diagnosis of Parkinson's Disease * Mild-moderate score at the Unified Parkinson's Disease Rating Scale (UPDRS) * Cognitively healthy (Mini-Mental State examination ≥ 26) * In case of taking medications for Parkinson's Disease: stable dosage for at least 6 months

    Diagnostic Test: Magnetic Resonance Imaging · Behavioral: Neuropsychological protocol · Behavioral: Eating habits · Diagnostic Test: Microbiome analyses · Diagnostic Test: Inflammatory markers

  • Patients with Multiple Sclerosis (N = 40)

    * Recent diagnosis of relapsing-remitting Multiple Sclerosis * Expanded Disability Status Scale score ≤ 4.0 * Cognitively healthy (Mini-Mental State examination ≥ 26) * In case of taking medications for Multiple Sclerosis: stable dosage for at least 6 months

    Diagnostic Test: Magnetic Resonance Imaging · Behavioral: Neuropsychological protocol · Behavioral: Eating habits · Diagnostic Test: Microbiome analyses · Diagnostic Test: Inflammatory markers

Interventions

  • Diagnostic testMagnetic Resonance Imaging

    The Magnetic Resonance Imaging protocol will comprise both structural and functional sequences.

  • BehavioralNeuropsychological protocol

    Neuropsychological tests will be administered to participants to assess general cognitive state and a range of high-level cognitive functions (memory, executive, language). In addition, disease-specific tests will be administered to patients to investigate disease staging and the level of disability and autonomy.

  • BehavioralEating habits

    Information on eating habits will be derived from food questionnaires.

  • Diagnostic testMicrobiome analyses

    The Microbiome analyses will be derived from a stool sample (16S rRNA sequencing targeted metagenomic analyses).

  • Diagnostic testInflammatory markers

    Inflammatory markers will be evaluated in terms RNA expression level in plasma blood sample.

  • Diagnostic testAlzheimer's Disease biomarkers

    The Alzheimer's Disease biomarkers will be measured in the plasma of prodromal Alzheimer's Disease patients.

05

What researchers measure

Primary outcomes

  1. Brain structural and functional properties

    Brain structural and functional properties will be derived from a multi-modal Magnetic Resonance Imaging protocol.

    Time frame: Day 1

  2. Microbiome profile

    Microbiome profile will be derived from a stool sample obtained from participants.

    Time frame: Day 1

Secondary outcomes

  1. Cognitive functioning

    Cognitive functions will be measured using a neuropsychological protocol.

    Time frame: Day 1

  2. Concentration of blood inflammatory markers

    A panel of key inflammatory mediators (for example, IFNgamma, IL-6, TNFalpha, IL1beta, IL10) will be evaluated in terms RNA expression level in plasma samples obtained from participants.

    Time frame: Day 1

  3. Eating habits

    Information on eating habits will be derived from food questionnaires.

    Time frame: Day 1

06

Study locations

3 of 3 sites recruiting
  • IRCCS San Camillo
    Venice-Lido, Venice 30126, Italy
    • Nicola Filippini · Contact · nicola.filippini@hsancamillo.it · +39 041 2207304
    • Nicola Filippini · Principal investigator
    • Rita Barresi · Sub investigator
    • Lisa Longo · Sub investigator
    • Mattia Spagna · Sub investigator
    • Giulia Serafica · Sub investigator
    Recruiting
  • IRCCS Istituto Centro San Giovanni di Dio Fatebenefratelli
    Brescia, 25125, Italy
    Recruiting
  • Università Ca' Foscari Venezia
    Venice, 30123, Italy
    Recruiting
07

Registry details

Key details

Study ID
NCT05934188
Lead sponsor
IRCCS San Camillo, Venezia, Italy
Collaborators
IRCCS Centro San Giovanni di Dio Fatebenefratelli, Università Ca' Foscari Venezia
Responsible party
Nicola Filippini (Principal Investigator, IRCCS San Camillo, Venezia, Italy) — Principal investigator
First posted
Jul 6, 2023
Start date
May 1, 2023
Primary completion
Apr 30, 2027 (estimated)
Completion
Apr 30, 2027 (estimated)
Last update
Jan 9, 2026

Study contacts

Nicola Filippini
Contact
nicola.filippini@hsancamillo.it
+39 041 2207304
Nicola Filippini
principal investigator · IRCCS San Camillo, Venezia, Italy

Oversight

FDA-regulated drug
No
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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