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Active, not recruitingNCT03409770COMETUpdated Aug 4, 2023

Optimising the Duration of Cooling in Mild Encephalopathy

An interventional study of Therapeutic hypothermia in Neonatal Encephalopathy, Hypothermia Neonatal and Magnetic Resonance Spectroscopy, sponsored by Thayyil, Sudhin. Active, not recruiting at 8 sites in 3 countries. Open to participants aged Up to 6 Hours. Per ClinicalTrials.gov, last updated 2023-08-04.

Sponsored by Thayyil, Sudhin · Not applicable, Interventional, and Treatment

Phase
Not applicable
Study type
Interventional
Enrollment
140
Allocation
Randomized
Ages
Up to 6 Hours
Sex
All
01

Study summary

Phase II randomised control trial of whole body cooling in mild neonatal encephalopathy.

Read the detailed description

Although therapeutic hypothermia for 72 hours reduces brain injury and improves long term neurodevelopmental outcomes after moderate or severe neonatal encephalopathy, the benefits and optimal duration of cooling therapy in mild encephalopathy is not known. Adverse neurodevelopmental outcomes at 2 years occur in 16% of babies with un-treated mild neonatal encephalopathy. In the phase I of the COMET trial, we have shown that it is feasible to identify and randomise babies with mild encephalopathy, and to obtain the primary outcome (proton MR spectroscopy levels of Thalamic N-acetyl Aspartate) accurately. The phase II of the COMET trial will examine the benefits and optimal duration of cooling therapy in babies with mild encephalopathy.

Research questions

  1. Does whole body cooling initiated within 6 hours of birth and continued for 72 hours increase thalamic MR spectroscopy N-acetyl aspartate levels in babies with mild encephalopathy, when compared with those who are not cooled? (Cohort 1)
  2. In babies with mild encephalopathy undergoing cooling therapy as clinical care, does rewarming at 48 hours as opposed to 72 hours result in similar thalamic N-acetyl aspartate levels? (Cohort 2)

Study Population Cohort 1: A total of 60 babies with mild encephalopathy (>36 weeks; >2Kg) aged less than 6 hours will be recruited from several tertiary neonatal units in the UK, Europe, USA and Canada, over a 2 year period. The babies will be randomised to usual care (no cooling) or cooling therapy (core temperature 33 to 34 C) for 72 hours within six hours of birth. MR imaging and spectroscopy will be performed between 4 to 14 days after birth.

Cohort 2: A total of 80 babies will mild encephalopathy (>36 weeks; >2Kg) aged 24 to 48 hours and undergoing cooling therapy as a part of standard clinical care will be recruited from several UK cooling centres, over a 2 year period. The babies will be randomised to rewarming after 48 hours or 72 hours of cooling therapy. MR imaging and spectroscopy will be performed between 4 to 14 days after birth. The babies recruited to cohort 1 will not be eligible for recruitment to cohort 2.

Primary outcome (both cohorts)

  • Proton MR spectroscopy Thalamic N-acetyl aspartate levels between 4 to 14 days of age.

Benefits of the trial These data will inform the national and international guidelines on management of babies with mild neonatal encephalopathy. If a shorter duration of cooling is as good or better than 3 days of cooling, this will reduce the intensive care stays, opioid use and separation from parents.

02

Conditions studied

  • Neonatal Encephalopathy
  • Hypothermia Neonatal
  • Magnetic Resonance Spectroscopy
03

Who can participate

Ages eligible
Up to 6 Hours
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

All of the following three criteria should be met:

  1. Age less than six hours. AND
  2. Evidence of acute perinatal asphyxia

    1. Metabolic acidosis (pH \<7.0 and/or BE >-16) in cord gas or a blood gas within one of birth.

      OR

    2. If the pH or BE is borderline (pH\<7.15 to 7.0) and/or BE >-10 to -16) in cord and/or blood gas within 1h of birth additional evidence of perinatal asphyxia is required, which includes either an acute obstetric event (e.g. cord prolapse, abruption, shoulder dystocia) OR Need for continued resuscitation or ventilation at 10 minutes and/or a 10 min Apgar score \<6
  3. Evidence of mild NE (at-least two abnormalities) on an NICHD neurological examination performed between 1 and 6h of birth.

Exclusion criteria

EXCLUSION CRITERIA

The following group of babies will be excluded prior to randomisation

  1. Babies without encephalopathy
  2. Babies with moderate or severe encephalopathy who meet the current NICE/AAP guidelines for cooling therapy.
  3. Babies with seizures (clinical and/or aEEG/EEG)
  4. Babies with moderate or severe abnormalities on aEEG voltage criteria.
  5. Babies with life threatening congenital malformations
04

Study design

Phase
Not applicable
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Parallel assignment
Masking
Single (Outcomes assessor)
Enrollment
140 participants (estimated)

Study arms

  • No intervention
    Usual care

    Usual care (normothermia) arm

  • Experimental
    Therapeutic hypothermia - 48 h

    Whole body cooling (33 to 34 C) for 48 hours

    Other: Therapeutic hypothermia

  • Experimental
    Therapeutic hypothermia - 72 h

    Whole body cooling (33 to 34 C) for 72 hours

    Other: Therapeutic hypothermia

Interventions

  • OtherTherapeutic hypothermia

    Whole body cooling using a servo controlled device

05

What researchers measure

Primary outcomes

  1. Thalamic N-acetyl aspartate level

    Feasibility of obtaining Proton MR spectroscopy thalamic N-acetyl aspartate level

    Time frame: 4 to 14 days after birth

Secondary outcomes

  1. Brain injury on conventional MR imaging

    Cortical, white matter or deep nuclei injury

    Time frame: 4 to 14 days after birth

  2. Hospital stay

    Duration of hospital stay

    Time frame: Upto 30 days after birth

06

Study locations

8 sites
  • Wayne State University
    Michigan Center, Michigan 48202, United States
  • Luigi Vanvitelli Hospital
    Naples, Italy
  • Birmingham Womens Hospital
    Birmingham, United Kingdom
  • Medway NHS Foundation Trust
    Gillingham, United Kingdom
  • Liverpool Womens Hospital
    Liverpool, United Kingdom
  • Homerton University Hospital
    London, United Kingdom
  • Imperial College London
    London, United Kingdom
  • The Newcastle Upon Tyne NHS Foundation Trust
    Newcastle, United Kingdom
07

References and documents

Publications

  • Prempunpong C, Chalak LF, Garfinkle J, Shah B, Kalra V, Rollins N, Boyle R, Nguyen KA, Mir I, Pappas A, Montaldo P, Thayyil S, Sanchez PJ, Shankaran S, Laptook AR, Sant'Anna G. Prospective research on infants with mild encephalopathy: the PRIME study. J Perinatol. 2018 Jan;38(1):80-85. doi: 10.1038/jp.2017.164. Epub 2017 Nov 2. PubMed 29095433 ↗
  • Oliveira V, Singhvi DP, Montaldo P, Lally PJ, Mendoza J, Manerkar S, Shankaran S, Thayyil S. Therapeutic hypothermia in mild neonatal encephalopathy: a national survey of practice in the UK. Arch Dis Child Fetal Neonatal Ed. 2018 Jul;103(4):F388-F390. doi: 10.1136/archdischild-2017-313320. Epub 2017 Sep 23. PubMed 28942433 ↗
  • Lally PJ, Montaldo P, Oliveira V, Swamy RS, Soe A, Shankaran S, Thayyil S. Residual brain injury after early discontinuation of cooling therapy in mild neonatal encephalopathy. Arch Dis Child Fetal Neonatal Ed. 2018 Jul;103(4):F383-F387. doi: 10.1136/archdischild-2017-313321. Epub 2017 Sep 21. PubMed 28935718 ↗
  • Lally PJ, Pauliah S, Montaldo P, Chaban B, Oliveira V, Bainbridge A, Soe A, Pattnayak S, Clarke P, Satodia P, Harigopal S, Abernethy LJ, Turner MA, Huertas-Ceballos A, Shankaran S, Thayyil S. Magnetic Resonance Biomarkers in Neonatal Encephalopathy (MARBLE): a prospective multicountry study. BMJ Open. 2015 Sep 30;5(9):e008912. doi: 10.1136/bmjopen-2015-008912. PubMed 26423856 ↗
  • Robertson NJ, Thayyil S, Cady EB, Raivich G. Magnetic resonance spectroscopy biomarkers in term perinatal asphyxial encephalopathy: from neuropathological correlates to future clinical applications. Curr Pediatr Rev. 2014;10(1):37-47. doi: 10.2174/157339631001140408120613. PubMed 25055862 ↗
  • Lally PJ, Price DL, Pauliah SS, Bainbridge A, Kurien J, Sivasamy N, Cowan FM, Balraj G, Ayer M, Satheesan K, Ceebi S, Wade A, Swamy R, Padinjattel S, Hutchon B, Vijayakumar M, Nair M, Padinharath K, Zhang H, Cady EB, Shankaran S, Thayyil S. Neonatal encephalopathic cerebral injury in South India assessed by perinatal magnetic resonance biomarkers and early childhood neurodevelopmental outcome. PLoS One. 2014 Feb 5;9(2):e87874. doi: 10.1371/journal.pone.0087874. eCollection 2014. Erratum In: PLoS One. 2014;9(3):e92526. PubMed 24505327 ↗
  • Thayyil S, Chandrasekaran M, Taylor A, Bainbridge A, Cady EB, Chong WK, Murad S, Omar RZ, Robertson NJ. Cerebral magnetic resonance biomarkers in neonatal encephalopathy: a meta-analysis. Pediatrics. 2010 Feb;125(2):e382-95. doi: 10.1542/peds.2009-1046. Epub 2010 Jan 18. PubMed 20083516 ↗

Individual participant data

Plan to share: Yes — Data can be shared unconditionally will be made available when scientific manuscripts are published. Data that cannot be shared publicly (e.g. to protect patient confidentiality) will be by request only. The PI will review each request on case-by-case basis. Upon approval the data requester will be asked to sign a data sharing agreement.

Supporting information: Study protocol, Sap, Icf, Csr, Analytic code

08

Registry details

Key details

Study ID
NCT03409770
Lead sponsor
Thayyil, Sudhin
Collaborators
Wayne State University
Responsible party
Sponsor
First posted
Jan 24, 2018
Start date
Oct 10, 2019
Primary completion
Jun 30, 2024 (estimated)
Completion
Aug 30, 2024 (estimated)
Last update
Aug 4, 2023

Study contacts

Sudhin Thayyil, PhD
principal investigator · Imperial College London

Oversight

Data monitoring committee
No
FDA-regulated drug
No
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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This study is active, not recruiting, as verified in Aug 2023. You cannot join it, but the record below documents what was studied.

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