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Status unknownNCT03272802Updated Mar 27, 2019

Treatment Effect of Edaravone in Patients With Amyotrophic Lateral Sclerosis (ALS)

A Phase 2/3 interventional study of Edaravone and Riluzole in Neuromuscular Diseases, sponsored by Isfahan University of Medical Sciences. Status unknown at 1 site in Iran, Islamic Republic of. Open to participants aged 18 Years to 75 Years. Per ClinicalTrials.gov, last updated 2019-03-27.

Sponsored by Isfahan University of Medical Sciences · Phase 2/3, Interventional, and Treatment

The sponsor has not verified this record recently (last verified Mar 2019), so the status shown — last known as Active, not recruiting — may be out of date.
Phase
Phase 2/3
Study type
Interventional
Enrollment
20
Allocation
Randomized
Ages
18 Years to 75 Years
Sex
All
01

Study summary

Amyotrophic Lateral Sclerosis (ALS) is a neurodegenerative disease that causes the death of 30,000 affected individual every year. Complex nature and unknown pathogenesis of this disease are 2 major reasons for failure of therapeutic interventions. Edaravone is a free radical scavenger that slows down functional decline and prevents from disease progression in ALS patients. FDA newly approved this drug in these patients (2017/5/5). In this study, investigators aimed to assess the treatment effect of this newly approved drug in patients with ALS in a representative Iranian population.

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Conditions studied

  • Neuromuscular Diseases

Keywords

  • Amyotrophic Lateral Sclerosis
  • Edaravone
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Who can participate

Ages eligible
18 Years to 75 Years
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  1. Patients diagnosed as definite or probable ALS according to El Escorial Criteria.
  2. ALS patients who are graded as mild or moderate according to ALS Health State Scale.
  3. Forced vital capacity of at least 80%
  4. Desire of the patient to participate in this study and Signing Written Informed Consent.

Exclusion criteria

Exclusion Criteria:

  1. Incidence of drug's side effects that requires discontinuation of the drug (Edaravone's side effects: Acute kidney injury, Acute allergic reactions, DIC, Thrombocytopenia, Leukopenia).
  2. Desire of the patient to discontinue participating in this study.
  3. the patient starts another drug or herb for ALS during the study.
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Study design

Phase
Phase 2 / Phase 3
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Parallel assignment
Masking
None (open label)
Enrollment
20 participants (estimated)

Study arms

  • Experimental
    Case group

    ALS patients who receive the usual treatment option (Riluzole) for this disease and Edaravone. Instructions: 1. Tab. Rilutek 50 mg PO q12hr on empty stomach. 2. Amp. Edaravone 60 mg per day IV infusion (in normal saline during 1 hour) for 14 days in the first 28 day cycle. 3. Amp. Edaravone 60 mg per day IV infusion (in normal saline during 1 hour) for 10 days in the following 28 day cycles after the first cycle (for 11 cycles).

    Drug: Edaravone · Drug: Riluzole

  • Active comparator
    Control group

    ALS patients who receive the usual treatment option (Riluzole) for this disease. Instructions: 1. Tab. Rilutek 50 mg PO q12hr on empty stomach.

    Drug: Riluzole

Interventions

  • DrugEdaravone

    Edaravone is a free radical scavenger. this drug showed desirable effects like slowing decline of physical function by 33 percent in previous studies.

    Also known as: Radicut, RADICAVA

  • DrugRiluzole

    Riluzole is a treatment option for amyotrophic lateral sclerosis. The occurrence of ventilator-dependence or tracheostomy is delayed in selected patients who treated with this drug.

    Also known as: Rilutek, Teglutik

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What researchers measure

Primary outcomes

  1. Functional evaluation of patient's muscle strength.

    Manual Muscle Testing (MMT) will be used to evaluate functional muscle strength. This procedure evaluates the strength of some proximal and distal muscles of each limb and also the neck region.

    Time frame: At the time of enrolling the patient to study, and then every 3 moths in the following period of 1 year.

  2. functional status of the patient.

    Amyotrophic Lateral Sclerosis Functional Rating Scale-Revised (ALSFRS-R) will be used to evaluate functional status of the patient.

    Time frame: At the time of enrolling the patient to study, and then every 3 moths in the following period of 1 year.

  3. Quality of life in the patients

    Amyotrophic Lateral Sclerosis Assessment Questionnaire (ALSAQ-40) will be used to assess Quality of life in the patients. The Persian version of this questionare will be used in this study.

    Time frame: At the time of enrolling the patient to study, and then every 3 moths in the following period of 1 year.

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Study locations

1 site
  • EMG Department, Alzahra Hospital
    Isfahan, Iran, Islamic Republic of
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References and documents

Publications

  • Shamshiri H, Fatehi F, Davoudi F, Mir E, Pourmirza B, Abolfazli R, Etemadifar M, Harirchian MH, Gharagozli K, Ayromlou H, Basiri K, Zamani B, Rohani M, Sedighi B, Roudbari A, Delavar Kasmaei H, Nikkhah K, Ranjbar Naeini A, Nafissi S. Amyotrophic lateral sclerosis progression: Iran-ALS clinical registry, a multicentre study. Amyotroph Lateral Scler Frontotemporal Degener. 2015;16(7-8):506-11. doi: 10.3109/21678421.2015.1074698. Epub 2015 Oct 5. PubMed 26437387 ↗
  • Abe K, Itoyama Y, Sobue G, Tsuji S, Aoki M, Doyu M, Hamada C, Kondo K, Yoneoka T, Akimoto M, Yoshino H; Edaravone ALS Study Group. Confirmatory double-blind, parallel-group, placebo-controlled study of efficacy and safety of edaravone (MCI-186) in amyotrophic lateral sclerosis patients. Amyotroph Lateral Scler Frontotemporal Degener. 2014 Dec;15(7-8):610-7. doi: 10.3109/21678421.2014.959024. Epub 2014 Oct 6. PubMed 25286015 ↗
  • Writing Group; Edaravone (MCI-186) ALS 19 Study Group. Safety and efficacy of edaravone in well defined patients with amyotrophic lateral sclerosis: a randomised, double-blind, placebo-controlled trial. Lancet Neurol. 2017 Jul;16(7):505-512. doi: 10.1016/S1474-4422(17)30115-1. Epub 2017 May 15. PubMed 28522181 ↗

Individual participant data

Plan to share: No

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Registry details

Key details

Study ID
NCT03272802
Lead sponsor
Isfahan University of Medical Sciences
Responsible party
Alireza Eishi Oskouei (MD, Isfahan University of Medical Sciences) — Principal investigator
First posted
Sep 6, 2017
Start date
Mar 16, 2017
Primary completion
Mar 16, 2019 (estimated)
Completion
Sep 16, 2019 (estimated)
Last update
Mar 27, 2019

Oversight

FDA-regulated drug
No
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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