Friedreich Ataxia: all 111 studies

Page 1 of 2. Open to participants first (28), then studies with results posted, then the rest; newest registration first within each.

• Study of NBIB-223 Gene Therapy in Friedreich's Ataxia (FACET)Not yet recruitingNCT07934303Phase 1
• A Study to Learn More About Friedrich's Ataxia in People Living in the Gulf Cooperation Council (GCC) Region of the WorldNot yet recruitingNCT07887828
• GV101 for Friedreich's Ataxia (FA) TreatmentNot yet recruitingNCT07870590Phase 2
• A Study to Investigate the Safety, Tolerability, and Pharmacokinetics of ATI-105 in Healthy AdultsNot yet recruitingNCT07869654Phase 1
• A Study to Evaluate the Efficacy and Safety of Subcutaneous Nomlabofusp in Subjects With Friedreich's AtaxiaRecruitingNCT07778836Phase 3
• Digital Outcome Assessment Using AI Active Gaming and Motion Capture in Friedreich AtaxiaNot yet recruitingNCT07731971
• Study of LX2006 Gene Therapy in Friedreich Ataxia CardiomyopathyRecruitingNCT07721025Phase 2
• Long-Term Efficacy Study of Vatiquinone for the Treatment of Friedreich's Ataxia (FA)Not yet recruitingNCT07681713Phase 3
• GABA and GSH in FRDAEnrolling by invitationNCT07635030
• Friedreich Ataxia Nerve UltrasundRecruitingNCT07508631
• Cardiac Output and Fatigue in Friedreich's AtaxiaRecruitingNCT07444333Not applicable
• A Study of SGT-212 Gene Therapy in Friedreich's AtaxiaRecruitingNCT07180355Phase 1
• Electroencephalogram in Patients With Friedreich's Ataxia for the Study of the Structural and Functional Connectome.RecruitingNCT07095062Not applicable
• The Use of Assistive Gait Devices Can Reduce the Risk of Falls in Patients With Neuromuscular Diseases Following a Training Period.Enrolling by invitationNCT07072676Not applicable
• Efficacy of Omaveloxolone Treatment for Dysphagia in French Patients With Friedreich's AtaxiaRecruitingNCT07013292
• A Multiple Ascending Dose Study of DT-216P2 in Patients With Friedreich's AtaxiaRecruitingNCT06874010Phase 1/2
• Clinical Course Of Disease In Participants With FA-CMRecruitingNCT06865482
• A Single Ascending Dose Study of DT-216P2 in Normal Healthy ParticipantsNot yet recruitingNCT06772870Phase 1
• A Study to Learn How BIIB141 (Omaveloxolone) Affects the Health of Participants With Friedrich's Ataxia Who Took it During Pregnancy and/or During Breastfeeding and About the Health of Their BabiesRecruitingNCT06628687
• A Study to Learn More About the Long-Term Safety of BIIB141 (Omaveloxolone) in Participants With Friedreich's Ataxia Who Are Prescribed it by Their Own DoctorsRecruitingNCT06623890
• Development and Validation of the FBIndex to Determine the Risk of Falls for Patients With Neuromuscular DisordersEnrolling by invitationNCT06605612
• An Open-Label Study of CTI-1601 in Subjects With Friedreich's AtaxiaRecruitingNCT06447025Phase 2
• Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History StudyRecruitingNCT06016946
• Patient-reported, Health Economic and Psychosocial Outcomes in Friedreich AtaxiaRecruitingNCT05943002
• Phase IA and IB Study of AAVrh.10hFXN Gene Therapy for the Cardiomyopathy of Friedreich's AtaxiaRecruitingNCT05302271Phase 1
• Biomarkers in Friedreich's AtaxiaRecruitingNCT02497534
• Characterization of the Cardiac Phenotype of Friedreich's Ataxia (FRDA)RecruitingNCT02316314
• Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at SanfordRecruitingNCT01793168
• FRDA Investigator Initiated Study (IIS) With ElamipretideCompletedNCT05168774Phase 1/2Results posted
• NAD+ Precursor Supplementation in Friedreich's AtaxiaCompletedNCT04817111Phase 2Results posted
• A Study to Assess the Efficacy and Safety of Vatiquinone for the Treatment of Participants With Friedreich AtaxiaCompletedNCT04577352Phase 2/3Results posted
• A Study to Assess Efficacy, Long Term Safety and Tolerability of RT001 in Subjects With Friedreich's AtaxiaCompletedNCT04102501Phase 3Results posted
• Neurology Measures in FA ChildrenCompletedNCT03418740Results posted
• Efficacy, Tolerability, and Pharmacokinetics of Multiple Doses of Oral TAK-831 in Adults With Friedreich AtaxiaCompletedNCT03214588Phase 2Results posted
• Rehabilitative Trial With Cerebello-Spinal tDCS in Neurodegenerative AtaxiaCompletedNCT03120013Not applicableResults posted
• Long-Term Safety Extension Study of ACTIMMUNE® (Interferon γ-1b) in Children and Young Adults With Friedreich's AtaxiaCompletedNCT02797080Phase 3Results posted
• (+) Epicatechin to Treat Friedreich's AtaxiaCompletedNCT02660112Phase 2Results posted
• Safety, Tolerability and Efficacy of ACTIMMUNE® Dose Escalation in Friedreich's Ataxia StudyCompletedNCT02593773Phase 3Results posted
• A First in Human Study of RT001 in Patients With Friedreich's AtaxiaCompletedNCT02445794Phase 1/2Results posted
• Safety, Tolerability and Efficacy of ACTIMMUNE® Dose Escalation in Friedreich's AtaxiaCompletedNCT02415127Phase 3Results posted
• A Study to Learn About the Effects and Safety of RTA 408 (Omaveloxolone) in People Aged 16 to 40 With Friedreich's AtaxiaCompletedNCT02255435Phase 2Results posted
• Interferon Gamma-1b in Friedreich Ataxia (FRDA)CompletedNCT01965327Phase 2Results posted
• Safety and Pharmacology Study of VP 20629 in Adults With Friedreich's AtaxiaCompletedNCT01898884Phase 1Results posted
• An Objective Double-blind Evaluation of Bupropion and Citalopram in an Individual With Friedreich AtaxiaCompletedNCT01716221Phase 4Results posted
• Patient Reported Outcomes in Friedreich's Ataxia Patients After Withdrawal From Treatment With Idebenone (PROTI)CompletedNCT01303406Phase 3Results posted
• A Study of Efficacy, Safety and Tolerability of Idebenone in the Treatment of Friedreich's Ataxia (FRDA) PatientsCompletedNCT00905268Phase 3Results posted
• Efficacy of EGb761 in Patients Suffering From Friedreich AtaxiaCompletedNCT00824512Phase 2Results posted
• Study to Assess the Safety and Tolerability of Idebenone in the Treatment of Friedreich's Ataxia PatientsCompletedNCT00697073Phase 3Results posted
• Study to Assess the Efficacy, Safety and Tolerability of Idebenone in the Treatment of Friedreich's AtaxiaCompletedNCT00537680Phase 3Results posted
• A Study to Learn More About the Effects and Long-Term Safety of Omaveloxolone (BIIB141) in Children and Teens With Friedreich's AtaxiaActive, not recruitingNCT06953583Phase 3
• Efficacy of Stabilometric Platform to Improve Standing Balance in Patients With Friedreich's AtaxiaActive, not recruitingNCT06692296Not applicable
• A Study to Assess Nomlabofusp in Adolescents and Children With Friedreich's AtaxiaTerminatedNCT06681766Phase 1
• Understanding the Natural History Early in the Course or Presentation of Friedreich AtaxiaWithdrawnNCT06560346
• Respiratory Training in Friedreich's AtaxiaCompletedNCT06539598Not applicable
• Measurement of Frataxin mRNA in BiofluidsCompletedNCT06496451
• A Study of ASP2016 in Adults Who Have Heart Disease Associated With Friedreich AtaxiaWithdrawnNCT06483802Phase 1
• A Study to Find Out How BIIB141 (Omaveloxolone) is Processed in the Body and to Learn More About Its Safety in Participants With Friedreich's Ataxia Aged 2 to 15 Years OldActive, not recruitingNCT06054893Phase 1
• Characterisation of the Cognitive Profile of Patients Suffering From Friedreich's AtaxiaActive, not recruitingNCT05874388
• A Double-Blind, Placebo-Controlled, Dose Exploration Study of CTI-1601 in Adult Subjects With Friedreich's AtaxiaCompletedNCT05579691Phase 2
• Study to Evaluate Multiple Ascending Dose and Multi-Dose of DT-216 in Adult Patients With Friedreich AtaxiaCompletedNCT05573698Phase 1
• A Study to Assess the Safety and Efficacy of Vatiquinone in Participants With Friedreich AtaxiaActive, not recruitingNCT05515536Phase 3
• A Study of Vatiquinone for the Treatment of Participants With Friedreich AtaxiaCompletedNCT05485987Phase 2
• Gene Therapy for Cardiomyopathy Associated With Friedreich's AtaxiaActive, not recruitingNCT05445323Phase 1/2
• Study to Evaluate DT-216 in Adult Patients With Friedreich AtaxiaCompletedNCT05285540Phase 1
• Determine Range of Tissue Frataxin Concentrations and Other Potential BiomarkersCompletedNCT05028764
• Evaluation of the Effect of Artesunate in Friedreich Ataxia (FA)CompletedNCT04921930Phase 1/2
• Evaluation of the Effects of Calcitriol's in the Neurological Symptoms of Friedreich's Ataxia PatientsCompletedNCT04801303Phase 4
• Coronary Artery Disease in Patients With Friedreich's AtaxiaCompletedNCT04649866Not applicable
• Longitudinal Analysis of Oral Communication in Friedreich's AtaxiaCompletedNCT04631224
• Home Based Tele-exercise for People With Chronic Neurological ImpairmentsActive, not recruitingNCT04564495Not applicable
• Biomarker for Friedreich's Ataxia (BioFridA)Status unknownNCT04548921
• Multiple Ascending Dose Study of CTI-1601 Versus Placebo in Subjects With Friedreich's AtaxiaCompletedNCT04519567Phase 1
• A Natural History Study to TRACK Brain and Spinal Cord Changes in Individuals with Friedreich Ataxia (TRACK-FA)Active, not recruitingNCT04349514
• Characterization of the Interruptions of the GAA Expansion and Study of Their Influence on the Severity of Friedreich's AtaxiaCompletedNCT04346238
• Safety and Efficacy of Etravirine in Friedreich Ataxia PatientsCompletedNCT04273165Phase 2
• Instrumented Data Exchange for Ataxia StudyCompletedNCT04268147
• A Study to Assess Variation in Potential Biomarkers in Friedreich AtaxiaCompletedNCT04255680
• Single Ascending Dose Study of CTI-1601 Versus Placebo in Subjects With Friedreich's AtaxiaCompletedNCT04176991Phase 1
• Micronised Resveratrol as a Treatment for Friedreich AtaxiaCompletedNCT03933163Phase 2
• A Clinical Study to Evaluate the Effect of MIN-102 on the Progression of Friedreich's Ataxia in Male and Female PatientsCompletedNCT03917225Phase 2
• Open Trail of γIFN for Friedreich AtaxiaCompletedNCT03888664Phase 2
• Study of the Efficacy and Safety of Nicotinamide in Patients With Friedreich AtaxiaWithdrawnNCT03761511Phase 2
• TCA Cycle in the Dentate in Friedreich's AtaxiaCompletedNCT03122925
• FA Clinical Outcome MeasuresActive, not recruitingNCT03090789
• A Study to Characterize the Cardiac Phenotype of Individuals With Friedreich's Ataxia (CARFA Study)CompletedNCT02840669Not applicable
• Rosuvastatin (Crestor) in Friedreich AtaxiaCompletedNCT02705547Early Phase 1
• Genetic and Environmental Determinants That Control Metabolism in Pulmonary HypertensionCompletedNCT02594917
• Methylprednisolone Treatment of Friedreich AtaxiaCompletedNCT02424435Early Phase 1
• Preliminary Study of the Scale To Assess Ataxia and Neurologic Dysfunction (STAND)CompletedNCT02179333
• Patient Registry of the European Friedreich's Ataxia Consortium for Translational Studies (EFACTS)CompletedNCT02069509
• A Phase IIa Trial to Test Safety and Efficacy Interferon Gamma Treatment in Elevating Frataxin Levels in FRDA PatientsCompletedNCT02035020Phase 2
• EPI-743 in Friedreich's Ataxia Point MutationsCompletedNCT01962363Phase 2
• An Open-label Study of the Effects of Acetyl-L-Carnitine on Cardiovascular Outcomes in Friedreich's AtaxiaStatus unknownNCT01921868Not applicable
• Early and Longitudinal Assessment of Neurodegeneration in the Brain and Spinal Cord in Friedreich's AtaxiaCompletedNCT01776164
• Safety and Efficacy of EPI-743 in Patients With Friedreich's AtaxiaCompletedNCT01728064Phase 2
• Efficacy Study of Epoetin Alfa in Friedreich AtaxiaCompletedNCT01493973Phase 2
• EPI-743 for Mitochondrial Respiratory Chain DiseasesNo longer availableNCT01370447
• A Study of Resveratrol as Treatment for Friedreich AtaxiaCompletedNCT01339884Phase 1/2
• Efficacy of Riluzole in Hereditary Cerebellar AtaxiaCompletedNCT01104649Phase 2/3
• Safety and Efficacy Study of A0001 in Subjects With Friedreich's AtaxiaCompletedNCT01035671Phase 2

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