Adrenoleukodystrophy: all 68 studies
Page 1 of 1. Open to participants first (19), then studies with results posted, then the rest; newest registration first within each.
- Adrenal Diseases in the Population of Modena: A Clinical-Epidemiological Database of Patients Referred to the Adrenal Disorders Outpatient Clinic of the Clinical Unit of Endocrinology at the Modena University Hospital (AOU Modena)RecruitingNCT07920198
- Epidural Spinal Cord Stimulation for Lower-limb Impairment in AdrenomyeloneuropathyRecruitingNCT06796920Not applicable
- A Study of Participants With Cerebral Adrenoleukodystrophy (CALD) Treated With Elivaldogene AutotemcelRecruitingNCT06224413
- Disease Progression in Women With X-linked AdrenoleukodystrophyRecruitingNCT06178120
- Registry of X-linked AdrenoleukodystrophyRecruitingNCT05939232
- Validation of a Prognostic Biomarker Using Brain Diffusion MRI in X-linked AdrenoleukodystrophyNot yet recruitingNCT05911919
- Home Exercise for Individuals With Neurodegenerative DiseaseRecruitingNCT05443906Not applicable
- Modeling Macrophages Activation Pattern in X-linked Adrenoleukodystrophy, Metachromatic Leukodystrophy and Adult Onset Leukoencephalopathy With Axonal Spheroids and Pigmented GliaRecruitingNCT04925349
- Longitudinal Study of Ultra-rare Inherited Metabolic and Degenerative Neurological Diseases.RecruitingNCT04880356
- Quality of Life in Women With X-linked AdrenoleukodystrophyRecruitingNCT04675749
- Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RICRecruitingNCT04528355
- Precision Exercise in Children With Malignant HemopathiesRecruitingNCT04090268Not applicable
- Adrenoleukodystrophy National Registry StudyRecruitingNCT03789721
- IT and IV Lentiviral Gene Therapy for X-ALDNot yet recruitingNCT03727555Not applicable
- The Myelin Disorders Biorepository ProjectRecruitingNCT03047369
- Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and AdrenoleukodystrophyRecruitingNCT02559830Phase 1/2
- UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like CellsRecruitingNCT02254863Phase 1
- Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCTRecruitingNCT01962415Phase 2
- Expanded Access to T-cell Depleted Haplo-Identical Stem Cells for Patients Receiving Haplo-Identical and Unrelated Cord Blood TransplantsAvailableNCT01881334
- A Study to Evaluate Administration of SBT101 Gene Therapy in Adult Patients With Adrenomyeloneuropathy (AMN)TerminatedNCT05394064Phase 1/2Results posted
- A Clinical Study to Assess the Efficacy and Safety of Gene Therapy for the Treatment of Cerebral Adrenoleukodystrophy (CALD)CompletedNCT03852498Phase 3Results posted
- Repetitive Transcranial Magnetic Stimulation as Therapy in Hereditary Spastic Paraplegia and AdrenomyeloneuropathyCompletedNCT03627416Not applicableResults posted
- Conditioning Regimen for Allogeneic Hematopoietic Stem-Cell TransplantationCompletedNCT03513328Phase 1/2Results posted
- LeukoSEQ: Whole Genome Sequencing as a First-Line Diagnostic Tool for LeukodystrophiesCompletedNCT02699190Results posted
- A Study of the Efficacy and Safety of Hematopoietic Stem Cells Transduced With Lenti-D Lentiviral Vector for the Treatment of Cerebral Adrenoleukodystrophy (CALD)CompletedNCT01896102Phase 2/3Results posted
- Reduced-Intensity Hematopoietic Stem Cell Transplant for High Risk Lysosomal and Peroxisomal DisordersCompletedNCT01626092Not applicableResults posted
- Exercise Study of Function and Pathology for Women With X-linked AdrenoleukodystrophyCompletedNCT01594853Not applicableResults posted
- Allogeneic Bone Marrow Transplant for Inherited Metabolic DisordersCompletedNCT01043640Phase 2Results posted
- HSCT for High Risk Inherited Inborn ErrorsCompletedNCT00383448Phase 2Results posted
- Stem Cell Transplant for Inborn Errors of MetabolismCompletedNCT00176904Phase 2/3Results posted
- Compassionate Treatment of Patients With Inborn Errors of Bile Acid Metabolism With Cholic AcidCompletedNCT00007020Phase 3Results posted
- Effect of Glycerol Trierucate on Clinical Course of AdrenoleukodystrophyTerminatedNCT00004418Phase 2Results posted
- MT2022-01: MSCs for ALDSuspendedNCT06030648Phase 1
- A Clinical Study to Assess the Efficacy and Safety of Leriglitazone in Adult Male Subjects With Cerebral AdrenoleukodystrophyActive, not recruitingNCT05819866Phase 3
- Baby Detect : Genomic Newborn ScreeningCompletedNCT05687474
- Study to Assess PXL065 in Subjects With Adrenomyeloneuropathy (AMN) Form of X-linked Adrenoleukodystrophy (X-ALD or ALD)WithdrawnNCT05200104Phase 2
- Study to Assess PXL770 in Subjects With Adrenomyeloneuropathy (AMN) Form of X-linked Adrenoleukodystrophy (X-ALD or ALD)WithdrawnNCT05146284Phase 2
- Study of Disease Progression in Adults With Inherited Forms of Spastic ParaplegiaTerminatedNCT05008874
- Treating Leg Symptoms in Women With X-linked AdrenoleukodystrophyActive, not recruitingNCT05003648Phase 4
- A Study to Assess the Pharmacodynamics of VK0214 in Male Subjects With AMNCompletedNCT04973657Phase 1
- SMART-ALD - A New Lifestyle Intervention to Improve Quality of Life in Women With X-linked Adrenoleukodystrophy (X-ALD)CompletedNCT04687007Not applicable
- A Clinical Study in Male Pediatric Patients With Cerebral X-linked Adrenoleukodystrophy (Cald) to Assess the Effects of MIN-102 Treatment on Disease Progression Prior to Human Stem Cell Transplant (HSCT)Status unknownNCT04528706Phase 2
- Plasma Exchange With Albumin in AMN PatientsCompletedNCT04303416Phase 2/3
- Effect of Pioglitazone Administered to Patients With AdrenomyeloneuropathyCompletedNCT03864523Phase 2
- Multi-center Clinical Study on the Diagnosis and Treatment Management of Rare Neurological Disease in ChildrenWithdrawnNCT03649919
- A Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of OP-101 After Intravenous Administration in Healthy VolunteersCompletedNCT03500627Phase 1
- A Study to Prospectively Assess Disease Progression in Male Children With X-ALDStatus unknownNCT03278899
- A Clinical Study to Evaluate the Efficacy and Safety of MIN-102 (IMP) in Male AMN PatientsCompletedNCT03231878Phase 2/3
- Safety, Pharmacokinetics and Pharmacodynamics of NV1205 in Pediatric Male Subjects With AdrenoleukodystrophyWithdrawnNCT03196765Phase 1/2
- MD1003-AMN MD1003 in AdrenomyeloneuropathyCompletedNCT02961803Phase 2/3
- Newborn Screening for AdrenoleukodystrophyCompletedNCT02952482
- Early Diagnosis Of Childhood Cerebral ALDWithdrawnNCT02948062
- Long-term Follow-up of Participants With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug ProductActive, not recruitingNCT02698579
- A Pilot Study of Vitamin D in Boys With X-linked AdrenoleukodystrophyCompletedNCT02595489Phase 1
- MT2014-14 IT-MSC for Advanced Cerebral Adrenoleukodystrophy (cALD)WithdrawnNCT02410239Phase 1
- Expanded Access for Lorenzo's Oil (GTO/GTE) in AdrenoleukodystrophyNo longer availableNCT02233257
- Observational Study to Evaluate Allogeneic HSCT Outcomes for Cerebral Adrenoleukodystrophy (CALD)TerminatedNCT02204904
- Safety and Pharmacodynamic Study of Sobetirome in X-Linked Adrenoleukodystrophy (X-ALD)WithdrawnNCT01787578Phase 1
- Human Placental-Derived Stem Cell TransplantationCompletedNCT01586455Phase 1
- A Clinical Trial for AMN: Validation of Biomarkers of Oxidative Stress, Efficacy and Safety of a Mixture of AntioxidantsCompletedNCT01495260Phase 2
- Phase I/II Pilot Study of Mixed Chimerism to Treat Inherited Metabolic DisordersTerminatedNCT01372228Phase 1/2
- The Effect of Bezafibrate on the Level of Very Long Chain Fatty Acids (VLCFA) in X-linked Adrenoleukodystrophy (X-ALD)CompletedNCT01165060Not applicable
- ALD-101 Adjuvant Therapy of Unrelated Umbilical Cord Blood Transfusion (UCBT) in Patients With Inherited Metabolic DiseasesTerminatedNCT00654433Phase 3
- A Phase III Trial of Lorenzo's Oil in AdrenomyeloneuropathyTerminatedNCT00545597Phase 3
- Clinical Study and Gene Mutation Analysis of Adrenoleukodystrophy in Taiwanese ChildrenStatus unknownNCT00278044Not applicable
- Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell TransplantationStatus unknownNCT00005900
- Randomized Study of Beta Interferon and Thalidomide in Patients With AdrenoleukodystrophyCompletedNCT00004450Not applicable
- Study of Bile Acids in Patients With Peroxisomal DisordersTerminatedNCT00004442Not applicable