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RecruitingNCT07011719Updated Sep 29, 2026

Study of Casdatifan and Cabozantinib Versus Placebo and Cabozantinib in Patients With Advanced Clear Cell Renal Cell Carcinoma

A Phase 3 interventional study of Casdatifan and Cabozantinib in Metastatic Clear Cell Renal Cell Carcinoma and Advanced Clear Cell Renal Cell Carcinoma, sponsored by Arcus Biosciences, Inc.. Recruiting at 183 sites in 17 countries. Open to participants aged 18 Years and older. Per ClinicalTrials.gov, last updated 2026-09-29.

Sponsored by Arcus Biosciences, Inc. · Phase 3, Interventional, and Treatment

Phase
Phase 3
Study type
Interventional
Enrollment
720
Allocation
Randomized
Ages
18 Years and older
Sex
All
01

Study summary

The purpose of the study is to evaluate the progression-free survival (PFS) of casdatifan versus placebo when each is given in combination with cabozantinib in adult patients with confirmed advanced or metastatic clear cell Renal Cell Carcinoma who have experienced progression on or after prior anti-PD-1 or anti-PD-L1 immunotherapy.

02

Conditions studied

  • Metastatic Clear Cell Renal Cell Carcinoma
  • Advanced Clear Cell Renal Cell Carcinoma

Keywords

  • Casdatifan
  • Metastatic Clear Cell Renal Cell Carcinoma
  • Advanced Clear Cell Renal Cell Carcinoma
  • Kidney Cancer
  • PEAK-1
  • AB521
  • ccRCC
03

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  • Unresectable and measurable locally advanced or metastatic renal cell carcinoma with a primary clear cell component.
  • A Karnofsky Performance Status (KPS) score ≥ 80%
  • At least 1 target lesion measurable by computed tomography/magnetic resonance imaging per RECIST 1.1, not within a field of prior radiation therapy.
  • Adequate organ and marrow function, ≤ 1 week prior to randomization.
  • Women of childbearing potential (WOCBP) must have a negative serum pregnancy test.

Exclusion criteria

Exclusion Criteria:

  • Received prior treatment with a HIF-2α inhibitor or cabozantinib.
  • Other prior malignancy active within the previous year except for locally curable cancers that have been apparently cured.
  • Ongoing clinically significant toxicities related to any prior anticancer treatment, or toxicities Grade ≥ 3 per National Cancer Institute Common Terminology Criteria for Adverse Events, version 5.0 (NCI CTCAE v5.0) regardless of relatedness to prior anticancer therapies.
  • Uncontrolled or poorly controlled hypertension, defined as a sustained blood pressure > 150 mmHg systolic or > 90 mmHg diastolic despite optimal antihypertensive treatment.
  • History of leptomeningeal disease or spinal cord compression.

NOTE: Other protocol defined Inclusion/Exclusion criteria may apply.

04

Study design

Phase
Phase 3
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Parallel assignment
Masking
Quadruple (Participant, Care provider, Investigator, Outcomes assessor)
Enrollment
720 participants (estimated)

Study arms

  • Experimental
    Arm A (Experimental Arm)

    Casdatifan and cabozantinib taken orally

    Drug: Casdatifan · Drug: Cabozantinib

  • Placebo comparator
    Arm B (Comparator Arm)

    Placebo and cabozantinib taken orally

    Drug: Cabozantinib · Drug: Placebo

Interventions

  • DrugCasdatifan

    Administered as specified in the treatment arm

    Also known as: AB521

  • DrugCabozantinib

    Administered as specified in the treatment arm

  • DrugPlacebo

    Administered as specified in the treatment arm

05

What researchers measure

Primary outcomes

  1. Progression-free Survival (PFS) as assessed by Blinded Independent Central Review (BICR) according to RECIST 1.1

    Time frame: up to approximately 33 months

Secondary outcomes

  1. Overall Survival (OS)

    Time frame: up to approximately 64 months

  2. Objective Response Rate (ORR) as assessed by Blinded Independent Central Review (BICR) according to RECIST 1.1

    Time frame: up to approximately 33 months

  3. Duration of Response (DOR) as assessed by Blinded Independent Central Review (BICR) according to RECIST 1.1

    Time frame: up to approximately 33 months

  4. Disease Control Rate (DCR) by Blinded Independent Central Review (BICR)

    Time frame: up to approximately 33 months

  5. The incidence and severity of treatment-emergent adverse events (TEAEs) and treatment-emergent serious adverse events (SAEs)

    Time frame: up to approximately 33 months

  6. Time to first symptom deterioration in National Comprehensive Cancer Network/Functional Assessment of Cancer Therapy-Kidney Symptom Index - Disease Related Symptoms (NFKSI-DRS) Items 1-9 sub-scale score.

    Time frame: up to approximately 33 months

06

Study locations

183 of 183 sites recruiting
  • Research Site
    Gilbert, Arizona 85234, United States
    Recruiting
  • Research Site
    Goodyear, Arizona 85338, United States
    Recruiting
  • Research Site
    Phoenix, Arizona 85054, United States
    Recruiting
  • Research Site
    Duarte, California 91010, United States
    Recruiting
  • Research Site
    Irvine, California 91304, United States
    Recruiting
  • Research Site
    La Jolla, California 92103, United States
    Recruiting
  • Research Site
    Los Angeles, California 90095, United States
    Recruiting
  • Research Site
    Palo Alto, California 94304, United States
    Recruiting
  • Research Site
    Sacramento, California 95817, United States
    Recruiting
  • Research Site
    San Diego, California 92103, United States
    Recruiting
  • Research Site
    Aurora, Colorado 80045, United States
    Recruiting
  • Research Site
    New Haven, Connecticut 06519, United States
    Recruiting
  • Research Site
    Washington D.C., District of Columbia 20057, United States
    Recruiting
  • Research Site
    Jacksonville, Florida 32224, United States
    Recruiting
  • Research Site
    Miami, Florida 33136, United States
    Recruiting
  • Research Site
    Orlando, Florida 32804, United States
    Recruiting
  • Research Site
    Atlanta, Georgia 30318, United States
    Recruiting
  • Research Site
    Atlanta, Georgia 30322, United States
    Recruiting
  • Research Site
    Newnan, Georgia 30265, United States
    Recruiting
  • Research Site
    Zion, Illinois 60099, United States
    Recruiting
  • Research Site
    Indianapolis, Indiana 46202, United States
    Recruiting
  • Research Site
    Louisville, Kentucky 40207, United States
    Recruiting
  • Research Site
    Jefferson, Louisiana 70121, United States
    Recruiting
  • Research Site
    Baltimore, Maryland 21287, United States
    Recruiting
  • Research Site
    Boston, Massachusetts 02114, United States
    Recruiting
  • Research Site
    Boston, Massachusetts 02215, United States
    Recruiting
  • Research Site
    Rochester, Minnesota 55905, United States
    Recruiting
  • Research Site
    St Louis, Missouri 63110, United States
    Recruiting
  • Research Site
    Omaha, Nebraska 68198, United States
    Recruiting
  • Research Site
    New Brunswick, New Jersey 08903, United States
    Recruiting
  • Research Site
    Buffalo, New York 14263, United States
    Recruiting
  • Research Site
    New York, New York 10461, United States
    Recruiting
  • Research Site
    Rochester, New York 14642, United States
    Recruiting
  • Research Site
    Chapel Hill, North Carolina 27514, United States
    Recruiting
  • Research Site
    Durham, North Carolina 27710, United States
    Recruiting
  • Research Site
    Cleveland, Ohio 44106, United States
    Recruiting
  • Research Site
    Portland, Oregon 97212, United States
    Recruiting
  • Research Site
    Monroeville, Pennsylvania 15146, United States
    Recruiting
  • Research Site
    Charleston, South Carolina 29425, United States
    Recruiting
  • Research Site
    Nashville, Tennessee 37203, United States
    Recruiting
  • Research Site
    Nashville, Tennessee 37232, United States
    Recruiting
  • Research Site
    Dallas, Texas 75390, United States
    Recruiting
  • Research Site
    Lubbock, Texas 79430, United States
    Recruiting
  • Research Site
    Salt Lake City, Utah 84112, United States
    Recruiting
  • Research Site
    Charlottesville, Virginia 22903, United States
    Recruiting
  • Research Site
    Seattle, Washington 98109, United States
    Recruiting
  • Research Site
    Buenos Aires, Argentina
    Recruiting
  • Research Site
    La Plata, Argentina
    Recruiting
  • Research Site
    Pilar, Argentina
    Recruiting
  • Research Site
    Rosario, Argentina
    Recruiting
  • Research Site
    Viedma, Argentina
    Recruiting
  • Research Site
    Box Hill, Australia
    Recruiting
  • Research Site
    Camperdown, Australia
    Recruiting
  • Research Site
    Chermside, Australia
    Recruiting
  • Research Site
    Elizabeth Vale, Australia
    Recruiting
  • Research Site
    Frankston, Australia
    Recruiting
  • Research Site
    Frenchs Forest, Australia
    Recruiting
  • Research Site
    Heidelberg, Australia
    Recruiting
  • Research Site
    Hobart, Australia
    Recruiting
  • Research Site
    Kurralta Park, Australia
    Recruiting
  • Research Site
    Macquarie Park, Australia
    Recruiting
  • Research Site
    South Brisbane, Australia
    Recruiting
  • Research Site
    St Albans, Australia
    Recruiting
  • Research Site
    Subiaco, Australia
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  • Research Site
    Westmead, Australia
    Recruiting
  • Research Site
    Calgary, Canada
    Recruiting
  • Research Site
    Edmonton, Canada
    Recruiting
  • Research Site
    Hamilton, Canada
    Recruiting
  • Research Site
    London, Canada
    Recruiting
  • Research Site
    Montreal, Canada
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  • Research Site
    Sherbrooke, Canada
    Recruiting
  • Research Site
    Toronto, Canada
    Recruiting
  • Research Site
    Vancouver, Canada
    Recruiting
  • Research Site
    Brno, Czechia
    Recruiting
  • Research Site
    Brno-střed, Czechia
    Recruiting
  • Research Site
    České Budějovice, Czechia
    Recruiting
  • Research Site
    Hradec, Czechia
    Recruiting
  • Research Site
    Prague, Czechia
    Recruiting
  • Research Site
    Angers, France
    Recruiting
  • Research Site
    Brest, France
    Recruiting
  • Research Site
    Caen, France
    Recruiting
  • Research Site
    Clermont-Ferrand, France
    Recruiting
  • Research Site
    Lille, France
    Recruiting
  • Research Site
    Marseille, France
    Recruiting
  • Research Site
    Montpellier, France
    Recruiting
  • Research Site
    Paris, France
    Recruiting
  • Research Site
    Pessac, France
    Recruiting
  • Research Site
    Poitiers, France
    Recruiting
  • Research Site
    Reims, France
    Recruiting
  • Research Site
    Rennes, France
    Recruiting
  • Research Site
    Strasbourg, France
    Recruiting
  • Research Site
    Toulouse, France
    Recruiting
  • Research Site
    Villejuif, France
    Recruiting
  • Research Site
    Berlin, Germany
    Recruiting
  • Research Site
    Dresden, Germany
    Recruiting
  • Research Site
    Essen, Germany
    Recruiting
  • Research Site
    Frankfurt, Germany
    Recruiting
  • Research Site
    Freiburg im Breisgau, Germany
    Recruiting
  • Research Site
    Halle, Germany
    Recruiting
  • Research Site
    Hanover, Germany
    Recruiting

Showing the first 100 of 183 sites across 17 countries.

07

References and documents

Publications

  • Mailyan AK, Mata G, Beatty JW, Drew SL, Fournier J, Yu K, Gal B, Kalisiak J, Yan X, Tran A, Su Y, Rosen BR, Jeffrey JL, Hardman C, Epplin M, Ginn E, Sun M, Chen A, Fabila P, Sivick KE, Schweickert PG, Piovesan D, Meleza C, Pham AT, Chen PY, Jin L, Walters MJ, Walker NP, Kwon HJ, Leleti MR, Powers JP, Lawson KV. Discovery of Casdatifan, Part II: A Potent and Orally Bioavailable Inhibitor of Hypoxia Inducible Factor-2alpha. J Med Chem. 2026 Jun 25;69(12):14952-14988. doi: 10.1021/acs.jmedchem.5c03724. Epub 2026 Jun 5. PubMed 42246926 ↗

Individual participant data

Plan to share: Yes — Arcus will provide access to individual de-identified participant data and related study documents (e.g., protocol, Statistical Analysis Plan \[SAP\], Clinical Study Report \[CSR\]) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions.

Supporting information: Study protocol, Sap, Csr

08

Registry details

Key details

Study ID
NCT07011719
Lead sponsor
Arcus Biosciences, Inc.
Responsible party
Sponsor
First posted
Jun 10, 2025
Start date
Sep 8, 2025
Primary completion
Apr 2028 (estimated)
Completion
Dec 2030 (estimated)
Last update
Sep 29, 2026

Study contacts

Medical Director
Contact
clinicaltrials@arcusbio.com
+1-510-462-3330
Medical Director
study director · Arcus Biosciences

Oversight

Data monitoring committee
Yes
FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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