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Active, not recruitingNCT06987643RESTOREUpdated Jul 8, 2026

A Clinical Study to Investigate the Effect of Oral Neflamapimod on Motor Recovery After Acute Ischaemic Stroke

A Phase 2 interventional study of Neflamapimod and Placebo in Moderate to Severe Acute Ischaemic Stroke and Ischaemic Stroke, sponsored by EIP Pharma Inc. Active, not recruiting at 10 sites in Australia. Open to participants aged 45 Years and older. Per ClinicalTrials.gov, last updated 2026-07-08.

Sponsored by EIP Pharma Inc · Phase 2, Interventional, and Treatment

Phase
Phase 2
Study type
Interventional
Enrollment
90
Allocation
Randomized
Ages
45 Years and older
Sex
All
01

Study summary

The purpose of this interventional study is to determine whether neflamapimod can improve residual physical disability and/or cognitive dysfunction after Moderate to Severe Acute Ischaemic Stroke.

02

Conditions studied

  • Moderate to Severe Acute Ischaemic Stroke
  • Ischaemic Stroke

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03

Who can participate

Ages eligible
45 Years and older
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  • Male or female participants must be aged 45 years or over at the time of signing the informed consent.
  • Confirmed acute ischaemic stroke in the anterior circulation (middle or anterior cerebral artery) with onset of symptoms between 2 and 7 days prior to screening and evaluation.
  • National Institutes of Health Stroke Scale (NIHSS) score between 5 and 20 (inclusive) and exhibiting unilateral motor deficit (i.e. motor NIHSS ≥ 2 on affected side of the body).
  • Fugl-Meyer Assessment of Motor Recovery after Ischaemic Stroke (FMMS) total motor components score of 80 or below.
  • No history of learning difficulties that may interfere with their ability to complete the cognitive tests.

Exclusion criteria

Exclusion Criteria:

  • Evidence of progressive or unstable stroke or intra-cerebral haemorrhage in the opinion of the investigator
  • Participants needing carotid surgery within 3 months
  • Ongoing major and active psychiatric disorder and/or other concurrent medical condition that, in the opinion of the Investigator, might compromise safety and/or compliance with study requirements.
  • History of alcohol or drug abuse within the previous 2 years.
  • Poorly controlled clinically significant medical illness, such as hypertension (blood pressure >180 mmHg systolic or 100 mmHg diastolic); myocardial infarction within 6 months; uncompensated congestive heart failure or other significant cardiovascular, pulmonary, renal, liver, infectious disease, immune disorder, or metabolic/endocrine disorders or other disease that would interfere with assessment of drug safety in the opinion of the Investigator.
  • Abnormal laboratory tests that, in the Investigator's assessment, mean that a participant is not appropriate for participation in this study, including, but not limited to:

    1. Aspartate aminotransferase (AST) or alanine aminotransferase (ALT) >2.0

      × the upper limit of normal (ULN),

    2. Total bilirubin >1.5 × ULN, and/or
    3. International Normalised Ratio (INR) >1.5 NOTE: Participants with Gilbert's syndrome can be included with total bilirubin >1.5 x ULN as long as direct bilirubin is ≤ 1.5 x ULN)
04

Study design

Phase
Phase 2
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Parallel assignment
Masking
Quadruple (Participant, Care provider, Investigator, Outcomes assessor)
Enrollment
90 participants (estimated)

Study arms

  • Active comparator
    Cohort 1 neflamapimod

    Neflamapimod will be administered with food for 12 weeks in subjects with Moderate to Severe Acute Ischaemic Stroke. Subjects will receive 3 capsules per day (TID) with food (i.e., with the morning, mid-day and evening meals).

    Drug: Neflamapimod

  • Placebo comparator
    Cohort 1 placebo

    Placebo will be administered with food for 12 weeks in subjects with Moderate to Severe Acute Ischaemic Stroke. Subjects will receive 3 capsules per day (TID) with food (i.e., with the morning, mid-day and evening meals).

    Drug: Placebo

  • Placebo comparator
    Cohort 2 placebo

    Placebo will be administered with food for 12 weeks in subjects with Moderate to Severe Acute Ischaemic Stroke. Subjects will receive 2 capsules twice per day (BID) with food (i.e., with the morning and evening meals).

    Drug: Placebo

  • Active comparator
    Cohort 2 neflamapimod

    Neflamapimod will be administered with food for 12 weeks in subjects with Moderate to Severe Acute Ischaemic Stroke. Subjects will receive 2 capsules twice per day (BID) with food (i.e., with the morning and evening meals).

    Drug: Neflamapimod

Interventions

  • DrugNeflamapimod

    Neflamapimod is a highly specific inhibitor of the intra-cellular enzyme mitogen-activated protein kinase14 (p38α) provided in 40mg capsules

    Also known as: VX-745

  • DrugPlacebo

    Placebo is a capsule that looks just like neflamapimod but without the active ingredients

05

What researchers measure

Primary outcomes

  1. Change from baseline to Week 12 in Fugl-Meyer Assessment of Motor Recovery after Stroke (FMMS) motor score (upper and lower) and total score

    The FMMS test has a maximum upper motor score of 66, maximum lower motor score of 34, and a maximum total score of 212, where an increase indicates improved motor function while a decrease indicates worsening impairment.

    Time frame: From enrollment until the end of treatment at 12 weeks

  2. Change from baseline to Week 12 in the Timed Up and Go Test (TUG)

    The TUG test is recorded in seconds. The test has no minimum or maximum value, and an increase in the time required to complete the TUG is a worse outcome.

    Time frame: From enrollment until the end of treatment at 12 weeks

  3. Change from baseline to Week 12 in National Institutes of Health Stroke Scale (NIHSS) motor score

    Scores for the NIHSS range from 0 to 42 where higher scores indicate greater impairment/worsening.

    Time frame: From enrollment until the end of treatment at 12 weeks

Secondary outcomes

  1. Proportion of participants with Modified Rankin Scale (mRS) score of ≤ 2 at Week 12

    The mRS scores range from 0 (no symptoms) to 6 (death) where higher scores indicate greater impairment/worsening.

    Time frame: From enrollment until the end of treatment at 12 weeks

  2. Change from baseline to Week 12 in mean Barthel score

    The Barthel Index (BI) for Activities of Daily Living scores range from 0 (total dependency) to 100 (independent) where higher scores indicate greater independence/improvement.

    Time frame: From enrollment until the end of treatment at 12 weeks

06

Study locations

10 sites
  • Campbelltown Hospital
    Campbelltown, New South Wales, Australia
  • Liverpool Hospital
    Liverpool, New South Wales, Australia
  • Sunshine Coast University Hospital
    Birtinya, Queensland, Australia
  • Royal Brisbane and Women's Hospital
    Brisbane, Queensland, Australia
  • Gold Coast University Hospital
    Southport, Queensland, Australia
  • Box Hill Hospital
    Box Hill, Victoria, Australia
  • Austin Hospital
    Heidelberg, Victoria, Australia
  • Alfred Hospital
    Melbourne, Victoria, Australia
  • Royal Melbourne Hospital
    Melbourne, Victoria, Australia
  • Western Health- Sunshine Hospital
    St Albans, Victoria, Australia
07

References and documents

Individual participant data

Plan to share: No

No publications or documents are linked to this record.

08

Registry details

Key details

Study ID
NCT06987643
Lead sponsor
EIP Pharma Inc
Collaborators
CervoMed, Inc.
Responsible party
Sponsor
First posted
May 23, 2025
Start date
Jun 20, 2025
Primary completion
Sep 30, 2026 (estimated)
Completion
Oct 31, 2026 (estimated)
Last update
Jul 8, 2026

Oversight

Data monitoring committee
No
FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

Not currently enrolling

This study is active, not recruiting, as verified in Jul 2026. You cannot join it, but the record below documents what was studied.

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