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RecruitingNCT06676904NeoPlaTTUpdated Mar 25, 2026

Neonatal Platelet Transfusion Threshold Trial

An interventional study of Higher Platelet Transfusion Threshold and Lower Platelet Transfusion Threshold in Thrombocytopenia, Neonatal and Platelet Transfusion, sponsored by NICHD Neonatal Research Network. Recruiting at 20 sites in United States. Open to participants aged 1 Hour to 48 Hours, including healthy volunteers. Per ClinicalTrials.gov, last updated 2026-03-25.

Sponsored by NICHD Neonatal Research Network · Not applicable, Interventional, and Prevention

Phase
Not applicable
Study type
Interventional
Enrollment
2,433
Allocation
Randomized
Ages
1 Hour to 48 Hours
Sex
All
01

Study summary

The objective of the NeoPlaTT trial is to test whether, among extremely preterm infants born at 23 0/7 to 26 6/7 weeks' gestation, a lower platelet transfusion threshold, compared to a higher threshold, improves survival without major or severe bleeding up to 40 0/7 weeks' postmenstrual age (PMA).

Read the detailed description

Thrombocytopenia, defined as a platelet count \<150 x 10\^9/L, is a common neonatal problem that affects 22% to 35% of infants admitted to the neonatal intensive care unit. Platelets are important for primary hemostasis to prevent blood extravasation after vascular injury. Based on the role of platelets in hemostasis, prophylactic platelet transfusions are routinely administered to preterm infants with thrombocytopenia to prevent bleeding. The incidence of thrombocytopenia and administration of platelet transfusion are both inversely related to the gestational age at birth. Currently, there is uncertainty regarding the optimal platelet transfusion threshold, particularly among the most immature infants in the first week of life, which represents the period of highest bleeding risk.

The NeoPlaTT trial was designed to address this pressing uncertainty in the highest risk population (\<27 weeks GA). It will test whether a threshold of 20x10\^9/L could be safely used after the first week of life, when the risk of serious bleeding is significantly lower, and reduce the need for platelet transfusion altogether. The results of this study have a potential to change clinical practice and improve outcomes in this vulnerable population, while also decreasing costs and resource utilization.

This is a randomized trial with 1:1 allocation to parallel arms. Infants, inborn or outborn, who are admitted to participating NICUs, and who meet the inclusion and exclusion criteria, will be invited to enroll into the trial for platelet count monitoring. Only consented and enrolled infants meeting the additional platelet count trigger of \< 50 x 10\^9/L (postnatal days 1-7) or \<35 x 10\^9/L (8 or more postnatal days) will be randomized. Postnatal day 1 starts at birth. Randomization will be allowed to occur up to 36 6/7 weeks' PMA; subjects will be monitored through 40 0/7 weeks PMA. Approximately 30% of consented and enrolled infants are expected to meet the platelet count threshold for randomization.

02

Conditions studied

  • Thrombocytopenia
  • Neonatal
  • Platelet Transfusion
  • Infant, Newborn, Diseases
  • Infant, Extremely Low Birth Weight
  • Infant, Small for Gestational Age
  • Thrombosis

Keywords

  • platelet transfusion
  • neonatal
  • thrombosis
03

Who can participate

Ages eligible
1 Hour to 48 Hours
Sexes eligible
All
Accepts healthy volunteers
Yes

Inclusion criteria

  • Gestational age of 23 0/7 to 26 6/7 weeks
  • Postnatal age of \< 48 hours

Exclusion criteria

Exclusion Criteria:

  • Comfort care or withdrawal of care planned
  • Neonatal alloimmune thrombocytopenia or suspected/confirmed congenital platelet or bleeding disorder
  • Receipt of platelet transfusion
  • No receipt of Vitamin K
  • Parents/guardian decline consent
04

Study design

Phase
Not applicable
Primary purpose
Prevention
Allocation
Randomized
Intervention model
Parallel assignment
Masking
Triple (Participant, Investigator, Outcomes assessor)
Enrollment
2,433 participants (estimated)

Study arms

  • Active comparator
    Higher Platelet Transfusion Threshold

    Infants randomized to this arm will be monitored for a platelet transfusion threshold of 50 x 10\^9/L during postnatal days 1-7, and then for a platelet transfusion threshold of 35 x 10\^9/L at 8 or more postnatal days of life. Infants will remain on this protocol-driven threshold through 40 0/7 weeks postmenstrual age. The platelet dose will be 10 ml/kg administered over 60-120 minutes.

    Procedure: Higher Platelet Transfusion Threshold

  • Other
    Lower Platelet Transfusion Threshold

    Infants randomized to this arm will be monitored for a platelet transfusion threshold of 25 x 10\^9/L during postnatal days 1-7, and then for a platelet transfusion threshold of 20 x 10\^9/L at 8 or more postnatal days of life. Infants will remain on this protocol-driven threshold through 40 0/7 weeks postmenstrual age. The platelet dose will be 10 ml/kg administered over 60-120 minutes.

    Procedure: Lower Platelet Transfusion Threshold

Interventions

  • ProcedureHigher Platelet Transfusion Threshold

    Infants randomized to this arm will be monitored for a platelet transfusion threshold of 50 x 10\^9/L during postnatal days 1-7, and then for a platelet transfusion threshold of 35 x 10\^9/L at 8 or more postnatal days of life. Infants will remain on this protocol-driven threshold through 40 0/7 weeks postmenstrual age. The platelet dose will be 10 ml/kg administered over 60-120 minutes.

    Also known as: Liberal Transfusion Threshold

  • ProcedureLower Platelet Transfusion Threshold

    Infants randomized to this arm will be monitored for a platelet transfusion threshold of 25 x 10\^9/L during postnatal days 1-7, and then for a platelet transfusion threshold of 20 x 10\^9/L at 8 or more postnatal days of life. Infants will remain on this protocol-driven threshold through 40 0/7 weeks postmenstrual age. The platelet dose will be 10 ml/kg administered over 60-120 minutes.

    Also known as: Restrictive Transfusion Threshold

05

What researchers measure

Primary outcomes

  1. Survival without major or severe bleeding

    Bleeding will be assessed using the neonatal Bleeding Assessment Tool (NeoBAT), a validated bleeding assessment tool (Venkatesh V, 2013)

    Time frame: Randomization to 40 0/7 weeks postmenstrual age, death, discharge, or transfer outside of the Study Center, whichever occurs first (an average of 98 days postnatal age)

Secondary outcomes

  1. Death

    Time frame: Randomization to 52 0/7 weeks' postmenstrual age, death, discharge, or transfer outside of the Study Center, whichever occurs first, per Neonatal Research Network Generic Research Database Registry protocol.

  2. Major or severe bleeding

    Bleeding will be assessed using the neonatal Bleeding Assessment Tool (NeoBAT), a validated bleeding assessment tool (Venkatesh V, 2013)

    Time frame: Randomization to 40 0/7 weeks postmenstrual age, death, discharge, or transfer outside of the Study Center, whichever occurs first (an average of 98 days postnatal age)

  3. Number of platelet transfusions

    Time frame: Randomization to 40 0/7 weeks postmenstrual age, death, discharge, or transfer outside of the Study Center, whichever occurs first (an average of 98 days postnatal age)

  4. At least one platelet transfusion

    Time frame: Randomization to 40 0/7 weeks postmenstrual age, death, discharge, or transfer outside of the Study Center, whichever occurs first (an average of 98 days postnatal age)

  5. Bronchopulmonary dysplasia among survivors to 36 weeks postmenstrual age

    Time frame: At 36 weeks postmenstrual age

  6. Retinopathy of Prematurity (ROP)

    Stage 3 ROP, or stage 1 or 2 in Zone 1, or plus disease

    Time frame: Randomization to 52 0/7 weeks' postmenstrual age, death, discharge, or transfer outside of the Study Center, whichever occurs first, per Neonatal Research Network Generic Research Database Registry protocol.

  7. Periventricular leukomalacia

    Time frame: Randomization to 52 0/7 weeks' postmenstrual age, death, discharge, or transfer outside of the Study Center, whichever occurs first, per Neonatal Research Network Generic Research Database Registry protocol.

Other outcomes

  1. Late-onset sepsis

    Time frame: Randomization to 40 0/7 weeks postmenstrual age, death, discharge, or transfer outside of the Study Center, whichever occurs first (an average of 98 days postnatal age)

  2. Necrotizing enterocolitis

    Modified Bells Stage IIA or greater

    Time frame: Randomization to 40 0/7 weeks postmenstrual age, death, discharge, or transfer outside of the Study Center, whichever occurs first (an average of 98 days postnatal age)

  3. Thrombosis requiring therapy

    Thrombosis requiring therapy such as heparin, enoxaparin, or aspirin

    Time frame: Randomization to 40 0/7 weeks postmenstrual age, death, discharge, or transfer outside of the Study Center, whichever occurs first (an average of 98 days postnatal age)

06

Study locations

20 of 20 sites recruiting
  • University of Alabama at Birmingham
    Birmingham, Alabama 35233, United States
    • Waldemar A Carlo, MD · Contact
    Recruiting
  • Stanford University
    Palo Alto, California 94304, United States
    • Valerie Chock, MD · Contact
    • Valerie Chock, MD · Principal investigator
    Recruiting
  • Sharp Mary Birch Hospital for Women & Newborns
    San Diego, California 92123, United States
    • Anup Katheria, MD · Contact
    • Anup Katheria, MD · Principal investigator
    Recruiting
  • University of Colorado
    Aurora, Colorado 80045, United States
    • Sunah Hwang, MD · Contact
    • Sunah Hwang, MD · Principal investigator
    Recruiting
  • Emory University
    Atlanta, Georgia 30303, United States
    • Ravi Patel, MD · Contact
    • Brenda Poindexter, MD · Sub investigator
    • Ravi Patel, MD · Principal investigator
    Recruiting
  • Northwestern Lurie Children's Hospital of Chicago
    Chicago, Illinois 60611, United States
    • Aaron Hamvas, MD · Contact
    • Aaron Hamvas, MD · Principal investigator
    Recruiting
  • University of Iowa
    Iowa City, Iowa 52242, United States
    • Tarah Colaizy, MD, MPH · Contact · 319-356-3508
    • Edward F. Bell, MD · Principal investigator
    Recruiting
  • Beth Israel Deaconess Medical Center
    Boston, Massachusetts 02215, United States
    • Helen Healy, MD · Contact
    • Helen Healy, MD · Principal investigator
    Recruiting
  • University of New Mexico
    Albuquerque, New Mexico 87131, United States
    • Janell Fuller, MD · Contact
    • Janell Fuller, MD · Principal investigator
    Recruiting
  • University of Rochester
    Rochester, New York 14642, United States
    • Carl T D'Angio, MD · Contact
    • Carl T D'Angio, MD · Principal investigator
    Recruiting
  • Duke University
    Durham, North Carolina 27710, United States
    • Michael Cotten, MD · Contact
    Recruiting
  • Cincinnati Children's Medical Center
    Cincinnati, Ohio 45267, United States
    • Stephanie Merhar, MD MS · Contact
    • Vivek Narendran, MD, MBA · Sub investigator
    • Stephanie Merhar, MD MS · Principal investigator
    Recruiting
  • Case Western Reserve University, Rainbow Babies and Children's Hospital
    Cleveland, Ohio 44106, United States
    • Anna Maria Hibbs, MD · Contact
    • Anna Maria Hibbs, MD · Principal investigator
    Recruiting
  • Nationwide Children's Hospital
    Columbus, Ohio 43205, United States
    • Pablo Sanchez, MD · Contact
    • Pablo Sanchez, MD · Principal investigator
    Recruiting
  • University of Pennsylvania
    Philadelphia, Pennsylvania 19104, United States
    • Sara DeMauro, MD · Contact
    • Sara DeMauro, MD · Principal investigator
    Recruiting
  • Vanderbilt University
    Nashville, Tennessee 37232, United States
    • Hendrick Weitkamp, MD · Contact
    • Hendrick Weitkamp, MD · Principal investigator
    Recruiting
  • University of Texas Southwestern Medical Center at Dallas
    Dallas, Texas 75235, United States
    • Myra Myckoff, MD · Contact
    • Myra Wyckoff, MD · Principal investigator
    Recruiting
  • University of Texas Health Science Center at Houston
    Houston, Texas 77030, United States
    • Jon Tyson · Contact
    • Jon Tyson, MD, MPH · Principal investigator
    Recruiting
  • Pediatrix Medical Group
    San Antonio, Texas 78229, United States
    • Kaashif Ahmad, MD · Contact
    • Kaashif Ahmad, MD · Principal investigator
    Recruiting
  • University of Utah
    Salt Lake City, Utah 84108, United States
    • Robin Ohls, MD · Contact
    • Robin Ohls, MD · Principal investigator
    Recruiting
07

References and documents

Publications

  • Venkatesh V, Curley A, Khan R, Clarke P, Watts T, Josephson C, Muthukumar P, New H, Seeney F, Morris S, Stanworth S. A novel approach to standardised recording of bleeding in a high risk neonatal population. Arch Dis Child Fetal Neonatal Ed. 2013 May;98(3):F260-3. doi: 10.1136/archdischild-2012-302443. Epub 2012 Nov 9. PubMed 23144007 ↗

Individual participant data

Plan to share: Yes — NIH has had a long-standing policy to share and make available to the public the results and accomplishments of the activities that it funds. The NRN plans to share de-identified data after final publication in an NIH supported data repository such as the NICHD Data and Specimen Hub (https://dash.nichd.nih.gov).

08

Registry details

Key details

Study ID
NCT06676904
Lead sponsor
NICHD Neonatal Research Network
Collaborators
National Heart, Lung, and Blood Institute (NHLBI)
Responsible party
Sponsor
First posted
Nov 6, 2024
Start date
Jun 13, 2025
Primary completion
Jan 31, 2031 (estimated)
Completion
Apr 30, 2031 (estimated)
Last update
Mar 25, 2026

Study contacts

Ravi M Patel, MD
Contact
rmpatel@emory.edu
404-727-5905
Abhik Das, PhD
Contact
adas@rti.org
301-230-4640
Ravi M Patel, MD
principal investigator · Emory University

Oversight

Data monitoring committee
Yes
FDA-regulated drug
No
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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