CClinicalTrials.gg
RecruitingNCT05039619POSTERITYUpdated Sep 3, 2026

A Study to Evaluate the Efficacy, Safety, and Pharmacokinetics of Obinutuzumab in Adolescents With Active Class III or IV Lupus Nephritis and the Safety and PK of Obinutuzumab in Pediatric Participants

A Phase 2 interventional study of Obinutuzumab and Placebo in Lupus Nephritis, sponsored by Hoffmann-La Roche. Recruiting at 43 sites in 12 countries. Open to participants aged 5 Years to 17 Years. Per ClinicalTrials.gov, last updated 2026-09-03.

Sponsored by Hoffmann-La Roche · Phase 2, Interventional, and Treatment

Phase
Phase 2
Study type
Interventional
Enrollment
40
Allocation
Randomized
Ages
5 Years to 17 Years
Sex
All
01

Study summary

This phase II, randomized, double-blind, placebo-controlled study is designed to evaluate the safety, efficacy and pharmacokinetics (PK) of obinutuzumab in adolescent participants (AP) aged 12 to less than 18 with biopsy-confirmed proliferative lupus nephritis (LN). It will also evaluate open label safety and PK of obinutuzumab in pediatric participants (PP), aged 5 to \<12 with LN.

02

Conditions studied

  • Lupus Nephritis

Browse trials for

03

Who can participate

Ages eligible
5 Years to 17 Years
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  • Participants who are age 12 to \<18 years at the time of randomization
  • Participants who are age 5 to \<12 years (younger participant cohort) at the time of randomization once recruitment is open. (Investigators will be notified by the Sponsor when recruitment is open to this younger population)
  • International Society of Nephrology and the Renal Pathology Society (ISN/RPS) 2003 Class III or IV active LN demonstrated on renal biopsy performed in the 12 months prior to or during screening
  • Class V disease may be present in addition to Class III or IV LN, but participants with isolated Class V disease are not eligible
  • Diagnosis of SLE according to the Systemic Lupus International Collaborating Clinics (SLICC) 2012 criteria
  • Significant proteinuria defined by a UPCR above > 0.5 based on a first-morning void (FMV) collection at screening
  • During the 12 months prior to or during screening, all participants must have received at least one dose of pulse-range IV methylprednisolone (typically 30 mg/kg, maximum of 1000 mg per dose) or equivalent for the treatment of the current episode of active LN.

Exclusion criteria

Exclusion Criteria:

  • Severe, active central nervous system (CNS) SLE, including retinitis, poorly controlled seizure disorder, acute confusional state, myelitis, stroke, cerebellar ataxia, or dementia
  • Sclerosis in >50% of glomeruli on renal biopsy
  • Purely chronic Class III(c) or Class IV(c) disease on renal biopsy, defined as the absence of any active lesions
  • Presence of rapidly progressive glomerulonephritis
  • Pure Class V LN
  • Intolerance or contraindication to study therapies
  • Active infection of any kind (excluding fungal infection of nail beds) or any major episode of infection requiring hospitalization or treatment with IV anti-infective medications within 4 weeks prior to screening, or completion of oral anti-infectives within 2 weeks prior to randomization
  • History of or currently active primary or secondary immunodeficiency, including known history of HIV infection and other severe Immunodeficiency blood disorders
  • History of serious recurrent or chronic infection
  • History of or current cancer, including solid tumors, hematological malignancies, and carcinoma in situ (except basal cell carcinoma and squamous cell carcinoma of the skin that have been excised and cured) within the past 5 years
  • Significant or uncontrolled concomitant medical disease which, in the investigator's opinion, would preclude participant participation
  • Currently active alcohol or drug abuse or history of alcohol or drug abuse
04

Study design

Phase
Phase 2
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Parallel assignment
Masking
Double (Participant, Investigator)
Enrollment
40 participants (estimated)

Study arms

  • Experimental
    Blinded Obinutuzumab

    Participants will receive obinutuzumab 1000 milligrams (mg) intravenous (IV) infusions on Day 1, Day 14, Week 24, Week 26 and Week 52. Participants with a body weight of 45 kg or more will receive the 1000 mg dose. Participants with a body weight below 45 kg will receive a weight adjusted dose of 20 mg/kilogram (kg).

    Drug: Obinutuzumab · Drug: Mycophenolate Mofetil · Drug: Acetaminophen/paracetamol · Drug: Diphenhydramine hydrochloride (HCl) · Drug: Methylprednisolone · Drug: Prednisone

  • Placebo comparator
    Placebo

    Placebo participants will receive obinutuzumab matched placebo on Day 1, Day 14, Week 24, Week 26 and Week 52.

    Drug: Placebo · Drug: Mycophenolate Mofetil · Drug: Acetaminophen/paracetamol · Drug: Diphenhydramine hydrochloride (HCl) · Drug: Methylprednisolone · Drug: Prednisone

  • Experimental
    Open-Label Obinutuzumab

    Younger participants aged 5 to \<12 will receive obinutuzumab 1000 mg IV infusions on Days 1, 14, Week 24, Week 26 and Week 52.

    Drug: Obinutuzumab · Drug: Mycophenolate Mofetil · Drug: Acetaminophen/paracetamol · Drug: Diphenhydramine hydrochloride (HCl) · Drug: Methylprednisolone · Drug: Prednisone

Interventions

  • DrugObinutuzumab

    Obinutuzumab will be administered by IV infusion at a dose of 1000 mg on Day 1, Day 14, Week 24, Week 26 and Week 52.

    Also known as: Gazyva

  • DrugPlacebo

    Placebo matching obinutuzumab will be administered by IV on Day 1, Day 14, Week 24, Week 26 and Week 52.

  • DrugMycophenolate Mofetil

    Mycophenolate Mofetil (MMF) will be taken by home administration orally at a target dose of 1200 mg/m\^2/day to a maximum of 2.5g/day from baseline (Day 1) onwards.

  • DrugAcetaminophen/paracetamol

    Acetaminophen 1000 mg will be administered as pre-medication prior to infusions.

  • DrugDiphenhydramine hydrochloride (HCl)

    Diphenhydramine HCl 50 mg will be administered as pre-medication prior to infusions.

  • DrugMethylprednisolone

    Methylprednisolone 80 mg IV will be administered as pre-medication prior to infusions.

  • DrugPrednisone

    Oral prednisone or equivalent corticosteroid will be taken by home administration daily to a maximum dose of 60mg/day followed by a guided taper to 5mg/day or less by Week 24.

05

What researchers measure

Primary outcomes

  1. Percentage of Participants who Achieve a Complete Renal Response (CRR) (AP)

    CRR is defined as achievement of all of the following: * Urinary protein-to-creatinine ratio (UPCR) \<0.5 g/g * Estimated Glomerular Filtration Rate (eGFR) \>=85% of baseline * No occurrence of intercurrent events

    Time frame: Week 76

  2. Percentage of Participants with Adverse Events (PP)

    Time frame: Baseline to Week 76

Secondary outcomes

  1. Percentage of Participants Achieving a CRR (AP)

    Time frame: Weeks 24 and 52

  2. Percentage of Participants who Achieve CRR with Successful Prednisone Taper (AP)

    Time frame: Week 76

  3. Percentage of Participants who Achieve a PRR (AP)

    Time frame: Week 76

  4. Percentage of Participants Achieving an Overall Response (CRR or PRR) (AP)

    PRR is defined as: achievement of all of the following: * \>=50% reduction in urinary protein-to-creatinine ratio (UPCR) from baseline * UPCR \< 1 g/g (or \< 3 g/g if the baseline UPCR was \>=3 g/g) * eGFR \>=85% of baseline * No occurrence of intercurrent events

    Time frame: Weeks 24, 52, and 76

  5. Change in UPCR (AP)

    Time frame: Baseline to Week 76

  6. Change in eGFR (AP)

    Time frame: Baseline to Week 76

  7. Time to Onset of CRR over the Course of 76 weeks (AP)

    Time frame: Up to Week 76

  8. Percentage of Participants who Experience Treatment Failure (AP)

    Time frame: Week 12 to Week 76

  9. Change in anti-dsDNA titers (AP)

    Time frame: Baseline to Week 76

  10. Change in C3 Complement Levels (AP)

    Time frame: Baseline to Week 76

  11. Change in C4 Complement Levels (AP)

    Time frame: Baseline to Week 76

  12. Percentage of Participants with Adverse Events According to National Cancer Institute Common Terminology Criteria for Adverse Events (NCI CTCAE) v5.0 (AP)

    Time frame: Baseline to Week 76

  13. Serum Concentrations of Obinutuzumab (AP)

    Time frame: Baseline to Week 76

  14. Percentage of Participants Achieving B-cell Depletion (AP)

    Time frame: Baseline, Weeks 4, 24, 52 and 76

  15. Change in Pediatric Quality of Life Inventory-Multidimensional Fatigue Scale (PedsQL)-Fatigue Total Score (AP)

    Time frame: Baseline to Week 76

  16. Change in Systemic Lupus Erythematosus Disease Activity Index 2000 (SLEDAI-2K) (AP)

    Time frame: Baseline to Week 76

  17. Change from Baseline in Child Health Questionnaire-Parent Form 28 (CHQ-PF28) Domain Scores (AP)

    Time frame: Baseline to Week 76

  18. Percentage of Participants with Anti-drug Antibodies (ADA) (AP)

    Time frame: Weeks 0, 24, 52 and 76

  19. Relationship Between ADA Status and Percentage of Participants Achieving a CRR (AP)

    Time frame: Weeks 24, 52 and 76

  20. Percentage of Participants Achieving a CRR (PP)

    Time frame: Week 76

  21. Percentage of Participants Achieving an Overall Response (PP)

    PRR is defined as achievement of all of the following: * \>=50% reduction in UPCR from baseline * UPCR \< 1 g/g (or \< 3 g/g if the baseline UPCR was \>=3 g/g) * eGFR \>=85% of baseline * No occurrence of intercurrent events

    Time frame: Week 76

  22. Percentage of Participants who Achieve CRR with Successful Prednisone Taper (PP)

    Time frame: Week 76

  23. Change in eGFR (PP)

    Time frame: Baseline to Week 76

  24. Percentage of Participants Achieving B-cell Depletion (PP)

    Time frame: Baseline, Weeks 4, 24, 52 and 76

  25. Percentage of Participants with ADAs (PP)

    Time frame: Weeks 0, 24, 52 and 76

  26. Change in anti-dsDNA titers (PP)

    Time frame: Baseline to Week 76

06

Study locations

33 of 43 sites recruiting
  • Loma Linda University health
    Loma Linda, California 92354, United States
    Recruiting
  • UCSF Benioff Childrens Hospital
    San Francisco, California 94158, United States
    Recruiting
  • Children's Hospital Colorado, Anchutz Medical Campus
    Aurora, Colorado 80045, United States
    Recruiting
  • Emory Children's Center
    Atlanta, Georgia 30322, United States
    Recruiting
  • Indiana University Health University Hospital
    Indianapolis, Indiana 46202, United States
    Recruiting
  • Louisiana State University
    Shreveport, Louisiana 71103, United States
    Recruiting
  • Hackensack University Medical Center
    Hackensack, New Jersey 07601, United States
    Recruiting
  • Cohen Children's Medical Center of New York
    Queens, New York 11042, United States
    Recruiting
  • Cincinnati Childrens Hospital
    Cincinnati, Ohio 45229, United States
    Recruiting
  • Chldren?s Hospital of Philadelphia
    Philadelphia, Pennsylvania 19104, United States
    Withdrawn
  • Texas Arthritis Center
    El Paso, Texas 79902, United States
    Withdrawn
  • Ser Servicos Especializados Em Reumatologia
    Salvador, Estado de Bahia 40150-150, Brazil
    Recruiting
  • Hospital Universitário Onofre Lopes - UFRN
    Petrópolis, Rio Grande do Norte 59012-300, Brazil
    Recruiting
  • Centro de Pesquisa São Lucas
    Campinas, São Paulo 13060-904, Brazil
    Recruiting
  • Hospital das Clinicas - FMUSP
    São Paulo, São Paulo 05403-000, Brazil
    Recruiting
  • Universidade Federal de Sao Paulo - UNIFES
    São Paulo, 04024-002, Brazil
    Active, not recruiting
  • The Hospital for Sick Children
    Toronto, Ontario M5G 1X8, Canada
    Recruiting
  • Hospital Sainte-Justine
    Montreal, Quebec H3T 1C5, Canada
    Recruiting
  • CH de Bicêtre
    Le Kremlin-Bicêtre, 94275, France
    Recruiting
  • Hôpital Robert Debré
    Paris, 75019, France
    Recruiting
  • Hop Necker Enfants Malades
    Paris, 75743, France
    Recruiting
  • CHU de Toulouse - Hôpital des Enfants
    Toulouse, 31000, France
    Recruiting
  • Ospedale Pediatrico Bambino Gesu
    Rome, Lazio 00165, Italy
    Recruiting
  • IRCCS G. Gaslini
    Genoa, Liguria 16148, Italy
    Recruiting
  • Clinica Pediatrica II De Marchi
    Milan, Lombardy 20122, Italy
    Recruiting
  • CREA Hospital Mexico Americano
    Guadalajara, Jalisco 44620, Mexico
    Recruiting
  • Clinstile S.A de C.V.
    Mexico City, Mexico CITY (federal District) 06700, Mexico
    Recruiting
  • Hospital Universitario Dr. Jose Eleuterio Gonzalez
    Monterrey, Nuevo León 64460, Mexico
    Recruiting
  • Instituto de Ginecología y Reproducción
    Lima, Peru
    Active, not recruiting
  • Clinica El Golf
    San Isidro, L27 Lima, Peru
    Active, not recruiting
  • Uniwersyteckie Centrum Kliniczne
    Gdansk, 80-294, Poland
    Recruiting
  • Szpital Specjalistyczny dla Dzieci i Doroslych
    Torun, 87-100, Poland
    Withdrawn
  • Saint-Petersburg State
    St-peterburg, Sankt-Peterburg 194100, Russia
    Withdrawn
  • Red Cross War Memorial Children?s Hospital
    Cape Town, 7700, South Africa
    Withdrawn
  • Groote Schuur Hospital
    Cape Town, 7925, South Africa
    Withdrawn
  • Panaroma Medical Center
    Panorama, 7500, South Africa
    Recruiting
  • Hospital Sant Joan De Deu
    Esplugas de Llobregat, Barcelona 08950, Spain
    Recruiting
  • Hospital Ramon y Cajal
    Madrid, 28034, Spain
    Recruiting
  • Hospital de La Paz
    Madrid, 28046, Spain
    Recruiting
  • Hospital Universitario la Fe: Servicio de Reumatologia Pediatrica
    Valencia, 46026, Spain
    Recruiting
  • Royal Hospital For Children
    Glasgow, G51 4TF, United Kingdom
    Withdrawn
  • Alder Hey Childrens Hospital
    Liverpool, L12 2AP, United Kingdom
    Recruiting
  • Great Ormond Street Hospital for Children
    London, WC1N 3JH, United Kingdom
    Recruiting
07

References and documents

Publications

  • Dossier C, Bonneric S, Baudouin V, Kwon T, Prim B, Cambier A, Couderc A, Moreau C, Deschenes G, Hogan J. Obinutuzumab in Frequently Relapsing and Steroid-Dependent Nephrotic Syndrome in Children. Clin J Am Soc Nephrol. 2023 Dec 1;18(12):1555-1562. doi: 10.2215/CJN.0000000000000288. Epub 2023 Sep 6. PubMed 37678236 ↗

Individual participant data

Plan to share: Yes — For eligible studies, qualified researchers may request access to individual patient level clinical data. See Roche's commitment to transparency of clinical study information here: https://go.roche.com/data\_sharing

08

Registry details

Key details

Study ID
NCT05039619
Lead sponsor
Hoffmann-La Roche
Collaborators
Genentech, Inc.
Responsible party
Sponsor
First posted
Sep 9, 2021
Start date
May 12, 2022
Primary completion
Jun 15, 2028 (estimated)
Completion
Jun 14, 2030 (estimated)
Last update
Sep 3, 2026

Study contacts

Reference Study ID Number: WA42985 https://forpatients.roche.com/ No attachments to email below.
Contact
global.rochegenentechtrials@roche.com
888-662-6728 (U.S. and Canada)
Fastest response: use the inquiry form. https://www.gene.com/contact-us/submit-medical-inquiry
Contact
Clinical Trials
study director · Hoffmann-La Roche

Oversight

Data monitoring committee
Yes
FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

Interested in this study?

Eligibility is decided by the study team. Share this record with your doctor or contact the team directly.

Contact study team

Follow this study

Get an email when the registry record changes — status, dates, results — or when someone posts here.

Sign in to follow

Discussion

Questions and observations about this study, from anyone following it. Not medical advice, and not a channel to the study team — their contact details are on the registry record.

Sign in to join the discussion. Reading takes no account; posting does. You choose a display name, and a pseudonym is the default.

Nothing here yet. If you are running this trial, taking part in it, or weighing whether to, this is the place to say so.

Start the discussion