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RecruitingNCT04879043Updated Sep 17, 2026

Study to Assess Safety of HDP-101 in Patients With Relapsed Refractory Multiple Myeloma

A Phase 1/2 interventional study of HDP-101 in Multiple Myeloma and Plasma Cell Disorder, sponsored by Heidelberg Pharma AG. Recruiting at 24 sites in 5 countries. Open to participants aged 18 Years and older. Per ClinicalTrials.gov, last updated 2026-09-17.

Sponsored by Heidelberg Pharma AG · Phase 1/2, Interventional, and Treatment

Phase
Phase 1/2
Study type
Interventional
Enrollment
78
Allocation
Not applicable
Ages
18 Years and older
Sex
All
01

Study summary

This study will assess the safety, tolerability, pharmacokinetics (PK) and the therapeutic potential of HDP-101 in patients with plasma cell disorders including multiple myeloma.

Read the detailed description

The study will consists of two parts: a Part 1 dose escalation phase and a Part 2a expansion phase for safety, tolerability, PK, PD, and clinical activity testing. The study will enroll subjects with relapsed/refractory MM or other plasma cell disorders expressing BCMA. An adaptive 2-parameter Bayesian logistic regression model (BLRM) for dose-escalation with overdose control will be used in the dose-escalation phase for determination of the MTD or the RP2D. Dose-expansion phase of the study aims to collect preliminary evidence of antitumor activity and to confirm the safety of the HDP-101 as a monotherapy.

02

Conditions studied

  • Multiple Myeloma
  • Plasma Cell Disorder
03

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  • Male or female aged ≥18 years.
  • Life expectancy >12 weeks.
  • Eastern Cooperative Oncology Group Performance Status (PS) of 0 to 2.
  • A confirmed diagnosis of active MM according to the diagnostic criteria established by the International Myeloma Working Group (IMWG).
  • Must have undergone SCT or is considered transplant ineligible.
  • Must have undergone prior treatments with antimyeloma therapy which must have included an immunomodulatory drug, proteasome inhibitor, and anti-CD38 treatment, alone or in combination. In addition, the patient should either refractory or intolerant to any established standard of care therapy providing a meaningful clinical benefit for the patient assessed by the Investigator.
  • Measurable disease as per IMWG criteria.
  • Adequate organ system function as defined in protocol.

Exclusion criteria

Exclusion Criteria:

  • For patient entering the Phase 2a part only: Prior treatment with any approved or experimental BCMA-targeting modalities are not allowed.
  • Known central nervous system involvement.
  • Plasma cell leukemia.
  • History of congestive heart failure.
  • Autologous or allogenic SCT within 12 weeks before the first infusion or is planning for autologous SCT.
  • Symptomatic graft versus host disease post allogenic hemopoietic cell transplant within 12 months prior to the first study treatment infusion.
  • Radiotherapy within 21 days prior to the first study treatment infusion.
  • History of any other malignancy known to be active.
  • Known human immunodeficiency virus infection.
  • Patients with active infection requiring systemic anti-infective.
  • Patients with positive test results for hepatitis B surface antigen or Hepatitis B core antigen.
  • Patients with positive test results for hepatitis C virus (HCV) infection.
  • Current active liver or biliary disease.
04

Study design

Phase
Phase 1 / Phase 2
Primary purpose
Treatment
Allocation
Not applicable
Intervention model
Single group
Masking
None (open label)
Enrollment
78 participants (estimated)

Study arms

  • Experimental
    HDP-101

    Participants will receive HDP-101 intravenously in a 21 day cycle until disease progression, intolerable toxicity, Investigator's discretion or patient withdrawal. During the phase 1 tolerability of different dose levels will be evaluated. During the phase 2a dose expansion part the recommended phase 2 dose (RP2D) of HDP-101 will be administered.

    Drug: HDP-101

Interventions

  • DrugHDP-101

    HDP-101 is available as lyophilized white powder for preparation of infusion.

05

What researchers measure

Primary outcomes

  1. Number of patients who experience dose-limiting toxicity (DLT) during the first cycle of treatment - Part 1 as defined in Clinical Study Protocol

    Time frame: Up to Day 21 (from first dose)

  2. Objective response rate (ORR)

    Proportion of enrolled subjects who achieve a partial response (PR) or better, i.e. stringent complete response (sCR), complete response (CR), very good partial response (VGPR) and PR, according to the IMWG criteria.

    Time frame: Through study completion, an average of 1 year

Secondary outcomes

  1. Assess the safety and tolerability of HDP-101

    Number of patients with serious and non-serious adverse events grouped by system organ class and preferred terms based on Common Terminology Criteria for Adverse Events (CTCAE v 5.0) classification.

    Time frame: Through study completion, an average of 1 year

  2. To assess the anticancer activity of HDP-101 in terms of time-to-event (TTE)

    Clinical efficacy of HDP-101 measured by Progression Free Survival (PFS) and Overall Survival (OS).

    Time frame: Through study completion, an average of 1 year

06

Study locations

11 of 24 sites recruiting
  • Winship Cancer Institute of Emory University
    Atlanta, Georgia 30322, United States
    Recruiting
  • Norton Healthcare, Inc.
    Louisville, Kentucky 40202, United States
    Not yet recruiting
  • Nebraska Cancer Institute
    Omaha, Nebraska 68130, United States
    Recruiting
  • Mount Sinai, The Tisch Cancer Instutute
    New York, New York 10029, United States
    Recruiting
  • MD Anderson Cancer Center
    Houston, Texas 77030, United States
    Recruiting
  • Charité - Campus Benjamin Franklin Med. Klinik m.S. Hämatologie, Onkologie
    Berlin, 12203, Germany
    Withdrawn
  • Klinikum Chemnitz gGmbH, Klinik f. Innere Medizin III
    Chemnitz, 09116, Germany
    Withdrawn
  • Universitätsklinikum Köln
    Cologne, 50937, Germany
    Withdrawn
  • Asklepios Klinik Altona, Haematologie und internistische Onkologie
    Hamburg, 22763, Germany
    Withdrawn
  • Universitätsklinikum Heidelberg
    Heidelberg, 69120, Germany
    Active, not recruiting
  • Universitätsklinikum Schleswig-Holstein
    Kiel, 24105, Germany
    Withdrawn
  • UKSH Campus Lübeck Klinik für Hämatologie und Onkologie
    Lübeck, 23538, Germany
    Active, not recruiting
  • Universitätsklinikum Mainz
    Mainz, 55131, Germany
    Withdrawn
  • Semmelweis University, Belgyogyaszati es Onkologiai Klinika
    Budapest, 1083, Hungary
    Recruiting
  • National Institute of Oncology, Department of Oncological Internal Medicine
    Budapest, 1122, Hungary
    Withdrawn
  • Pécsi Tudományegyetem Klinikai Központ
    Pécs, 7624, Hungary
    Not yet recruiting
  • Pratia Onkologia Katowice
    Katowice, 40-568, Poland
    Recruiting
  • Pratia Onkologia Kraków
    Krakow, 40-519, Poland
    Recruiting
  • Wojewodzkie Wielospecjalistyczne Centrum Onkologii i Traumatologii im. M. Kopernika w Lodzi
    Lodz, 93-513, Poland
    Withdrawn
  • Szpital Wojewodzki w Opolu
    Opole, 45-061, Poland
    Withdrawn
  • AIDPORT Sp. zo.o.
    Skórzewo, 60-185, Poland
    Recruiting
  • MICS Centrum Medyczne Torun
    Torun, 87-100, Poland
    Recruiting
  • Arensia Clinics SRL
    Bucharest, Romania
    Recruiting
  • Oncology Institute Prof. Dr. Ion Chiricuta I.O.C.N.
    Cluj-Napoca, Romania
    Recruiting
07

References and documents

Publications

  • Strassz A, Raab MS, Orlowski RZ, Kulke M, Schiedner G, Pahl A. A First in Human Study Planned to Evaluate HDP-101, an Anti-BCMA Amanitin Antibody-Drug Conjugate with a New Payload and a New Mode of Action, in Multiple Myeloma. Blood 2020; 136 (Supplement 1): 34. doi: https://doi.org/10.1182/blood-2020-142285

Individual participant data

Plan to share: No

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Registry details

Key details

Study ID
NCT04879043
Lead sponsor
Heidelberg Pharma AG
Responsible party
Sponsor
First posted
May 10, 2021
Start date
Feb 7, 2022
Primary completion
Mar 2028 (estimated)
Completion
Sep 2028 (estimated)
Last update
Sep 17, 2026

Study contacts

Lei Wang, MD
Contact
clinical@hdpharma.com
+ 49 6203 1009 0

Oversight

Data monitoring committee
Yes
FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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