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CompletedNCT04540133Updated Dec 15, 2023Results posted

Dexamethasone Solution and Dexamethasone in Mucolox™

A Phase 2 interventional study of dexamethasone 0.5mg/5ml solution and dexamethasone 0.5mg/5ml solution in Mucolox™ in Oral Lichen Planus, Mucous Membrane Pemphigoid and Pemphigus Vulgaris, sponsored by University of California, San Francisco. Completed at 1 site in United States. Open to participants aged 18 Years and older, including healthy volunteers. Per ClinicalTrials.gov, last updated 2023-12-15.

Sponsored by University of California, San Francisco · Phase 2, Interventional, and Treatment

Phase
Phase 2
Study type
Interventional
Enrollment
29
Allocation
Randomized
Ages
18 Years and older
Sex
All
01

Study summary

Topical steroid therapy is considered the first line of treatment for Oral Inflammatory Ulcerative Diseases with current treatment regimens requiring multiple application or rinses daily. Using Mucolox™ as a vehicle to deliver topical dexamethasone to the oral mucosa has the potential to effectively prolong contact time between the medication. The primary objective of this study is to determine the clinical efficacy and tolerability of compound dexamethasone at 0.5 mg/5 mL in Mucolox™ for the treatment of Oral Inflammatory Ulcerative Diseases as measured by a reduction in oral symptoms between patients treated with compounded dexamethasone 0.5mg/5ml solution in Mucolox™ (group A) and patients treated with topical commercial dexamethasone 0.5mg/5ml solution only (group B). and mucosa, leading to improved clinical outcomes due to the need for less frequent application.

02

Conditions studied

  • Oral Lichen Planus
  • Mucous Membrane Pemphigoid
  • Pemphigus Vulgaris
  • Chronic Graft-versus-host-disease
03

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All
Accepts healthy volunteers
Yes

Inclusion criteria

  • Age 18 years and older.
  • Patients with symptomatic biopsy proven Oral Inflammatory Ulcerative Diseases (worst VAS sensitivity score ≥ 7 over the last week).
  • Ability to understand and the willingness to sign a written informed consent document.

Exclusion criteria

Exclusion Criteria:

  • Patients already on topical or systemic steroids.
  • Inability to comply with study instructions.
  • Uncontrolled intercurrent illness or psychiatric illness/social situations that would limit compliance with study requirements.
  • VAS sensitivity score \< 7.
  • Pregnant women. A urine pregnancy test will be performed for women of child bearing potential.
  • Allergy to fluconazole.
04

Study design

Phase
Phase 2
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Parallel assignment
Masking
None (open label)
Enrollment
29 participants (actual)

Study arms

  • Experimental
    dexamethasone 0.5mg/5ml solution in Mucolox™ (group A)

    Dexamethasone solution (0.5mg/5ml) in Mucolox™ three times a day (TID) swish and spit for 4 weeks

    Drug: dexamethasone 0.5mg/5ml solution in Mucolox™

  • Active comparator
    dexamethasone 0.5mg/5ml solution (Arm B)

    Dexamethasone solution (0.5mg/5ml) TID swish and spit for 4 weeks

    Drug: dexamethasone 0.5mg/5ml solution

Interventions

  • Drugdexamethasone 0.5mg/5ml solution

    Patient with oral ulcerative conditions will be asked to rinse with dexamethasone 0.5mg/5ml solution three times a day for 4 weeks and expectorate

    Also known as: dexamethasone

  • Drugdexamethasone 0.5mg/5ml solution in Mucolox™

    Patient with oral ulcerative conditions will be asked to rinse with dexamethasone 0.5mg/5ml solution in Mucolox™ three times a day for 4 weeks and expectorate

    Also known as: dexamethasone solution in Mucolox™

05

What researchers measure

Primary outcomes

  1. Mean Change From Baseline in Oral Pain Scores on the Visual Analog Scale (VAS) at 4 Weeks

    Oral Pain Scores were measured on the Visual Analog Scale (VAS), the score ranges from 0-10, zero indicating no pain and 10 indicating the worst pain. The pain score measured on a VAS scale will be compared between group A and group B to detect any significant differences pre and post treatment at 4 weeks.

    Time frame: 4 weeks

Secondary outcomes

  1. Mean Change From Baseline in Reticulation/Keratosis, Erythema, and Ulceration (REU) Scores at 4 Weeks

    Oral lesions were scored using the REU (reticulation,erythema and ulcer) system (form 0 till 49.5). Reticulations were scored from 0 to 1 (0 = no white striations, 1 = presence of white striations or keratotic papules); erythematous lesions from 0 to 3 by area of involvement (0 = no lesion, 1 = lesions less than 1 cm2, 2 = lesions from 1 to 3 cm2, 3 = lesions greater than 3 cm2); ulcers from 0 to 3 by area of involvement. The higher is the score the more severe is the disease. In order to evaluate the clinical improvement in clinician-reported outcome measures for oral lesions, REU scores within the compound dexamethasone solution in Mucolox™ group (Arm A) will be compared to that in the dexamethasone solution only group (Arm B). The REU scores will be summarized descriptively for each arm at pre-treatment, post-treatment, and pre-to-post treatment change. The pre-to-post treatment change will be compared between the arms using either student's t-test o

    Time frame: 4 weeks

06

Results

Posted Dec 15, 2023

Participant flow

Participant flow — Overall Study
MilestoneDexamethasone 0.5mg/5ml Solution in Mucolox™ (Group A)Dexamethasone 0.5mg/5ml Solution (Arm B)
Started1514
Completed1414
Not completed10
Withdrew: Lost to follow-up10

Outcome measures

PrimaryMean Change From Baseline in Oral Pain Scores on the Visual Analog Scale (VAS) at 4 Weeks

Oral Pain Scores were measured on the Visual Analog Scale (VAS), the score ranges from 0-10, zero indicating no pain and 10 indicating the worst pain. The pain score measured on a VAS scale will be compared between group A and group B to detect any significant differences pre and post treatment at 4 weeks.

Time frame:
4 weeks
Reported as:
Mean · score on a scale
Mean Change From Baseline in Oral Pain Scores on the Visual Analog Scale (VAS) at 4 Weeks
score on a scaleDexamethasone 0.5mg/5ml Solution in Mucolox™ (Group A)Dexamethasone 0.5mg/5ml Solution (Arm B)
Mean Change From Baseline in Oral Pain Scores on the Visual Analog Scale (VAS) at 4 Weeks6.3 ± 2.44.4 ± 3.3
SecondaryMean Change From Baseline in Reticulation/Keratosis, Erythema, and Ulceration (REU) Scores at 4 Weeks

Oral lesions were scored using the REU (reticulation,erythema and ulcer) system (form 0 till 49.5). Reticulations were scored from 0 to 1 (0 = no white striations, 1 = presence of white striations or keratotic papules); erythematous lesions from 0 to 3 by area of involvement (0 = no lesion, 1 = lesions less than 1 cm2, 2 = lesions from 1 to 3 cm2, 3 = lesions greater than 3 cm2); ulcers from 0 to 3 by area of involvement. The higher is the score the more severe is the disease. In order to evaluate the clinical improvement in clinician-reported outcome measures for oral lesions, REU scores within the compound dexamethasone solution in Mucolox™ group (Arm A) will be compared to that in the dexamethasone solution only group (Arm B). The REU scores will be summarized descriptively for each arm at pre-treatment, post-treatment, and pre-to-post treatment change. The pre-to-post treatment change will be compared between the arms using either student's t-test o

Time frame:
4 weeks
Reported as:
Mean · score on a scale
Mean Change From Baseline in Reticulation/Keratosis, Erythema, and Ulceration (REU) Scores at 4 Weeks
score on a scaleDexamethasone 0.5mg/5ml Solution in Mucolox™ (Group A)Dexamethasone 0.5mg/5ml Solution (Arm B)
Mean Change From Baseline in Reticulation/Keratosis, Erythema, and Ulceration (REU) Scores at 4 Weeks2.5 ± 3.13.2 ± 1.7

Adverse events

Collected over 1 month (study period). Non-serious events are listed at a 0% frequency threshold.

Adverse event summary by group
GroupDeathsSeriousOther
Dexamethasone 0.5mg/5ml Solution in Mucolox™ (Group A)0/14 (0%)0/14 (0%)0/14 (0%)
Dexamethasone 0.5mg/5ml Solution (Arm B)0/14 (0%)0/14 (0%)0/14 (0%)

Baseline characteristics

Age, Continuous
Age, Continuous(years)Dexamethasone 0.5mg/5ml Solution in Mucolox™ (Group A)Dexamethasone 0.5mg/5ml Solution (Arm B)Total
Median58 (30 to 79)67 (18 to 78)58 (18 to 79)
Sex: Female, Male
Sex: Female, Male(Participants)Dexamethasone 0.5mg/5ml Solution in Mucolox™ (Group A)Dexamethasone 0.5mg/5ml Solution (Arm B)Total
Female101222
Male527
Race and Ethnicity Not Collected
Race and Ethnicity Not Collected(Participants)Dexamethasone 0.5mg/5ml Solution in Mucolox™ (Group A)Dexamethasone 0.5mg/5ml Solution (Arm B)Total
Count of participants——0
Region of Enrollment
Region of Enrollment(Participants)Dexamethasone 0.5mg/5ml Solution in Mucolox™ (Group A)Dexamethasone 0.5mg/5ml Solution (Arm B)Total
United States151429
07

Study locations

1 site
  • Sol Silverman Oral Medicine Clinic - UCSF
    San Francisco, California 94117, United States
08

References and documents

Study documents

  • Protocol and statistical analysis plan · Nov 18, 2020

Documents are hosted by the registry — open the source record to download them.

Individual participant data

Plan to share: No — Final results will be submitted for publication on a peer reviewed journal

09

Registry details

Key details

Study ID
NCT04540133
Lead sponsor
University of California, San Francisco
Responsible party
Sponsor
First posted
Sep 7, 2020
Start date
Dec 26, 2020
Primary completion
Jan 6, 2023
Completion
Jan 6, 2023
Results posted
Dec 15, 2023
Last update
Dec 15, 2023

Study contacts

Alessandro Villa, DDS, PhD, MPH
principal investigator · University of California, San Francisco

Oversight

Data monitoring committee
No
FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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