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RecruitingNCT03900286Updated Dec 5, 2024

Low Energy Diet and Familial Partial Lipodystrophy

An interventional study of Total Dietary Replacement in Lipodystrophy, Diabetes and Diet Modification, sponsored by Cambridge University Hospitals NHS Foundation Trust. Recruiting at 1 site in United Kingdom. Open to participants aged 18 Years to 99 Years. Per ClinicalTrials.gov, last updated 2024-12-05.

Sponsored by Cambridge University Hospitals NHS Foundation Trust · Not applicable, Interventional, and Treatment

Phase
Not applicable
Study type
Interventional
Enrollment
20
Allocation
Not applicable
Ages
18 Years to 99 Years
Sex
All
01

Study summary

To evaluate the therapeutic efficacy and metabolic impact of a low energy diet (LED) in people with familial partial lipodystrophy and diabetes. Participants will be provided with a LED (total diet replacement) for 12 weeks, before the introduction of a stepped food transition. Metabolic effects will continue to be assessed for 1 year. In order to better understand why this intervention changes insulin sensitivity, we will also collect adipose and muscle tissue samples at baseline and 12 weeks into the intervention in participants willing to have these procedures performed. These samples will be used for histological, metabolite, gene expression and protein expression analyses.

02

Conditions studied

  • Lipodystrophy
  • Diabetes
  • Diet Modification

Keywords

  • Familial Partial Lipodystrophy
  • FPLD
  • Diet
  • Total Diet Replacement
  • Diabetes
03

Who can participate

Ages eligible
18 Years to 99 Years
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  • Familial Partial Lipodystrophy
  • Age >= 18 yrs
  • T2DM
  • Willingness to check daily blood sugars
  • HbA1c between 53mmol(7%)- 108 mmol(12%)
  • Weight stable for 3 months
  • Capacity to consent

Exclusion criteria

Exclusion Criteria:

  • Pregnancy
  • Untreated thyroid dysfunction (patients who have been euthyroid on medication for at least 3 months can be included)
  • Use of medication adversely that affects diabetes control (e.g. steroids/ immunosuppressants/ certain antipsychotics)
  • Incapacity to give informed consent
  • History of an eating disorder/ purging behaviour
  • Previous gastric bypass/ banding
  • Use of Leptin Therapy
  • Untreated retinopathy
04

Study design

Phase
Not applicable
Primary purpose
Treatment
Allocation
Not applicable
Intervention model
Single group
Masking
None (open label)
Enrollment
20 participants (estimated)

Study arms

  • Experimental
    Single Arm Study

    Total Diet Replacement for 12 weeks, food reintroduction 6 weeks

    Dietary Supplement: Total Dietary Replacement

Interventions

  • Dietary supplementTotal Dietary Replacement

    Total Dietary Replacement

05

What researchers measure

Primary outcomes

  1. A change from baseline in HbA1c

    mmol/mol

    Time frame: 12 weeks

Secondary outcomes

  1. A change from baseline in HbA1c

    mmol/mol

    Time frame: 1 year

  2. A change from baseline in fasting glucose

    mmol/l

    Time frame: 12 weeks, 1 year

  3. A change from baseline in triglycerides

    mmol/l

    Time frame: 12 weeks, 1 year

  4. A change from baseline in liver fat

    % liver fat on MRI

    Time frame: 12 weeks, 1 year

  5. A change from baseline in pancreatic fat

    % pancreatic fat on MRI

    Time frame: 12 weeks, 1 year

  6. A change from baseline in insulin sensitivity

    Insulin pmol/l values during oral glucose tolerance test

    Time frame: 12 weeks, 1 year

  7. A change from baseline in quality of life scores

    Change in scores of EQ-5D-3L Quality of Life measurement from baseline. EQ-5D-3L is a standardized instrument developed by the EuroQol Group as a measure of health-related quality of life. It comprises the following five dimensions: mobility, self-care, usual activities, pain/discomfort and anxiety/depression. Each dimension has 3 levels: no problems, some problems, and extreme problems. The patient is asked to indicate his/her health state by ticking the box next to the most appropriate statement in each of the five dimensions. This decision results into a 1-digit number that expresses the level selected for that dimension. The digits for the five dimensions can be combined into a 5-digit number that describes the patient's health state. The EQ VAS records the patient's self-rated health on a vertical visual analogue scale where the endpoints are labelled 'Best imaginable health state' and 'Worst imaginable health state'.

    Time frame: 12 weeks, 1 year

  8. A change from baseline in anxiety scores

    Change in scores of Generalised Anxiety Disorder-7 (GAD 7) from baseline. Change in scores of Generalised Anxiety Disorder-7 (GAD 7) from baseline. The Generalised Anxiety Disorder-7 (GAD 7) Questionnaire is a 7 item measurement that is used to measure or assess the severity of generalised anxiety disorder (GAD) The index scores are as follows: 0 - 4 No Anxiety 5 - 10 Mild Anxiety 11 - 15 Moderate Anxiety 15 - 21 Severe Anxiety

    Time frame: 12 weeks, 1 year

  9. A change from baseline in depression scores

    Change in scores of Patient Health Questionnaire-9 (PHQ9), from baseline. The PHQ-9 is a multipurpose instrument for screening, diagnosing, monitoring and measuring the severity of depression. The responses for each of the 9 items are: * 0 - Not at all * 1 - Several days * 2 - More than half the day * 3 - Nearly every day The score ranges are: 0 - 4 None 5 - 9 Mild 10 - 14 Moderate 15 - 19 Moderately Severe 20 - 27 Severe

    Time frame: 12 weeks, 1 year

  10. A change from baseline in antidiabetic medication use

    A change in the amount of antidiabetic drugs taken and/or a change in dose.

    Time frame: 12 weeks, 1 year

  11. Adult Eating Behaviour Questionnaire

    Change in scores in eating behaviour

    Time frame: 12 weeks, 1 year

  12. The Three Factor Eating Questionnaire

    Change in scores in The Three Factor Eating Questionnaire

    Time frame: 12 weeks, 1 year

06

Study locations

1 of 1 sites recruiting
  • Cambridge University Hospital NHS Foundation Trust
    Cambridge, United Kingdom
    • Mandour O Mandour, MBBS, MRCP · Contact · mom30@cam.ac.uk · +441233768455
    • David Savage · Principal investigator
    Recruiting
07

References and documents

Publications

  • Lim EL, Hollingsworth KG, Aribisala BS, Chen MJ, Mathers JC, Taylor R. Reversal of type 2 diabetes: normalisation of beta cell function in association with decreased pancreas and liver triacylglycerol. Diabetologia. 2011 Oct;54(10):2506-14. doi: 10.1007/s00125-011-2204-7. Epub 2011 Jun 9. PubMed 21656330 ↗
  • Lean ME, Leslie WS, Barnes AC, Brosnahan N, Thom G, McCombie L, Peters C, Zhyzhneuskaya S, Al-Mrabeh A, Hollingsworth KG, Rodrigues AM, Rehackova L, Adamson AJ, Sniehotta FF, Mathers JC, Ross HM, McIlvenna Y, Stefanetti R, Trenell M, Welsh P, Kean S, Ford I, McConnachie A, Sattar N, Taylor R. Primary care-led weight management for remission of type 2 diabetes (DiRECT): an open-label, cluster-randomised trial. Lancet. 2018 Feb 10;391(10120):541-551. doi: 10.1016/S0140-6736(17)33102-1. Epub 2017 Dec 5. PubMed 29221645 ↗

Study documents

  • Study protocol · Apr 11, 2019

Documents are hosted by the registry — open the source record to download them.

Individual participant data

Plan to share: No

08

Registry details

Key details

Study ID
NCT03900286
Lead sponsor
Cambridge University Hospitals NHS Foundation Trust
Responsible party
Mandour Omer Mandour (Wellcome Trust Senior Clinical Fellow, Cambridge University Hospitals NHS Foundation Trust) — Principal investigator
First posted
Apr 3, 2019
Start date
Jan 16, 2020
Primary completion
Apr 2025 (estimated)
Completion
May 2025 (estimated)
Last update
Dec 5, 2024

Study contacts

Mandour O Mandour
Contact
mom30@cam.ac.uk
01223768625
David Savage
principal investigator · Wellcome Trust-MRC Institute of Metabolic Science, University of Cambridge

Oversight

Data monitoring committee
No
FDA-regulated drug
No
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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