ClinicalTrials.gg
TerminatedNCT03421496Updated Jun 7, 2023Results posted

A Study to Assess Cannabidiol Oral Solution With Vigabatrin as Initial Therapy in Participants With Infantile Spasms

A Phase 3 interventional study of Cannabidiol Oral Solution and Placebo in Infantile Spasm, sponsored by Radius Pharmaceuticals, Inc.. Terminated at 5 sites in United States. Open to participants aged 1 Month to 24 Months. Per ClinicalTrials.gov, last updated 2023-06-07.

Sponsored by Radius Pharmaceuticals, Inc. · Phase 3, Interventional, and Treatment

Why this study was terminated
The study was terminated due to slow enrollment and failure to identify adequate patients that met entry criteria.
Phase
Phase 3
Study type
Interventional
Enrollment
2
Allocation
Randomized
Ages
1 Month to 24 Months
Sex
All
01

Study summary

The primary purpose of this study was to evaluate the efficacy, safety, and tolerability of Cannabidiol Oral Solution (CBD) as adjunctive therapy with vigabatrin as initial therapy, compared to vigabatrin alone in the treatment of infants newly diagnosed with Infantile Spasms (IS).

Read the detailed description

This was a randomized, double-blind, placebo-controlled, parallel-group study in which participants were randomized in a 1:1 ratio to 1 of 2 treatment groups. During the Initial Treatment Period, participants received either vigabatrin plus CBD or vigabatrin plus matching placebo and were dosed approximately every 12 hours, with a meal. This study was comprised of five periods: Screening, Initial Treatment, Extended Treatment, Taper, and Follow up Periods, with a maximum duration of approximately 140 days.

02

Conditions studied

  • Infantile Spasm

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Keywords

  • Infantile spasm
  • Vigabatrin
  • Cannabidiol oral solution
03

In context

Spasms, Infantile

47 studies on the registry are indexed under Spasms, Infantile; 8 are open to participants now.

This study's enrollment of 2 is below the median of 40 across 33 interventional studies indexed under Spasms, Infantile.

Browse Spasms, Infantile studies →

Lead sponsor

Radius Pharmaceuticals, Inc. is the lead sponsor of 9 studies on the registry; none are open to participants now.

Of its 7 completed or terminated interventional studies of FDA-regulated products, 7 (100%) have results posted.

Counted across the registry records on this site, refreshed daily.

04

Who can participate

Ages eligible
1 Month to 24 Months
Sexes eligible
All
Accepts healthy volunteers
No

Go through the criteria one by one — yes, no or not sure — and take the list to your doctor or the study team. Kept in this browser only.

Inclusion criteria

  1. Parent(s)/caregiver(s) fully comprehends and signs the form, understands all study procedures, and can communicate satisfactorily with the Investigator and study coordinator, in accordance with applicable laws, regulations, and local requirements.
  2. Clinical diagnosis of Infantile Spasms, confirmed by video-EEG (including at least one cluster of electroclinical spasms [≥3 in any 10-minute epoch] and hypsarrythmia) obtained during the Screening Period and read by a central reader.
  3. General good health (defined as the absence of any abnormalities as determined by the Investigator) based on physical and neurological examinations, medical history, and clinical laboratory values completed during the Screening Visit).
  4. In the opinion of the investigator, the parent(s)/caregiver(s) is (are) willing and able to comply with the study procedures and visit schedules.

Exclusion criteria

Exclusion Criteria:

  1. Is considered by the investigator, for any reason (including, but not limited to, the risks described as precautions, warnings, and in the current version of the Investigator's Brochure for Cannabidiol Oral Solution) to be an unsuitable candidate to receive the study drug.
  2. Known or suspected allergy to cannabidiol.
  3. History of an allergic reaction or a known or suspected sensitivity to any substance that is contained in the product formulation.
  4. Use of any cannabidiol/cannabis product within 30 days of study entry.
  5. Participant is diagnosed or suspected of having tuberous sclerosis.
  6. Participant has received treatment with either vigabatrin, ACTH, or high-dose previously.
  7. Previous or concomitant therapy with felbamate, clobazam, valproic acid, or the ketogenic diet.
  8. Participant currently on any disallowed -related medication (phenytoin, fluvoxamine, carbamazepine, and St. John's Wort).
  9. Previously received any investigational drug or device or investigational therapy within 30 days before Screening.
  10. abnormal laboratory values, including: liver function tests (LFTs) such as albumin, direct , total bilirubin, (AST), and alanine aminotransferase (ALT) ≥3 times the (ULN). The investigator may deem the participant eligible if he or she judges the laboratory values to be not clinically significant.
Terms in these criteria, in plain language(9)

Underlined terms in the criteria open these too. Explained by clinicaltrials.gg, not part of the registry record. The study team decides who can take part.

Informed consent

Before you join, the study team explains what taking part involves — its purpose, what happens, the risks and possible benefits — and answers your questions, so you can decide freely. Consent is usually recorded on a form (the informed consent form, ICF) signed by you or, where the law allows, by someone legally authorised to decide for you.

You can keep asking questions during the study, you are told of new information that matters, and you can choose to leave at any time.

Clinically significant

Judged by the study doctor to matter for your health or for the study. It is a doctor’s decision, so ask the study team if you are unsure whether something counts.

Contraindication

A reason a treatment, test or procedure should not be given to a particular person, such as an allergy, another illness or a medicine they take.

Investigational drug or device

A drug or device being studied in a clinical trial.

It may be new, or already approved and being studied for another use, dose or form. Criteria often leave out people who took part in another study of one within a recent period, commonly 30 days or five half-lives.

Corticosteroids (steroids)

Anti-inflammatory medicines such as prednisone, prednisolone and dexamethasone — not the anabolic steroids used for muscle.

Studies differ in what they allow: check which steroid medicines, routes (tablets, injections, creams, inhalers, eye drops) and doses this study accepts.

CYP3A (CYP3A4) inhibitors and inducers

CYP3A is a group of enzymes, mainly CYP3A4, in the liver and gut that break down many medicines. Some medicines, supplements and foods (grapefruit, St John’s wort) slow them down or speed them up, which changes how much of a study drug stays in the body.

Studies list them so they can be avoided or switched; bring a list of everything you take, including supplements.

Bilirubin

A yellow substance made when red blood cells are broken down, which the liver clears. A high level can mean a problem with the liver or the bile ducts.

Criteria often allow more for people with Gilbert’s syndrome, a harmless inherited condition that raises bilirubin.

ALT and AST (liver enzymes)

Two enzymes measured in a routine blood test of the liver. Higher levels can mean the liver is under strain or damaged. SGPT and SGOT are older names for ALT and AST.

Criteria usually give a limit as a multiple of the upper limit of normal (ULN), often higher when cancer has spread to the liver.

ULN (upper limit of normal)

The top of the normal range for a blood test, as set by the laboratory that runs it. Each lab prints its own range next to your result.

“≤ 2.5 × ULN” means the result can be up to two and a half times that top value.

05

Study design

Phase
Phase 3
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Parallel assignment
Masking
Quadruple (Participant, Care provider, Investigator, Outcomes assessor)
Enrollment
2 participants (actual)

Study arms

  • Experimental
    CBD with Vigabatrin

    Participants received up to 40 milligrams per kilogram per day (mg/kg/day) divided twice daily (BID) of CBD with food. Participants also received up to 150 mg/kg/day BID of vigabatrin with food.

    Drug: Cannabidiol Oral Solution · Drug: Vigabatrin

  • Placebo comparator
    Placebo with Vigabatrin

    Participants received a matching placebo to CBD with food, and also received up to 150 mg/kg/day BID of vigabatrin with food.

    Drug: Placebo · Drug: Vigabatrin

Interventions

  • An oral solution containing pharmaceutical grade cannabidiol (nonplant-based).

  • DrugPlacebo

    Matching oral solution

  • Powder suspension

    Also known as: Sabril

06

What researchers measure

Primary outcomes

  1. Percentage of Participants Considered Complete Responders

    Complete response is defined as complete resolution of spasms and hypsarrhythmia confirmed by 24-hour video-electroencephalogram (EEG).

    Time frame: Up to Day 15

Secondary outcomes

  1. Percentage of Participants With Resolution of Infantile Spasms

    Resolution of IS was assessed by 24-hour video-EEG.

    Time frame: Up to Day 15

  2. Percentage of Participants With Resolution of Hypsarrhythmia

    Resolution of hypsarrhythmia was assessed by 24-hour video-EEG.

    Time frame: Up to Day 15

  3. Investigator Impression of Efficacy and Tolerability of Study Drug Clinical Global Impression- Global Improvement (CGI-I)

    Investigators will use the CGI-I scale, which is a 7-point scale that requires the clinician to assess how much the participant's illness has improved or worsened relative to a baseline state at the beginning of the intervention and is rated as: 1=very much improved; 2=much improved; 3=minimally improved; 4=no change; 5=minimally worse; 6=much worse; 7=very much worse. Higher scores indicated worse condition.

    Time frame: Day 15

  4. Percentage of Participants With Increase in Number of Spasm-Free Days Between Day 1 and Day 15

    Increase in spasm-free days will be determined by seizure diary entries.

    Time frame: Up to Day 15

  5. Percentage of Participants With Complete Response During the Initial Treatment Period Who Relapse During the Extended Treatment Period

    Relapse during the extended treatment period will be confirmed by video-EEG following parent report of relapse.

    Time frame: Up to Day 75

  6. Time to Relapse During the Extended Treatment Period

    Time frame: Up to Day 75

07

Results

Posted Jun 7, 2023
Limitations and caveats
This study was terminated by the Sponsor. The Sponsor terminated the study due to slow enrollment and a failure to identify adequate participants that met eligibility criteria. Due to study termination and only 2 participants being enrolled there are concerns regarding participant confidentiality, therefore no data are being reported.

Participant flow

This study was terminated by the Sponsor. The Sponsor terminated the study due to slow enrollment and a failure to identify adequate participants that met eligibility criteria. Due to study termination and only 2 participants being enrolled there are concerns regarding participant confidentiality, therefore no data are being reported.

Participant flow — Overall Study
MilestoneCBD With VigabatrinPlacebo With Vigabatrin
Started00
Completed00
Not completed00

Outcome measures

PrimaryPercentage of Participants Considered Complete Responders

Complete response is defined as complete resolution of spasms and hypsarrhythmia confirmed by 24-hour video-electroencephalogram (EEG).

Time frame:
Up to Day 15

No measurements were reported for this outcome.

SecondaryPercentage of Participants With Resolution of Infantile Spasms

Resolution of IS was assessed by 24-hour video-EEG.

Time frame:
Up to Day 15

No measurements were reported for this outcome.

SecondaryPercentage of Participants With Resolution of Hypsarrhythmia

Resolution of hypsarrhythmia was assessed by 24-hour video-EEG.

Time frame:
Up to Day 15

No measurements were reported for this outcome.

SecondaryInvestigator Impression of Efficacy and Tolerability of Study Drug Clinical Global Impression- Global Improvement (CGI-I)

Investigators will use the CGI-I scale, which is a 7-point scale that requires the clinician to assess how much the participant's illness has improved or worsened relative to a baseline state at the beginning of the intervention and is rated as: 1=very much improved; 2=much improved; 3=minimally improved; 4=no change; 5=minimally worse; 6=much worse; 7=very much worse. Higher scores indicated worse condition.

Time frame:
Day 15

No measurements were reported for this outcome.

SecondaryPercentage of Participants With Increase in Number of Spasm-Free Days Between Day 1 and Day 15

Increase in spasm-free days will be determined by seizure diary entries.

Time frame:
Up to Day 15

No measurements were reported for this outcome.

SecondaryPercentage of Participants With Complete Response During the Initial Treatment Period Who Relapse During the Extended Treatment Period

Relapse during the extended treatment period will be confirmed by video-EEG following parent report of relapse.

Time frame:
Up to Day 75

No measurements were reported for this outcome.

SecondaryTime to Relapse During the Extended Treatment Period
Time frame:
Up to Day 75

No measurements were reported for this outcome.

Adverse events

Collected over This study was terminated by the Sponsor. The Sponsor terminated the study due to slow enrollment and a failure to identify adequate participants that met eligibility criteria. Due to study termination and only 2 participants being enrolled there are concerns regarding participant confidentiality, therefore no data are being reported.. Non-serious events are listed at a 0% frequency threshold.

Adverse event summary by group
GroupDeathsSeriousOther
CBD With Vigabatrin———
Placebo With Vigabatrin———

Baseline characteristics

This study was terminated by the Sponsor. The Sponsor terminated the study due to slow enrollment and a failure to identify adequate participants that met eligibility criteria. Due to study termination and only 2 participants being enrolled there are concerns regarding participant confidentiality, therefore no data are being reported.

Age, Continuous
Age, ContinuousCBD With VigabatrinPlacebo With VigabatrinTotal
Sex: Female, Male
Sex: Female, MaleCBD With VigabatrinPlacebo With VigabatrinTotal
Female———
Male———
Ethnicity (NIH/OMB)
Ethnicity (NIH/OMB)CBD With VigabatrinPlacebo With VigabatrinTotal
Hispanic or Latino———
Not Hispanic or Latino———
Unknown or Not Reported———
08

Study locations

5 sites
  • Nicklaus Children's Hospital
    Miami, Florida 33155, United States
  • Beaumont Children's Hospital
    Royal Oak, Michigan 48073, United States
  • Akron Children's Hospital
    Akron, Ohio 44308, United States
  • Oregon Health & Science University
    Portland, Oregon 97239, United States
  • Institute for Research and Innovation | MultiCare Health System
    Tacoma, Washington 98405, United States
09

References and documents

Study documents

PDFs hosted by the registry, ClinicalTrials.gov.

10

Updates

Tracking since Sep 25, 2026
No changes since tracking began. The registry record was last updated on Jun 7, 2023, before this site started recording changes on Sep 25, 2026. Its history is on ClinicalTrials.gov ↗
11

Registry details

Key details

Study ID
NCT03421496
Lead sponsor
Radius Pharmaceuticals, Inc.
Responsible party
Sponsor
First posted
Feb 5, 2018
Start date
Sep 5, 2018
Primary completion
May 29, 2019
Completion
May 29, 2019
Results posted
Jun 7, 2023
Last update
Jun 7, 2023

Oversight

Data monitoring committee
Yes
FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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