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CompletedNCT03292809Updated Dec 22, 2022Results posted

CyclASol for the Treatment of Signs and Symptoms of Dry Eye Disease (DED)

A Phase 2/3 interventional study of CyclASol topical ocular, eye drops and Vehicle topical ocular, eye drops in Dry Eye Disease, sponsored by Novaliq GmbH. Completed at 9 sites in United States. Open to participants aged 18 Years and older. Per ClinicalTrials.gov, last updated 2022-12-22.

Sponsored by Novaliq GmbH · Phase 2/3, Interventional, and Treatment

Phase
Phase 2/3
Study type
Interventional
Enrollment
328
Allocation
Randomized
Ages
18 Years and older
Sex
All
01

Study summary

The objective of this study is to assess the efficacy, safety, and tolerability of CyclASol Ophthalmic Solution in comparison to vehicle for the treatment of the signs and symptoms of DED.

Read the detailed description

This Phase 2b/3 study will assess the efficacy, safety and and tolerability of CyclASol Ophthalmic Solution as one drop twice daily versus vehicle.

02

Conditions studied

03

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  • Signed ICF (Informed Consent Form) and HIPAA (Health Insurance Portability and Accountability Act)
  • Patient-reported history of DED in both eyes
  • Current use of OTC (over-the-counter) and/or artificial tears for dry eye symptoms
  • Ability and willingness to follow instructions, including participation in all study assessments and visits

Exclusion criteria

Exclusion Criteria:

  • Women who are pregnant, nursing or planning a pregnancy
  • Unwillingness to submit a urine pregnancy test at screening and the last visit (or early termination visit) if of childbearing potential, or unwillingness to use acceptable means of birth control
  • Clinically significant slit-lamp findings or abnormal lid anatomy at screening
  • Ocular/periocular malignancy
  • History of herpetic keratitis
  • Active ocular allergies or ocular allergies that may become active during the study period
  • Ongoing ocular or systemic infection at screening or baseline
  • Wear of contact lenses within 3 months prior to screening or anticipated use of contact lenses during the study
  • History of no response to previous topical Cyclosporine A and/or use of topical Cyclosporine A or Liftigrast within 2 months prior to screening
  • Intraocular surgery or ocular laser surgery within the previous 6 months, or have any planned ocular and/or lid surgeries over the study period
  • Presence of uncontrolled systemic diseases
  • Presence of known allergy and/or sensitivity to the study drug or its components
04

Study design

Phase
Phase 2 / Phase 3
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Parallel assignment
Masking
Double (Participant, Investigator)
Enrollment
328 participants (actual)

Study arms

  • Experimental
    CyclASol Ophthalmic Solution

    Cylclosporine A solution in vehicle

    Drug: CyclASol topical ocular, eye drops

  • Placebo comparator
    Vehicle Ophthalmic Solution

    Vehicle only

    Drug: Vehicle topical ocular, eye drops

Interventions

  • DrugCyclASol topical ocular, eye drops

    Cyclosporine A solution in vehicle

    Also known as: Ciclosporine (CsA)

  • DrugVehicle topical ocular, eye drops

    Vehicle

    Also known as: Vehicle

05

What researchers measure

Primary outcomes

  1. Change From Baseline in Total Corneal Fluorescein Staining at Day 29

    CFS was assessed in each eye using the National Eye Institute (NEI) scale. A standardized grading system of 0-3 is used for each of the five areas on each cornea. Grade 0 will be specified when no staining is present. The maximum total score for each eye is 15. Higher values describe greater staining and corneal damage.

    Time frame: baseline and 1 month [day 29]

  2. Change From Baseline in Ocular Surface Disease Index at Day 29

    The OSDI score is a composite measure built on 12 questions,with totals ranging from 0 to 100, and higher scores representing a worse disease index.

    Time frame: baseline and 1 month [day 29]

06

Results

Posted May 21, 2021

Participant flow

Participant flow — Overall Study
MilestoneCyclASol Ophthalmic SolutionVehicle Ophthalmic Solution
Started162166
Completed155163
Not completed73

Outcome measures

PrimaryChange From Baseline in Total Corneal Fluorescein Staining at Day 29

CFS was assessed in each eye using the National Eye Institute (NEI) scale. A standardized grading system of 0-3 is used for each of the five areas on each cornea. Grade 0 will be specified when no staining is present. The maximum total score for each eye is 15. Higher values describe greater staining and corneal damage.

Time frame:
baseline and 1 month [day 29]
Reported as:
Mean · score on a scale
Change From Baseline in Total Corneal Fluorescein Staining at Day 29
score on a scaleCyclASol Ophthalmic SolutionVehicle Ophthalmic Solution
Change From Baseline in Total Corneal Fluorescein Staining at Day 29-2.9 ± 2.59-2.2 ± 2.73
PrimaryChange From Baseline in Ocular Surface Disease Index at Day 29

The OSDI score is a composite measure built on 12 questions,with totals ranging from 0 to 100, and higher scores representing a worse disease index.

Time frame:
baseline and 1 month [day 29]
Reported as:
Mean · score on a scale
Change From Baseline in Ocular Surface Disease Index at Day 29
score on a scaleCyclASol Ophthalmic SolutionVehicle Ophthalmic Solution
Change From Baseline in Ocular Surface Disease Index at Day 29-7.08 ± 18.650-5.37 ± 15.291

Adverse events

Collected over 85 Days ± 2 (Randomization until Study Exit). Non-serious events are listed at a 2% frequency threshold.

Adverse event summary by group
GroupDeathsSeriousOther
CyclASol Ophthalmic Solution0/162 (0%)0/162 (0%)26/162 (16%)
Vehicle Ophthalmic Solution0/166 (0%)3/166 (1.8%)23/166 (13.9%)
Most frequent serious events
Most frequent serious events
EventCyclASol Ophthalmic SolutionVehicle Ophthalmic Solution
Small intestinal obstructionGastrointestinal disorders0/1621/166
PneumoniaInfections and infestations0/1621/166
Intervertebral disc degenerationMusculoskeletal and connective tissue disorders0/1621/166
Most frequent other events
Most frequent other events
EventCyclASol Ophthalmic SolutionVehicle Ophthalmic Solution
Upper respiratory tract infectionInfections and infestations8/1627/166
NasopharyngitisInfections and infestations7/1627/166
Visual acuity reducedEye disorders5/1623/166
Instillation site painEye disorders4/1622/166
Vision blurredEye disorders2/1624/166

Baseline characteristics

Age, Continuous
Age, Continuous(years)CyclASol Ophthalmic SolutionVehicle Ophthalmic SolutionTotal
Mean61.5 ± 13.661.3 ± 12.6661.4 ± 13.11
Sex: Female, Male
Sex: Female, Male(Participants)CyclASol Ophthalmic SolutionVehicle Ophthalmic SolutionTotal
Female116119235
Male464793
Ethnicity (NIH/OMB)
Ethnicity (NIH/OMB)(Participants)CyclASol Ophthalmic SolutionVehicle Ophthalmic SolutionTotal
Hispanic or Latino151126
Not Hispanic or Latino147155302
Unknown or Not Reported000
Race (NIH/OMB)
Race (NIH/OMB)(Participants)CyclASol Ophthalmic SolutionVehicle Ophthalmic SolutionTotal
American Indian or Alaska Native112
Asian141933
Native Hawaiian or Other Pacific Islander112
Black or African American161430
White130127257
More than one race033
Unknown or Not Reported011
Region of Enrollment
Region of Enrollment(participants)CyclASol Ophthalmic SolutionVehicle Ophthalmic SolutionTotal
United States162166328
07

Study locations

9 sites
  • CYS-003 Investigational Site
    Newport Beach, California 92663, United States
  • CYS-003 Investigational Site
    Torrance, California 90505, United States
  • CYS-003 Investigational Site
    Indianapolis, Indiana 46290, United States
  • CYS-003 Investigational Site
    Louisville, Kentucky 40206, United States
  • CYS-003 Investigational Site
    Andover, Massachusetts 01810, United States
  • CYS-003 Investigational Site
    Raynham, Massachusetts 02767, United States
  • CYS-003 Investigational Site
    Memphis, Tennessee 38119, United States
  • CYS-003 Investigational Site
    Nashville, Tennessee 37205, United States
  • CYS-003 Investigational Site
    Norfolk, Virginia 23502, United States
08

References and documents

Publications

  • Sheppard JD, Wirta DL, McLaurin E, Boehmer BE, Ciolino JB, Meides AS, Schluter T, Ousler GW, Usner D, Krosser S. A Water-free 0.1% Cyclosporine A Solution for Treatment of Dry Eye Disease: Results of the Randomized Phase 2B/3 ESSENCE Study. Cornea. 2021 Oct 1;40(10):1290-1297. doi: 10.1097/ICO.0000000000002633. PubMed 34481407 ↗

Study documents

  • Protocol and statistical analysis plan · Jan 29, 2018

Documents are hosted by the registry — open the source record to download them.

Individual participant data

Plan to share: No

09

Registry details

Key details

Study ID
NCT03292809
Lead sponsor
Novaliq GmbH
Responsible party
Sponsor
First posted
Sep 26, 2017
Start date
Oct 19, 2017
Primary completion
May 22, 2018
Completion
Jun 20, 2018
Results posted
May 21, 2021
Last update
Dec 22, 2022

Study contacts

Sonja Kroesser, PhD
study director · Novaliq GmbH

Oversight

Data monitoring committee
No
FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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