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CompletedNCT02764697Updated Jul 2, 2018Results posted

Study of H.P. ACTHAR Subcutaneous Gelatin (Gel)(Highly Purified Gel Injection) in Uveitis Patients

A Phase 4 interventional study of H.P. ACTHAR SUBCUTANEOUS GEL INJECTION in Uveitis, Anterior Uveitis and Intermediate Uveitis, sponsored by Tampa Bay Uveitis Center, LLC. Completed at 1 site in United States. Open to participants aged 18 Years and older. Per ClinicalTrials.gov, last updated 2018-07-02.

Sponsored by Tampa Bay Uveitis Center, LLC · Phase 4, Interventional, and Treatment

Phase
Phase 4
Study type
Interventional
Enrollment
6
Allocation
Not applicable
Ages
18 Years and older
Sex
All
01

Study summary

Uveitis represents a heterogeneous group of diseases that results from ocular inflammatory reaction involving ocular tissue and vasculature. The inflammation usually causes pain, redness, photophobia and blurred vision. This inflammation, is typically treated with regional or systemic therapy. The regional therapy typically consists of topical corticosteroids or periocular or regional corticosteroids. Regional therapy can lead to a steroid response glaucoma, which is increased intraocular pressure.This pilot study aims to evaluate the possible effectiveness of H.P. Acthar in patients with active ocular inflammatory disease, and currently on treatment for glaucoma or have a history of glaucoma.

Read the detailed description

Uveitis represents a heterogeneous group of diseases that results from ocular inflammatory reaction involving ocular tissue and vasculature. The inflammation usually causes pain, redness, photophobia and blurred vision.

H.P Acthar Gel stimulate the adrenal cortex to secrete cortisol. Additionally H.P. Acthar gel is also reported to bind to melanocortin receptors. Melanocortin receptor activation has been shown to exert marked anti-inflammatory and immune-modulatory effects in animal studies, by modulating pro inflammatory cytokines, followed by induction of anti- inflammatory mediators and subsequent leukocyte migration. Specifically melanocortins down regulate Tumor Necrosis Factor (TNF) alpha, Interleukin (IL) -2, Interferon gamma and T-cell proliferation and upregulates IL-10 and regulatory T cells. For this reason H.P. Acthar is an approved treatment for ocular inflammatory disease.

Ocular inflammatory disease is typically treated with regional or systemic therapy. The regional therapy typically consists of topical corticosteroids or periocular or regional corticosteroids. Regional therapy can lead to a steroid response glaucoma, which is increased intraocular pressure.This pilot study aims to evaluate the possible effectiveness of H.P. Acthar in patients with active ocular inflammatory disease, and currently on treatment for glaucoma or have a history of glaucoma.

Subjects will be treated with H P Acthar subcutaneous gel, 40 U/ml, given twice weekly x 8 weeks, followed by once weekly x 4 weeks: a total 20 doses with the same cumulative units to be administered, using the approved route, with the option to do 4 additional doses if resolution is incomplete.

This will be a prospective open-label, non-randomized pilot study: 12 week treatment for active non-infectious uveitis, endpoint assessment and safety assessment; additional 12 week assessment for uveitis activity/quiescence and safety assessment.

02

Conditions studied

  • Uveitis
  • Anterior Uveitis
  • Intermediate Uveitis
  • Posterior Uveitis
  • Scleritis
  • Clinically Significant Macular Edema

Keywords

  • Glaucoma associated with uveitis
03

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  • Subject has the ability to understand and sign the informed consent document
  • Subject is 18 years of age or older
  • Subject can be male or female
  • Subject has negative Purified Protein Derivative (Tuberculosis skin test) or quantiferon TB Gold Test (blood test for TB) testing done in 3 months
  • Subject has active ocular inflammation in at least one eye
  • Subject has visual acuity in at least one eye of 20/400 or better.
  • Subject has a history of glaucoma or has actively treated glaucoma
  • Subject is willing and able to comply with the study procedures
  • Female subjects of childbearing potential must not be pregnant or breast-feeding, must have a negative pregnancy test at screening and must be willing to undergo pregnancy testing throughout the study

Exclusion criteria

Exclusion Criteria:

  • Subject has any ocular infection
  • Subject has any systemic infection
  • Participant has documented immunocompromised or immune-incompetent state
  • Subject has any ocular co-morbidity than prevents assessment of intraocular inflammation
  • Subject has had any intra-ocular surgery in previous 6 weeks
  • Subject has any planned elective surgery ocular or systemic during study duration
  • Subject is pregnant or breast-feeding
  • Subject had a recent vaccination with live or attenuated vaccines
  • Subject has a sensitivity to Porcine derived proteins
  • Subject has a medical history which is a contraindication to receiving H.P. Acthar
04

Study design

Phase
Phase 4
Primary purpose
Treatment
Allocation
Not applicable
Intervention model
Single group
Masking
None (open label)
Enrollment
6 participants (actual)

Study arms

  • Other
    H.P. Acthar Subcutaneous Gel Injection

    For the current protocol we are proposing, 40 U/ml, given twice weekly x 8 weeks, followed by once weekly x 4 weeks: a total 20 doses, using the approved route, with the option to do 4 additional doses if resolution is incomplete.

    Drug: H.P. ACTHAR SUBCUTANEOUS GEL INJECTION

Interventions

  • DrugH.P. ACTHAR SUBCUTANEOUS GEL INJECTION

    Subcutaneous injection twice weekly

    Also known as: Acthar

05

What researchers measure

Primary outcomes

  1. Number of Participants With Photographic Haze Reduced to Grade 0 or Down 2 Steps Documented With Fundus Photography

    Subjects will have fundus photography at baseline and 12 weeks. Intermediate uveitis is graded by haze; it is done using the photographic scale: grades 0-4 (lower values are a better outcome), utilized by the SUN criteria, based on the Nussenblatt photographic vitreous haze scale

    Time frame: 12 Weeks

  2. Number of Participants With Clinically Significant Improvement of Macular Edema

    Clinically Significant Uveitic Macular Edema: Clinical Improvement of Macular Edema with OCT Documentation of central foveal thickness \< 300 microns

    Time frame: 12 weeks

06

Results

Posted Jul 2, 2018
Limitations and caveats
Small sample size

Participant flow

The recruitment period was 06/31/2016 through 08/10/2016 Active follow-up period 06/31/2016 through 12/07/2016 The study was conducted at 1 site Tampa Bay Uveitis Center, LLC 5800 49th Street North, St Petersburg Fl 33709: Outpatient Medical Clinic

Participant flow — Overall Study
MilestoneH.P. Acthar Subcutaneous Gel Injection
Started5
Completed2
Not completed3
Withdrew: Lack of efficacy3

Outcome measures

PrimaryNumber of Participants With Photographic Haze Reduced to Grade 0 or Down 2 Steps Documented With Fundus Photography

Subjects will have fundus photography at baseline and 12 weeks. Intermediate uveitis is graded by haze; it is done using the photographic scale: grades 0-4 (lower values are a better outcome), utilized by the SUN criteria, based on the Nussenblatt photographic vitreous haze scale

Time frame:
12 Weeks
Reported as:
Count of participants · Participants
Number of Participants With Photographic Haze Reduced to Grade 0 or Down 2 Steps Documented With Fundus Photography
ParticipantsH.P. Acthar Subcutaneous Gel Injection
1 Step of VH Improvement3
2 Step of VH1
No VH Improvement1
PrimaryNumber of Participants With Clinically Significant Improvement of Macular Edema

Clinically Significant Uveitic Macular Edema: Clinical Improvement of Macular Edema with OCT Documentation of central foveal thickness \< 300 microns

Time frame:
12 weeks
Reported as:
Count of participants · Participants
Number of Participants With Clinically Significant Improvement of Macular Edema
ParticipantsH.P. Acthar Subcutaneous Gel Injection
Decrease in Central Foveal Thickness <3000
Decrease in central Fovea > 300 Microns5

Adverse events

Collected over 3 months. Non-serious events are listed at a 0% frequency threshold.

Adverse event summary by group
GroupDeathsSeriousOther
H.P. Acthar Subcutaneous Gel Injection0/5 (0%)0/5 (0%)0/5 (0%)

Baseline characteristics

Age, Categorical
Age, Categorical(Participants)H.P. Acthar Subcutaneous Gel Injection
<=18 years0
Between 18 and 65 years4
>=65 years1
Sex: Female, Male
Sex: Female, Male(Participants)H.P. Acthar Subcutaneous Gel Injection
Female3
Male2
Race (NIH/OMB)
Race (NIH/OMB)(Participants)H.P. Acthar Subcutaneous Gel Injection
American Indian or Alaska Native0
Asian0
Native Hawaiian or Other Pacific Islander0
Black or African American4
White1
More than one race0
Unknown or Not Reported0
Region of Enrollment
Region of Enrollment(participants)H.P. Acthar Subcutaneous Gel Injection
United States5
07

Study locations

1 site
  • Tampa Bay Uveitis Center
    Saint Petersburg, Florida 33709, United States
08

References and documents

Individual participant data

Plan to share: No

No publications or documents are linked to this record.

09

Registry details

Key details

Study ID
NCT02764697
Lead sponsor
Tampa Bay Uveitis Center, LLC
Collaborators
Mallinckrodt
Responsible party
Sponsor
First posted
May 6, 2016
Start date
Jun 30, 2016
Primary completion
Dec 7, 2016
Completion
Dec 20, 2016
Results posted
Jul 2, 2018
Last update
Jul 2, 2018

Study contacts

Grace L Clarke
principal investigator · Tampa Bay Uveitis Center, LLC

Oversight

Data monitoring committee
No
View the source record on ClinicalTrials.gov ↗

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