Rett Syndrome: all 96 studies
Page 1 of 1. Open to participants first (19), then studies with results posted, then the rest; newest registration first within each.
- Adapting a Psychosocial Support Intervention for the Rett Syndrome CommunityNot yet recruitingNCT07730112Not applicable
- Lamivudine as a Novel Clinical Effort for Rett SyndromeEnrolling by invitationNCT07640503Phase 2
- Auditory EEG and Behavioral Assessments in Individuals With Rett SyndromeRecruitingNCT07569445
- A Phase 3 Study of Fenfluramine Hydrochloride in Rett SyndromeRecruitingNCT07503444Phase 3
- Efficacy and Safety of NTI164 in Children and Young Adults With Rett SyndromeNot yet recruitingNCT07257978Phase 2/3
- Rett REVOLUTION Trial: An Exploratory Evaluation of the Safety and Efficacy of Vorinostat in Rett SyndromeRecruitingNCT07150013Phase 1
- To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett SyndromeRecruitingNCT06840496Phase 3
- GCB-002 in Treatment of Patients With Rett SyndromeEnrolling by invitationNCT06739434Not applicable
- Cognitive Function in Rett Syndrome During Trofinetide TreatmentRecruitingNCT06705816
- ATTUNE: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Intrathecally-Administered ION440 in Participants With Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome (MDS)RecruitingNCT06430385Phase 1/2
- Biomarkers in Rett SyndromeRecruitingNCT06346444
- The Diagnostic Experience of Male Rett SyndromeRecruitingNCT06346106
- Neurophysiologic Biomarkers in Rett SyndromeRecruitingNCT05932589
- Gene Editing as a Therapeutic Approach for Rett SyndromeRecruitingNCT05740761
- Rett Syndrome RegistryRecruitingNCT05432349
- The Rett Syndrome Global RegistryRecruitingNCT04900493
- GROWing Up With Rare GENEtic SyndromesRecruitingNCT04463316
- A Pilot Study of an Antioxidant Cocktail vs. Placebo in the Treatment of Children and Adolescents With Rett SyndromeRecruitingNCT04041713Phase 2
- Parent and Infant Inter(X)Action Intervention (PIXI)Enrolling by invitationNCT03836300Not applicable
- An Open-Label Study of Trofinetide for the Treatment of Girls Two to Five Years of Age Who Have Rett SyndromeTerminatedNCT04988867Phase 2/3Results posted
- Open-Label Extension Study of Trofinetide for Rett SyndromeTerminatedNCT04776746Phase 3Results posted
- Open-Label Extension Study of Trofinetide for the Treatment of Girls and Women With Rett SyndromeCompletedNCT04279314Phase 3Results posted
- A Long-term Safety Study of Cannabidiol Oral Solution (GWP42003-P, CBD-OS) in Patients With Rett SyndromeTerminatedNCT04252586Phase 3Results posted
- Study of Trofinetide for the Treatment of Girls and Women With Rett Syndrome (LAVENDER™)CompletedNCT04181723Phase 3Results posted
- Efficacy and Safety of Cannabidiol Oral Solution (GWP42003-P, CBD-OS) in Patients With Rett SyndromeTerminatedNCT03848832Phase 3Results posted
- A Study to Evaluate Ketamine for the Treatment of Rett SyndromeCompletedNCT03633058Phase 2Results posted
- Evaluation of the Efficacy, Safety, and Tolerability of Sarizotan in Rett Syndrome With Respiratory SymptomsTerminatedNCT02790034Phase 2/3Results posted
- Pharmacological Treatment of Rett Syndrome With StatinsCompletedNCT02563860Phase 2Results posted
- Pharmacological Treatment of Rett Syndrome With Glatiramer Acetate (Copaxone)CompletedNCT02153723Phase 2Results posted
- Treatment of Rett Syndrome With Recombinant Human IGF-1CompletedNCT01777542Phase 2Results posted
- Placebo Controlled Trial of Dextromethorphan in Rett SyndromeCompletedNCT01520363Phase 2Results posted
- Treatment of Rett Syndrome With rhIGF-1 (Mecasermin [rDNA]Injection)CompletedNCT01253317Phase 1Results posted
- Trial of Dextromethorphan in Rett SyndromeTerminatedNCT00593957Phase 2Results posted
- Safety and Preliminary Efficacy of TSHA-102 Gene Therapy in Pediatric Females Aged >2 to <4 Years With Rett SyndromeActive, not recruitingNCT07480564Phase 3
- Technology-supported Motor Rehabilitation for People With Rett SyndromeActive, not recruitingNCT07418905Not applicable
- Obi Medical Robot: Evaluating Effectiveness Related to UsabilityActive, not recruitingNCT07151950
- Single-Dose AAV-MECP2 Safety/Tolerability and Efficacy in Rett SyndromeActive, not recruitingNCT06856759Early Phase 1
- To Study the Efficacy & Safety of Oral NA-921 (Bionetide) in Girls and Women with Rett SyndromeCompletedNCT06849973Phase 2/3
- Assessing the Safety and Efficacy of Full-Spectrum Medicinal Cannabis Plant Extract 0.08% THC (NTI164) in the Treatment of Rett Syndrome (RTT)CompletedNCT06621043Phase 1/2
- Validating Innovative Biosensors for Rett Autonomic Symptom TrackingActive, not recruitingNCT06338267
- Assessment of Nutritional and Growth Status in Rett Syndrome PatientsCompletedNCT06335368
- Esketamine for the Treatment of Rett SyndromeCompletedNCT06199700Early Phase 1
- Safety and Efficacy of TSHA-102 in Pediatric Females With Rett Syndrome (REVEAL Pediatric Study)Active, not recruitingNCT06152237Phase 1/2
- Web Intervention for Parents of Youth With Genetic Syndromes (WINGS)Active, not recruitingNCT06139172Not applicable
- Observational Study to Characterize Biomarkers and Disease Progression in Participants With Methyl CpG Binding Protein 2 (MECP2) Duplication SyndromeTerminatedNCT06014541
- A Novel, Regulated Gene Therapy (NGN-401) Study for Females With Rett SyndromeActive, not recruitingNCT05898620Phase 3
- Tolerability of the Immersive Virtual Reality System Grail in Subjects Affected by Rett SyndromeCompletedNCT05691582Not applicable
- Osteopathic Manipulative Treatment for Constipation in People With Rett SyndromeCompletedNCT05687214Not applicable
- Study of VYNT-0126 in the Treatment of Rett Syndrome in Adult PatientsStatus unknownNCT05625568Phase 2
- A Phase 1/2/3 Study of TSHA-102 Gene Therapy in Females With Rett Syndrome (REVEAL Pivotal Study)Active, not recruitingNCT05606614Phase 3
- Intensive Anti-Scoliosis Postural Intervention for Individuals With Rett Syndrome Supported by a Smartphone ApplicationCompletedNCT05488938Not applicable
- Protective Role of Pre-/ Post-biotics on Gut Inflammation, Dysbiosis, and Life Quality in Rett Syndrome (Biotics_RTT)CompletedNCT05420805Not applicable
- The Role of Dietary Calcium for the Treatment of Osteopenia in Girls With Rett SyndromeCompletedNCT05352373Not applicable
- Measuring Impact of Computer Gaming on Arm Use in Rett SyndromeActive, not recruitingNCT05012475Not applicable
- Development of the ORCA Communication Measure for Rett SyndromeCompletedNCT04920110
- ASSESSING EMERALD AND MC10 BIOSTAMP nPOINT BIOSENSORS FOR RETT SYNDROMECompletedNCT04514549
- ANAVEX2-73 Study in Pediatric Patients With Rett SyndromeCompletedNCT04304482Phase 2/3
- Telehealth Support to Increase Physical Activity in Rett SyndromeStatus unknownNCT04167059Not applicable
- Patients With RETT SyndromeCompletedNCT04014985Not applicable
- ANAVEX2-73 Study in Patients With Rett SyndromeCompletedNCT03941444Phase 3
- 'Uptime' Participation Intervention in Girls and Women With Rett SyndromeCompletedNCT03848442Not applicable
- Study of ANAVEX2-73 in Patients With Rett SyndromeCompletedNCT03758924Phase 2
- Early Check: Expanded Screening in NewbornsActive, not recruitingNCT03655223
- The Role of Probiotics PS128 in Movement DisordersStatus unknownNCT03259971Not applicable
- Development of a Behavioral Outcome Measure for Rett Syndrome (RettBe)CompletedNCT03196323
- Open Label Trial of Triheptanoin (UX007) in Treatment of Rett Syndrome.Status unknownNCT03059160Phase 2
- The Findings of MR Imaging in Rett SyndromeStatus unknownNCT02903056
- New Genes Involved in Molecular Etiology of Rett Syndrome Through DNA Microarray Comparative Genomic HybridizationCompletedNCT02885090Not applicable
- Natural History of Rett Syndrome & Related DisordersCompletedNCT02738281
- A Safety Study of NNZ-2566 in Pediatric Rett SyndromeCompletedNCT02715115Phase 2
- Biobanking of Rett Syndrome and Related DisordersCompletedNCT02705677
- Treatment of Mitochondrial Dysfunction in Rett Syndrome With TriheptanoinStatus unknownNCT02696044Phase 2
- Sleep Abnormalities in Rare Genetic Disorders: AS, RTT, and PWCompletedNCT02670694
- An Exploratory Trial of Ketamine for the Treatment of Rett SyndromeTerminatedNCT02562820Phase 1
- Effects of Standing on Non-Ambulatory Children With Neuromuscular ConditionsCompletedNCT02428673Not applicable
- Analysis of the Glutathione Cycle in Children With Rett SyndromeWithdrawnNCT02360436
- An Exploratory Open Label Study of EPI-743 (Vincerinone TM) in Children With Autism Spectrum DisorderWithdrawnNCT02226458Phase 2
- Osteoporosis in RETT SyndromeCompletedNCT02110797Not applicable
- Study to Assess Safety and Efficacy of Fingolimod in Children With Rett SyndromeCompletedNCT02061137Phase 1/2
- An Open Label, Exploratory Study to Investigate the Treatment Effect of Glatiramer Acetate on Girls Woth Rett SyndromeStatus unknownNCT02023424Phase 1
- Phase 2 Study of EPI-743 for Treatment of Rett SyndromeCompletedNCT01822249Phase 2
- A Safety Study of NNZ-2566 in Patients With Rett SyndromeCompletedNCT01703533Phase 2
- Creatine Metabolism in Rett SyndromeCompletedNCT01198015
- Effects of Creatine Supplementation in Rett SyndromeCompletedNCT01147575Not applicable
- Pilot Study of the Effects of the Desipramine on the Neurovegetative Parameters of the Child With Rett SyndromeCompletedNCT00990691Phase 2
- The Role of Family Functioning in Adaptation to Being a Caregiver of an Individual With Rett SyndromeCompletedNCT00891956
- Metabolic Evaluation of Nutrition in Rett SyndromeCompletedNCT00786071
- Functional Abilities in Rett SyndromeCompletedNCT00630422
- Predictors of Caregiver Adaptation to Pervasive Developmental DisordersCompletedNCT00496210
- Advanced Grandparental Age as a Risk Factor for AutismCompletedNCT00464477
- Genetic and Physical Characteristics of Rett SyndromeCompletedNCT00299312
- A Study of the Effectiveness and Safety of Risperidone Versus Placebo in the Treatment of Children With Autistic Disorder and Other Pervasive Developmental Disorders (PDD)CompletedNCT00261508Phase 3
- Independent Studies of Dextromethorphan and of Donepezil Hydrochloride for Rett SyndromeStatus unknownNCT00069550Phase 3
- Study of the Pathogenesis of Rett SyndromeCompletedNCT00004807Not applicable
- Study of Cardiac and Paroxysmal Abnormalities in Rett SyndromeCompletedNCT00004773
- Nutritional Aspects of Rett SyndromeCompletedNCT00004656Not applicable