Hepatolenticular Degeneration: all 80 studies
Page 1 of 1. Open to participants first (31), then studies with results posted, then the rest; newest registration first within each.
- A Study of the Safety and Efficacy of Prime Editing (PM577) in Participants With Wilson Disease (WD)RecruitingNCT07748403Phase 1/2
- Phase I/II Clinical Study to Evaluate the Safety, Tolerability and Efficacy of LY-M003 Injection in Adult Patients With Wilson's DiseaseNot yet recruitingNCT07641140Phase 1/2
- Trientine Tetrahydrochloride Administered Once a Day for the First Line Treatment of Wilson's Disease Patients.RecruitingNCT07465718Phase 3
- Off Treatment Urinary Copper Excretion in Wilson Disease, Pilot StudyRecruitingNCT07301216
- Multifaceted Assessment of Patients With Wilson's Disease in a Low-Resource Setting in Upper Egypt: Service Integration, Psychosocial Burden, Dietary Practices, and the Geo-Spatial Disease MapNot yet recruitingNCT07241832
- A Clinical Study on the Treatment of Wilson Disease With ATP7B mRNA/LNP (DSL101)RecruitingNCT07240896Early Phase 1
- Endocrine Dysfunction in Pediatric Wilson's DiseaseNot yet recruitingNCT07208565
- Phase I/II Clinical Study to Evaluate the Safety, Tolerability, and Efficacy of GC310 Injection in Patients With Wilson's Disease (WD)Not yet recruitingNCT07173933Phase 1/2
- Gene Therapy for Wilson Disease Evaluated by 64Cu PET/CTEnrolling by invitationNCT07159581
- Description of Renal Involvement in Wilson's DiseaseRecruitingNCT07075393
- Wilson's Disease Treated With D-Penicillamine: Characterization of Skin Damage Secondary to Treatment by Measuring Skin ElasticityRecruitingNCT06945081Not applicable
- Daily Versus Alternate Day Plasma Exchange in Wilson Disease With Acute Liver Failure in ChildrenNot yet recruitingNCT06698991Not applicable
- A Clinical Study to Evaluate the Safety and Efficacy of LY-M003 Injection in Patients With Wilson DiseaseRecruitingNCT06650319Early Phase 1
- Institutional Registry of Rare DiseasesRecruitingNCT06573723
- Spanish Wilson Disease RegistryRecruitingNCT06466291
- Circadian Variation of Urinary Copper Excretion in Wilson Disease PatientsRecruitingNCT06430359
- Clinical Value of DWI-ADC Matching in the Short-term Prognosis of Wilson's DiseaseNot yet recruitingNCT06196931
- Evaluation of Cognitive Dysfunction and Psychiatric ComorbiditiesNot yet recruitingNCT06179394
- Early Detection of Cardiac Affection in Patients of Wilson's DiseaseNot yet recruitingNCT06051734
- Clinical Profile and Out Come of Children With Wilson's DiseaseNot yet recruitingNCT05792319
- Cardiac Involvement in Wilson's DiseaseRecruitingNCT05493605Not applicable
- Oral Health and Wilson's Disease: SOMAWIRecruitingNCT05444127
- Gandouling in the Treatment of Wilson's DiseaseRecruitingNCT05305872Phase 4
- International Wilson's Disease Patient Registry (iWilson Registry)RecruitingNCT05239858
- French Wilson Disease RegistryRecruitingNCT05231876
- Description of the Copper Concentration in Breast Milk in Women Treated for Wilson's DiseaseRecruitingNCT05183165Not applicable
- Role for Biochemical Assays and Kayser-Fleischer Rings in Diagnosis of Wilson DiseaseRecruitingNCT04965545
- Longitudinal Study of Ultra-rare Inherited Metabolic and Degenerative Neurological Diseases.RecruitingNCT04880356
- A Registered Cohort Study on Wilson's DiseaseRecruitingNCT04012658
- Natural History of Wilson DiseaseRecruitingNCT03334292
- China Registry for Genetic / Metabolic Liver DiseasesRecruitingNCT03131427
- Study Comparing Once Daily Dose of 900mg of TETA 4HCL Against Cuprior® (450mg Trientine Base, Twice Daily).CompletedNCT06128954Phase 1Results posted
- Pharmacokinetic Study of Oral ALXN1840 in Japanese and Non-Japanese Adult Healthy ParticipantsCompletedNCT05641311Phase 1Results posted
- Study of ALXN1840 Versus Standard of Care in Pediatric Participants With Wilson DiseaseTerminatedNCT05047523Phase 3Results posted
- Copper and Molybdenum Balance in Participants With Wilson Disease Treated With ALXN1840CompletedNCT04573309Phase 2Results posted
- A Study of the Cardiac Effects of ALXN1840 in Healthy AdultsCompletedNCT04560816Phase 1Results posted
- A Phase I/II Study of VTX-801 in Adult Patients With Wilson's DiseaseActive, not recruitingNCT04537377Phase 1/2Results posted
- Study of ALXN1840 on the Metabolism of a CYP2B6 Substrate in Healthy ParticipantsCompletedNCT04526210Phase 1Results posted
- Phase 1 Study of ALXN1840 on the Metabolism of a CYP2C9 Substrate in Healthy Participants.CompletedNCT04526197Phase 1Results posted
- Copper Concentration & Histopathologic Changes in Liver Biopsy in Participants With Wilson Disease Treated With ALXN1840CompletedNCT04422431Phase 2Results posted
- Trientine Tetrahydrochloride (TETA 4HCL) for the Treatment of Wilson's DiseaseCompletedNCT03539952Phase 3Results posted
- Efficacy and Safety of ALXN1840 Administered for 48 Weeks Versus Standard of Care in Participants With Wilson DiseaseTerminatedNCT03403205Phase 3Results posted
- The Assessment of Copper Parameters in Wilson Disease Participants on Standard of Care TreatmentCompletedNCT02763215Results posted
- Efficacy and Safety Study of WTX101 (ALXN1840) in Adult Wilson Disease PatientsCompletedNCT02273596Phase 2Results posted
- Single Daily Dosage of Trientine for Maintenance Treatment for Wilson DiseaseCompletedNCT01472874Not applicableResults posted
- Efficacy and Safety, Long-term Study of Zinc Acetate to Treat Wilson's Disease in Japan.CompletedNCT00212355Phase 3Results posted
- Subclinical Myocardial Dysfunction in Children With Wilson's DiseaseActive, not recruitingNCT07765472
- Exchangeable and Relative Exchangeable Copper as an Alternative to 24-Hour Urinary Copper in Wilson's Disease MonitoringCompletedNCT07462026
- Prescreening Study to Identify Potential Wilson Disease Participants for Gene-Editing Clinical TrialActive, not recruitingNCT07226622
- The Exploratory Handheld Optical Coherence Tomography Study in Wilson's DiseaseCompletedNCT07046507Not applicable
- Patient Preference Study: Standard of Care Versus Once-daily Trientine TetrahydrochlorideCompletedNCT07010575Phase 2
- The Clinical Study of Botulinum Toxin Type A Injection in the Treatment of Wilson DiseaseCompletedNCT06762509
- An Exploratory Study to Evaluate the Tolerability and Safety of MWAV201 in Subjects With Wilson DiseaseActive, not recruitingNCT06663878Not applicable
- Performance and Safety of MEX-CD1 Low-volume Continuous Veno-venous Haemodialysis Medical Device for Copper-extraction in Patients With Wilson's DiseaseTerminatedNCT05917327Not applicable
- Real World Evidence Study in Subjects With Wilson's DiseaseCompletedNCT05783687
- Baby Detect : Genomic Newborn ScreeningCompletedNCT05687474
- Early Access Program for ALXN1840 in Patients With Wilson DiseaseNo longer availableNCT05686564
- Impact of the Lockdown Due to the COVID Pandemic in French Wilson's Disease PatientsTerminatedNCT05004701
- Clinical Features and Outcome of Wilson's Disease With Generalized Epilepsy in Chinese PatientsCompletedNCT04965571
- rTMS in Wilson Disease DysarthriaCompletedNCT04910581Not applicable
- Adeno-Associated Virus (AAV) Antibody Study in Subjects OTC Deficiency, GSDIa, and Wilson DiseaseTerminatedNCT04909346
- A Phase 1/2/3 Study of UX701 Gene Therapy in Adults With Wilson DiseaseActive, not recruitingNCT04884815Phase 1/2
- Clinical Evaluation and Assessment of Instruments and Biomarkers in Subjects With Wilson DiseaseCompletedNCT04531189
- Study of Retinal Vascular Parameters in Patients With Wilson's DiseaseCompletedNCT04408300Not applicable
- Cohort Research on Wilson's DiseaseStatus unknownNCT04212195
- The Individual Therapy for Patients With Wilson's DiseaseStatus unknownNCT03957720Early Phase 1
- Establishment of Human Cellular Disease Models for Wilson DiseaseCompletedNCT03867526
- A Controlled Study of Potential Therapeutic Effect of Oral Zinc in Manifesting Carriers of Wilson DiseaseStatus unknownNCT03659331Not applicable
- Early Check: Expanded Screening in NewbornsActive, not recruitingNCT03655223
- Plasma Exchange and Continuous Hemodiafiltration in Treatment of Wilson's Disease-related Liver FailureStatus unknownNCT03589820Not applicable
- A Retrospective Study to Assess the Clinical Efficacy and Safety of Trientine in Wilson's Disease PatientsCompletedNCT03299829
- sCD163 and sMR in Wilsons Disease - Associations With Disease Severity and FibrosisCompletedNCT02702765Not applicable
- WILSTIM - DBS (WILson STIMulation - Deep Brain Stimulation)CompletedNCT02552628Not applicable
- Study to Assess Long-Term Outcomes of Trientine in Wilson Disease Patients Withdrawn From Therapy With d-PenicillamineStatus unknownNCT02426905Phase 4
- ExAblate Transcranial MRgFUS for the Management of Treatment-Refractory Movement DisordersActive, not recruitingNCT02252380Not applicable
- Inhibitory rTMS in Dystonic Wilson PatientsCompletedNCT01980433Not applicable
- A Phase 1 Study to Assess the Effects in the Body of a Single Dose of Trientine Dihydrochloride in Wilson's Disease PatientsCompletedNCT01874028Phase 1
- Efficacy of Invitro Expanded Bone Marrow Derived Allogeneic Mesenchymal Stem Cell Transplantation Via Portal Vein or Hepatic Artery or Peripheral Vein in Patients With Wilson CirrhosisCompletedNCT01378182Not applicable
- Study of Tetrathiomolybdate in Patients With Wilson DiseaseCompletedNCT00004339Phase 3
- Study of Zinc for Wilson DiseaseCompletedNCT00004338Phase 4