Aniridia clinical trials
The registry lists 23 studies for Aniridia across 8 countries. 8 are recruiting or about to start. 12 of them are mainly about Aniridia (how this is decided). Per ClinicalTrials.gov, last updated 2026-11-06.
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Who runs them
National Eye Institute (NEI) (3) · PTC Therapeutics (2) · University of Minnesota (2) · Fondation Ophtalmologique Adolphe de Rothschild (1) · Assistance Publique - Hôpitaux de Paris (1) · IRCCS Ospedale San Raffaele (1) · Implandata Ophthalmic Products GmbH (1) · University of California, Los Angeles (1)
Who these studies take
Of the 7 Aniridia studies recruiting now, 6 (86%) set no upper age limit and 0 (0%) stop at 75 or younger. 6 (86%) take children under 18. 0 (0%) are for women only and 0 (0%) for men only; 1 (14%) take healthy volunteers.
| Age | Women | Men |
|---|---|---|
| 10 | 6 (86%) | 6 (86%) |
| 18 | 7 (100%) | 7 (100%) |
| 30 | 7 (100%) | 7 (100%) |
| 40 | 7 (100%) | 7 (100%) |
| 50 | 7 (100%) | 7 (100%) |
| 65 | 7 (100%) | 7 (100%) |
| 75 | 7 (100%) | 7 (100%) |
| 85 | 7 (100%) | 7 (100%) |
Across all 23 studies, recruiting or not: 0% stop at 75 or younger and 0% at 65; 61% take children; 0% are for women only and 0% for men only; 22% take healthy volunteers. From each study’s registry entry; the criteria on its page decide.
Studies
Recruiting first, then most recently updated. Showing 23 of 23. search them.
- National Ophthalmic Genotyping and Phenotyping Network (eyeGENE (Registered Trademark)), Stage 3 - Expansion of DNA and Data Repositories for Rare Inherited Ophthalmic DiseasesRecruitingNCT064916151 country
- Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at SanfordRecruitingNCT017931681 country
- National Cohort on Congenital Defects of the EyeRecruitingNCT059544031 country
- Congenital Aniridia Patient QuestionnaireRecruitingNCT053908011 country
- Modeling Ocular Developmental Diseases From 3D Cultures of Optic Vesicle Organoids Derived From hiPSCs of Patients With Ocular MalformationsRecruitingNCT064087011 country
- Comparison of the Healing Properties on Corneal Cells of Groth Factor-enriched Plasma and Autologous Serum From Aniridia PatientsRecruitingNCT054005901 country
- Validation of Human Drugs Target of Repurposed Drugs and Novel TherapiesNot yet recruitingNCT06412718
- Safety and Effectiveness of the CustomFlex Artificial Iris Prosthesis for the Treatment of Iris DefectsRecruitingNCT01860612Not applicable1 country
- Cultivated Stem Cell Transplantation for the Treatment of Limbal Stem Cell DeficiencyCompletedNCT00845117Not applicable1 country
- Treatment of LSCD With DMCompletedNCT05909735Phase 11 country
- Ultrahigh-resolution Optical Coherence Tomography Imaging of the Anterior Eye Segment StructuresCompletedNCT03461978Not applicable1 country
- RAFT - Clinical Trial of RAFT for Aniridia Related KeratopathyCompletedNCT05044598Phase 1/21 country
- Safety and Performance Study of the ARGOS-IO System in Patients Undergoing Boston Keratoprosthesis ImplantationCompletedNCT02945176Not applicable1 country
- Proteomic Study of Tears From Patients With a PAX6 MutationCompletedNCT05562115Not applicable1 country
- Study of Ataluren in Participants With Nonsense Mutation AniridiaCompletedNCT02647359Phase 22 countries
- Clinical Evaluation of Morcher Artificial Iris DiaphragmsCompletedNCT00812708Not applicable1 country
- Genetics of Wilms' Tumor and/or the Associated Conditions of Aniridia, Hemihypertrophy, and Genitourinary AnomaliesStatus unknownNCT005038931 country
- Characterization of WAGR Syndrome and Other Chromosome 11 Gene DeletionsCompletedNCT007581081 country
- Positive Angle KappaCompletedNCT016445521 country
- A Phase 2 Open Label Extension Study in Participants With Nonsense Mutation AniridiaWithdrawnNCT04117880Phase 2
- Clinical Outcomes of Implantationof Black Diaphragm Intraocular Lens in Complete Aniridia and Aphakia Due to Posttraumatic Eye RuptureCompletedNCT035818641 country
- Correlation of Gene Abnormalities and Clinical Manifestations of AniridiaCompletedNCT002655901 country
- Abnormalities of the Eye's Anterior Chamber, Iris, Cornea and LensCompletedNCT000011611 country