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RecruitingNCT07604974Updated Sep 3, 2026

A Study to Assess the Safety, Tolerability and Efficacy of ION775

A Phase 2 interventional study of ION775 in Hypertriglyceridemia and Severe Hypertriglyceridemia, sponsored by Ionis Pharmaceuticals, Inc.. Recruiting at 17 sites in 2 countries. Open to participants aged 18 Years and older. Per ClinicalTrials.gov, last updated 2026-09-03.

Sponsored by Ionis Pharmaceuticals, Inc. · Phase 2, Interventional, and Treatment

Phase
Phase 2
Study type
Interventional
Enrollment
72
Allocation
Randomized
Ages
18 Years and older
Sex
All
01

Study summary

The main objective of this study is to evaluate the effect of ION775 on fasting triglyceride (TG) levels in participants with hypertriglyceridemia (HTG) and severe hypertriglyceridemia (sHTG).

Read the detailed description

This is an open-label, parallel-dose study consisting of a 4-6 week screening period, a 6-month treatment period and a 6-month post-treatment follow-up period.

02

Conditions studied

  • Hypertriglyceridemia
  • Severe Hypertriglyceridemia

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03

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All
Accepts healthy volunteers
No

Eligibility criteria

Key Inclusion Criteria:

  1. Adult males and females with HTG (fasting TG more than or equal to (≥) 350 milligrams per deciliter (mg/dL) [3.95 millimoles per liter (mmol/L)] or with sHTG (fasting TG ≥ 500 mg/dL [5.65 mmol/L]).
  2. Participants should be on standard of care lipid-lowering medications per local guidelines.

Key Exclusion Criteria:

  1. Hemoglobin A1c (HbA1c) ≥ 8.5% at Screening.
  2. Alanine aminotransferase or aspartate aminotransferase > 2.0 × upper limit of normal.
  3. Total bilirubin > 1.5 upper limit of normal unless due to Gilbert's syndrome.
  4. Estimated GFR \< 30 mL/min/1.73 m\^2.

Note: Other protocol pre-specified inclusion/exclusion criteria may apply.

04

Study design

Phase
Phase 2
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Parallel assignment
Masking
None (open label)
Enrollment
72 participants (estimated)

Study arms

  • Experimental
    ION775: Cohot A

    Participants will be randomized to receive ION775 by subcutaneous (SC) injection.

    Drug: ION775

  • Experimental
    ION775: Cohot B

    Participants will be randomized to receive ION775 by SC injection.

    Drug: ION775

  • Experimental
    ION775: Cohot C

    Participants will be randomized to receive ION775 by SC injection.

    Drug: ION775

Interventions

  • DrugION775

    ION775 will be administered by SC injection.

05

What researchers measure

Primary outcomes

  1. Percent Change From Baseline in Fasting Triglyceride (TG)

    Time frame: Baseline, Month 6

Secondary outcomes

  1. Number of Participants With at Least One Treatment-Emergent Adverse Events (TEAEs)

    Time frame: Up to 12 Months

  2. Number of Participants who Experience Abnormalities in Clinical Laboratory Evaluations

    Time frame: Up to 12 Months

  3. Percent Change From Baseline in Fasting Apolipoprotein C-III (apoC-III)

    Time frame: Baseline, Month 6

  4. Percent Change From Baseline in Very Low-Density Lipoprotein Cholesterol (VLDL-C)

    Time frame: Baseline, Month 6

  5. Percent Change From Baseline in Remnant Cholesterol When Directly Measured

    Time frame: Baseline, Month 6

  6. Percent Change From Baseline in Non-High-Density Lipoprotein Cholesterol (non-HDL-C)

    Time frame: Baseline, Month 6

06

Study locations

17 of 17 sites recruiting
  • Ionis Investigative Site
    Lincoln, California 95648, United States
    Recruiting
  • Ionis Investigative Site
    Aurora, Colorado 80045, United States
    Recruiting
  • Ionis Investigative Site
    Boca Raton, Florida 33434, United States
    Recruiting
  • Ionis Investigative Site
    Miami, Florida 33184, United States
    Recruiting
  • Ionis Investigative Site
    Miramar, Florida 33027, United States
    Recruiting
  • Ionis Investigative Site
    Columbus, Georgia 31904, United States
    Recruiting
  • Ionis Investigative Site
    Carmel, Indiana 46290, United States
    Recruiting
  • Ionis Investigative Site
    Louisville, Kentucky 40213, United States
    Recruiting
  • Ionis Investigative Site
    Flint, Michigan 48504, United States
    Recruiting
  • Ionis Investigative Site
    Munroe Falls, Ohio 44262, United States
    Recruiting
  • Ionis Investigative Site
    Little River, South Carolina 29566, United States
    Recruiting
  • Ionis Investigative Site
    Houston, Texas 77040, United States
    Recruiting
  • Ionis Investigative Site
    Lampasas, Texas 76550, United States
    Recruiting
  • Ionis Investigative Site
    McKinney, Texas 75071, United States
    Recruiting
  • Ionis Investigative Site
    Mesquite, Texas 75071, United States
    Recruiting
  • Ionis Investigative Site
    San Antonio, Texas 78209, United States
    Recruiting
  • Ionis Investigative Site
    Québec, G1V 4W2, Canada
    Recruiting
07

References and documents

Individual participant data

Plan to share: Yes — Ionis may share anonymized individual participant data, aggregated clinical data, and other types of data that support the results in this study. Data requests from qualified researchers will be considered once all three of the following criteria are met: (1) 12 months from marketing approval of the study drug in both the United States and European Union; (2) 18 months from conclusion of the study; and (3) 6 months from publication of study article. Access would be via a secure environment and is contingent upon approval of a research proposal and entry into an appropriate data use agreement. Requests to access data can be submitted via the website https://vivli.org/ourmember/ionis/.

No publications or documents are linked to this record.

08

Registry details

Key details

Study ID
NCT07604974
Lead sponsor
Ionis Pharmaceuticals, Inc.
Responsible party
Sponsor
First posted
May 22, 2026
Start date
May 12, 2026
Primary completion
Sep 2027 (estimated)
Completion
Mar 2028 (estimated)
Last update
Sep 3, 2026

Study contacts

Ionis Pharmaceuticals, Inc.
Contact
IonisION775-CS2@clinicaltrialmedia.com
1-844-828-3770

Oversight

Data monitoring committee
Yes
FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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