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RecruitingNCT04789148Updated Jul 23, 2026

Effects of Intranasal Oxytocin in Patients With Arginine-vasopressin Deficiency

A Phase 1 interventional study of Intranasal Oxytocin (IN-OXT) and Intranasal Oxytocin (IN-OXT) in Vasopressin Deficiency, sponsored by Elizabeth Austen Lawson. Recruiting at 1 site in United States. Open to participants aged 18 Years and older. Per ClinicalTrials.gov, last updated 2026-07-23.

Sponsored by Elizabeth Austen Lawson · Phase 1, Interventional, and Basic science

Phase
Phase 1
Study type
Interventional
Enrollment
40
Allocation
Randomized
Ages
18 Years and older
Sex
All
01

Study summary

This is a randomized, double-blind, placebo-controlled crossover pilot study of single-dose intranasal oxytocin (6 IU and 24 IU) vs. placebo in adult men and women (aged 18 years and above) with arginine-vasopressin deficiency to evaluate the effect of oxytocin on anxiety, depression, and socioemotional functioning (Part A), with an optional randomized, double-blind, placebo-controlled 2-week repeated dose substudy of intranasal oxytocin 6 IU or placebo (Part B).

Following a screening visit to determine eligibility, participants will return for three main study visits in Part A. During the main study visits, study participants will receive either oxytocin or placebo, followed by assessments of emotional behavior.

In Part A, thirty participants will be equally randomized to one of six possible groups:

  1. 6 IU oxytocin - 24 IU oxytocin - placebo
  2. 6 IU oxytocin - placebo - 24 IU oxytocin
  3. 24 IU oxytocin - 6 IU oxytocin - placebo
  4. 24 IU oxytocin - placebo - 6 IU oxytocin
  5. placebo - 6 IU oxytocin - 24 IU oxytocin
  6. placebo - 24 IU oxytocin - 6 IU oxytocin

Following completion of the Part A crossover portion of the study, in Part B participants may also choose to continue participation in an optional, randomized, double-blind, placebo-controlled substudy of intranasal oxytocin 6 IU or placebo three times a day for two weeks, followed by assessments of emotional behavior.

02

Conditions studied

  • Vasopressin Deficiency

Keywords

  • Hypopituitarism
  • posterior pituitary
  • oxytocin
  • psychopathology
  • anxiety
  • depressive symptoms
  • socioemotional functioning
03

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  • Age 18 and above
  • Arginine-vasopressin deficiency
  • Normal FT4 or T4
  • Normal serum/plasma sodium
  • Stable hormone replacement

Exclusion criteria

Exclusion Criteria:

  • Active substance use disorder within the last 6 months
  • History of psychosis
  • Suicidal behavior and/or active suicidal ideation with plan and/or intent, e.g., suicidal ideation of type 4 or type 5 as assessed by the Columbia Suicide Severity Rating Scale (C-SSRS), in the last month
  • Medication changes within 4 weeks of enrollment or planned medication changes during the study
  • History of chronic nasal obstruction or local pathology in nostril pathway which, in the opinion of the investigator, would prevent appropriate nasal administration of the study drug.
  • History of cardiac disease, including arrhythmias, coronary heart disease, coronary artery spasms, valvular heart disease, hypertrophic cardiomyopathy (hypertension is not exclusionary)
  • History of chronic kidney disease stage III and above
  • History of liver cirrhosis
  • Pregnancy or breastfeeding within the last 8 weeks
  • Unwilling to use a medically acceptable form of contraception throughout the study period (female of child-bearing potential only)
  • Any significant illness, condition, drug or medical device that the Investigator determines could interfere with study participation, data collection, or safety
04

Study design

Phase
Phase 1
Primary purpose
Basic science
Allocation
Randomized
Intervention model
Crossover assignment
Masking
Quadruple (Participant, Care provider, Investigator, Outcomes assessor)
Enrollment
40 participants (estimated)

Study arms

  • Experimental
    Part A Arm 1

    Main visit 1: 6 IU intranasal oxytocin; Main visit 2: 24 IU intranasal oxytocin; Main visit 3: intranasal placebo

    Drug: Intranasal Oxytocin (IN-OXT) · Drug: Placebo

  • Experimental
    Part A Arm 2

    Main visit 1: 6 IU intranasal oxytocin; Main visit 2: intranasal placebo; Main visit 3: 24 IU intranasal oxytocin

    Drug: Intranasal Oxytocin (IN-OXT) · Drug: Placebo

  • Experimental
    Part A Arm 3

    Main visit 1: 24 IU intranasal oxytocin; Main visit 2: 6 IU intranasal oxytocin; Main visit 3: intranasal placebo

    Drug: Intranasal Oxytocin (IN-OXT) · Drug: Placebo

  • Experimental
    Part A Arm 4

    Main visit 1: 24 IU intranasal oxytocin; Main visit 2: intranasal placebo; Main visit 3: 6 IU intranasal oxytocin

    Drug: Intranasal Oxytocin (IN-OXT) · Drug: Placebo

  • Experimental
    Part A Arm 5

    Main visit 1: intranasal placebo; Main visit 2: 6 IU intranasal oxytocin; Main visit 3: 24 IU intranasal oxytocin

    Drug: Intranasal Oxytocin (IN-OXT) · Drug: Placebo

  • Experimental
    Part A Arm 6

    Main visit 1: intranasal placebo; Main visit 2: 24 IU intranasal oxytocin; Main visit 3: 6 IU intranasal oxytocin

    Drug: Intranasal Oxytocin (IN-OXT) · Drug: Placebo

  • Active comparator
    Part B Arm 1

    Intranasal oxytocin 6 IU three times a day for 14 days

    Drug: Intranasal Oxytocin (IN-OXT)

  • Experimental
    Part B Arm 2

    Intranasal placebo three times a day for 14 days

    Drug: Placebo

Interventions

  • DrugIntranasal Oxytocin (IN-OXT)

    6 IU single dose

  • DrugIntranasal Oxytocin (IN-OXT)

    IN-OXT 6 IU three times a day for 2 weeks

  • DrugPlacebo

    Intranasal placebo three times a day for 2 weeks

  • DrugIntranasal Oxytocin (IN-OXT)

    24 IU single dose

  • DrugPlacebo

    placebo single dose

05

What researchers measure

Primary outcomes

  1. Dot-probe task - anxious behavior between low dose oxytocin and placebo

    Difference in response times (in milliseconds) to dots appearing in the location of the previously shown negative versus the neutral face between 6 IU oxytocin vs placebo in the dot-probe task.

    Time frame: 20 minutes following intervention at each main visit

Secondary outcomes

  1. Dot-probe task - anxious behavior between all three interventions

    Difference in response time (in milliseconds) to dots appearing in the location of the previously shown negative versus neutral face between 6 IU oxytocin, 24 IU oxytocin, and placebo in the dot-probe task.

    Time frame: 20 minutes following intervention

  2. Depressive behavior - probabilistic reward task between all three interventions

    Response bias developed toward the more frequently reinforced alternative between 6 IU oxytocin, 24 IU oxytocin, and placebo in the probabilistic reward task.

    Time frame: 30 minutes following intervention at each main visit

  3. Socioemotional functioning - Emotion recognition task between all three interventions

    Accuracy in identifying correct emotion between 6 IU oxytocin, 24 IU oxytocin, and placebo in the emotion recognition task.

    Time frame: 40 minutes following intervention at each main visit

06

Study locations

1 of 1 sites recruiting
  • Massachusetts General Hospital, Neuroendocrine Unit
    Boston, Massachusetts 02114, United States
    Recruiting
07

References and documents

Individual participant data

Plan to share: No

No publications or documents are linked to this record.

08

Registry details

Key details

Study ID
NCT04789148
Lead sponsor
Elizabeth Austen Lawson
Collaborators
Tonix Pharmaceuticals, Inc.
Responsible party
Elizabeth Austen Lawson (Associate Professor of Medicine, Harvard Medical School; Director, Interdisciplinary Oxytocin Research Program, Neuroendocrine Unit, Massachusetts General Hospital, Massachusetts General Hospital) — Sponsor-investigator
First posted
Mar 9, 2021
Start date
Sep 10, 2025
Primary completion
Jun 2027 (estimated)
Completion
Jun 2027 (estimated)
Last update
Jul 23, 2026

Study contacts

Francesca Galbiati, MD
Contact
FGALBIATI@BWH.HARVARD.EDU
(617) 726-3870
Elisa Asanza, MSN, MPH
Contact
easanza@mgh.harvard.edu
617-726-3870
Elizabeth A Lawson, MD, MMSc
principal investigator · Massachusetts General Hospital

Oversight

Data monitoring committee
No
FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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