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RecruitingNCT04512638BETCONUpdated May 23, 2023

Best Treatment Choice for Osteonecrosis of the Jaw

A Phase 4 interventional study of Antibiotics and Chlorhexidine mouthwash in Medication Related Osteonecrosis of the Jaw, sponsored by Tim Van den Wyngaert. Recruiting at 4 sites in Belgium. Open to participants aged 18 Years and older. Per ClinicalTrials.gov, last updated 2023-05-23.

Sponsored by Tim Van den Wyngaert · Phase 4, Interventional, and Treatment

Phase
Phase 4
Study type
Interventional
Enrollment
125
Allocation
Randomized
Ages
18 Years and older
Sex
All
01

Study summary

BETCON is a pragmatic randomized controlled open-label multi-center study in patients with newly diagnosed stage I-II MRONJ designed to answer the question whether minimally invasive management with LPRF membranes or primary surgical treatment is better than the standard of care of conservative therapy alone. The primary end-point is the time to mucosal healing. Secondary end-points consist of supporting measures of efficacy, patient reported symptoms, quality of life, well-being, and functioning.

Read the detailed description

While effective for symptom control and well tolerated, conservative treatment of MRONJ yields highly variable mucosal healing rates ranging between 20 to 50%. In an effort to improve these suboptimal outcomes, many adjunct treatment modalities have been studied, of which the use of minimally invasive surgery with autologous platelet rich plasma (LPRF) to improve wound healing has attracted considerable attention, with reported mucosal closure rates of up to 86% in single arm case series. More recently, improved understanding of the need for pre-operative infection control and adaptation of surgical protocols has renewed the interest in the primary surgical treatment of MRONJ with mucosal closure achieved in up to 90% of patients in some case series.

Therapeutic studies of MRONJ have almost exclusively focused on mucosal healing as the desired end-point of MRONJ treatment, with little or no attention to patient symptoms, quality of life, functioning and well-being during treatment, even though the resolution of MRONJ symptoms and limiting treatment related adverse events may be equally important to patients.

This comparative effectiveness research (CER) study is a randomized controlled open-label multi-center study in patients with newly diagnosed stage I-II MRONJ and is designed to answer the question whether minimally invasive treatment with LPRF membranes or primary surgical treatment improves outcomes when added to the standard of care of conservative treatment alone. The study also incorporates pragmatic design elements and uses patient reported outcomes (PRO) to determine which treatment offers the best humanistic outcomes considering both efficacy and measures of quality of life, functioning, well-being and symptom control. Indeed, this study will not use an investigational new drug (or drug regimen), device, or surgical technique, but rather evaluate their relative efficacy to guide future clinical management. Finally, plasma and saliva will be collected to identify prognostic and predictive biomarkers of outcome.

02

Conditions studied

  • Medication Related Osteonecrosis of the Jaw

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03

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  • >18 years of age
  • Provision of signed informed consent
  • A history of at least one administration of, or an ongoing treatment with, a bone modifying agent in dose registered for the prevention of skeletal related events in bone metastatic disease or multiple myeloma
  • Diagnosis of stage I-II MRONJ according to AAOMS 2014 criteria not more than 8 weeks prior to the date of screening

Exclusion criteria

Exclusion criteria:

  • Any prior treatment for MRONJ other than local antiseptic rinses, systemic antibiotics, or analgesics
  • Prior radiotherapy to the head and neck region
  • Medical contraindication to receive any of the possible study treatments
  • Stage III MRONJ characterized by very extensive bone necrosis, pathological fracture, or fistulas to the skin or sinuses
  • Multiple MRONJ lesions that cannot be closed in a single surgical procedure
04

Study design

Phase
Phase 4
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Parallel assignment
Masking
None (open label)
Enrollment
125 participants (estimated)

Study arms

  • Active comparator
    Conservative treatment

    Amoxicillin-based antibiotics and chlorhexidine oral rinse. Minor debridement. Primary wound closure is not part of this treatment strategy.

    Drug: Antibiotics · Drug: Chlorhexidine mouthwash

  • Experimental
    Minimally invasive approach + LPRF

    Amoxicillin-based antibiotics and chlorhexidine oral rinse. Minimally-invasive surgical treatment, including sequestrectomy, debridement of soft tissue, and application of LPRF membranes before tension-free wound closure is obtained. Marginal resection of all necrotic bone is not part of this treatment strategy.

    Drug: Antibiotics · Drug: Chlorhexidine mouthwash · Procedure: Minimally invasive surgery with LPRF

  • Experimental
    Primary surgical management

    Amoxicillin-based antibiotics and chlorhexidine oral rinse. Removal of the necrotic bone without excessive resection of healthy bone. Buccal mucoperiosteal flaps will be used to achieve a tension-free mucosal coverage.

    Drug: Antibiotics · Drug: Chlorhexidine mouthwash · Procedure: Surgical resection

Interventions

  • DrugAntibiotics

    Antibiotic treatment is the same in all groups. Monotherapy for 4 weeks with: No penicillin contra-indication * Amoxicillin-clavulanate 875mg tid PO Penicillin contra-indication or intolerance * Clindamycin 300mg tid PO After 4 weeks patients will be switched to consolidation antibiotics: No penicillin contra-indication * Amoxicillin 1g bid PO Penicillin contra-indication or intolerance * Clindamycin 300mg tid PO Antibiotic treatment can be discontinued after 4 weeks when the MRONJ lesions has healed.

    Also known as: amoxicillin

  • DrugChlorhexidine mouthwash

    Patients in all treatment groups will be prescribed aqueous chlorhexidine 0.12% tid rinse for 2 weeks, with subsequent switch to 0.05% for the duration of the study or until healing of the MRONJ lesion has occurred.

    Also known as: chlorhexidine

  • ProcedureMinimally invasive surgery with LPRF

    Minimally-invasive surgical treatment, including sequestrectomy, debridement of soft tissue, and application of LPRF membranes before tension-free wound closure is obtained. Marginal resection of all necrotic bone is not part of this treatment strategy.

  • ProcedureSurgical resection

    Primary surgical management consisting of the removal of the necrotic bone without excessive resection of healthy bone. Buccal mucoperiosteal flaps will be used to achieve a tension-free mucosal coverage.

05

What researchers measure

Primary outcomes

  1. Time to confirmed mucosal healing

    Time after randomization until the observation of healed mucosa (without presence of surgical suturing material) at the site of MRONJ, with a first observation of healed mucosa requiring confirmation after 4 weeks.

    Time frame: 12 months

Secondary outcomes

  1. Mucosal closure

    Proportion of patients with mucosal closure 6 months after randomization

    Time frame: 6 months

  2. Time to MRONJ healing

    Time to resolution of MRONJ symptoms after start of treatment

    Time frame: 12 months

  3. Relapse rate of MRONJ

    Incidence of patients with relapse at the site of MRONJ

    Time frame: 12 months

  4. Antibiotics use

    Total duration of exposure to antimicrobial agents

    Time frame: 12 months

  5. Evolution of cancer health-related quality-of-life

    Changes over time as measured with the EORTC QLQ-C30 questionnaire.

    Time frame: 12 months

  6. Evolution of general health status

    Changes over time as measured with the EUROQOL 5D (EQ-5D-5L) questionnaire.

    Time frame: 12 months

  7. Evolution of oral health-specific quality-of-life

    Changes over time as measured with the Oral Health Impacts Profile (OHIP-14) and the SWOG0702 Oral Health and Oral Health-related Quality of Life questionnaires.

    Time frame: 12 months

Other outcomes

  1. Treatment related adverse events

    Incidence and intensity of treatment emergent adverse events

    Time frame: Through study completion, an average of 1 year

  2. Quality-adjusted Time Without Symptoms and Toxicity (Q-TWiST)

    This analysis analysis considers three health states: toxicity, time without symptoms and toxicity (TWiST), and relapse. The toxicity state comprises the total time after randomization and before relapse of MRONJ symptoms spent with toxicity, regardless of when the toxicity started or gaps between toxicities. The TWiST state is defined as the time of relapse of MRONJ symptoms minus time with toxicities. The duration of the relapse state is defined as overall survival time minus time to relapse of MRONJ symptoms.

    Time frame: Through study completion, an average of 1 year

06

Study locations

4 of 4 sites recruiting
  • ZNA Middelheim
    Antwerp, 2020, Belgium
    • Olivier Lenssen, MD, DDS · Contact
    Recruiting
  • Antwerp University Hospital
    Edegem, 2650, Belgium
    • Tim Van den Wyngaert, MD, PhD · Contact
    Recruiting
  • UZ Leuven
    Leuven, 3000, Belgium
    • Constantinus Politis, MD, DDS, PhD · Contact
    Recruiting
  • AZ Nikolaas
    Sint Niklaas, 9100, Belgium
    • Vincent Lenaerts, MD, DDS · Contact
    Recruiting
07

References and documents

Publications

  • Beth-Tasdogan NH, Mayer B, Hussein H, Zolk O, Peter JU. Interventions for managing medication-related osteonecrosis of the jaw. Cochrane Database Syst Rev. 2022 Jul 12;7(7):CD012432. doi: 10.1002/14651858.CD012432.pub3. PubMed 35866376 ↗

Related links

Individual participant data

Plan to share: No

08

Registry details

Key details

Study ID
NCT04512638
Lead sponsor
Tim Van den Wyngaert
Collaborators
Kom Op Tegen Kanker
Responsible party
Tim Van den Wyngaert (Principal Investigator, University Hospital, Antwerp) — Sponsor-investigator
First posted
Aug 13, 2020
Start date
Jan 1, 2021
Primary completion
Oct 1, 2025 (estimated)
Completion
Jan 1, 2026 (estimated)
Last update
May 23, 2023

Study contacts

Tim Van den Wyngaert, MD, PhD
Contact
tim.van.den.wyngaert@uza.be
003238213568
Tim Van den Wyngaert, MD, PhD
principal investigator · University Hospital, Antwerp

Oversight

Data monitoring committee
No
FDA-regulated drug
No
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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