CClinicalTrials.gg
CompletedNCT03442673MOCCCAUpdated Mar 28, 2025

Chemotherapy and G-CSF for Mobilization

A Phase 2 interventional study of Vinorelbine and Gemcitabine in Multiple Myeloma, sponsored by Insel Gruppe AG, University Hospital Bern. Completed at 1 site in Switzerland. Open to participants aged 18 Years and older. Per ClinicalTrials.gov, last updated 2025-03-28.

Sponsored by Insel Gruppe AG, University Hospital Bern · Phase 2, Interventional, and Treatment

Phase
Phase 2
Study type
Interventional
Enrollment
137
Allocation
Randomized
Ages
18 Years and older
Sex
All
01

Study summary

This study aims to demonstrate that the mobilization with cytokine stimulation with G-CSF alone is non-inferior as compared to the standard mobilization with chemotherapy and G-CSF while associated with fewer side effects in myeloma patients.

Read the detailed description

Background and Rationale High-dose chemotherapy (HDCT) with melphalan and autologous stem cell transplantation (ASCT) remains an integral component of the myeloma treatment algorithm for patients considered eligible for the procedure, nowadays performed in myeloma patients up to the age of 75 years. Until the advent of the novel agents, the initial therapy regimens commonly used were vincristine, doxorubicin, and dexamethasone (VAD) or single-agent dexamethasone, both of which shared the advantage of having little impact on stem cell mobilization and collection. Previous studies had shown that alkylating agents can potentially affect the stem cell pool and thus interfere with the ability to collect adequate numbers of stem cells. However, VAD is no longer uses nowadays, whereas current lenalidomide-containing combinations significantly affect stem cell collection. .In Switzerland, the combination of non-myeloablative chemotherapy with vinorelbine or gemcitabine and G-CSF is the current standard procedure. With the predominant use of bortezomib during induction treatment more patients have pre-existing neurotoxicity. Vinorelbine can aggravate this problem. Recently data have shown that a mobilization with gemcitabine together with G-CSF is safe and effective in myeloma patients. Whether chemotherapy is mandatory at all to achieve the same reliable and cost-effective mobilization is currently unknown. The investigators therefore consider that a direct comparison between vinorelbine/gemcitabine and G-CSF versus G-CSF alone is justified.

Objective:

The primary objective is to show non-inferiority of cytokine stimulation with G-CSF compared to chemotherapy stimulation with vinorelbine (or gemcitabine) together with G-CSF for the mobilization of autologous stem cells in myeloma patients in first remission.

Study Duration:

The anticipated total study duration is 42 months.

02

Conditions studied

  • Multiple Myeloma

Keywords

  • Multiple Myeloma
  • Vinorelbine
  • Gemcitabine
  • G-CSF
  • ASCT
03

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  • Myeloma or amyloidosis patients after standard first-line induction treatment. (Additional induction regimens in refractory myeloma patients are allowed)
  • Patients must be considered being clinically fit for subsequent consolidation with high-dose melphalan-based chemotherapy with autologous stem cell support.
  • Patients must be aged ≥18 years.
  • Female patients of child-bearing potential must have a negative pregnancy test (urine or serum) within 14 days prior to study treatment mobilisation, and they must implement adequate measures (hormonal treatment p.o. or i.m., intra uterine surgical devices, or latex condoms) to avoid pregnancy during study treatment and for additional 12 months.
  • Patients must have given voluntary written informed consent

Exclusion criteria

Exclusion Criteria:

  • Patients with concurrent other malignant disease can be included, but previous treatment for other malignancies must have been terminated at least 2 months before registration. Endocrine treatment (such as for breast cancer) is allowed.
  • Pregnancy or lactating female patients.
  • The use of any anti-cancer investigational agents within 14 days prior to the expected start of trial treatment.
04

Study design

Phase
Phase 2
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Parallel assignment
Masking
None (open label)
Enrollment
137 participants (actual)

Study arms

  • Active comparator
    CG (Chemotherapy/G-CSF) - Regime

    Vinorelbine 35 mg/m2 at day 1 as an i.v. infusion over 10 minutes or gemcitabine 1250 mg/m2 as a 30 minutes infusion at day 1. G-CSF will be started at day 4 at 10mcg/kg b.w. split in two daily doses, until the end of the stem cell collection procedure, with the first collection attempt on day 8.

    Drug: Vinorelbine · Drug: Gemcitabine · Drug: G-CSF

  • Experimental
    G (G-CSF) - Regime

    G-CSF at 10mcg/kg b.w. split in two daily doses starting from day 1 until the end of the stem cell collection procedure, with the first collection attempt on day 5.

    Drug: G-CSF

Interventions

  • DrugVinorelbine

    Stimulation with vinorelbine together with G-CSF for mobilization of autologous stem cells

  • DrugGemcitabine

    Stimulation with gemcitabine together with G-CSF for mobilization of autologous stem cells

  • DrugG-CSF

    Cytokine stimulation with G-CSF for mobilization of autologous stem cells

05

What researchers measure

Primary outcomes

  1. Number of patients achieving a sufficient number of stem cells

    Number of patients achieving a sufficient number (at least 5.0 Mio/kg) of stem cells at the planned day in a single day procedure without the use of the rescue compound plerixafor

    Time frame: 8 days

Secondary outcomes

  1. Adverse events

    Number of patients experiencing toxicities/adverse events assessed according to the CTCAE 5.0 during the study period

    Time frame: 30 days after ASCT

  2. Quality of life

    Assessment of quality of life before and after mobilization. The EORTC Q30 questionnaire will be given to patients at screening and after mobilization

    Time frame: 8 days

  3. Pain

    Assessment of pain associated with the mobilization procedure. Pain is measured with visual analogue scale before and after mobilization

    Time frame: 8 days

  4. Use of plerixafor

    Number of patients requiring plerixafor for mobilization

    Time frame: 8 days

  5. Hematologic engraftment after ASCT

    First day (after ASCT) of neutrophils rising again above 0.5 G/l, and of platelets rising again above 20 G/L in the absence of platelet transfusions in the previous 3 days.

    Time frame: 30 days

  6. Cellular composition of the peripheral blood and the grafts

    Standard multiparameter flowcytometric assessment will determine CD4, CD8, sCD3, CD56 and CD19 cellular subsets.

    Time frame: 30 days

  7. Flowcytometric MRD levels in the peripheral blood and the grafts

    Assessed by standard multiparameter flowcytometry.

    Time frame: 30 days

  8. Overall survival

    Time from ASCT until death of any cause or date of last follow-up.

    Time frame: 60 months

  9. Progression free survival

    Time from ASCT until first recurrence of myeloma or date of last follow-up whatever occurs first.

    Time frame: 60 months

06

Study locations

1 site
  • Department for Medical Oncology University Hospital/Inselspital
    Berne, 3010, Switzerland
07

References and documents

Individual participant data

Plan to share: Yes

No publications or documents are linked to this record.

08

Registry details

Key details

Study ID
NCT03442673
Lead sponsor
Insel Gruppe AG, University Hospital Bern
Responsible party
Sponsor
First posted
Feb 22, 2018
Start date
Sep 17, 2018
Primary completion
Mar 1, 2023
Completion
May 1, 2024
Last update
Mar 28, 2025

Study contacts

Barbara Jeker, MD
study chair · Department for Medical Oncology University Hospital/Inselspital 3010 Bern Switzerland

Oversight

Data monitoring committee
No
FDA-regulated drug
No
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

Not currently enrolling

This study is completed, as verified in Mar 2025. You cannot join it, but the record below documents what was studied.

Follow this study

Get an email when the registry record changes — status, dates, results — or when someone posts here.

Sign in to follow

Discussion

Questions and observations about this study, from anyone following it. Not medical advice, and not a channel to the study team — their contact details are on the registry record.

Sign in to join the discussion. Reading takes no account; posting does. You choose a display name, and a pseudonym is the default.

Nothing here yet. If you are running this trial, taking part in it, or weighing whether to, this is the place to say so.

Start the discussion