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CompletedNCT03350048ScreenTBUpdated Feb 1, 2023

Evaluation of Host Biomarker-based Point-of-care Tests for Targeted Screening for Active TB

An observational study in Pulmonary Tuberculosis, sponsored by Prof Gerhard Walzl. Completed at 10 sites in 8 countries. Open to participants aged 18 Years to 70 Years. Per ClinicalTrials.gov, last updated 2023-02-01.

Sponsored by Prof Gerhard Walzl · Observational

Study type
Observational
Model
Cohort
Time perspective
Prospective
Enrollment
969
Ages
18 Years to 70 Years
Sex
All
01

Study summary

Title: Evaluation of host biomarker-based point-of-care tests for targeted screening for active TB (Screen TB)

Introduction: Tuberculosis (TB) places severe pressure on health care services of the developing world. Despite the introduction of the highly sensitive and specific GeneXpert MTB/RIF (GeneXpert) test [1] with a potential turn-around time of two hours, many people in high TB prevalence areas still do not have access to efficient TB diagnostic services due to logistical constraints in these settings. A cost effective, rapid, point-of-care screening test with high sensitivity would identify people with a high likelihood for active TB and would prioritize them for testing with more expensive, technically or logistically demanding assays including GeneXpert or liquid culture, facilitating cost-effective diagnostic work-up in resource-limited settings. A serum cytokine signature for active TB disease, discovered in the AE-TBC project, with a sensitivity of 89% (CI 78 - 95%) and specificity of 76% (CI 68 - 83%), will be optimised and utilized in a point-of-care format (TransDot) to rapidly test for TB disease in symptomatic people.

Hypothesis: The TransDot test will achieve a sensitivity of > 90% for TB disease, in a training set of people suspected of having TB disease, and be validated (achieve similarly high sensitivity) subsequently in a prospective test set of people suspected of having TB disease, when compared to a composite gold standard of sputum culture, smear, GeneXpert, chest X-ray, TB symptoms and TB treatment response.

Objectives: The overall objective of the study is to incorporate a six-marker serum signature into a multiplex UCP-LFA format, referred to as TransDot, for finger-prick blood testing. The end point of the study is the accuracy (sensitivity and specificity) of the UCP-LFA TransDot test on finger-prick blood for active TB and will be prospectively compared against gold standard composite diagnostic criteria (GeneXpert, MGIT culture, TB sputum smear, CXR, TB symptom screen and response to TB treatment).

Primary: The primary outcome of interest will be accuracy, sensitivity and specificity of the TransDot finger-prick test when compared with the composite gold standard tests.

Read the detailed description

Protocol Summary Title: Evaluation of host biomarker-based point-of-care tests for targeted screening for active TB (Screen TB)

Population: A total of 800 people presenting at primary health care clinics with presumed active pulmonary tuberculosis, aged 18 to 70 years, male or female gender, will be recruited. They should be willing to give informed, written consent, including consent for HIV testing. They should have symptoms that could be compatible with active TB (cough > two weeks, plus at least one of the following: fever, weight loss, haemoptysis and night sweats). Participants should not have been on TB treatment for the past 90 days and should not have received immune suppressive therapy, be known with alcohol of drug abuse, have a haemoglobin level \<9g/dl or be pregnant or breastfeeding. HIV co-infection is not an exclusion criterion. Participants will be recruited from primary health care clinics in Cape Town, South Africa, Windhoek in Namibia, Addis Ababa in Ethiopia, Banjul in The Gambia and Kampala in Uganda.

Number of Sites: Five sites

Study Duration: 3 years

Subject Duration: 18 months for TB cases, 2 months for non-TB cases

Objectives:

The overall objective of the study is to incorporate a six-marker serum signature into a multiplex UCP-LFA format, referred to as TransDot, for finger-prick blood testing. The end point of the study is the accuracy (sensitivity and specificity) of the UCP-LFA TransDot test on finger-prick blood for active TB and will be prospectively compared against gold standard composite diagnostic criteria (GeneXpert, MGIT culture, TB sputum smear, CXR, TB symptom screen and response to TB treatment).

02

Conditions studied

  • Pulmonary Tuberculosis

Keywords

  • Tuberculosis
  • Point-of-care test
  • Diagnostics
  • Biomarkers
03

Who can participate

Ages eligible
18 Years to 70 Years
Sexes eligible
All
Sampling method
Non-probability sample

Study population

Adult participants with suspected active TB disease will be recruited in South Africa, the Gambia, Uganda, Namibia and Ethiopia. Each site will recruit approximately 160 participants with suspected TB, until the desired overall total of about 800 participants is reached. In South Africa, up to 300 participants will be recruited from primary health care clinics (Adriaanse, Elsiesriver, Uitsig, Ravensmead, Fisantekraal, Durbanville and Dunoon) in Cape Town.

Patients presenting to the health care facility with symptomatic pulmonary disease and a high likelihood of having tuberculosis will be enrolled and followed up for outcome classification. Participants who had previous TB, extra-pulmonary TB in addition to pulmonary TB, drug resistance detected on GeneXpert or culture or other concomitant diseases, will not be excluded from enrolment. Both HIV positive and HIV negative individuals will be enrolled.

Inclusion criteria

  • Symptoms suggestive of TB disease: cough for more than two weeks with fever, malaise, weight loss, night sweats, haemoptysis, chest pain or loss of appetite.
  • Willingness to give consent to take part in the study.
  • Willingness to undergo HIV testing or be willing to have their HIV infection status disclosed to the study field workers.
  • Eighteen years or older and aged 70 years or younger.

Exclusion criteria

Exclusion Criteria:

  • Permanent residence in study area for less than 3 months or with no permanent address.
  • Pregnancy or breastfeeding.
  • HB\<9g/l
  • On TB treatment currently or in the last ninety days.
  • HIV positive patients currently on INH prophylaxis, or in the last ninety days.
  • Known quinolone or aminoglicozide antibiotic use reported in the past 60 days.
04

Study design

Observational model
Cohort
Time perspective
Prospective
Enrollment
969 participants (actual)
Patient registry
No
Biospecimen retention
Samples with dna

Groups and cohorts

  • Training Set

    First 500 participants recruited for the Training Set: * Blood collection for optimization and validation (vs ELISA) of TransDot point-of-care test at LUMC and later for lab-based TransDot at local site laboratory * Blood, sputum, saliva and urine collection for secondary objectives and repository

  • Test Set

    Subsequent 300 participants to be used for the Test Set: * Fingerprick TransDot point-of-care test performed at field site after symptom screen and clinical evaluation and before CXR * Blood, sputum, saliva and urine collection for secondary objectives and repository

    Diagnostic Test: Trans-Dot point-of-care test

Interventions

  • Diagnostic testTrans-Dot point-of-care test

    Training set participants will be recruited and receive investigations for TB. Blood samples will also be collected from them for performance of ELISAs and laboratory-based TransDot tests. These blood samples will be drawn at baseline, week 8 and week 24 at end of treatment for confirmed TB cases and at baseline for non-TB cases. Test set participants will be recruited and receive investigations for TB. A POC TransDot test will be performed on fingerprick blood at baseline, and at week 8 and week 24 in participants on TB treatment, as well as a laboratory based TransDot test on serum at baseline. The week 8 and week 24 TransDot tests will be used to investigate the test's utility as an indicator of treatment response.

05

What researchers measure

Primary outcomes

  1. Diagnostic performance of the TransDot finger-prick test

    The primary outcome of interest will be accuracy, sensitivity and specificity of the TransDot finger-prick test when compared with the composite gold standard tests.

    Time frame: 3 years

Secondary outcomes

  1. POC TransDOT test versus lab-based tests

    To evaluate the agreement between the POC TransDot test and laboratory based ELISAs first (both on serum), and subsequently between POC TransDot (on fingerprick blood) and laboratory based TransDot (on serum).

    Time frame: 3 years

  2. TransDOT as treatment response marker

    To investigate the utility of a TransDot test at month 2 and month 6 as a marker of treatment response.

    Time frame: 3 years

  3. Identification of additional host marker signatures

    To identify additional host marker signatures that can be utilized for future improvement of diagnostic tests in the TransDot format or other point-of care tests that might become available in the future

    Time frame: 3 years

  4. Evaluation of the serum signature's underlying biological processes

    To evaluate the biological processes (cell-based immune profile and components) underlying the six-marker serum signature model during TB disease and treatment response. In parallel, the peripheral profile will compare this to the corresponding profile at the lung infection site.

    Time frame: 3 years

  5. Optimisation of ultra-sensitive TB culture techniques

    To refine and optimise ultra-sensitive TB culture techniques on sputum and compare these to standard techniques and the TransDot test results, at baseline and month 6.

    Time frame: 3 years

  6. Biomarker Biorepository Samples

    To collect appropriate additional host samples for future biomarker research

    Time frame: 3 years

06

Study locations

10 sites
  • Armauer Hansen Research Institute
    Addis Ababa, Ethiopia
  • Medical Research Council The Gambia
    Banjul, Gambia
  • European Research and Project Office GmbH
    Saarbrücken, Saarland 66123, Germany
  • LINQ Management GmbH
    Berlin, 14057, Germany
  • University of Namibia
    Windhoek, 13301, Namibia
  • The European & Developing Countries Clinical Trials Partnership Association (EDCTP)
    The Hague, South Holland 2593 HW, Netherlands
  • Leiden University Medical Center (Academisch Ziekenhuis Leiden, LUMC)
    Leiden, 2333 ZA, Netherlands
  • Stellenbosch University
    Cape Town, Western Cape 7505, South Africa
  • Makerere University
    Kampala, Uganda
  • London School of Hygiene and Tropical Medicine
    London, WC1E 7HT, United Kingdom
07

References and documents

Study documents

  • Protocol and statistical analysis plan · May 5, 2016

Documents are hosted by the registry — open the source record to download them.

08

Registry details

Key details

Study ID
NCT03350048
Lead sponsor
Prof Gerhard Walzl
Collaborators
Armauer Hansen Research Institute, Ethiopia, Medical Research Council Unit, The Gambia, Leiden University Medical Center, Makerere University, London School of Hygiene and Tropical Medicine, European and Developing Countries Clinical Trials Partnership (EDCTP), LINQ Management GMBH
Responsible party
Prof Gerhard Walzl (Prof, University of Stellenbosch) — Sponsor-investigator
First posted
Nov 22, 2017
Start date
Apr 1, 2016
Primary completion
Apr 30, 2019
Completion
Jul 31, 2020
Last update
Feb 1, 2023

Study contacts

Gerhard Walzl, PhD, MD
principal investigator · Head of Department of Biomedical Sciences

Oversight

Data monitoring committee
No
FDA-regulated drug
No
FDA-regulated device
No
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