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WithdrawnNCT03298958Updated Jun 12, 2019

Secondary Prevention Trial of Rapamycin in Patients With Resected Non-muscle Invasive Bladder Cancer

A Phase 3 interventional study of Rapamycin and Placebo Oral Tablet in Bladder Cancer, sponsored by The University of Texas Health Science Center at San Antonio. Withdrawn at 1 site in United States. Open to participants aged 18 Years and older. Per ClinicalTrials.gov, last updated 2019-06-12.

Sponsored by The University of Texas Health Science Center at San Antonio · Phase 3, Interventional, and Treatment

Why this study was withdrawn
No funding was received, no subjects were enrolled
Phase
Phase 3
Study type
Interventional
Enrollment
0
Allocation
Randomized
Ages
18 Years and older
Sex
All
01

Study summary

The study is a multi-site Phase 3 double-blinded randomized placebo-controlled trial. Subjects are randomly assigned to receive either a placebo or oral Sirolimus: 0.5 mg daily. All subjects will be treated for 2 years or until disease recurrence. Patients will undergo endoscopic evaluation of the bladder every 3 months for the first 2 years following enrollment and then every 6 months for an additional 2 years on study. Selection of BCG immune therapy is at the discretion of the treating urologist but in general is reserved for high-risk patients. Patients concurrently receiving BCG immune therapy will receive standard BCG therapy including induction (weekly for 6 weeks) and maintenance (weekly for 3 weeks at 3 months, 6 months, and then every 6 months following tumor resection).

02

Conditions studied

03

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  • Pathologically (histologically) proven diagnosis of non-muscle invasive (Ta, Tis or T1) bladder cancer within 60 days prior to enrollment
  • Be able to give informed consent
  • Be age 18 or older
  • Not be in an immunosuppressed state (e.g. HIV, use of chronic steroids)
  • Not have active, uncontrolled infections
  • Not be on agents known to alter rapamycin metabolism significantly
  • Not have a reported history of liver disease (e.g. cirrhosis)
  • Not have a prior history of non-bladder cancer unless the cancer is clinically stable and not requiring active treatment except basal cell carcinoma or squamous cell carcinoma of the skin.
  • Not pregnant, or taking effective contraception before rapamycin therapy, during therapy and for 12 weeks after discontinuation of therapy.

Exclusion criteria

Exclusion Criteria:

  • Have muscle-invasive (≥T2) bladder cancer
  • Unable to give informed consent
  • Age \< 18
  • Immunosuppressed state (e.g. HIV, use of chronic steroids)
  • Active, uncontrolled infections
  • On agents known to alter rapamycin metabolism significantly
  • Another cancer requiring active treatment (except basal cell carcinoma or squamous cell carcinoma of the skin)
  • Patients at risk of pregnancy who are unwilling or unable to take effective contraception before rapamycin therapy, during therapy, and for 12 weeks after discontinuation of therapy.
  • Individuals with a reported history of liver disease (e.g. cirrhosis)
04

Study design

Phase
Phase 3
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Parallel assignment
Masking
Double (Participant, Investigator)
Enrollment
0 participants (actual)

Study arms

  • Placebo comparator
    Placebo Oral Tablet

    Subject will be randomized to take the Placebo once daily for 2 years or until disease recurrence

    Drug: Placebo Oral Tablet

  • Active comparator
    Sirolimus (Rapamycin) 0.5 mg/day for 2 years

    Subject will be randomized to take Sirolimus (Rapamycin) 0.5mg once daily for 2 years or until disease recurrence

    Drug: Rapamycin

Interventions

  • DrugRapamycin

    Subject will be randomized to one of the 2 arms

    Also known as: Sirolimus

  • DrugPlacebo Oral Tablet

    Subject will be randomized to one of the 2 arms

05

What researchers measure

Primary outcomes

  1. Test the hypothesis that rapamycin 0.5 mg daily increases recurrence-free survival for patients with non-muscle invasive bladder cancer

    Recurrence is defined as histologically-proven bladder cancer (stage CIS, Ta, T1 or ≥T2)

    Time frame: Patients are treated for 2 years or until disease relapse

Secondary outcomes

  1. To determine effects of rapamycin on recurrence-free survival (RFS) for subgroup of patients with non-muscle invasive bladder cancer concurrently receiving BCG immune therapy.

    Recurrence is defined as histologically-proven bladder cancer (stage CIS, Ta, T1 or ≥T2)

    Time frame: Patients are treated for 2 years or until disease relapse

  2. To compare the effects of rapamycin on BCG-specific immunity during treatment of non-muscle invasive bladder cancer with maintenance BCG.

    BCG antigen-specific IFN-gamma ELISPOT responses will be measured

    Time frame: baseline and 6 months after registration

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Study locations

1 site
  • University of Texas Health Science Center at San Antonio
    San Antonio, Texas 78229, United States
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References and documents

Individual participant data

Plan to share: No

No publications or documents are linked to this record.

08

Registry details

Key details

Study ID
NCT03298958
Lead sponsor
The University of Texas Health Science Center at San Antonio
Responsible party
Sponsor
First posted
Oct 2, 2017
Start date
Nov 1, 2018
Primary completion
Feb 1, 2022 (estimated)
Completion
May 1, 2022 (estimated)
Last update
Jun 12, 2019

Oversight

Data monitoring committee
Yes
FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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