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Active, not recruitingNCT03293173Bio-CHICUpdated Jun 21, 2024

Biomarker Driven Intensified ChemoImmunotherapy With Early CNS Prophylaxis

A Phase 2 interventional study of R-CHOEP and DA-EPOCH-R in Lymphoma, Large B-Cell, Diffuse, sponsored by Nordic Lymphoma Group. Active, not recruiting at 16 sites in 4 countries. Open to participants aged 18 Years to 64 Years. Per ClinicalTrials.gov, last updated 2024-06-21.

Sponsored by Nordic Lymphoma Group · Phase 2, Interventional, and Treatment

Phase
Phase 2
Study type
Interventional
Enrollment
120
Allocation
Non-randomized
Ages
18 Years to 64 Years
Sex
All
01

Study summary

This study is testing whether stratification of the patients according to biological risk factors for different treatment groups will improve the outcome of patients with clinically high diffuse large B-cell lymphoma (DLBCL).

Read the detailed description

For young clinically high-risk diffuse large B-cell lymphoma (DLBCL) patients the optimal therapy has not been established. Previous Nordic phase II studies, where dose-dense chemoimmunotherapy (R-CHOEP-14) with systemic CNS prophylaxis (HD-Mtx and HD-AraC) was given, demonstrated favorable outcome in comparison to historical controls. However, the patients with biological risk factors, such as translocation of bcl2 and myc oncogenes or and/or high BCL2 and MYC expression or deletion 17p and/or high P53 expression had significantly higher risk of death, as compared to patients without aberrations. The figures provide evidence for an unmet clinical need for the patients with biological risk factors, and underscore the importance of a clinical trial, where both biological and clinical risk factors play a role in the treatment planning.

In this trial treatment intensity varies according to presence or absence of biological risk factors. All patients receive a prephase medication consisting of prednisone and vincristine and two cycles of R-CHOP and high dose (HD) methotrexate. Subsequently, depending on the biological risk factors either four additional cycles of R-CHOEP (standard arm with no risk factors) or four dose adjusted R-EPOCH courses (experimental arm with risk factors) are given, followed by one course of high dose cytarabine (Ara-C) and R. R-CHOEP courses should be given with a two-week and R-EPOCH with a three-week interval.

02

Conditions studied

  • Lymphoma, Large B-Cell, Diffuse

Keywords

  • DLBCL
  • Chemoimmunotherapy
  • High risk
  • CNS prophylaxis
  • Biomarker-driven
03

Who can participate

Ages eligible
18 Years to 64 Years
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  • Age 18 - 64 years
  • Histologically confirmed CD20+ DLBCL based on revised WHO 2008 Lymphoma Classification. The following subgroups and variants can be included:

    • ALK-positive large B-cell lymphoma
    • Intravascular large B-cell lymphoma
    • T-cell rich B-cell lymphoma
    • Myc/BCL-2 double hit lymphoma
    • Follicular lymphomas grade 3b
    • DLBCL with previously undiagnosed concurrent small cell infiltration in bone marrow, lymph node, or extranodal site and lymphomas intermediate between DLBCL and Burkitt's lymphoma are allowed
    • Posttransplantation lymphoma (PTLD), discordant or transformed lymphoma are NOT allowed
  • Patients in at least stage II with age adjusted IPI score of 2 or 3:

    • Stage III /IV and elevated LDH
    • Stage III/IV and WHO performance status 2 - 3
    • Stage II and elevated LDH and WHO performance status 2 - 3
  • And/or patients with site specific risk factors for CNS recurrence defined as follows

    • More than one extranodal site
    • Testicular lymphoma, stage IIE and higher
    • Paranasal sinus and orbital lymphoma with destruction of bone
    • Large cell lymphoma infiltration of the bone marrow
  • Previously untreated, except steroids allowed
  • WHO performance status 0-3
  • Written informed consent

Exclusion criteria

Exclusion Criteria:

  • Severe cardiac disease: cardiac function grade 3-4, left ventricular ejection fraction \<45%
  • Impaired bone marrow liver, renal or other organ function not caused by lymphoma, which will interfere with the treatment schedule (Hemoglobin \< 9 g/dL, ANC \< 1.5 × 109/L, Platelet count \< 75 × 109/L, creatinine clearance \< 40 mL/min, ALT/AST > 2.5 x ULN, bilirubin 1.5 x ULN, INR > 1.5)
  • Pregnancy/lactation
  • Men and women of reproductive potential not agreeing to use effective contraception during treatment and for 18 months after completion of treatment (Effective contraception is combined (estrogen and progestogen containing) hormonal contraception associated with inhibition of ovulation (oral, intravaginal or transdermal), progestogen-only hormonal contraception associated with inhibition of ovulation (oral, injectable or implantable), intrauterine device (IUD), hormone-releasing IUD, bilateral tubal occlusion, vasectomised partner, or sexual abstinence
  • Patients with other severe medical problems, including active infections, cardiac or pulmonary disease, history of PML and with an expected short survival for non-lymphoma reasons
  • Known HIV positivity
  • Active or chronic hepatitis B virus (HBV) infection (defined as positive HBsAg serology), or active hepatitis C virus (HCV) infection (defined by antibody serology testing). HBsAg, HBcAb, and HCVAb must be tested during screening. Patients who have protective titers of HBsAb along negative HBsAg after vaccination or prior but cured hepatitis B are eligible.
  • Vaccination with a live vaccine within one month prior to randomization
  • Patients with a malignancy that has been treated but not with curative intent, unless the malignancy has been in remission without treatment for ≥ 5 years prior to enrollment
  • Earlier treatment containing anthracyclines
  • Psychiatric or mental disorder which make the patient unable to give an informed consent and/or adhere to the protocol
  • CNS disease as diagnosed by MRI or CSF cytology. Positive CSF flow cytometry below diagnostic threshold level by cytology is allowed
  • Transformed lymphoma
  • Primary mediastinal B-cell lymphoma
  • Pleural or peritoneal fluid that cannot be drained safely
  • Hypersensitivity to the active substance or any of the other ingredients
  • History of severe allergic or anaphylactic reactions to humanized or murine monoclonal antibodies or known sensitivity or allergy to murine products
  • Patients participating in other clinical studies, unless followed for survival
  • Lower urinary tract constriction, which cannot be treated adequately
  • Degenerative and toxic encephalopathy
  • Neuromuscular disease
04

Study design

Phase
Phase 2
Primary purpose
Treatment
Allocation
Non-randomized
Intervention model
Parallel assignment
Masking
None (open label)
Enrollment
120 participants (estimated)

Study arms

  • Experimental
    Group A

    Biologically low risk group, R-CHOEP-14

    Combination Product: R-CHOEP

  • Experimental
    Group B

    Biologically high risk group, DA-EPOCH-R

    Combination Product: DA-EPOCH-R

Interventions

  • Combination productR-CHOEP

    rituximab, cyclophosphamide, doxorubicin, etoposide, vincristine, prednisone

  • Combination productDA-EPOCH-R

    dose-adjusted etoposide, prednisone, vincristine, cyclophosphamide, doxorubicin, rituximab

05

What researchers measure

Primary outcomes

  1. Time to treatment failure (TTF) of the patients with biological risk factors

    Interval between the registration date and the date of documented progression or lack of response, first relapse, death for any reason or discontinuation/change of therapy because of toxicity, whichever occurs first. Otherwise, patients will be censored at the last date they were known to be alive. For patients not responding at any time point on study treatment, TTF is defined as one day.

    Time frame: At 3 years

Secondary outcomes

  1. Time to treatment failure (TTF) at 3 years from date of registration of all patients and the patients in the low risk group

    Interval between the registration date and the date of documented progression or lack of response, first relapse, death for any reason or discontinuation/change of therapy because of toxicity, whichever occurs first. Otherwise, patients will be censored at the last date they were known to be alive. For patients not responding at any time point on study treatment, TTF is defined as one day.

    Time frame: At 3 years

  2. Incidence of treatment-emergent adverse events (Safety and tolerability)

    Number of patients with treatment-related adverse events graded according to the NCI CTCAE v 4.03

    Time frame: During the treatment period at the end of each cycle (14 or 21 days) up to 6 months. In addition, severe late toxicities during follow-up at 6 months intervals through study completion, an average of 5.5 years.

  3. Clinical response rate of all patients and the patients with biological risk factors

    Number of patients with complete or partial response

    Time frame: At the end of treatment cycles 2 and 7. Each cycle is two (group A) or three weeks (group B)

  4. CNS relapse rate

    Number of patients with CNS progression

    Time frame: At 1,5 years

  5. Progression free survival rate (PFS) of all patients and the patients with biological risk factors

    Time frame: At 3 years

  6. Overall survival rate (OS) of all patients and the patients with biological risk factors

    Time frame: At 3 years

  7. Molecular correlates for survival

    Identification of genomic aberrations (for example mutations and translocations), gene expression profiles and protein expression from the tumor tissue and circulation that predict clinical course of the disease

    Time frame: At 3 years

06

Study locations

16 sites
  • Aarhus University Hospital
    Aarhus, Denmark
  • Dept of Haematology, Rigshospitalet
    Copenhagen, 2100, Denmark
  • Dept of Haematology, Herlev Hospital, Copenhagen
    Herlev, Denmark
  • Dept haematology, Odense University hospital
    Odense, 5000, Denmark
  • Dept of Haematology, Sjaellands University hospital, Roskilde
    Roskilde, 4000, Denmark
  • Helsinki University Hospital Cancer Centre
    Helsinki, 00029, Finland
  • Keski-Suomen keskussairaala
    Jyväskylä, 40620, Finland
  • Kuopio University Hospital
    Kuopio, 70029, Finland
  • TAYS
    Tampere, 33521, Finland
  • Turku University Hospital, Syöpäklinikka
    Turku, 20520, Finland
  • Dept. of Oncology, Helse Bergen HF Haukeland sykehus
    Bergen, 5021, Norway
  • Oslo University Hospital
    Oslo, Norway
  • Dept. of Haematology and Oncology, Helse Stavander HF sykehuset
    Stavanger, 4011, Norway
  • Dept. of Oncology, Universitetssykehuset i Nord-Norge HF
    Tromsø, 9038, Norway
  • Dept of Oncology, St. Olavs hospital HF
    Trondheim, 7006, Norway
  • Skåne University Hospital
    Lund, Sweden
07

References and documents

Publications

  • Fiskvik I, Beiske K, Delabie J, Yri O, Spetalen S, Karjalainen-Lindsberg ML, Leppa S, Liestol K, Smeland EB, Holte H. Combining MYC, BCL2 and TP53 gene and protein expression alterations improves risk stratification in diffuse large B-cell lymphoma. Leuk Lymphoma. 2015 Jun;56(6):1742-9. doi: 10.3109/10428194.2014.970550. Epub 2014 Nov 19. PubMed 25284491 ↗
  • Holte H, Leppa S, Bjorkholm M, Fluge O, Jyrkkio S, Delabie J, Sundstrom C, Karjalainen-Lindsberg ML, Erlanson M, Kolstad A, Fossa A, Ostenstad B, Lofvenberg E, Nordstrom M, Janes R, Pedersen LM, Anderson H, Jerkeman M, Eriksson M. Dose-densified chemoimmunotherapy followed by systemic central nervous system prophylaxis for younger high-risk diffuse large B-cell/follicular grade 3 lymphoma patients: results of a phase II Nordic Lymphoma Group study. Ann Oncol. 2013 May;24(5):1385-92. doi: 10.1093/annonc/mds621. Epub 2012 Dec 17. PubMed 23247661 ↗

Individual participant data

Plan to share: Yes — individual deidentified participant data (including data dictionaries) will be shared

Supporting information: Study protocol, Sap, Icf, Csr

08

Registry details

Key details

Study ID
NCT03293173
Lead sponsor
Nordic Lymphoma Group
Collaborators
Helsinki University Central Hospital, Aarhus University Hospital
Responsible party
Sponsor
First posted
Sep 26, 2017
Start date
Aug 4, 2017
Primary completion
Jan 31, 2021
Completion
Dec 31, 2024 (estimated)
Last update
Jun 21, 2024

Study contacts

Sirpa Leppa, prof
principal investigator · Helsinki University Hospital Cancer Centre

Oversight

Data monitoring committee
Yes
FDA-regulated drug
No
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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