CClinicalTrials.gg
CompletedNCT03264339Updated Sep 9, 2021

The Small Step Program - Early Intervention for Children With High Risk of Developing Cerebral Palsy

An interventional study of Small Step Program in Cerebral Palsy, sponsored by St. Olavs Hospital. Completed at 1 site in Norway. Open to participants aged 3 Months to 8 Months. Per ClinicalTrials.gov, last updated 2021-09-09.

Sponsored by St. Olavs Hospital · Not applicable, Interventional, and Treatment

Phase
Not applicable
Study type
Interventional
Enrollment
12
Allocation
Not applicable
Ages
3 Months to 8 Months
Sex
All
01

Study summary

Children with cerebral palsy (CP) have life-long motor disorders caused by brain injuries which occur around birth. These children go through extensive treatment during childhood, but the treatment has generally been started late due to late diagnosis (median age 15 months). New recommendations state that the clinical diagnosis "high risk of CP" should be given before 6 months corrected age, in order to be able to intervene as early as possible, and have the best possibilities to prevent or limit the adverse neurodevelopmental consequences of brain injuries occurring around birth. Thus, there is a great need to develop evidence-based early interventions for children at high risk of developing cerebral palsy.

The Small Step program is developed at Karolinska Institutet (KI) in Stockholm, Sweden and is based upon theories of brain plasticity induced by early learning. The efficacy of the program is presently being investigated at KI. Preliminary results indicate a large individual variation in response to the program among the participating children.

The aim of the present study is therefore to explore individual responses to the Small Step Program in infants at risk of developing cerebral palsy.

The main hypothesis is that infant characteristics, such as severity of brain pathology, are associated with differential response to the program. Also, infants with absent fidgety movements and children with sporadic fidgety movements are believed to respond differently to the program.

Read the detailed description

The efficacy of the Small Step program is presently being investigated through a randomized controlled trial (NCT02166801) at Karolinska Institutet (KI) in Stockholm, Sweden. In the original project proposal for the current study, the plan was to contribute with inclusion of children from St. Olavs Hospital to the randomized controlled study initiated at KI. This project proposal has previously been approved by the Regional Ethical Committee (REK) for Medical Research in Mid-Norway (2016/1366). However, the researchers at KI have now completed the inclusion of participants for the randomized controlled study, and their preliminary results indicate that there is a large individual variation among the included participants regarding effect of the Small Step program. In agreement with the researchers at KI, it was therefore decided to change the design of the current study using Single Subject Research Design, a study design that is more appropriate to investigate individual response to treatment. The change in study design has been approved by REK (2016/1366-10).

Participation in this study is based on informed consent from the parents, and the child and the family participating in the project will be offered a potentially effective early intervention program that they would otherwise not be able to access.

The Small Step intervention program has three alternating treatment foci (B, C, and D) divided into five different steps, each lasting for 6 weeks (in total 30 weeks). The three treatment foci are Communication, Hand function and Mobility/gross motor function. The Hand function and Mobility steps will be conducted during two time-periods and the order will be randomised. Communication will have one intervention period during step III. The training will be conducted in the children's home by the parents on a daily basis under weekly supervision by the therapist responsible for each specific step of the intervention. General principles for the small step program are: a) collaborative goal-setting; b) promote infant's self-initiated actions; c) use of enriched home environment, d) intensity and repetition.

Before and after the intervention, there is a baseline phase with no treatment (A) and a withdrawal phase with no treatment (A), resulting in the following design: A-B-C-D-B-C-A. In addition, there is a follow-up phase when the children are 2 years of age.

02

Conditions studied

  • Cerebral Palsy

Browse trials for

Keywords

  • Infant
  • Hand/Growth & Development
  • Motor activity
  • Exercise
  • Communication
03

Who can participate

Ages eligible
3 Months to 8 Months
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  • increased perinatal risk factors, such as preterm birth, hypoxic ischemic encephalopathy (asphyxia), and morphological brain abnormalities. These "at-risk" children are included in the regular clinical follow-up program at St. Olavs University Hospital comprising a standard examination at 3 months of age (for preterm born children: 3 months post term, so-called corrected age). At this examination, infants who exhibit two or more of the following additional risk factors will be eligible for study participation:

    • Neurological signs assessed with Hammersmith Infant Neurological Examination (HINE) with a cut-off score of \< 57 (20).
    • Delayed psycho-motor development measured with Alberta Infant Motor Scale (AIMS) using 2SD as the cut-off.
    • Absent or sporadic fidgety movements assessed with the General Movements Assessment (GMA)
    • Pathological findings on cerebral imaging (magnetic resonance imaging-MRI/cerebral ultrasound) done in regular clinical practice.

Exclusion criteria

Exclusion Criteria:

  • unstable medical condition
  • progressive disorders
  • diagnosis with a specific syndrome.
  • neither parent is fluent in Norwegian or English. Satisfactory skills in either language are required for participation in data collection and the coaching and education program.
04

Study design

Phase
Not applicable
Primary purpose
Treatment
Allocation
Not applicable
Intervention model
Single group
Masking
None (open label)
Enrollment
12 participants (actual)

Study arms

  • Experimental
    Smal step

    Small Step Program, comprising 3 treatment focus areas (Hand use, Mobility, Communication)

    Behavioral: Small Step Program

Interventions

  • BehavioralSmall Step Program

    The Small Step intervention program has three alternating treatment foci (Hand use, Mobility, Communication) divided into five different steps, each lasting for 6 weeks (in total 30 weeks).

05

What researchers measure

Primary outcomes

  1. Peabody Developmental Motor Scales, second edition (PDMS-2)

    PDMS-2 is a standard measurement that assesses gross and fine motor skills in young children from birth through age 5 years. The PDMS-2 is composed of six subtests that assess related motor abilities that develop early in life. In this study, the Stationary, Locomotion, Grasping, and Visual-Motor Integration subtests will be used. The scores on these subtests are presented as percentiles, standard scores, and age equivalents.

    Time frame: up to 2 years

Secondary outcomes

  1. Hand Assessment for Infants (HAI)

    identifies and measures upper limb asymmetry and general manual development from 3-12 months

    Time frame: up to 2 years

  2. Alberta Infant Motor Scale (AIMS)

    identifies infants with delayed or deviant motor development up to 18 months of age

    Time frame: up to 2 years

  3. Gross Motor Function Measure (GMFM-66)

    an observational, standardized and criterion-referenced measure, developed to evaluate change in gross motor function in children with cerebral palsy (CP)

    Time frame: up to 2 years

  4. Parent-Child Early Relational Assessment (PC-ERA)

    assesses parent-child interactions to capture the affective and behavioral characteristics that parent and child bring to the interaction, and the quality or tone of the relationship

    Time frame: up to 2 years

  5. Treatment Expectancy and Credibility Survey (TCS) - modification

    assesses treatment expectations

    Time frame: up to 2 years

Other outcomes

  1. Hammersmith Infant Neurological Examination (HINE)

    Identifies neurological signs in infants and is used to estimate the neurological development of infants aged two-24 months

    Time frame: at baseline, after the intervention at 30 weeks and at follow-up up at 2 years

  2. The Working Model of the Child Interview (WMCI)

    a semi-structured, open-ended interview designed to assess parent´s representations of their infant/ child and their relationship with their infant/ child. The WMCI will be used to measure change over time

    Time frame: at baseline, after the intervention at 30 weeks and at follow-up up at 2 years

  3. The Ages & Stages Questionnaire: Social and Emotional (ASQ:SE)

    a questionnaire to be completed by parents for assessing social and emotional difficulties in babies and young children

    Time frame: at baseline, after the intervention at 30 weeks and at follow-up up at 2 years

  4. Norwegian Parenting Stress Index (PSI)

    used to measure changes in perceived parental stress over time

    Time frame: at baseline, after the intervention at 30 weeks and at follow-up up at 2 years

  5. The Hospital Anxiety and Depression Scale (HADS)

    a self-assessment scale for parents and is used to detect changes in states of depression, anxiety and emotional distress over time among parents

    Time frame: at baseline, after the intervention at 30 weeks and at follow-up up at 2 years

  6. Pediatric Evaluation of the Disability Inventory (PEDI)

    used to evaluate functional skills and caregiver assistance in the domains self-care, mobility, and social function over time. The child is assessed by structured interviews with the parents. The summary scores can be converted to normative standard scores and scaled scores, meaning that the child's performance will be compared with norms taken from typically developing children

    Time frame: at 2 years

  7. Bayley Scales of Infant Development (BSID-III)

    a standard measurements to assess the motor (fine and gross), language (receptive and expressive), and cognitive development of infants and toddlers, ages 0-3. These scores will be used to determine the child's performance at two years of age compared with norms taken from typically developing children

    Time frame: at 2 years

  8. Norwegian Communicative Development Inventory (NCDI)

    a parent questionnaire for assessing early language development of children. The NCDI involve questions about communication and language capacities corresponding to the child's ability to comprehend and use communication and language and will be collected

    Time frame: at 2 years

  9. Structural magnetic resonance imaging (MRI)/cerebral ultrasound

    used to identify neuroanatomical abnormalities and underlying brain lesions. Neuroimaging data will be assessed by experienced neuroradiologists in accordance with well-established clinical assessment protocols at the hospital. This means that the children included in the project will not undergo any extra structural MRI examinations outside the normal clinical routine.

    Time frame: before 2 years corrected age

  10. General Movements Assessment (GMA)

    identifies reduced movement quality (i.e. absent or sporadic fidgety movements) in infants at 3 months corrected age. The GMA is part of the clinical assessment performed at the hospital and is assessed by certified and experienced physiotherapists

    Time frame: at 3 months corrected age

06

Study locations

1 site
  • St Olavs Hospital
    Trondheim, Norway
07

References and documents

Publications

  • Eliasson AC, Holmstrom L, Aarne P, Nakeva von Mentzer C, Weiland AL, Sjostrand L, Forssberg H, Tedroff K, Lowing K. Efficacy of the small step program in a randomised controlled trial for infants below age 12 months with clinical signs of CP; a study protocol. BMC Pediatr. 2016 Nov 3;16(1):175. doi: 10.1186/s12887-016-0711-x. PubMed 27809886 ↗

Individual participant data

Plan to share: Yes — (in progress)

08

Registry details

Key details

Study ID
NCT03264339
Lead sponsor
St. Olavs Hospital
Collaborators
Norwegian University of Science and Technology
Responsible party
Sponsor
First posted
Aug 29, 2017
Start date
Sep 7, 2017
Primary completion
Jun 7, 2021
Completion
Jun 7, 2021
Last update
Sep 9, 2021

Study contacts

Elisabeth Selvaag, md
study director · St Olavs Hospital, Children's Clinic

Oversight

Data monitoring committee
No
FDA-regulated drug
No
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

Not currently enrolling

This study is completed, as verified in Sep 2021. You cannot join it, but the record below documents what was studied.

Follow this study

Get an email when the registry record changes — status, dates, results — or when someone posts here.

Sign in to follow

Discussion

Questions and observations about this study, from anyone following it. Not medical advice, and not a channel to the study team — their contact details are on the registry record.

Sign in to join the discussion. Reading takes no account; posting does. You choose a display name, and a pseudonym is the default.

Nothing here yet. If you are running this trial, taking part in it, or weighing whether to, this is the place to say so.

Start the discussion