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CompletedNCT03252223Updated Sep 8, 2021

Ovarian Response to Recombinant Follicle Stimulating Hormone in Women With PCOS

A Phase 4 interventional study of Recombinant Follicle Stimulating Hormone in Polycystic Ovary Syndrome, Healthy and Anovulation, sponsored by University of California, San Diego. Completed at 1 site in United States. Open to female participants aged 18 Years to 37 Years, including healthy volunteers. Per ClinicalTrials.gov, last updated 2021-09-08.

Sponsored by University of California, San Diego · Phase 4, Interventional, and Other

Phase
Phase 4
Study type
Interventional
Enrollment
33
Allocation
Non-randomized
Ages
18 Years to 37 Years
Sex
Female
01

Study summary

Women with PCOS suffer from anovulation and, as a result, infertility. Efforts to clinically induce ovulation in these women using follicle stimulating hormone (FSH) administered subcutaneously seemingly requires prolonged administration compared to that of ovulatory women without PCOS. The apparent differing ovarian responsiveness to FSH between PCOS and normal women has not been carefully studied. We propose to address this issue by performing a dose-response study and examine ovarian follicle (estrogen, E2) responses to FSH administered subcutaneously in women with PCOS compared to responses observed in normal women.

Read the detailed description

In women with polycystic ovary syndrome (PCOS) androgen excess is fundamental to the clinical and physiological alterations of this disorder. In particular, androgen overproduction induces distinctive PCO morphology and appears to influence follicle function. Studies conducted in animals and nonhuman primates have demonstrated that androgens increase follicle number and in small antral follicles enhance granulosa cell (GC) responsiveness to gonadotropin stimulation. However, androgens also have been shown to clearly inhibit GC aromatase activity, and in PCOS follicular fluid, androgen content is abnormally increased. Efforts to reconcile these differences are nonexistent. Moreover, appropriate clinical studies to examine the effects of androgen on follicle health in women are lacking. Excessive androgen exposure in women due to functional tumors or high-dose testosterone treatment in F-M transsexuals has been associated with PCO morphology. Use of androgen therapy to promote follicle growth prior to ovarian hyperstimulation in women undergoing in vitro fertilization has not provided consistent results. However, in these studies GC responses to FSH were not carefully assessed, study populations were exclusively women with previously poor ovarian responses to FSH, and women with PCOS were not included. In fact, there are essentially no clinical studies that have addressed in detail the impact of androgen on follicle function in normal or PCOS women. We hypothesize that androgen facilitates GC responses to FSH in normal women and androgen excess further amplifies follicle growth and function in women with PCOS. We propose to study the effect of increased ovarian androgen on follicle function by increasing intraovarian androgen accumulation using aromatase inhibition followed by FSH stimulation. The experiments in this project are designed to provide insight into whether androgen excess facilitates or interferes with follicle function and ovulation in women with PCOS.

02

Conditions studied

  • Polycystic Ovary Syndrome
  • Healthy
  • Anovulation
  • Hyperandrogenism

Keywords

  • polycystic ovary syndrome
  • anovulation
  • hyperandrogenism
03

Who can participate

Ages eligible
18 Years to 37 Years
Sexes eligible
Female
Accepts healthy volunteers
Yes

Inclusion criteria

  • Subjects determined to have PCOS based on clinical history of irregular menses and clinical or laboratory evidence of hyperandrogenism and polycystic ovaries on ultrasound OR
  • Subjects determined to have a clinical history of regular periods.

Exclusion criteria

Exclusion Criteria:

  1. Women with hemoglobin less than 11 gm/dl at screening evaluation
  2. Women with untreated thyroid abnormalities
  3. Pregnant women or women who are nursing
  4. Women with BMI > 37
  5. Women with known sensitivity to the agents being used
  6. Women with diabetes, or renal, liver, or heart disease
  7. Women with any hormonal therapy or metformin for at least 2 months prior to study start.
04

Study design

Phase
Phase 4
Primary purpose
Other
Allocation
Non-randomized
Intervention model
Parallel assignment
Masking
None (open label)
Enrollment
33 participants (actual)

Study arms

  • Active comparator
    Women with normal menses

    Drug: Recombinant Follicle Stimulating Hormone

  • Active comparator
    Women with Polycystic Ovary Syndrome

    Drug: Recombinant Follicle Stimulating Hormone

Interventions

  • DrugRecombinant Follicle Stimulating Hormone

    A modified dose-response study will be done using recombinant FSH (r-FSH), injected sc for 3 days at any one dose. r-FSH will be administered at weight-adjusted doses equivalent to 37.5, 75, and 150 IU based on an average weight of 70 kg, which approximates the weight of the average woman in the United States according to the Centers for Disease Control. Therefore, the actual dose of r-FSH will be 0.53 IU/kg for the 37.5 dose group. Accordingly, r-FSH will be repeated at doses of 1.1 IU/kg and 2.2 IU/kg that are equivalent to 75 and 150 IU for a 70 kg subject. Each FSH stimulation test will be assigned randomly and be separated by an interval of 8 weeks.

05

What researchers measure

Primary outcomes

  1. Change in granulosa cell function in 24 hours intervals following FSH administration

    Granulosa function will be assessed using estradiol and inhibin levels

    Time frame: Serum levels will be assessed daily during each 3 day FSH stimulation test and for five days following the initial FSH administration

  2. Change in follicle count in following FSH administration

    Number of ovarian follicles will be assessed by pelvic ultrasound

    Time frame: With each dose tested, a pelvic ultrasound will be done before and 3 days after commencing FSH

  3. Change in follicular size in following FSH administration

    Size of ovarian follicles will be assessed by pelvic ultrasound

    Time frame: With each dose tested, a pelvic ultrasound will be done before and 3 days after commencing FSH

06

Study locations

1 site
  • University of California, San Diego
    La Jolla, California 92037, United States
07

References and documents

Individual participant data

Plan to share: No

No publications or documents are linked to this record.

08

Registry details

Key details

Study ID
NCT03252223
Lead sponsor
University of California, San Diego
Collaborators
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
Responsible party
Jeffrey Chang, MD (Professor, University of California, San Diego) — Principal investigator
First posted
Aug 17, 2017
Start date
Oct 2, 2017
Primary completion
Jun 30, 2021
Completion
Jun 30, 2021
Last update
Sep 8, 2021

Study contacts

R. Jeffrey Chang, MD
principal investigator · University of California, San Diego

Oversight

FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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