CClinicalTrials.gg
CompletedNCT03194217CASPARUpdated Mar 10, 2025Results posted

BEN-2001 in Parkinson Disease Patients With Excessive Daytime Sleepiness

A Phase 2 interventional study of BEN-2001 and Placebo in Excessive Daytime Sleepiness and Parkinson Disease, sponsored by BenevolentAI Bio. Completed at 1 site in United States. Open to participants aged 50 Years to 80 Years. Per ClinicalTrials.gov, last updated 2025-03-10.

Sponsored by BenevolentAI Bio · Phase 2, Interventional, and Treatment

Phase
Phase 2
Study type
Interventional
Enrollment
244
Allocation
Randomized
Ages
50 Years to 80 Years
Sex
All
01

Study summary

This phase 2b study is designed as multicentre, multinational, randomized, double blind, parallel group and placebo controlled with three doses of Bavisant (0.5, 1, and 3 mg/d) in subjects with excessive daytime sleepiness with Parkinson's disease.

Read the detailed description

Phase 2b study will be conducted with the aim of investigating the efficacy and safety of three fixed doses of Bavisant (0.5, 1 and 3 mg/d) compared to placebo for the treatment of excessive daytime sleepiness (EDS) in subjects with Parkinson's disease.

02

Conditions studied

  • Excessive Daytime Sleepiness
  • Parkinson Disease
03

Who can participate

Ages eligible
50 Years to 80 Years
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  • Subjects of either sex aged 50 to 80 years *Subjects with previous diagnosis of Parkinson's disease (following the UK Parkinson's disease society brain bank clinical diagnostic criteria)*
  • Subjects capable of understanding and complying with protocol requirements
  • Subjects with medical history of excessive daytime sleepiness

Exclusion criteria

Exclusion Criteria:

  • Subjects with excessive daytime sleepiness due to conditions other than Parkinson's disease (including narcolepsy)
  • Subjects with clinical evidence of depression with significant psychiatric comorbidities (Hamilton Rating Scale for Depression - HAM-D score greater than or equal to 17; with or without treatment)
  • Subjects with evidence of significant fatigue (Fatigue Severity Scale - FSS greater than or equal to 36
  • Subjects with known history of abuse of alcohol or other addictive substances in the 6 months prior to inclusion.
  • Subjects with known allergies or hypersensitivity to Bavisant or any of its excipients.
  • Subjects who are pregnant or lactating.
04

Study design

Phase
Phase 2
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Parallel assignment
Masking
Quadruple (Participant, Care provider, Investigator, Outcomes assessor)
Enrollment
244 participants (actual)

Study arms

  • Experimental
    BEN-2001, 0.5mg

    Experimental treatment

    Drug: BEN-2001

  • Placebo comparator
    Placebo

    Placebo comparator

    Drug: Placebo

  • Experimental
    BEN-2001, 1.0mg

    Experimental treatment

    Drug: BEN-2001

  • Experimental
    BEN-2001, 3.0mg

    Experimental treatment

    Drug: BEN-2001

Interventions

  • DrugBEN-2001

    Bavisant dihydrochloride monohydrate for oral use

    Also known as: Bavisant

  • DrugPlacebo

    Placebo

05

What researchers measure

Primary outcomes

  1. Measurement of Sleepiness Using the Epworth Sleepiness Scale (ESS) at Baseline and Post Dose.

    Mean absolute change of Bavisant treatment groups in the Epworth Sleepiness Scale (ESS) from baseline to the end of the 6-week treatment period. The ESS score (sum of 8 item scores) ranges from 0 to 24 with higher score corresponding to higher average sleep propensity in daily life (higher daytime sleepiness). Eligibility determined based on ESS score of 13 and above.

    Time frame: 6 weeks

06

Results

Posted Nov 24, 2020

Participant flow

Participant flow — Overall Study
MilestonePlaceboBEN-2001, 0.5mgBEN-2001, 1.0mgBEN-2001, 3.0mg
Started60606064
Completed60575660
Not completed0344
Withdrew: Adverse event0233
Withdrew: Failure to meet randomisation criteria0001
Withdrew: Other0110

Outcome measures

PrimaryMeasurement of Sleepiness Using the Epworth Sleepiness Scale (ESS) at Baseline and Post Dose.

Mean absolute change of Bavisant treatment groups in the Epworth Sleepiness Scale (ESS) from baseline to the end of the 6-week treatment period. The ESS score (sum of 8 item scores) ranges from 0 to 24 with higher score corresponding to higher average sleep propensity in daily life (higher daytime sleepiness). Eligibility determined based on ESS score of 13 and above.

Time frame:
6 weeks
Reported as:
Least squares mean · units on a scale
Measurement of Sleepiness Using the Epworth Sleepiness Scale (ESS) at Baseline and Post Dose.
units on a scalePlaceboBEN-2001, 0.5mgBEN-2001, 1.0mgBEN-2001, 3.0mg
Measurement of Sleepiness Using the Epworth Sleepiness Scale (ESS) at Baseline and Post Dose.-4.34 ± 0.5-4.64 ± 0.51-3.46 ± 0.51-4.73 ± 0.5
Statistical analysis
  • BEN-2001, 0.5mg · ANCOVA · p = 0.668 · Mean difference (final values): -0.30 · 95% CI -1.68 to 1.08
  • BEN-2001, 1.0mg · ANCOVA · p = 0.213 · Mean difference (final values): 0.88 · 95% CI -0.50 to 2.26
  • BEN-2001, 3.0mg · ANCOVA · p = 0.575 · Mean difference (final values): -0.39 · 95% CI -1.76 to 0.98

Adverse events

Collected over 70 days. Non-serious events are listed at a 2% frequency threshold.

Adverse event summary by group
GroupDeathsSeriousOther
Placebo0/60 (0%)1/60 (1.7%)11/60 (18.3%)
BEN-2001, 0.5mg0/60 (0%)0/60 (0%)16/60 (26.7%)
BEN-2001, 1.0mg0/60 (0%)0/60 (0%)27/60 (45%)
BEN-2001, 3.0mg0/64 (0%)2/64 (3.1%)26/64 (40.6%)
Most frequent serious events
Most frequent serious events
EventPlaceboBEN-2001, 0.5mgBEN-2001, 1.0mgBEN-2001, 3.0mg
cholecystectomySurgical and medical procedures1/600/600/600/64
ConstipationGastrointestinal disorders0/600/600/601/64
Muscular weaknessMusculoskeletal and connective tissue disorders0/600/600/601/64
Most frequent other events
Showing 10 of 19
Most frequent other events
EventPlaceboBEN-2001, 0.5mgBEN-2001, 1.0mgBEN-2001, 3.0mg
NauseaGastrointestinal disorders1/602/604/603/64
NasopharygitisInfections and infestations3/602/601/601/64
Initial InsomniaPsychiatric disorders2/603/601/603/64
Triglycerous increaseInvestigations1/601/603/600/64
InsomniaPsychiatric disorders0/600/600/603/64
Middle InsomniaPsychiatric disorders0/600/602/603/64
InfluenzaInfections and infestations0/600/602/600/64
Head acheNervous system disorders0/601/602/601/64
Cataract NuclearEye disorders0/600/602/600/64
DiarrhoeaGastrointestinal disorders0/600/602/600/64

Baseline characteristics

ITT

Age, Categorical
Age, Categorical(Participants)PlaceboBEN-2001, 0.5mgBEN-2001, 1.0mgBEN-2001, 3.0mgTotal
<=18 years00000
Between 18 and 65 years1821182784
>=65 years42394237160
Sex: Female, Male
Sex: Female, Male(Participants)PlaceboBEN-2001, 0.5mgBEN-2001, 1.0mgBEN-2001, 3.0mgTotal
Female2123172081
Male39374344163
Race (NIH/OMB)
Race (NIH/OMB)(Participants)PlaceboBEN-2001, 0.5mgBEN-2001, 1.0mgBEN-2001, 3.0mgTotal
American Indian or Alaska Native00000
Asian02002
Native Hawaiian or Other Pacific Islander00000
Black or African American11002
White59575964239
More than one race00000
Unknown or Not Reported00101
Region of Enrollment
Region of Enrollment(participants)PlaceboBEN-2001, 0.5mgBEN-2001, 1.0mgBEN-2001, 3.0mgTotal
United States1312111147
Europe47484953197
07

Study locations

1 site
  • MaxBlue Institute
    Miami, Florida 33018, United States
08

References and documents

Study documents

  • Study protocol · Nov 7, 2018
  • Statistical analysis plan · Oct 25, 2018

Documents are hosted by the registry — open the source record to download them.

Individual participant data

Plan to share: No

09

Registry details

Key details

Study ID
NCT03194217
Lead sponsor
BenevolentAI Bio
Responsible party
Sponsor
First posted
Jun 21, 2017
Start date
Nov 10, 2017
Primary completion
May 28, 2019
Completion
May 28, 2019
Results posted
Nov 24, 2020
Last update
Mar 10, 2025

Study contacts

William G Ondo, M.D
principal investigator · Methodist Neurological Institute

Oversight

Data monitoring committee
No
FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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