CClinicalTrials.gg
CompletedNCT03181503Updated Feb 19, 2020Results posted

Safety and Efficacy of Nemolizumab in PN

A Phase 2 interventional study of CD14152 Dose A and CD14152 placebo in Prurigo Nodularis, sponsored by Galderma R&D. Completed at 16 sites in 4 countries. Open to participants aged 18 Years and older. Per ClinicalTrials.gov, last updated 2020-02-19.

Sponsored by Galderma R&D · Phase 2, Interventional, and Treatment

Phase
Phase 2
Study type
Interventional
Enrollment
70
Allocation
Randomized
Ages
18 Years and older
Sex
All
01

Study summary

The aim of this study is to assess the safety and efficacy of nemolizumab in subjects with prurigo nodularis.

Read the detailed description

This is a randomized, placebo-controlled, double-blinded, parallel group, multicenter study to evaluate the safety and efficacy of nemolizumab over a 12-week treatment period in patients suffering from prurigo nodularis compared to its placebo.

02

Conditions studied

  • Prurigo Nodularis

Browse trials for

03

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  1. Male or female of at least 18 years at screening
  2. Clinical diagnosis of PN for at least 6 months with:

    • Prurigo lesions on upper limbs with or without lesions on the trunk or lower limbs
    • At least 20 nodules on the entire body with a bilateral distribution
  3. Severe pruritus defined as follows on a Numerical Rating Scale (NRS)

    • At the Screening visit 1: Mean of the worst daily intensity of the NRS score is ≥ 7 over the previous 3 days
    • At the Baseline visit: Mean of the worst daily intensity of the NRS score is ≥ 7 over the previous week; NOTE: NRS score should be measured on at least 5 days during the week preceding the baseline visit.
  4. Female subjects must fulfill one of the criteria below:

    • Female subjects of non-childbearing potential (postmenopausal [absence of menstrual bleeding for 1 year prior to screening, without any other medical reason], hysterectomy or bilateral oophorectomy);
    • Female subjects of childbearing potential who agree to a true abstinence (when in line with the preferred and usual lifestyle of the subject), or to use an effective method of contraception throughout the clinical trial and for 120 days after the last study drug administration:

Exclusion criteria

Exclusion Criteria:

  1. Chronic pruritus resulting from another condition than PN such as scabies, insect bite, lichen simplex chronicus, psoriasis, acne, folliculitis, habitual picking, lymphomatoid papulosis, chronic actinic dermatitis, dermatitis herpetiformis, sporotrichosis, bullous disease
  2. Unilateral lesions of prurigo (e.g only one arm affected)
  3. Cutaneous bacterial or viral infection within 1 week before the baseline visit.
  4. Infection requiring treatment with oral or parenteral antibiotics, antivirals, antiparasitics or antifungals within 1 week before the screening visit, or during the screening period, unless completely resolved at the screening/ baseline visits respectively,
  5. Any uncontrolled or serious disease, or any medical or surgical condition, that may either interfere with the interpretation of the clinical trial results and/or put the subject at Chronic pruritus resulting from another condition than PN such as scabies, insect bite, lichen simplex chronicus, psoriasis, acne, folliculitis, habitual picking, lymphomatoid papulosis, chronic actinic dermatitis, dermatitis herpetiformis, sporotrichosis, bullous disease
04

Study design

Phase
Phase 2
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Parallel assignment
Masking
Quadruple (Participant, Care provider, Investigator, Outcomes assessor)
Enrollment
70 participants (actual)

Study arms

  • Placebo comparator
    Placebo

    Participants received 3 subcutaneous injections of placebo (matched to nemolizumab) every 4 weeks (Q4W) up to Week 8.

    Drug: CD14152 placebo

  • Experimental
    Nemolizumab 0.5 mg/kg

    Participants received 3 subcutaneous injections of nemolizumab 0.5 milligram per kilogram (mg/kg) Q4W up to Week 8.

    Drug: CD14152 Dose A

Interventions

  • DrugCD14152 Dose A

    3 subcutaneous injections (every 4 weeks during the 12-week treatment period)

    Also known as: Nemolizumab

  • DrugCD14152 placebo

    3 subcutaneous injections (every 4 weeks during the 12-week treatment period)

    Also known as: Placebo

05

What researchers measure

Primary outcomes

  1. Percent Change From Baseline in Weekly Average of the Peak Pruritus Numeric Rating Scale (NRS) Score at Week 4 Using Last Observation Carried Forward (LOCF) Approach

    Pruritus NRS is a scale used by the participants to report the intensity of their pruritus (itch) during the last 24 hours. Participants completed the assessment once daily at home in the evening. Participants were asked the following questions in their local language: 1) For average itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch overall during the previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch at the worst moment during the previous 24 hours?". Where, higher score indicated worst imaginable itch. Missing values including those who took rescue medication were replaced by LOCF approach.

    Time frame: Baseline, Week 4

  2. Percent Change From Baseline in Weekly Average of the Peak Pruritus Numeric Rating Scale Score at Week 4 Using Multiple Imputation (MI) Method

    Pruritus NRS is a scale used by the participants to report the intensity of their pruritus (itch) during the last 24. Participants completed the assessment once daily at home in the evening. Participants were asked the following questions in their local language: 1) For average itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch overall during the previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch at the worst moment during the previous 24 hours?". Where, higher score indicated worst imaginable itch. Multiple imputation generated twenty-five sets of data with missing values imputed from observed data using linear regression.

    Time frame: Baseline, Week 4

  3. Percent Change From Baseline in Weekly Average of the Peak Pruritus Numeric Rating Scale Score at Week 4 Using Observed Data

    Pruritus NRS is a scale used by the participants to report the intensity of their pruritus (itch) during the last 24 hours. Participants completed the assessment once daily at home in the evening. Participants were asked the following questions in their local language: 1) For average itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch overall during the previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch at the worst moment during the previous 24 hours?". Where, higher score indicated worst imaginable itch.

    Time frame: Baseline, Week 4

Secondary outcomes

  1. Percent Change From Baseline in Weekly Average of the Peak Pruritus Numeric Rating Scale Score at Each Visit Using LOCF Approach

    Pruritus NRS is a scale used by the participants to report the intensity of their pruritus (itch) during the last 24 hours. Participants completed the assessment once daily at home in the evening. Participants were asked the following questions in their local language: 1) For average itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch overall during the previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch at the worst moment during the previous 24 hours?". Where, higher score indicated worst imaginable itch. Missing values including those who took rescue medication were replaced by LOCF approach.

    Time frame: Baseline, Weeks 1, 2, 4, 8, 12, 16 and 18

  2. Absolute Change From Baseline in Weekly Average of the Peak Pruritus Numeric Rating Scale Score at Each Visit Using LOCF Approach

    Pruritus NRS is a scale used by the participants to report the intensity of their pruritus (itch) during the last 24 hours. Participants completed the assessment once daily at home in the evening. Participants were asked the following questions in their local language: 1) For average itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch overall during the previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch at the worst moment during the previous 24 hours?". Where, higher score indicated worst imaginable itch. Missing values including those who took rescue medication were replaced by LOCF approach.

    Time frame: Baseline, Weeks 1, 2, 4, 8, 12, 16 and 18

  3. Percent Change From Baseline in Weekly Average of the Average Pruritus Numeric Rating Scale Score at Each Visit Using LOCF Approach

    Pruritus NRS is a scale used by the participants to report the intensity of their pruritus (itch) during the last 24. Participants completed the assessment once daily at home in the evening. Participants were asked the following questions in their local language: 1) For average itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch overall during the previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch at the worst moment during the previous 24 hours?". Where, higher score indicated worst imaginable itch. Missing values including those who took rescue medication were replaced by LOCF approach.

    Time frame: Baseline, Weeks 1, 2, 4, 8, 12, 16 and 18

  4. Absolute Change From Baseline in Weekly Average of the Average Pruritus Numeric Rating Scale Score at Each Visit Using LOCF Approach

    Pruritus NRS is a scale used by the participants to report the intensity of their pruritus (itch) during the last 24 hours. Participants completed the assessment once daily at home in the evening. Participants were asked the following questions in their local language: 1) For average itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch overall during the previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch at the worst moment during the previous 24 hours?". Where, higher score indicated worst imaginable itch. Missing values including those who took rescue medication were replaced by LOCF approach.

    Time frame: Baseline, Weeks 1, 2, 4, 8, 12, 16 and 18

  5. Percent Change From Baseline in Weekly Average of the Peak of Pruritus Verbal Rating Scale (VRS) Score at Each Visit Using LOCF Approach

    VRS consists of a list of adjectives describing different levels of symptom intensity used by participants to report intensity of their pruritus (itch) over last 24 hours. Participants marked on a 5-point VRS (0=no itch, 1=mild itch, 2=moderate itch, 3=severe itch, 4=very severe itch), a response that best described their pruritus intensity in last 24 hours. Participants were asked following questions in their local language: 1) For average itch intensity: "on a scale of 0-4, with 0 being 'no itch' and 4 being 'very severe itch', how would you rate your itch overall during previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0-4, with 0 being 'no itch' and 4 being 'very severe itch', how would you rate your worst itch during previous 24 hours?". Where, higher score indicated very severe itch. Missing values including those who took rescue medication were replaced by LOCF approach.

    Time frame: Baseline, Weeks 1, 2, 4, 8, 12, 16 and 18

  6. Absolute Change From Baseline in Weekly Average of the Peak of Pruritus Verbal Rating Scale Score at Each Visit Using LOCF Approach

    VRS consists of a list of adjectives describing different levels of symptom intensity used by participants to report intensity of their pruritus (itch) over last 24 hours. Participants marked on a 5-point VRS (0=no itch, 1=mild itch, 2=moderate itch, 3=severe itch, 4=very severe itch), a response that best described their pruritus intensity in last 24 hours. Participants were asked following questions in their local language: 1) For average itch intensity: "on a scale of 0-4, with 0 being 'no itch' and 4 being 'very severe itch', how would you rate your itch overall during previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0-4, with 0 being 'no itch' and 4 being 'very severe itch', how would you rate your worst itch during previous 24 hours?". Where, higher score indicated very severe itch. Missing values including those who took rescue medication were replaced by LOCF approach.

    Time frame: Baseline, Weeks 1, 2, 4, 8, 12,16 and 18

  7. Percent Change From Baseline in Weekly Average of the Average Pruritus Verbal Rating Scale Score at Each Visit Using LOCF Approach

    VRS consists of a list of adjectives describing different levels of symptom intensity used by participants to report intensity of their pruritus (itch) over last 24 hours. Participants marked on a 5-point VRS (0=no itch, 1=mild itch, 2=moderate itch, 3=severe itch, 4=very severe itch), a response that best described their pruritus intensity in last 24 hours. Participants were asked following questions in their local language: 1) For average itch intensity: "on a scale of 0-4, with 0 being 'no itch' and 4 being 'very severe itch', how would you rate your itch overall during previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0-4, with 0 being 'no itch' and 4 being 'very severe itch', how would you rate your worst itch during previous 24 hours?". Where, higher score indicated very severe itch. Missing values including those who took rescue medication were replaced by LOCF approach.

    Time frame: Baseline, Weeks 1, 2, 4, 8, 12, 16 and 18

  8. Absolute Change From Baseline in Weekly Average of the Average Verbal Rating Scale Score at Each Visit Using LOCF Approach

    VRS consists of a list of adjectives describing different levels of symptom intensity used by participants to report intensity of their pruritus (itch) over last 24 hours. Participants marked on a 5-point VRS (0=no itch, 1=mild itch, 2=moderate itch, 3=severe itch, 4=very severe itch), a response that best described their pruritus intensity in last 24 hours. Participants were asked following questions in their local language: 1) For average itch intensity: "on a scale of 0-4, with 0 being 'no itch' and 4 being 'very severe itch', how would you rate your itch overall during previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0-4, with 0 being 'no itch' and 4 being 'very severe itch', how would you rate your worst itch during previous 24 hours?". Where, higher score indicated very severe itch. Missing values including those who took rescue medication were replaced by LOCF approach.

    Time frame: Baseline, Weeks 1, 2, 4, 8, 12,16 and 18

  9. Dynamic Pruritus Score (DPS) at 24, 48, and 72 Hours After First Injection and Before Second Injection (Week 4)

    The 9-point DPS is a dynamic scale used by participants to evaluate the change of their pruritus compared with an earlier time point. The scale ranges from 0 (strongly worsened pruritus) to 8 (\[almost\] no pruritus anymore), including intermediate marks for slightly improved/worsened, moderately improved/worsened, and rather improved/worsened. Participants recorded their DPS score in their local language, and completed the assessment 24, 48 and 72 hours after the first injection at baseline and at week 4 before the second injection.

    Time frame: After 24, 48, 72 hours of first Injection and before second injection (Week 4)

  10. Prurigo Activity Score (PAS) Item 5: Overall Number of Prurigo Lesions at Week 12

    PAS includes 7-descriptive items; 1) lesions type (papules nodules/plaques/umbilicated ulcers/ulcers/hypo-/hyperpigmented maculae); 2) number (prurigo lesions on whole body); 3) distribution (disseminated/localized \[only 1/2 areas affected\]/neither of them); 4) affected areas (forearm/upper arm/lower and upper leg/trunk/head); 5) number of prurigo lesions in selected area; 6) activity (prurigo lesions with excoriations/crusts and healed prurigo lesions compared to all prurigo lesions) and 7) front and back, areas of marked monitor lesions to recognize on next visit.

    Time frame: Baseline, Week 12

  11. Prurigo Activity Score (PAS) Item 6: Number of Participants With Defined Stages of Excoriation/Crusts and Healed Lesions at Each Visit

    PAS includes 7-descriptive items; 1) lesions type (papules nodules/plaques/umbilicated ulcers/ulcers/hypo-/hyperpigmented maculae); 2) number (prurigo lesions on whole body); 3) distribution (disseminated/localized \[only 1/2 areas affected\]/neither of them); 4) affected areas (forearm/upper arm/lower and upper leg/trunk/head); 5) number of prurigo lesions in selected area; 6) activity (prurigo lesions with excoriations/crusts and healed prurigo lesions compared to all prurigo lesions) and 7) front and back, areas of marked monitor lesions to recognize on next visit. Item 6 has 5 stages (0-4) where each stage represents percentage of prurigo lesions with excoriations/crusts and healed prurigo lesions compared to all prurigo lesions: excoriations/crusts lesions; stage 0=0%, 1=1-25%, 2=26-50%, 3=51-75%, 4=76-100%; for healed lesions; stage 0=100%, 1=75-99%, 2=50-74%, 3=25-49%, 4=0-24%.

    Time frame: Day 1 (Baseline), Weeks 4, 8, 12 and 18

  12. Investigator Global Assessment (IGA) Score at Each Visit

    IGA is a 5-point scale used by the investigator or trained designee to evaluate the severity of the disease ranging from 0 to 4 where, 0 = clear, 1= almost clear, 2 = mild, 3 = moderate and 4 severe. IGA corresponds to the overall assessment of the severity of prurigo including presence of crust and nodules or skin bleeding. Higher score indicated greater severity of disease.

    Time frame: Day 1 (Baseline), Weeks 4, 8, 12 and 18

  13. Percentage of Participants Achieving Investigator Global Assessment Success (Defined as IGA= 0 [Clear] or IGA = 1 [Almost Clear] With Two-point Improvement From Baseline) at Week 12

    IGA is a 5-point scale used by the investigator or trained designee to evaluate the severity of the disease ranging from 0 to 4 where, 0 = clear, 1= almost clear, 2 = mild, 3 = moderate and 4 severe. IGA corresponds to the overall assessment of the severity of prurigo including presence of crust and nodules or skin bleeding. Higher score indicated greater severity of disease.

    Time frame: Week 12

06

Results

Posted Feb 19, 2020

Participant flow

The study was conducted at 16 sites in 4 countries.

Participant flow — Overall Study
MilestonePlaceboNemolizumab 0.5 mg/kg
Started3634
Treated3634
Completed2931
Not completed73
Withdrew: Adverse event22
Withdrew: Protocol violation10
Withdrew: Withdrawal by subject30
Withdrew: Lost to follow-up11

Outcome measures

PrimaryPercent Change From Baseline in Weekly Average of the Peak Pruritus Numeric Rating Scale (NRS) Score at Week 4 Using Last Observation Carried Forward (LOCF) Approach

Pruritus NRS is a scale used by the participants to report the intensity of their pruritus (itch) during the last 24 hours. Participants completed the assessment once daily at home in the evening. Participants were asked the following questions in their local language: 1) For average itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch overall during the previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch at the worst moment during the previous 24 hours?". Where, higher score indicated worst imaginable itch. Missing values including those who took rescue medication were replaced by LOCF approach.

Time frame:
Baseline, Week 4
Reported as:
Mean · Percent change
Percent Change From Baseline in Weekly Average of the Peak Pruritus Numeric Rating Scale (NRS) Score at Week 4 Using Last Observation Carried Forward (LOCF) Approach
Percent changePlaceboNemolizumab 0.5 mg/kg
Percent Change From Baseline in Weekly Average of the Peak Pruritus Numeric Rating Scale (NRS) Score at Week 4 Using Last Observation Carried Forward (LOCF) Approach-13.8 ± 16.10-52.6 ± 33.96
PrimaryPercent Change From Baseline in Weekly Average of the Peak Pruritus Numeric Rating Scale Score at Week 4 Using Multiple Imputation (MI) Method

Pruritus NRS is a scale used by the participants to report the intensity of their pruritus (itch) during the last 24. Participants completed the assessment once daily at home in the evening. Participants were asked the following questions in their local language: 1) For average itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch overall during the previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch at the worst moment during the previous 24 hours?". Where, higher score indicated worst imaginable itch. Multiple imputation generated twenty-five sets of data with missing values imputed from observed data using linear regression.

Time frame:
Baseline, Week 4
Reported as:
Mean · Percent change
Percent Change From Baseline in Weekly Average of the Peak Pruritus Numeric Rating Scale Score at Week 4 Using Multiple Imputation (MI) Method
Percent changePlaceboNemolizumab 0.5 mg/kg
Percent Change From Baseline in Weekly Average of the Peak Pruritus Numeric Rating Scale Score at Week 4 Using Multiple Imputation (MI) Method-18.3 ± 22.39-52.0 ± 33.94
SecondaryPercent Change From Baseline in Weekly Average of the Peak Pruritus Numeric Rating Scale Score at Each Visit Using LOCF Approach

Pruritus NRS is a scale used by the participants to report the intensity of their pruritus (itch) during the last 24 hours. Participants completed the assessment once daily at home in the evening. Participants were asked the following questions in their local language: 1) For average itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch overall during the previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch at the worst moment during the previous 24 hours?". Where, higher score indicated worst imaginable itch. Missing values including those who took rescue medication were replaced by LOCF approach.

Time frame:
Baseline, Weeks 1, 2, 4, 8, 12, 16 and 18
Reported as:
Mean · percent change
Percent Change From Baseline in Weekly Average of the Peak Pruritus Numeric Rating Scale Score at Each Visit Using LOCF Approach
percent changePlaceboNemolizumab 0.5 mg/kg
Week 1-6.1 ± 11.45-26.0 ± 21.93
Week 2-7.4 ± 14.85-41.7 ± 30.31
Week 4-13.8 ± 16.10-52.6 ± 33.96
Week 8-19.7 ± 20.03-56.5 ± 34.73
Week 12-18.7 ± 22.80-61.8 ± 34.95
Week 16-20.8 ± 22.29-61.1 ± 35.35
Week 18-21.7 ± 22.95-59.6 ± 35.89
SecondaryAbsolute Change From Baseline in Weekly Average of the Peak Pruritus Numeric Rating Scale Score at Each Visit Using LOCF Approach

Pruritus NRS is a scale used by the participants to report the intensity of their pruritus (itch) during the last 24 hours. Participants completed the assessment once daily at home in the evening. Participants were asked the following questions in their local language: 1) For average itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch overall during the previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch at the worst moment during the previous 24 hours?". Where, higher score indicated worst imaginable itch. Missing values including those who took rescue medication were replaced by LOCF approach.

Time frame:
Baseline, Weeks 1, 2, 4, 8, 12, 16 and 18
Reported as:
Mean · Units on a scale
Absolute Change From Baseline in Weekly Average of the Peak Pruritus Numeric Rating Scale Score at Each Visit Using LOCF Approach
Units on a scalePlaceboNemolizumab 0.5 mg/kg
Week 1-0.5 ± 0.87-2.1 ± 1.66
Week 2-0.6 ± 1.21-3.4 ± 2.38
Week 4-1.2 ± 1.33-4.3 ± 2.77
Week 8-1.6 ± 1.62-4.7 ± 2.90
Week 12-1.5 ± 1.84-5.1 ± 2.95
Week 16-1.7 ± 1.81-5.1 ± 3.00
Week 18-1.8 ± 1.87-4.9 ± 3.07
SecondaryPercent Change From Baseline in Weekly Average of the Average Pruritus Numeric Rating Scale Score at Each Visit Using LOCF Approach

Pruritus NRS is a scale used by the participants to report the intensity of their pruritus (itch) during the last 24. Participants completed the assessment once daily at home in the evening. Participants were asked the following questions in their local language: 1) For average itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch overall during the previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch at the worst moment during the previous 24 hours?". Where, higher score indicated worst imaginable itch. Missing values including those who took rescue medication were replaced by LOCF approach.

Time frame:
Baseline, Weeks 1, 2, 4, 8, 12, 16 and 18
Reported as:
Mean · Percent change
Percent Change From Baseline in Weekly Average of the Average Pruritus Numeric Rating Scale Score at Each Visit Using LOCF Approach
Percent changePlaceboNemolizumab 0.5 mg/kg
Week 1-7.5 ± 12.82-26.6 ± 21.25
Week 2-9.6 ± 15.28-44.0 ± 29.54
Week 4-16.5 ± 18.25-53.4 ± 33.23
Week 8-24.6 ± 23.38-57.3 ± 34.78
Week 12-23.0 ± 26.31-62.6 ± 34.98
Week 16-25.9 ± 24.89-62.4 ± 35.93
Week 18-26.2 ± 25.39-60.4 ± 36.15
SecondaryAbsolute Change From Baseline in Weekly Average of the Average Pruritus Numeric Rating Scale Score at Each Visit Using LOCF Approach

Pruritus NRS is a scale used by the participants to report the intensity of their pruritus (itch) during the last 24 hours. Participants completed the assessment once daily at home in the evening. Participants were asked the following questions in their local language: 1) For average itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch overall during the previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch at the worst moment during the previous 24 hours?". Where, higher score indicated worst imaginable itch. Missing values including those who took rescue medication were replaced by LOCF approach.

Time frame:
Baseline, Weeks 1, 2, 4, 8, 12, 16 and 18
Reported as:
Mean · Units on a scale
Absolute Change From Baseline in Weekly Average of the Average Pruritus Numeric Rating Scale Score at Each Visit Using LOCF Approach
Units on a scalePlaceboNemolizumab 0.5 mg/kg
Week 1-0.5 ± 0.82-1.9 ± 1.47
Week 2-0.8 ± 1.14-3.2 ± 2.03
Week 4-1.3 ± 1.41-3.9 ± 2.44
Week 8-1.9 ± 1.80-4.2 ± 2.60
Week 12-1.8 ± 2.05-4.6 ± 2.71
Week 16-2.0 ± 1.97-4.6 ± 2.86
Week 18-2.1 ± 2.02-4.5 ± 2.94
SecondaryPercent Change From Baseline in Weekly Average of the Peak of Pruritus Verbal Rating Scale (VRS) Score at Each Visit Using LOCF Approach

VRS consists of a list of adjectives describing different levels of symptom intensity used by participants to report intensity of their pruritus (itch) over last 24 hours. Participants marked on a 5-point VRS (0=no itch, 1=mild itch, 2=moderate itch, 3=severe itch, 4=very severe itch), a response that best described their pruritus intensity in last 24 hours. Participants were asked following questions in their local language: 1) For average itch intensity: "on a scale of 0-4, with 0 being 'no itch' and 4 being 'very severe itch', how would you rate your itch overall during previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0-4, with 0 being 'no itch' and 4 being 'very severe itch', how would you rate your worst itch during previous 24 hours?". Where, higher score indicated very severe itch. Missing values including those who took rescue medication were replaced by LOCF approach.

Time frame:
Baseline, Weeks 1, 2, 4, 8, 12, 16 and 18
Reported as:
Mean · Percent change
Percent Change From Baseline in Weekly Average of the Peak of Pruritus Verbal Rating Scale (VRS) Score at Each Visit Using LOCF Approach
Percent changePlaceboNemolizumab 0.5 mg/kg
Week 1-9.8 ± 14.24-27.6 ± 17.21
Week 2-12.3 ± 17.64-39.1 ± 25.38
Week 4-15.6 ± 20.95-50.7 ± 29.37
Week 8-20.7 ± 21.22-54.3 ± 30.61
Week 12-19.4 ± 23.60-56.9 ± 32.64
Week 16-21.2 ± 22.24-55.6 ± 34.48
Week 18-23.0 ± 21.97-53.4 ± 36.56
SecondaryAbsolute Change From Baseline in Weekly Average of the Peak of Pruritus Verbal Rating Scale Score at Each Visit Using LOCF Approach

VRS consists of a list of adjectives describing different levels of symptom intensity used by participants to report intensity of their pruritus (itch) over last 24 hours. Participants marked on a 5-point VRS (0=no itch, 1=mild itch, 2=moderate itch, 3=severe itch, 4=very severe itch), a response that best described their pruritus intensity in last 24 hours. Participants were asked following questions in their local language: 1) For average itch intensity: "on a scale of 0-4, with 0 being 'no itch' and 4 being 'very severe itch', how would you rate your itch overall during previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0-4, with 0 being 'no itch' and 4 being 'very severe itch', how would you rate your worst itch during previous 24 hours?". Where, higher score indicated very severe itch. Missing values including those who took rescue medication were replaced by LOCF approach.

Time frame:
Baseline, Weeks 1, 2, 4, 8, 12,16 and 18
Reported as:
Mean · Units on a scale
Absolute Change From Baseline in Weekly Average of the Peak of Pruritus Verbal Rating Scale Score at Each Visit Using LOCF Approach
Units on a scalePlaceboNemolizumab 0.5 mg/kg
Week 1-0.3 ± 0.47-0.9 ± 0.57
Week 2-0.4 ± 0.61-1.3 ± 0.83
Week 4-0.6 ± 0.74-1.6 ± 1.00
Week 8-0.7 ± 0.74-1.8 ± 1.06
Week 12-0.7 ± 0.83-1.8 ± 1.09
Week 16-0.7 ± 0.78-1.8 ± 1.16
Week 18-0.8 ± 0.77-1.7 ± 1.26
SecondaryPercent Change From Baseline in Weekly Average of the Average Pruritus Verbal Rating Scale Score at Each Visit Using LOCF Approach

VRS consists of a list of adjectives describing different levels of symptom intensity used by participants to report intensity of their pruritus (itch) over last 24 hours. Participants marked on a 5-point VRS (0=no itch, 1=mild itch, 2=moderate itch, 3=severe itch, 4=very severe itch), a response that best described their pruritus intensity in last 24 hours. Participants were asked following questions in their local language: 1) For average itch intensity: "on a scale of 0-4, with 0 being 'no itch' and 4 being 'very severe itch', how would you rate your itch overall during previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0-4, with 0 being 'no itch' and 4 being 'very severe itch', how would you rate your worst itch during previous 24 hours?". Where, higher score indicated very severe itch. Missing values including those who took rescue medication were replaced by LOCF approach.

Time frame:
Baseline, Weeks 1, 2, 4, 8, 12, 16 and 18
Reported as:
Mean · percent change
Percent Change From Baseline in Weekly Average of the Average Pruritus Verbal Rating Scale Score at Each Visit Using LOCF Approach
percent changePlaceboNemolizumab 0.5 mg/kg
Week 1-10.5 ± 19.72-29.6 ± 16.90
Week 2-13.0 ± 19.20-42.9 ± 24.22
Week 4-16.4 ± 24.10-52.1 ± 27.63
Week 8-23.5 ± 22.89-55.4 ± 30.63
Week 12-21.9 ± 25.90-62.1 ± 29.98
Week 16-25.1 ± 24.15-62.0 ± 32.48
Week 18-26.2 ± 24.40-58.7 ± 34.81
SecondaryAbsolute Change From Baseline in Weekly Average of the Average Verbal Rating Scale Score at Each Visit Using LOCF Approach

VRS consists of a list of adjectives describing different levels of symptom intensity used by participants to report intensity of their pruritus (itch) over last 24 hours. Participants marked on a 5-point VRS (0=no itch, 1=mild itch, 2=moderate itch, 3=severe itch, 4=very severe itch), a response that best described their pruritus intensity in last 24 hours. Participants were asked following questions in their local language: 1) For average itch intensity: "on a scale of 0-4, with 0 being 'no itch' and 4 being 'very severe itch', how would you rate your itch overall during previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0-4, with 0 being 'no itch' and 4 being 'very severe itch', how would you rate your worst itch during previous 24 hours?". Where, higher score indicated very severe itch. Missing values including those who took rescue medication were replaced by LOCF approach.

Time frame:
Baseline, Weeks 1, 2, 4, 8, 12,16 and 18
Reported as:
Mean · Units on a scale
Absolute Change From Baseline in Weekly Average of the Average Verbal Rating Scale Score at Each Visit Using LOCF Approach
Units on a scalePlaceboNemolizumab 0.5 mg/kg
Week 1-0.4 ± 0.50-0.9 ± 0.49
Week 2-0.4 ± 0.61-1.3 ± 0.68
Week 4-0.6 ± 0.73-1.6 ± 0.84
Week 8-0.7 ± 0.72-1.7 ± 0.96
Week 12-0.7 ± 0.82-1.9 ± 0.94
Week 16-0.8 ± 0.78-1.9 ± 1.06
Week 18-0.8 ± 0.79-1.8 ± 1.16
SecondaryDynamic Pruritus Score (DPS) at 24, 48, and 72 Hours After First Injection and Before Second Injection (Week 4)

The 9-point DPS is a dynamic scale used by participants to evaluate the change of their pruritus compared with an earlier time point. The scale ranges from 0 (strongly worsened pruritus) to 8 (\[almost\] no pruritus anymore), including intermediate marks for slightly improved/worsened, moderately improved/worsened, and rather improved/worsened. Participants recorded their DPS score in their local language, and completed the assessment 24, 48 and 72 hours after the first injection at baseline and at week 4 before the second injection.

Time frame:
After 24, 48, 72 hours of first Injection and before second injection (Week 4)
Reported as:
Mean · Units on a scale
Dynamic Pruritus Score (DPS) at 24, 48, and 72 Hours After First Injection and Before Second Injection (Week 4)
Units on a scalePlaceboNemolizumab 0.5 mg/kg
First injection, after 24 hours4.3 ± 0.965.0 ± 1.20
First injection, after 48 hours4.0 ± 1.695.3 ± 1.40
First injection, after 72 hours4.0 ± 1.375.7 ± 1.34
Before Second Injection (Week 4)4.4 ± 1.076.3 ± 1.89
SecondaryPrurigo Activity Score (PAS) Item 5: Overall Number of Prurigo Lesions at Week 12

PAS includes 7-descriptive items; 1) lesions type (papules nodules/plaques/umbilicated ulcers/ulcers/hypo-/hyperpigmented maculae); 2) number (prurigo lesions on whole body); 3) distribution (disseminated/localized \[only 1/2 areas affected\]/neither of them); 4) affected areas (forearm/upper arm/lower and upper leg/trunk/head); 5) number of prurigo lesions in selected area; 6) activity (prurigo lesions with excoriations/crusts and healed prurigo lesions compared to all prurigo lesions) and 7) front and back, areas of marked monitor lesions to recognize on next visit.

Time frame:
Baseline, Week 12
Reported as:
Mean · Prurigo Lesions
Prurigo Activity Score (PAS) Item 5: Overall Number of Prurigo Lesions at Week 12
Prurigo LesionsPlaceboNemolizumab 0.5 mg/kg
Baseline87.1 ± 5.4284.9 ± 5.50
Week 1274.2 ± 6.8354.8 ± 6.42
SecondaryPrurigo Activity Score (PAS) Item 6: Number of Participants With Defined Stages of Excoriation/Crusts and Healed Lesions at Each Visit

PAS includes 7-descriptive items; 1) lesions type (papules nodules/plaques/umbilicated ulcers/ulcers/hypo-/hyperpigmented maculae); 2) number (prurigo lesions on whole body); 3) distribution (disseminated/localized \[only 1/2 areas affected\]/neither of them); 4) affected areas (forearm/upper arm/lower and upper leg/trunk/head); 5) number of prurigo lesions in selected area; 6) activity (prurigo lesions with excoriations/crusts and healed prurigo lesions compared to all prurigo lesions) and 7) front and back, areas of marked monitor lesions to recognize on next visit. Item 6 has 5 stages (0-4) where each stage represents percentage of prurigo lesions with excoriations/crusts and healed prurigo lesions compared to all prurigo lesions: excoriations/crusts lesions; stage 0=0%, 1=1-25%, 2=26-50%, 3=51-75%, 4=76-100%; for healed lesions; stage 0=100%, 1=75-99%, 2=50-74%, 3=25-49%, 4=0-24%.

Time frame:
Day 1 (Baseline), Weeks 4, 8, 12 and 18
Reported as:
Count of participants · Participants
Prurigo Activity Score (PAS) Item 6: Number of Participants With Defined Stages of Excoriation/Crusts and Healed Lesions at Each Visit
ParticipantsPlaceboNemolizumab 0.5 mg/kg
Excoriation/Crusts: Day 1: Stage 000
Excoriation/Crusts: Day 1: Stage 124
Excoriation/Crusts: Day 1: Stage 275
Excoriation/Crusts: Day 1: Stage 31412
Excoriation/Crusts: Day 1: Stage 41313
Excoriation/Crusts: Week 4: Stage 022
Excoriation/Crusts: Week 4: Stage 1610
Excoriation/Crusts: Week 4: Stage 279
Excoriation/Crusts: Week 4: Stage 3109
Excoriation/Crusts: Week 4: Stage 493
Excoriation/Crusts: Week 8: Stage 024
Excoriation/Crusts: Week 8: Stage 1513
Excoriation/Crusts: Week 8: Stage 276
Excoriation/Crusts: Week 8: Stage 3119
Excoriation/Crusts: Week 8: Stage 470
Excoriation/CrustsWeek 12: Stage 013
Excoriation/Crusts: Week 12: Stage 1717
Excoriation/Crusts: Week 12: Stage 259
Excoriation/Crusts: Week 12: Stage 3123
Excoriation/Crusts: Week 12: Stage 450
Excoriation/Crusts: Week 18: Stage 016
Excoriation/Crusts: Week 18: Stage 1412
Excoriation/Crusts: Week 18: Stage 284
Excoriation/Crusts: Week 18: Stage 3115
Excoriation/Crusts: Week 18: Stage 464
Healed Lesions: Day 1: Stage 010
Healed Lesions: Day 1: Stage 101
Healed Lesions: Day 1: Stage 235
Healed Lesions: Day 1: Stage 3139
Healed Lesions: Day 1: Stage 41919
Healed Lesions: Week 4: Stage 023
Healed Lesions: Week 4: Stage 125
Healed Lesions: Week 4: Stage 265
Healed Lesions: Week 4: Stage 31114
Healed Lesions: Week 4: Stage 4136
Healed Lesions: Week 8: Stage 023
Healed Lesions: Week 8: Stage 138
Healed Lesions: Week 8: Stage 278
Healed Lesions: Week 8: Stage 3912
Healed Lesions: Week 8: Stage 4111
Healed Lesions: Week 12: Stage 012
Healed Lesions: Week 12: Stage 129
Healed Lesions: Week 12: Stage 2716
Healed Lesions: Week 12: Stage 385
Healed Lesions: Week 12: Stage 4120
Healed Lesions: Week 18: Stage 013
Healed Lesions: Week 18: Stage 1212
Healed Lesions: Week 18: Stage 277
Healed Lesions: Week 18: Stage 385
Healed Lesions: Week 18: Stage 4124
SecondaryInvestigator Global Assessment (IGA) Score at Each Visit

IGA is a 5-point scale used by the investigator or trained designee to evaluate the severity of the disease ranging from 0 to 4 where, 0 = clear, 1= almost clear, 2 = mild, 3 = moderate and 4 severe. IGA corresponds to the overall assessment of the severity of prurigo including presence of crust and nodules or skin bleeding. Higher score indicated greater severity of disease.

Time frame:
Day 1 (Baseline), Weeks 4, 8, 12 and 18
Reported as:
Mean · Units on a scale
Investigator Global Assessment (IGA) Score at Each Visit
Units on a scalePlaceboNemolizumab 0.5 mg/kg
Day 1 (Baseline)3.4 ± 0.493.5 ± 0.51
Week 43.3 ± 0.612.8 ± 0.81
Week 83.1 ± 0.672.4 ± 0.80
Week 122.8 ± 0.822.0 ± 0.80
Week 183.0 ± 0.932.0 ± 1.11
SecondaryPercentage of Participants Achieving Investigator Global Assessment Success (Defined as IGA= 0 [Clear] or IGA = 1 [Almost Clear] With Two-point Improvement From Baseline) at Week 12

IGA is a 5-point scale used by the investigator or trained designee to evaluate the severity of the disease ranging from 0 to 4 where, 0 = clear, 1= almost clear, 2 = mild, 3 = moderate and 4 severe. IGA corresponds to the overall assessment of the severity of prurigo including presence of crust and nodules or skin bleeding. Higher score indicated greater severity of disease.

Time frame:
Week 12
Reported as:
Number · percentage of participants
Percentage of Participants Achieving Investigator Global Assessment Success (Defined as IGA= 0 [Clear] or IGA = 1 [Almost Clear] With Two-point Improvement From Baseline) at Week 12
percentage of participantsPlaceboNemolizumab 0.5 mg/kg
Percentage of Participants Achieving Investigator Global Assessment Success (Defined as IGA= 0 [Clear] or IGA = 1 [Almost Clear] With Two-point Improvement From Baseline) at Week 122.820.6
PrimaryPercent Change From Baseline in Weekly Average of the Peak Pruritus Numeric Rating Scale Score at Week 4 Using Observed Data

Pruritus NRS is a scale used by the participants to report the intensity of their pruritus (itch) during the last 24 hours. Participants completed the assessment once daily at home in the evening. Participants were asked the following questions in their local language: 1) For average itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch overall during the previous 24 hours?"; 2) For maximum itch intensity: "on a scale of 0 to 10, with 0 being 'no itch' and 10 being 'worst itch imaginable', how would you rate your itch at the worst moment during the previous 24 hours?". Where, higher score indicated worst imaginable itch.

Time frame:
Baseline, Week 4
Reported as:
Mean · Percent change
Percent Change From Baseline in Weekly Average of the Peak Pruritus Numeric Rating Scale Score at Week 4 Using Observed Data
Percent changePlaceboNemolizumab 0.5 mg/kg
Percent Change From Baseline in Weekly Average of the Peak Pruritus Numeric Rating Scale Score at Week 4 Using Observed Data-15.2 ± 17.42-54.9 ± 33.80

Adverse events

Collected over Up to 18 Weeks. Non-serious events are listed at a 5% frequency threshold.

Adverse event summary by group
GroupDeathsSeriousOther
Placebo0/36 (0%)3/36 (8.3%)22/36 (61.1%)
Nemolizumab 0.5 mg/kg0/34 (0%)4/34 (11.8%)26/34 (76.5%)
Most frequent serious events
Most frequent serious events
EventPlaceboNemolizumab 0.5 mg/kg
NeurodermatitisSkin and subcutaneous tissue disorders3/360/34
Dermatitis PsoriasiformSkin and subcutaneous tissue disorders0/361/34
Eczema NummularSkin and subcutaneous tissue disorders0/361/34
Clavicle FractureInjury, poisoning and procedural complications0/361/34
FibromyalgiaMusculoskeletal and connective tissue disorders0/361/34
Calculus BladderRenal and urinary disorders0/361/34
Spinal FractureInjury, poisoning and procedural complications1/360/34
Back PainMusculoskeletal and connective tissue disorders1/360/34
Most frequent other events
Showing 10 of 16
Most frequent other events
EventPlaceboNemolizumab 0.5 mg/kg
NasopharyngitisInfections and infestations4/365/34
NeurodermatitisSkin and subcutaneous tissue disorders5/362/34
ConjunctivitisInfections and infestations2/363/34
Dermatitis AtopicSkin and subcutaneous tissue disorders0/363/34
BronchitisInfections and infestations0/362/34
Dermatitis ContactSkin and subcutaneous tissue disorders0/362/34
Abdominal PainGastrointestinal disorders0/362/34
DiarrhoeaGastrointestinal disorders0/362/34
LymphadenopathyBlood and lymphatic system disorders0/362/34
Increased AppetiteMetabolism and nutrition disorders0/362/34

Baseline characteristics

Analysis was performed on all randomized participants.

Age, Continuous
Age, Continuous(years)PlaceboNemolizumab 0.5 mg/kgTotal
Mean52.4 ± 17.4759.7 ± 13.1656.0 ± 15.85
Sex: Female, Male
Sex: Female, Male(Participants)PlaceboNemolizumab 0.5 mg/kgTotal
Female221941
Male141529
Race (NIH/OMB)
Race (NIH/OMB)(Participants)PlaceboNemolizumab 0.5 mg/kgTotal
American Indian or Alaska Native000
Asian000
Native Hawaiian or Other Pacific Islander000
Black or African American112
White353368
More than one race000
Unknown or Not Reported000
Presence or absence of background of atopy
Presence or absence of background of atopy(Participants)PlaceboNemolizumab 0.5 mg/kgTotal
Presence6511
Absence302959
07

Study locations

16 sites
  • LKH-Univ. Klinikum Graz
    Graz, Austria
  • Centre-Hospitalier Universitaire (CHU) - Hopital Morvan - Br
    Brest, France
  • CHU de Nice - Hôpital Archet 2
    Nice, France
  • Hopital Saint-Louis - Dermatology
    Paris, France
  • Centre Hospitalier Universitaire De Toulouse
    Toulouse, France
  • Charite - Campus Charite Mitte (CCM) - Dermatologie & Allergologie - Dermatologie & Allergologie
    Berlin, Germany
  • Universitätsklinikum Bonn AöR
    Bonn, Germany
  • Klinikum der Johann-Wolfgang Goethe-Universität
    Frankfurt, Germany
  • Unikl. Schleswig-Holstein - Lübeck
    Lubeck, Germany
  • Universitätsmedizin Mainz
    Mainz, Germany
  • Klinikum Der Universität München - Campus Innenstadt - Dermatologie und Allergologie
    München, Germany
  • Universitätsklinikum Münster
    Münster, Germany
  • Eberhard-Karls Universitaet Tuebingen - Universitaets Hautkl
    Tuebingen, Germany
  • Kliniczny Szpital Wojew. nr 1 im. F.Chopina w Rzeszowie
    Rzeszów, Poland
  • Centrum Medyczne DERMED
    Łódź, Poland
  • Dermoklinika Centrum Medyczne s.c. M.Kierstan, J.Narbutt, A.Lesiak
    Łódź, Poland
08

References and documents

Publications

  • Stander S, Yosipovitch G, Legat FJ, Lacour JP, Paul C, Narbutt J, Bieber T, Misery L, Wollenberg A, Reich A, Ahmad F, Piketty C. Trial of Nemolizumab in Moderate-to-Severe Prurigo Nodularis. N Engl J Med. 2020 Feb 20;382(8):706-716. doi: 10.1056/NEJMoa1908316. PubMed 32074418 ↗

Study documents

  • Study protocol · May 30, 2017
  • Statistical analysis plan · May 21, 2019

Documents are hosted by the registry — open the source record to download them.

Individual participant data

Plan to share: No

09

Registry details

Key details

Study ID
NCT03181503
Lead sponsor
Galderma R&D
Responsible party
Sponsor
First posted
Jun 8, 2017
Start date
Oct 2, 2017
Primary completion
Sep 26, 2018
Completion
Sep 26, 2018
Results posted
Feb 19, 2020
Last update
Feb 19, 2020

Oversight

Data monitoring committee
No
FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

Not currently enrolling

This study is completed, as verified in Nov 2019. You cannot join it, but the record below documents what was studied.

Follow this study

Get an email when the registry record changes — status, dates, results — or when someone posts here.

Sign in to follow

Discussion

Questions and observations about this study, from anyone following it. Not medical advice, and not a channel to the study team — their contact details are on the registry record.

Sign in to join the discussion. Reading takes no account; posting does. You choose a display name, and a pseudonym is the default.

Nothing here yet. If you are running this trial, taking part in it, or weighing whether to, this is the place to say so.

Start the discussion