CClinicalTrials.gg
CompletedNCT01617005Updated Dec 1, 2016Results posted

A Study of Tocilizumab in Participants With Active Rheumatoid Arthritis (RA) and an Inadequate Response to Non-Biological Disease-modifying Anti-rheumatic Drugs (DMARDs)

An observational study in Rheumatoid Arthritis, sponsored by Hoffmann-La Roche. Completed at 1 site in Montenegro. Open to participants aged 18 Years and older. Per ClinicalTrials.gov, last updated 2016-12-01.

Sponsored by Hoffmann-La Roche · Observational

Study type
Observational
Model
Cohort
Time perspective
Prospective
Enrollment
50
Ages
18 Years and older
Sex
All
01

Study summary

This observational study will evaluate the safety and efficacy of tocilizumab in participants with active moderate to severe RA and an inadequate response to non-biologic DMARDs. Data will be collected from each eligible participant initiating tocilizumab treatment over 6 months.

02

Conditions studied

  • Rheumatoid Arthritis
03

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All
Accepts healthy volunteers
No
Sampling method
Non-probability sample

Study population

Participants with RA and an inadequate response to non-biologic DMARDs.

Inclusion criteria

  • Moderate to severe active RA (European League Against Rheumatism [EULAR] criteria)
  • Inadequate response to DMARDs or tumor necrosis factor (TNF) antagonists
  • Initiating treatment with tocilizumab according to SPC

Exclusion criteria

Exclusion Criteria:

  • Rheumatic autoimmune disease other than RA
  • Prior history or current inflammatory joint disease other than RA
  • Previous treatment with any biological drug used in the treatment of RA
  • Previous treatment with tocilizumab
  • Any contraindication to treatment with tocilizumab
  • Major surgery (including joint surgery) within 8 weeks prior to screening or planned major surgery within 6 months following enrollment
  • Pregnant women or nursing (breastfeeding) mothers
04

Study design

Observational model
Cohort
Time perspective
Prospective
Enrollment
50 participants (actual)

Groups and cohorts

  • Tocilizumab in Moderate to Severe Active RA

    Moderate to severe active RA participants, receiving tocilizumab treatment according to effective official Summary of Product Characteristics (SPC), will be observed. The choice of therapy will be based exclusively on the medical decision of the treating physician before study enrollment. The study protocol does not enforce treatment initiation and also does not specify any treatment regimen.

    Drug: Tocilizumab

Interventions

  • DrugTocilizumab

    Participants will receive tocilizumab treatment according to effective official SPC. The study protocol does not enforce treatment initiation and also does not specify any treatment regimen.

    Also known as: RoActemra, L04AC07

05

What researchers measure

Primary outcomes

  1. Number of Participants With Adverse Events (AEs) and Serious AEs (SAEs)

    An AE was any untoward medical occurrence in a participant who received study drug without regard to possibility of causal relationship. A SAE was an AE resulting in any of the following outcomes or deemed significant for any other reason: death; initial or prolonged inpatient hospitalization; life-threatening experience (immediate risk of dying); persistent or significant disability/incapacity; congenital anomaly. AEs include both SAEs as well as non-serious AEs.

    Time frame: Baseline up to Week 24

Secondary outcomes

  1. Number of Participants With Good or Moderate Response According to European League Against Rheumatism (EULAR) Criteria

    EULAR response was based on 28-joint disease activity score (DAS28). The DAS28-based EULAR response criteria were used to measure individual response as none, good, and moderate, depending on the extent of change from baseline (CFB) in DAS28 score and the level of disease activity reached (absolute DAS28 score). Good responders had a CFB greater than (\>) 1.2 with a DAS28 score less than or equal to (\<=) 3.2; moderate responders had a CFB \>1.2 with a DAS28 score \>3.2 to \<= 5.1 or a change from baseline \>0.6 to \<= 1.2 with a DAS28 score \<= 5.1; non-responders had a CFB \<=0.6 or CFB \>0.6 to \<=1.2 with DAS28 \>5.1. Number of participants who achieved EULAR good response and EULAR moderate response were reported.

    Time frame: Baseline, Week 24

  2. Number of Participants Who Discontinued Treatment Due to Lack of Efficacy

    Time frame: Baseline up to Week 24

  3. Time to Discontinuation Due to Lack of Efficacy

    Time frame: Baseline up to Week 24

06

Results

Posted Dec 1, 2016

Participant flow

Participant flow — Overall Study
MilestoneTocilizumab in Moderate to Severe Active RA
Started50
Completed48
Not completed2
Withdrew: Pregnancy1
Withdrew: Lack of motivation for treatment1

Outcome measures

PrimaryNumber of Participants With Adverse Events (AEs) and Serious AEs (SAEs)

An AE was any untoward medical occurrence in a participant who received study drug without regard to possibility of causal relationship. A SAE was an AE resulting in any of the following outcomes or deemed significant for any other reason: death; initial or prolonged inpatient hospitalization; life-threatening experience (immediate risk of dying); persistent or significant disability/incapacity; congenital anomaly. AEs include both SAEs as well as non-serious AEs.

Time frame:
Baseline up to Week 24
Reported as:
Number · participants
Number of Participants With Adverse Events (AEs) and Serious AEs (SAEs)
participantsTocilizumab in Moderate to Severe Active RA
SAEs0
AEs38
SecondaryNumber of Participants With Good or Moderate Response According to European League Against Rheumatism (EULAR) Criteria

EULAR response was based on 28-joint disease activity score (DAS28). The DAS28-based EULAR response criteria were used to measure individual response as none, good, and moderate, depending on the extent of change from baseline (CFB) in DAS28 score and the level of disease activity reached (absolute DAS28 score). Good responders had a CFB greater than (\>) 1.2 with a DAS28 score less than or equal to (\<=) 3.2; moderate responders had a CFB \>1.2 with a DAS28 score \>3.2 to \<= 5.1 or a change from baseline \>0.6 to \<= 1.2 with a DAS28 score \<= 5.1; non-responders had a CFB \<=0.6 or CFB \>0.6 to \<=1.2 with DAS28 \>5.1. Number of participants who achieved EULAR good response and EULAR moderate response were reported.

Time frame:
Baseline, Week 24
Reported as:
Number · participants
Number of Participants With Good or Moderate Response According to European League Against Rheumatism (EULAR) Criteria
participantsTocilizumab in Moderate to Severe Active RA
EULAR Good Response0
EULAR Moderate Response40
SecondaryNumber of Participants Who Discontinued Treatment Due to Lack of Efficacy
Time frame:
Baseline up to Week 24
Reported as:
Number · participants
Number of Participants Who Discontinued Treatment Due to Lack of Efficacy
participantsTocilizumab in Moderate to Severe Active RA
Number of Participants Who Discontinued Treatment Due to Lack of Efficacy0
SecondaryTime to Discontinuation Due to Lack of Efficacy
Time frame:
Baseline up to Week 24

No measurements were reported for this outcome.

Adverse events

Collected over Baseline up to Week 24. Non-serious events are listed at a 0% frequency threshold.

Adverse event summary by group
GroupDeathsSeriousOther
Tocilizumab in Moderate to Severe Active RA—0/50 (0%)38/50 (76%)
Most frequent other events
Showing 10 of 20
Most frequent other events
EventTocilizumab in Moderate to Severe Active RA
NeutropeniaBlood and lymphatic system disorders15/50
Hepatic transaminases increasedInvestigations10/50
HypercholesterolemiaMetabolism and nutrition disorders9/50
Leukopenia with neutropeniaBlood and lymphatic system disorders8/50
HypertensionVascular disorders2/50
PancytopeniaBlood and lymphatic system disorders2/50
LeukopeniaBlood and lymphatic system disorders2/50
ThrombocytopeniaBlood and lymphatic system disorders2/50
LeukocytosisBlood and lymphatic system disorders1/50
GastralgiaGastrointestinal disorders1/50

Baseline characteristics

All participants who were enrolled in the study.

Age, Continuous
Age, Continuous(years)Tocilizumab in Moderate to Severe Active RA
Mean51.9 ± 11.1
Sex: Female, Male
Sex: Female, Male(Participants)Tocilizumab in Moderate to Severe Active RA
Female41
Male9
07

Study locations

1 site
  • Podgorica, 81000, Montenegro
08

Registry details

Key details

Study ID
NCT01617005
Lead sponsor
Hoffmann-La Roche
Responsible party
Sponsor
First posted
Jun 12, 2012
Start date
May 2012
Primary completion
Sep 2014
Completion
Sep 2014
Results posted
Dec 1, 2016
Last update
Dec 1, 2016

Study contacts

Clinical Trials
study director · Hoffmann-La Roche

Oversight

Data monitoring committee
No
View the source record on ClinicalTrials.gov ↗

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