Duke University: Glycogen Storage Disease Type II trials
The registry lists 13 Glycogen Storage Disease Type II studies with Duke University as lead sponsor. 2 are open to participants now and 1 have results posted.
Phase 1 2Phase 2 2No phase 10(a study in two phases counts in both)
Studies
Open to participants first, then studies with results posted, then the rest; newest registration first within each.
- Cognitive and Neurological Pathologies in Pompe DiseaseRecruitingNCT04639336
- Determination of CRIM Status and Longitudinal Follow-up of Individuals With Pompe DiseaseRecruitingNCT01665326
- Safety and Efficacy of Albuterol in Individuals With Late-onset Pompe DiseaseCompletedNCT01885936Phase 1/2Results posted
- Phase II Clinical Trial of Clenbuterol in Adult Patients With Pompe DiseaseWithdrawnNCT04094948Phase 2
- Developing a Management Approach for Patients With "Late-Onset" Pompe DiseaseActive, not recruitingNCT03694561
- Pompe Gene Therapy- Screening for EligibilityCompletedNCT03285126
- Lingual Muscle Training in Late-Onset Pompe Disease (LOPD)CompletedNCT03255213Not applicable
- Pompe Telemedicine Developmental StudyCompletedNCT02950298
- Respiratory Muscle Training in L-Onset Pompe Disease (LOPD)CompletedNCT02801539Not applicable
- Identification of Tongue Involvement in Late-Onset Pompe DiseaseCompletedNCT02765828
- Pompe Disease QMUS and EIMCompletedNCT02742298Not applicable
- Albuterol in Individuals With Late Onset Pompe Disease (LOPD)CompletedNCT01859624Phase 1
- The Effects of Respiratory Muscle Strength Training (RMST) on Inspiratory and Expiratory Muscle Strength in Adults and Children With Pompe DiseaseCompletedNCT01701154