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Biological

NTLA-2001 clinical trials

Also written NTLA-2001.

studies test it
3
open now
1
in phase 3
2
first study started
2020

How each study uses NTLA-2001 is sorted by a rule, right about nine times in ten. Readers can ask us to read every study one by one.Ask us to read each study

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Breast cancer · Recruiting: 2 came in, 3 changed

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Approvals

The first approval found in each region, with its record

United States
Not in FDA's approval records
European Union
Not in EMA's list of EU-wide authorisations

From FDA's Drugs@FDA and Purple Book (through openFDA) and the European Medicines Agency, files of Sept 2026 and 27 Oct 2026. National approvals in Europe and other countries are not included. How this is worked out

How studies write it

Studies that test it under each name

Development codes

NTLA-2001
3

Studies by the year they started

3 studies that test it; most in 2020 (1)

Studies that test NTLA-2001, by start year
YearStudies
20201
20231
20241

By phase

A phase 1/2 study counts in both.

Phase 1
1
Phase 3
2

What it is tested for

Each study’s main condition, where its own words name it, so a study counts once.

Peripheral Nervous System Diseases
1
Amyloid Neuropathies, Familial
1
Amyloidosis, Hereditary, Transthyretin-Related
1

Who runs them

Industry 3 · Other 0

Intellia Therapeutics (3)

Coming up

From the study records. Dates are the sponsors’ own estimates and often move.

Reaching primary completion within a year · 1, 1 in phase 3

Studies that test NTLA-2001, phase 3 first.

Studies

Open first, then newest update. How each study uses NTLA-2001 is read from its arms, and is right about nine times in ten. Ask us to read each study. These are the studies that list it as an intervention; a search of ClinicalTrials.gov also finds studies that mention it only in a description, such as earlier treatment.

Testing it · 3

Codes

What other systems call NTLA-2001 · ClinicalTrials.gg INT001698

  • MeSH (NLM) C000718870NTLA-2001One source ClinicalTrials.gov

“Confirmed” means two independent publishers link the code to this drug; “one source”, one does and its name agrees.