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Prader-Willi Syndrome clinical trials

The registry lists 144 studies for Prader-Willi Syndrome across more than 10 countries. 23 are recruiting or about to start. 122 of them are mainly about Prader-Willi Syndrome (how this is decided). Per ClinicalTrials.gov, last updated 2026-11-10.

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Status

Completed
81
Terminated
16
Recruiting
16
Status unknown
11
Withdrawn
7
Active, not recruiting
6

Phase

Phase 2
33
Phase 3
27
Phase 1
12
Phase 4
7

Where

United States
69
France
27
Canada
15
United Kingdom
12
Spain
11
Australia
8

Who runs them

University Hospital, Toulouse (17) · Samsung Medical Center (6) · Soleno Therapeutics, Inc. (6) · Radius Pharmaceuticals, Inc. (4) · University of Florida (4) · Assistance Publique - Hôpitaux de Paris (4) · Istituto Auxologico Italiano (4) · Taipei Tzu Chi Hospital, Buddhist Tzu Chi Medical Foundation (3)

What is being tested here

Drugs under test in Prader-Willi Syndrome studies, those with the most open studies first. Medicines only given beside them are not counted. How drugs are counted

DrugOpenPhase 3All
Pitolisant223
BMB-101101
Prebiotics101
Galactomannan101
Oligofructose101
Tirzepatide101
Oxytocin0312
Diazoxide choline046
Human Growth Hormone025
Denatonium acetate monohydrate023

Drug classes tested here GLP-1 receptor agonists 1 open

Coming up

4phase 3 studies under way
8studies finish main data collection within a year2 of them phase 3

Studies recruiting or running, from their records. “Main data collection” ends at the primary completion date, the sponsor’s own estimate, which often moves.

All 8, phase 3 first

Who these studies take

Of the 16 Prader-Willi Syndrome studies recruiting now, 7 (44%) set no upper age limit and 9 (56%) stop at 75 or younger. 11 (69%) take children under 18. 0 (0%) are for women only and 0 (0%) for men only; 1 (6%) take healthy volunteers.

Recruiting studies that take each age, of 16
AgeWomenMen
108 (50%)8 (50%)
1812 (75%)12 (75%)
3010 (63%)10 (63%)
4010 (63%)10 (63%)
5010 (63%)10 (63%)
657 (44%)7 (44%)
757 (44%)7 (44%)
857 (44%)7 (44%)

Across all 144 studies, recruiting or not: 74% stop at 75 or younger and 73% at 65; 76% take children; 1% are for women only and 1% for men only; 24% take healthy volunteers. From each study’s registry entry; the criteria on its page decide.

How long Prader-Willi Syndrome studies take

Of 19 interventional studies with no phase under Prader-Willi Syndrome, half reached primary completion within 29 months of starting, counting those still running.

Start to primary completionEvery sponsorIndustryNon-industry
Interventional, no phase29 mo14–43 · 19 studies——

Each figure is the month by which half the studies had reached primary completion, with the range in which the middle half did. Studies still running count until their last registry update; studies that stopped early are left out. Phase 1 includes early phase 1; observational means prospective or not stated, as retrospective and cross-sectional studies date a window of data rather than a study. How these figures are worked out

Studies

Recruiting first, then most recently updated. Showing 50 of 144. Browse all 144 → or search them.