Muscular Dystrophies: all 550 studies

Page 5 of 6. Open to participants first (89), then studies with results posted, then the rest; newest registration first within each.

• Genetics of Pediatric-Onset Motor Neuron and Neuromuscular DiseasesCompletedNCT02532244
• HT-100 Long-term Study in DMD Patients Who Completed HALO-DMD-02TerminatedNCT02525302Phase 2
• A Peer E-mentoring Intervention to Improve EmploymentCompletedNCT02522507Not applicable
• Improved Muscle Function in Duchenne Muscular Dystrophy Through L-Arginine and MetforminCompletedNCT02516085Phase 1
• Natural History of Cardiac and Respiration Function in Patients With Muscular Dystrophies on Home Mechanical VentilationStatus unknownNCT02501083
• Efficacy of Stem Cell Therapy in Ambulatory and Non-ambulatory Children With Duchenne Muscular Dystrophy - Phase 1-2Status unknownNCT02484560Phase 1
• Cardiac Involvement in Patients With Duchenne/Becker Muscular DystrophyCompletedNCT02470962
• Phenomics in Autoimmune and Inflammatory DiseasesCompletedNCT02466217
• Upper Limb Assessment in Duchenne Muscular DystrophyStatus unknownNCT02436720
• Sodium Nitrate for Muscular DystrophyCompletedNCT02434627Phase 1
• Myocardial Fibrosis Progression in Duchenne and Becker Muscular Dystrophy - ACE Inhibitor Therapy TrialCompletedNCT02432885Phase 3
• Effects of Standing on Non-Ambulatory Children With Neuromuscular ConditionsCompletedNCT02428673Not applicable
• Strength Training in Duchenne Muscular DystrophyCompletedNCT02421523Not applicable
• 2D Strain Evaluation: Children With Duchenne Muscular Dystrophy Versus Healthy ChildrenCompletedNCT02418338Not applicable
• Modified Diet Trial: A Study of SMT C1100 in Paediatric Patients With DMD Who Follow a Balanced DietCompletedNCT02383511Phase 1
• Clinical Intramuscular Gene Transfer Trial of rAAVrh74.MCK.Micro-Dystrophin to Patients With Duchenne Muscular DystrophyCompletedNCT02376816Phase 1
• Effects of Standing on Non-Ambulatory Children With Spinal Muscular AtrophyCompletedNCT02341053Not applicable
• A Device for Rapid, Painless, Bedside Muscle Evaluation of ChildrenCompletedNCT02340923
• Open Label, Extension Study of PRO044 in Duchenne Muscular Dystrophy (DMD)TerminatedNCT02329769Phase 2
• Continuation Protocol to Protocol BBCO-001CompletedNCT02328482Phase 3
• European Home Mechanical Ventilation RegistryTerminatedNCT02315339
• An Open-Label, Long-Term Extension Study to Evaluate the Safety and Tolerability DeflazacortCompletedNCT02295748Phase 1
• Efficacy of Umbilical Cord Mesenchymal Stem Cells in Duchenne Muscular DystrophyStatus unknownNCT02285673Phase 1/2
• A Pharmacokinetic Study of Oral Deflazacort in Children and Adolescent Subjects With Duchenne Muscular DystrophyCompletedNCT02251600Phase 1
• Cell Therapy in Limb Girdle Muscular DystrophyWithdrawnNCT02245711Phase 1
• Stem Cell Therapy in Muscular DystrophyWithdrawnNCT02241928Phase 1
• Stem Cell Therapy in Duchenne Muscular DystrophyWithdrawnNCT02241434Phase 1
• Allogeneic Human Umbilical Cord Mesenchymal Stem Cells for a Single Male Patient With Duchenne Muscular Dystrophy (DMD)CompletedNCT02235844Phase 1
• Transplantation of Myoblasts to Duchenne Muscular Dystrophy (DMD) PatientsStatus unknownNCT02196467Phase 1/2
• Assessment of Cardiopulmonary Function in Duchenne Muscular DystrophyCompletedNCT02195999
• Where Does Hope Fit In? The Relationship Between Hope, Uncertainty, and Coping Efficacy in Mothers of Children With Duchenne/Becker Muscular DystrophyCompletedNCT02194725
• Magnetic Resonance and Optical Imaging of Dystrophic and Damaged MuscleCompletedNCT02168114Not applicable
• Muscle MRI in Becker Muscular Dystrophy and in Limb-girdle Muscular Dystrophy Type 2ICompletedNCT02165358
• High Intensity Training in Patients With Facioscapulohumeral Muscular DystrophyCompletedNCT02159963Not applicable
• 1 Year MRI Followup in Facioscapulohumeral Muscular DystrophyCompletedNCT02159612
• Effect of Aerobic Training in Patients With Oculopharyngeal Muscular DystrophyStatus unknownNCT02158156Not applicable
• Calibration and Validation of the PROMIS and Neuro-QOL Questionnaires in Cerebral Palsy and Congenital Muscular DystrophyCompletedNCT02153970
• Effects of Sodium Nitrate on Blood Flow in Becker Muscular DystrophyCompletedNCT02147639Phase 2/3
• National Registry for Egyptian Pediatric Neuromuscular DiseasesStatus unknownNCT02124616
• Evaluation of Muscle miRNA as Biomarkers in DystrophinopathiesStatus unknownNCT02109692Not applicable
• Innovative Ultrasound Technology in Neuromuscular DiseaseCompletedNCT02104921
• Exploratory Study of NS-065/NCNP-01 in DMDCompletedNCT02081625Phase 1
• A Phase 1b Study of SMT C1100 in Subjects With Duchenne Muscular Dystrophy (DMD)CompletedNCT02056808Phase 1
• Stem Cell Therapy in Limb Girdle Muscular DystrophyWithdrawnNCT02050776Phase 1
• A Trial of Chronotherapy of Corticosteroids in Duchenne Muscular DystrophyWithdrawnNCT02036463Phase 2
• Peak Cough Flow and Cough Clearance in Patients With Muscular DystrophyCompletedNCT02034305
• Neurological and Psychiatric Comorbidities Patients With FSHD 1 and 2CompletedNCT02032979Not applicable
• L-citrulline and Metformin in Becker's Muscular DystrophyCompletedNCT02018731Phase 2
• L-citrulline and Metformin in Duchenne's Muscular DystrophyCompletedNCT01995032Phase 3
• Study of Morphology and Functional Magnetic Resonance Imaging (MRI) Muscle Patients With Muscular Dystrophy Type FSHD Benefiting a Physical Training Introduced.CompletedNCT01990976
• Optimum Insufflation Capacity in NMDCompletedNCT01981915Not applicable
• Open Label Extension Study of HT-100 in Patients With DMDTerminatedNCT01978366Phase 2
• Clinical, Genetic and Epigenetic Characterization of Patients With FSHD Type 1 and FSHD Type 2CompletedNCT01970735Not applicable
• Duchenne Muscular Dystrophy < 18y in Norway: Genotype/Phenotype, Growth, Puberty, Bone Health and Quality of Life.CompletedNCT01963897
• Evaluating a New Knee-Ankle-Foot Brace to Improve Gait in Children With Movement DisordersCompletedNCT01961557Not applicable
• A Phase I/II Study of BMN053 in Subjects With Duchenne Muscular Dystrophy (DMD)TerminatedNCT01957059Phase 1/2
• Whole Body Vibration Therapy in Boys With Duchenne Muscular DystrophyCompletedNCT01954940Not applicable
• LAMA2-related Muscular Dystrophy Brain StudyWithdrawnNCT01952028
• Muscle Tissue Bank for Muscular DystrophyCompletedNCT01950897
• At-Home Research Study for Patients With Autoimmune, Inflammatory, Genetic, Hematological, Infectious, Neurological, CNS, Oncological, Respiratory, Metabolic ConditionsCompletedNCT01931644
• Mother-caregivers of Children With Duchenne Muscular DystrophyCompletedNCT01921374Not applicable
• Phase II Study of NPC-14 (Arbekacin Sulfate) to Explore Safety, Tolerability, and Efficacy in Duchenne Muscular DystrophyStatus unknownNCT01918384Phase 2
• A Phase I/II, Open Label, Escalating Dose, Pilot Study to Assess Effect, Safety, Tolerability and PK of Multiple SC Doses of Drisapersen in Patients With Duchenne Muscular Dystrophy and to Assess the Potential for IV Dosing as an Alternative Route of AdministrationTerminatedNCT01910649Phase 2
• The Effect of Aerobic Exercise, on Fitness and Functional Muscle Strength, in Patients With Muscular DystrophyCompletedNCT01895283Not applicable
• Drisapersen Duchenne Muscular Dystrophy (DMD) Treatment ProtocolWithdrawnNCT01890798Phase 3
• Assessment of Response to Treatment of Osteoporosis With Oral Bisphosphonates in Patients With Muscular DystrophyCompletedNCT01882400Phase 4
• Safety, Tolerability, and Pharmacokinetics of Single and Multiple Doses of HT-100 in Duchenne Muscular DystrophyTerminatedNCT01847573Phase 1/2
• A Study to Test Lung Stretch Therapy (Hyperinsufflation) in Children With Collagen VI Muscular DystrophyCompletedNCT01836627Not applicable
• Study Safety and Efficacy of Bone Marrow Derived Autologous Cells for the Treatment of Muscular Dystrophy.Status unknownNCT01834066Phase 1/2
• Study Safety and Efficacy of BMMNC for the Patient With Duchenne Muscular DystrophyStatus unknownNCT01834040Phase 1/2
• Phase IIb Study of PRO045 in Subjects With Duchenne Muscular DystrophyTerminatedNCT01826474Phase 1/2
• Endomysial Fibrosis, Muscular Inflammatory Response and Calcium Homeostasis Dysfunction in Duchenne Muscular DystrophyStatus unknownNCT01823783Not applicable
• A Study of the Safety, Tolerability & Efficacy of Long-term Administration of Drisapersen in US & Canadian SubjectsTerminatedNCT01803412Phase 3
• Power Over Pain (POP) StudyCompletedNCT01800604Not applicable
• Limb Girdle Muscular Dystrophy (LGMD) Natural HistoryCompletedNCT01783509
• Duchenne Muscular Dystrophy Tissue Bank for Exon SkippingStatus unknownNCT01772043
• A Prospective Natural History Study of Progression of Subjects With Duchenne Muscular Dystrophy.TerminatedNCT01753804
• Myocardial Involvement in Carriers of Duchenne Muscular Dystrophy: An MRI-studyCompletedNCT01712152
• Prospective Study for 24-months of Physical Training Introduced in Lifestyle of Patients With FSHD : Tolerance, Sustainability and Efficiency of Unsupervised Training Program.CompletedNCT01689480
• Heart Imaging in Children With Muscular DystrophyTerminatedNCT01633242
• Protein Supplementation and Exercise in Patients With FSH Muscular Dystrophy- a Randomized Placebo Controlled StudyCompletedNCT01618331Not applicable
• Safety and Efficacy of Umbilical Cord Mesenchymal Stem Cell Therapy for Patients With Duchenne Muscular DystrophyStatus unknownNCT01610440Phase 1/2
• Effects Antioxidants Supplementation on Muscular Function Patients Facioscapulohumeral Dystrophy (FSHD)CompletedNCT01596803Not applicable
• PDE Inhibitors in DMD Study (Acute Dosing Study)CompletedNCT01580501Phase 1
• Genetic and Physical Study of Childhood Nerve and Muscle DisordersCompletedNCT01568658
• CRD007 for the Treatment of Duchenne Muscular Dystrophy, Becker Muscular Dystrophy and Symptomatic CarriersCompletedNCT01540604Phase 2
• Becker Muscular Dystrophy - A Natural History Study to Predict Efficacy of Exon SkippingStatus unknownNCT01539772
• Follistatin Gene Transfer to Patients With Becker Muscular Dystrophy and Sporadic Inclusion Body MyositisCompletedNCT01519349Phase 1
• Double Push Acoustic Radiation Force (DP ARF) Ultrasound for Monitoring Degeneration in Duchenne Muscular DystrophyCompletedNCT01506518
• Electrical Impedance Myography and Ultrasound as Biomarkers of Duchenne Muscular DystrophyCompletedNCT01491555
• Open Label Study of GSK2402968 in Subjects With Duchenne Muscular DystrophyTerminatedNCT01480245Phase 3
• To Compare the Pharmacokinetics Profiles of ISO 20, IBU 200 and IBU Plus ISO Combinations 200 + 20CompletedNCT01478022Phase 1
• Genetic Study of Familial and Sporadic ALS/Motor Neuron Disease, Miyoshi Myopathy and Other Neuromuscular DisordersWithdrawnNCT01459302
• Studying Skeletal Muscle, Heart, and Diaphragm Imaging in Boys With Duchenne Muscular DystrophyCompletedNCT01451281
• Low Protein Diet in Patients With Collagen VI Related MyopathiesCompletedNCT01438788Phase 2
• A Multicenter Collaborative Study on the Clinical Features, Expression Profiling, and Quality of Life of Infantile Onset FSHDCompletedNCT01437345
• Safety, Tolerability and Effects of L-Arginine in Boys With Dystrophinopathy on CorticosteroidsCompletedNCT01388764Phase 1
• The Role of Family Functioning in Promoting Adaptation in Siblings of Individuals With Duchenne Muscular Dystrophy (DMD)TerminatedNCT01386515
• Observational Study of Patients With Duchenne Muscular Dystrophy Theoretically Treatable With Exon 53 SkippingStatus unknownNCT01385917
• Research of Biomarkers in Duchenne Muscular Dystrophy PatientsCompletedNCT01380964

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