Muscular Dystrophies: all 550 studies

Page 2 of 6. Open to participants first (89), then studies with results posted, then the rest; newest registration first within each.

• Efficacy and Safety of Losmapimod in Treating Subjects With Facioscapulohumeral Muscular Dystrophy (FSHD) With Open-Label Extension (OLE)TerminatedNCT04264442Phase 2Results posted
• A 48-Week, Open Label, Study to Evaluate the Efficacy and Safety of AMONDYS 45, EXONDYS 51, VYONDYS 53 in Subjects With DuchenneMuscular Dystrophy Carrying Eligible DMD Duplications.CompletedNCT04179409Phase 2Results posted
• Study to Assess the Efficacy and Safety of Viltolarsen in Ambulant Boys With DMD (RACER53)CompletedNCT04060199Phase 3Results posted
• Weekly Steroids in Muscular DystrophyCompletedNCT04054375Phase 2Results posted
• Evaluation of Safety, Tolerability, and Changes in Biomarker and Clinical Outcome Assessments of Losmapimod for FSHD1 With ExtensionTerminatedNCT04004000Phase 2Results posted
• Efficacy and Safety of Losmapimod in Subjects With Facioscapulohumeral Muscular Dystrophy (FSHD)CompletedNCT04003974Phase 2Results posted
• Transmembrane Electromyography (TM-EMG) for the Assessment of Neuromuscular Function in the OropharynxCompletedNCT03986671Not applicableResults posted
• A Study to Evaluate Safety, Tolerability, and Efficacy of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) Who Have Completed Study 4658-102 (NCT03218995)TerminatedNCT03985878Phase 2Results posted
• Extension Study to Evaluate the Long-Term Effects of ACE-083 in Patients With Facioscapulohumeral Muscular Dystrophy (FSHD) and Charcot-Marie Tooth (CMT) Disease Types 1 and X (CMT1 and CMTX)TerminatedNCT03943290Phase 2Results posted
• Efficacy and Safety Study of WVE-210201 (Suvodirsen) With Open-label Extension in Ambulatory Patients With Duchenne Muscular DystrophyTerminatedNCT03907072Phase 2/3Results posted
• The Effectiveness of Participation-focused Interventions on Body Functions of Youth With Physical DisabilitiesCompletedNCT03851107Not applicableResults posted
• A Study to Assess Dystrophin Levels in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) Who Have Been Treated With AtalurenCompletedNCT03796637Phase 2Results posted
• A Study of Deflazacort (Emflaza®) in Participants With Limb-Girdle Muscular Dystrophy 2I (LGMD2I)TerminatedNCT03783923Phase 3Results posted
• Spironolactone Versus Prednisolone in DMDTerminatedNCT03777319Phase 1Results posted
• A Randomized, Double-blind, Placebo-controlled Study of Delandistrogene Moxeparvovec (SRP-9001) for Duchenne Muscular Dystrophy (DMD)CompletedNCT03769116Phase 1/2Results posted
• A Natural History Study In Chinese Male Patients With Duchenne Muscular DystrophyCompletedNCT03760029Not applicableResults posted
• Phase III Study of Edasalonexent in Boys With Duchenne Muscular DystrophyCompletedNCT03703882Phase 3Results posted
• An Open-Label Extension Study for Patients With Duchenne Muscular Dystrophy Who Participated in Studies of SRP-5051 (Vesleteplirsen)TerminatedNCT03675126Phase 1/2Results posted
• A Study to Assess Dystrophin Levels in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)CompletedNCT03648827Phase 2Results posted
• First Time in Human (FTIH) Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Single and Repeat Doses of GSK3439171A in Healthy Subjects and to Assess Food EffectCompletedNCT03627494Phase 1Results posted
• An Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular DystrophyTerminatedNCT03532542Phase 3Results posted
• Use of Dynamic Arm Supports to Promote Activities of Daily Living in Individuals With DMDTerminatedNCT03531788Not applicableResults posted
• A Study to Assess the Efficacy and Safety of Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)CompletedNCT03439670Phase 2Results posted
• A Study of CAP-1002 in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular DystrophyCompletedNCT03406780Phase 2Results posted
• A Study to Assess the Efficacy and Safety of MNK-1411 in Duchenne Muscular DystrophyTerminatedNCT03400852Phase 2Results posted
• A Gene Transfer Therapy Study to Evaluate the Safety of Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD)CompletedNCT03375164Phase 1/2Results posted
• Gene Transfer Clinical Trial to Deliver rAAVrh74.MCK.GALGT2 for Duchenne Muscular DystrophyCompletedNCT03333590Phase 1/2Results posted
• Clinical Study to Evaluate the Efficacy and Safety of Givinostat in Ambulant Patients With Becker Muscular DystrophyCompletedNCT03238235Phase 2Results posted
• (-)- Epicatechin Becker Muscular DystrophyCompletedNCT03236662Phase 2Results posted
• Study of Eteplirsen in Young Participants With Duchenne Muscular Dystrophy (DMD) Amenable to Exon 51 SkippingCompletedNCT03218995Phase 2Results posted
• Long-Term Outcomes of Ataluren in Duchenne Muscular DystrophyCompletedNCT03179631Phase 3Results posted
• Extension Study of NS-065/NCNP-01 in Boys With Duchenne Muscular Dystrophy (DMD)CompletedNCT03167255Phase 2Results posted
• Study of Testosterone and rHGH in FSHDCompletedNCT03123913Phase 1Results posted
• Clinical Trial to Evaluate the Efficacy, Safety, and Tolerability of RO7239361 in Ambulatory Boys With Duchenne Muscular DystrophyCompletedNCT03039686Phase 2/3Results posted
• Long-term Extension Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)CompletedNCT03038399Phase 2Results posted
• Plus Epicatechin Duchenne Muscular Dystrophy in Non-ambulatory AdolescentsCompletedNCT02964377Phase 1/2Results posted
• Study of ACE-083 in Patients With Facioscapulohumeral Muscular Dystrophy (FSHD)TerminatedNCT02927080Phase 2Results posted
• An Open-label Extension Study To Evaluate Safety Of PF-06252616 In Boys With Duchenne Muscular DystrophyTerminatedNCT02907619Phase 2Results posted
• Proof of Concept Study to Assess Activity and Safety of SMT C1100 (Ezutromid) in Boys With Duchenne Muscular Dystrophy (DMD)TerminatedNCT02858362Phase 2Results posted
• Clinical Study to Evaluate the Efficacy and Safety of Givinostat in Ambulant Patients With Duchenne Muscular DystrophyCompletedNCT02851797Phase 3Results posted
• Study to Evaluate the Long-Term Safety, Tolerability, and Biological Activity of ATYR1940 in Participants With Limb Girdle and Facioscapulohumeral Muscular Dystrophy (FSHD)CompletedNCT02836418Phase 1/2Results posted
• Study of Ataluren in ≥2 to <5 Year-Old Male Participants With Duchenne Muscular DystrophyCompletedNCT02819557Phase 2Results posted
• A Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)CompletedNCT02760264Phase 2Results posted
• A Phase IIa Study of TAS-205 for Duchenne Muscular DystrophyCompletedNCT02752048Phase 2Results posted
• Safety and Dose Finding Study of NS-065/NCNP-01 in Boys With Duchenne Muscular Dystrophy (DMD)CompletedNCT02740972Phase 2Results posted
• Rimeporide in Patients With Duchenne Muscular DystrophyCompletedNCT02710591Phase 1Results posted
• Study of DS-5141b in Patients With Duchenne Muscular DystrophyCompletedNCT02667483Phase 1/2Results posted
• Trial of Pamrevlumab (FG-3019), in Non-Ambulatory Participants With Duchenne Muscular Dystrophy (DMD)TerminatedNCT02606136Phase 2Results posted
• Evaluate Safety and Biological Activity of ATYR1940 in Participants With Early Onset Facioscapulohumeral Muscular DystrophyCompletedNCT02603562Phase 1/2Results posted
• Evaluate Safety and Biological Activity of ATYR1940 in Participants With Limb Girdle Muscular Dystrophy 2B (LGMD2B) and Facioscapulohumeral Muscular Dystrophy (FSHD)CompletedNCT02579239Phase 1/2Results posted
• Safety, Tolerability, Pharmacokinetics (PK), and Activity of ATYR1940 in Participants With Muscular Dystrophy - Study ExtensionCompletedNCT02531217Phase 1/2Results posted
• Dose-Titration and Open-label Extension Study of SRP-4045 in Advanced Stage Duchenne Muscular Dystrophy (DMD) PatientsCompletedNCT02530905Phase 1Results posted
• Study of an Investigational Drug, RO7239361 (BMS-986089), in Ambulatory Boys With DMDTerminatedNCT02515669Phase 1/2Results posted
• HOPE-Duchenne (Halt cardiomyOPathy progrEssion in Duchenne)CompletedNCT02485938Phase 2Results posted
• Phase 1/2 Study in Boys With Duchenne Muscular DystrophyCompletedNCT02439216Phase 1/2Results posted
• Safety Study of Eteplirsen to Treat Early Stage Duchenne Muscular DystrophyCompletedNCT02420379Phase 2Results posted
• Bone Health in Facioscapulohumeral Muscular DystrophyCompletedNCT02413190Results posted
• Clinical Intramuscular Gene Transfer of rAAV1.CMV.huFollistatin344 Trial to Patients With Duchenne Muscular DystrophyCompletedNCT02354781Phase 1/2Results posted
• Therapeutic Potential for Aldosterone Inhibition in Duchenne Muscular DystrophyCompletedNCT02354352Phase 3Results posted
• Phase I/II Study of SRP-4053 in DMD PatientsCompletedNCT02310906Phase 1/2Results posted
• A Phase 2 Study to Evaluate the Safety, Efficacy, Pharmacokinetics and Pharmacodynamics of PF-06252616 in Duchenne Muscular DystrophyTerminatedNCT02310763Phase 2Results posted
• Safety Study of Eteplirsen to Treat Advanced Stage Duchenne Muscular DystrophyCompletedNCT02286947Phase 2Results posted
• Study of Eteplirsen in DMD PatientsCompletedNCT02255552Phase 3Results posted
• A Study of TAS-205 for Duchenne Muscular DystrophyCompletedNCT02246478Phase 1Results posted
• Safety, Tolerability, Pharmacokinetics, and Biological Activity of ATYR1940 in Adult Participants With Muscular DystrophyCompletedNCT02239224Phase 1/2Results posted
• WREX Outcome StudyCompletedNCT02218593Results posted
• Historically Controlled Trial of Corticosteroids in Young Boys With Duchenne Muscular DystrophyCompletedNCT02167217Phase 2Results posted
• An Extension Study of Ataluren (PTC124) in Participants With Nonsense Mutation DystrophinopathyTerminatedNCT02090959Phase 3Results posted
• Safety Tolerability and Efficacy Study of Cabaletta to Treat Oculopharyngeal Muscular Dystrophy (OPMD) PatientsCompletedNCT02015481Phase 2Results posted
• Stacking Exercises Aid the Decline in FVC and Sick TimeCompletedNCT01999075Phase 4Results posted
• Cardiomyopathy in DMD: Lisinopril vs. LosartanCompletedNCT01982695Not applicableResults posted
• A Gene Transfer Therapy Study to Evaluate the Safety of SRP-9004 (Patidistrogene Bexoparvovec) in Participants With Limb-Girdle Muscular Dystrophy, Type 2D (LGMD2D)CompletedNCT01976091Phase 1/2Results posted
• Duchenne Muscular Dystrophy Clinical TrialCompletedNCT01874275Not applicableResults posted
• A Study of Tadalafil for Duchenne Muscular DystrophyTerminatedNCT01865084Phase 3Results posted
• Use of (-)-Epicatechin in the Treatment of Becker Muscular Dystrophy (Pilot Study)CompletedNCT01856868Phase 1/2Results posted
• Phase 3 Study of Ataluren in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)CompletedNCT01826487Phase 3Results posted
• Effect of EPA and DHA in the Inflammation and Metabolic Disorders in DMD/DMB PatientsCompletedNCT01826422Not applicableResults posted
• Congenital Muscular Dystrophy Ascending Multiple Dose Cohort Study Analyzing Pharmacokinetics at Three Dose Levels In Children and Adolescents With Assessment of Safety and Tolerability of Omigapil (CALLISTO)CompletedNCT01805024Phase 1Results posted
• Ultrasound in Muscle BiopsyCompletedNCT01790178Not applicableResults posted
• A Study to Assess Safety/Tolerability, pk, Effects on Histology, Clinical Parameters of Givinostat in Children With DMDCompletedNCT01761292Phase 1/2Results posted
• Sedation During Muscle Biopsy in Patients With Duchenne Muscular DystrophyCompletedNCT01645098Not applicableResults posted
• Finding the Optimum Regimen for Duchenne Muscular DystrophyCompletedNCT01603407Phase 3Results posted
• Study of Ataluren for Previously Treated Participants With Nonsense Mutation Duchenne/Becker Muscular Dystrophy (nmDBMD) in Europe, Israel, Australia, and CanadaCompletedNCT01557400Phase 3Results posted
• Efficacy, Safety, and Tolerability Rollover Study of Eteplirsen in Subjects With Duchenne Muscular DystrophyCompletedNCT01540409Phase 2Results posted
• DART Electrical Impedance Myography (EIM) Trial in Duchenne Muscular Dystrophy (DMD) and Healthy ControlsCompletedNCT01523964Not applicableResults posted
• Eplerenone for Subclinical Cardiomyopathy in Duchenne Muscular DystrophyCompletedNCT01521546Not applicableResults posted
• A Clinical Study to Assess Two Doses of GSK2402968 in Subjects With Duchenne Muscular Dystrophy (DMD)CompletedNCT01462292Phase 2Results posted
• Flu Vaccine Study in Neuromuscular Patients 2011CompletedNCT01422200Phase 4Results posted
• Efficacy Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy PatientsCompletedNCT01396239Phase 2Results posted
• ECoG Direct Brain Interface for Individuals With Upper Limb ParalysisCompletedNCT01393444Not applicableResults posted
• A Clinical Study to Assess the Efficacy and Safety of GSK2402968 in Subjects With Duchenne Muscular DystrophyCompletedNCT01254019Phase 3Results posted
• Safety and Efficacy Study of IGF-1 in Duchenne Muscular DystrophyCompletedNCT01207908Phase 1/2Results posted
• Revatio for Heart Disease in Duchenne Muscular Dystrophy and Becker Muscular DystrophyTerminatedNCT01168908Phase 2Results posted
• Study of ACE-031 in Subjects With Duchenne Muscular DystrophyTerminatedNCT01099761Phase 2Results posted
• Phase I/II Study of PRO044 in Duchenne Muscular Dystrophy (DMD)CompletedNCT01037309Phase 1/2Results posted
• Phase III Study of Idebenone in Duchenne Muscular Dystrophy (DMD)CompletedNCT01027884Phase 3Results posted
• Study of Ataluren (PTC124) in Nonambulatory Participants With Nonsense-Mutation-Mediated Duchenne/Becker Muscular Dystrophy (nmDMD/BMD)TerminatedNCT01009294Phase 2Results posted
• Safety Study of Transvenous Limb Perfusion in Human Muscular DystrophyCompletedNCT00873782Phase 1Results posted
• Phase 2B Extension Study of Ataluren (PTC124) in Duchenne/Becker Muscular Dystrophy (DMD/BMD)TerminatedNCT00847379Phase 2Results posted
• Dose-Ranging Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy (DMD) PatientsCompletedNCT00844597Phase 1/2Results posted

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