Mucopolysaccharidosis VI clinical trials

The registry lists 36 studies for Mucopolysaccharidosis VI across more than 10 countries. 4 are recruiting or about to start. 10 of them are mainly about Mucopolysaccharidosis VI (how this is decided). Per ClinicalTrials.gov, last updated 2026-11-03.

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Status

Completed: 19
Terminated: 6
Active, not recruiting: 4
Recruiting: 3
Status unknown: 2
Enrolling by invitation: 1

Phase

Phase 2: 12
Phase 1: 7
Phase 3: 4
Phase 4: 1

Where

United States: 30
France: 5
United Kingdom: 4
Germany: 4
Portugal: 4
Italy: 3

Who runs them

BioMarin Pharmaceutical (7) · Masonic Cancer Center, University of Minnesota (5) · University of California, San Francisco (3) · Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center (3) · University of Minnesota (2) · National MPS Society (1) · Hospital de Clinicas de Porto Alegre (1) · Aldagen (1)

What is being tested here

Drugs under test in Mucopolysaccharidosis VI studies, those with the most open studies first. Medicines only given beside them are not counted. How drugs are counted

Drug	Open	Phase 3	All
Laronidase	1	0	1
N-Acetylgalactosamine-4-Sulfatase	0	2	4
Cyclophosphamide	0	0	3
Busulfan	0	0	3
Adalimumab	0	0	2
Alemtuzumab	0	0	2
Vosoritide	0	0	1
Odiparcil	0	0	1
Cyclosporine	0	0	1
Mycophenolic Acid	0	0	1

Drug classes tested here Alkylating agents 3

Coming up

0phase 3 studies under way

3studies finish main data collection within a year

Studies recruiting or running, from their records. “Main data collection” ends at the primary completion date, the sponsor’s own estimate, which often moves.

All 3

Nov 2026Early Check: Expanded Screening in Newborns · RTI International
Dec 2026MPS (RaDiCo Cohort) (RaDiCo-MPS) · Institut National de la Santé Et de la Recherche Médicale, France
Jan 2027Study to Evaluate the Safety and Efficacy of Adalimumab in MPS I, II, and VI · Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center

Who these studies take

Of the 3 Mucopolysaccharidosis VI studies recruiting now, 1 (33%) set no upper age limit and 2 (67%) stop at 75 or younger. 2 (67%) take children under 18. 1 (33%) are for women only and 0 (0%) for men only; 0 (0%) take healthy volunteers.

Recruiting studies that take each age, of 3
Age	Women	Men
10	2 (67%)	2 (67%)
18	3 (100%)	2 (67%)
30	3 (100%)	2 (67%)
40	3 (100%)	2 (67%)
50	3 (100%)	2 (67%)
65	1 (33%)	1 (33%)
75	1 (33%)	1 (33%)
85	1 (33%)	1 (33%)

Across all 36 studies, recruiting or not: 58% stop at 75 or younger and 58% at 65; 97% take children; 3% are for women only and 3% for men only; 8% take healthy volunteers. From each study’s registry entry; the criteria on its page decide.

Studies

Recruiting first, then most recently updated. Showing 36 of 36. search them.