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RecruitingNCT05564936Updated Apr 11, 2025

The ME&MG Digital Solution for Autonomous Assessment of Myasthenia Gravis

An interventional study of ME&MG mobile application in Myasthenia Gravis, sponsored by Ad scientiam. Recruiting at 19 sites in 2 countries. Open to participants aged 18 Years and older, including healthy volunteers. Per ClinicalTrials.gov, last updated 2025-04-11.

Sponsored by Ad scientiam · Not applicable, Interventional, and Other

Phase
Not applicable
Study type
Interventional
Enrollment
144
Allocation
Non-randomized
Ages
18 Years and older
Sex
All
01

Study summary

ME\&MG is a standalone software (digital solution) running on patients smartphones, connected to a web portal for physicians. It is intended to be used as an unsupervised digital self-assessment tool for the monitoring of disabilities in patients living with MG.

ME\&MG contains digital active tests for the assessment of ptosis, breathing, dysarthria, upper- and lower-limb (arms and legs) weakness, treatment follow-up, and validated e-questionnaires related to daily activities, pain, fatigue, sleep, and depression disorders.

The objectives of this study are to validate the accuracy, reliability and reproducibility of the unsupervised at-home self-assessment of symptoms on the patient's smartphone with ME\&MG versus the standard in-clinic testing, as well as to evaluate the safety of the solution, its usability and satisfaction.

Read the detailed description

Myasthenia gravis (MG) is an autoimmune neuromuscular disease characterised by fatigable muscle weakness due to autoantibodies targeting components of the neuromuscular junction.

Deficits are measured using validated clinical scales such as the Quantitative Myasthenia Gravis score (QMG) QMG, Myasthenia Gravis Composite Score (MCS), Myasthenia Gravis Activities of Daily Living score (MG-ADL), etc., Unfortunately, this type of assessment might require expensive material, time, and personnel training, which make MG assessment difficult for clinicians in routine care.

Research on the matter has highlighted the importance of Patient-Reported Outcomes (PROs), composite measures of disease severity and quality-of-life measurements. This has led to the development of a number of tools for the self-assessment of PROs with validated questionnaires. However, there is no tool that overcomes the constraints of standard tests such as the QMG while allowing for the collection of objective data and PROs between visits.

ME\&MG is a standalone software (digital solution) running on patients smartphones, connected to a web portal for physicians. It is intended to be used as an unsupervised digital self-assessment tool for the monitoring of disabilities in patients living with MG.

ME\&MG contains digital active tests for the assessment of ptosis, breathing, dysarthria, upper- and lower-limb (arms and legs) weakness, treatment follow-up, and validated e-questionnaires related to daily activities, pain, fatigue, sleep, and depression disorders.

The objectives of this study are to validate the accuracy, reliability and reproducibility of the unsupervised at-home self-assessment of symptoms on the patient's smartphone with ME\&MG versus the standard in-clinic testing, as well as to evaluate the safety of the solution, its usability and satisfaction.

02

Conditions studied

  • Myasthenia Gravis
03

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All
Accepts healthy volunteers
Yes

Inclusion criteria

  • Aged over 18 Years
  • Diagnosed with gMG at screening with generalized muscle weakness meeting the clinical criteria for diagnosis of MG, as defined by the MGFA Clinical Classification Class II, III, or IV, and likely not in need of a respirator for the duration of the study, as judged by the investigator
  • With positive serologic testing for anti-AChR autoantibody at screening
  • Have read the information sheet and signed the informed consent form
  • Own a personal smartphone which software version is above 13 for IOS and 8 for Android included
  • Able to use a smartphone
  • Able to read language in which the mobile application is available (French, English, Spanish) and able to understand pictograms

Exclusion criteria

Exclusion Criteria:

  • Subjects having undergone thymectomy Plasma Exchange Therapy or Intravenous Immunoglobulin Therapy within four weeks of screening
  • Subjects having initiated FcRn inhibitor therapy within the four weeks preceding screening
  • Known medical or psychological condition(s) or risk factor(s) that, as judged by the investigator, might interfere with the subject's full participation in the study, pose any additional risk for the subject, or confound the assessment of the subject or outcome of the study.
  • Pregnant and nursing women
  • Person under guardianship or curatorship
  • Current drugs or/and alcohol abuse that could influence performance on the tests, as judged by the investigator
  • Participant included in another ME\&MG clinical study
  • Participant has participated in another clinical study within the previous 30 days of screening or is currently participating in another study that, in the opinion of the Investigator, might interfere with the subject's full participation in the study or confound the assessment of the subject or outcome of the study.
04

Study design

Phase
Not applicable
Primary purpose
Other
Allocation
Non-randomized
Intervention model
Single group
Masking
None (open label)
Enrollment
144 participants (estimated)

Study arms

  • Experimental
    MG patients

    MG patients will perform 3 in-clinic visits and use the ME\&MG app at-home during 12 months

    Device: ME&MG mobile application

  • Other
    Healthy volunteers

    Healthy volunteers will perform one in-clinic visit and will use the app at-home once

    Device: ME&MG mobile application

Interventions

  • DeviceME&MG mobile application

    ME\&MG is a standalone software (digital solution) running on patients smartphones, connected to a web portal for physicians. It is intended to be used as an unsupervised digital self-assessment tool for the monitoring of disabilities in patients living with MG.

05

What researchers measure

Primary outcomes

  1. To demonstrate that ME&MG tests results performed at-home, under unsupervised condition, are correlated to standard tests results performed in-clinic, under supervised conditions

    Pearson correlation coefficient will be used to assess the relationship between digital tests versus standard tests

    Time frame: baseline

Secondary outcomes

  1. To compare results between in-clinic digital tests and in-clinic standard tests, test to test

    pearson correlation coefficient between digital tests and standard tests

    Time frame: baseline

  2. To assess reproducibility between in-clinic digital tests and at-home digital tests

    intraclass correlation coefficient

    Time frame: baseline, day 1, day 89, day 90

  3. To assess test-retest reliability of at-home digital tests

    intraclass correlation coefficient mean k raters (ICCk; k=day)

    Time frame: Day1, Day 2, Day 3, Day 87, Day 88, Day 89

  4. To compare results obtained with the at-home ME&MG composite score and the in-clinic standard QMG composite score

    Pearson correlation coefficient between digital composite score and QMG score

    Time frame: baseline, day 1

  5. To assess adverse events related to the use of the mobile application

    Descriptive analysis of adverse events (AEs) related to the use of the application

    Time frame: through study completion, an average of 1 year

  6. To assess satisfaction and user experience with the smartphone application

    descriptive analysis of questionnaires resulsts

    Time frame: through study completion, an average of 1 year

  7. To assess correlation of the at-home ME&MG composite score with the Myasthenia Gravis Activities of Daily Living (MG-ADL) score

    Pearson's correlation coefficient between ME\&MG composite score and MG-ADL scores

    Time frame: baseline, day 90, day 365

  8. to assess daily activites

    Myasthenia Gravis Activities of Daily Living (MG-ADL)

    Time frame: 12 months

  9. to assess depression

    Patient Health Questionnaire-8 (PHQ8)

    Time frame: 12 months

  10. to assess pain

    pain likert scale

    Time frame: 12 months

  11. to assess insomnia

    Insomnia Severity Index

    Time frame: 12 months

  12. To assess at-home compliance to the ME&MG smartphone application

    descriptive analysis of adherence data

    Time frame: through study completion, an average of 1 year

  13. To assess quality of life

    36-Item Short Form Survey (SF-36)

    Time frame: Baseline, day 90, Day 365

06

Study locations

15 of 19 sites recruiting
  • University of Colorado Denver
    Aurora, Colorado 80204, United States
    Recruiting
  • University of Florida Health
    Jacksonville, Florida 32209, United States
    Recruiting
  • HealthParterns Institute
    Bloomington, Indiana 47401, United States
    Completed
  • Indiana University Health
    Indianapolis, Indiana 46123, United States
    Recruiting
  • University of Kentucky
    Lexington, Kentucky 40536, United States
    Recruiting
  • Neurological Associates of Long Island, P.C.
    Lake Success, New York 11042, United States
    Recruiting
  • Duke University
    Durham, North Carolina 27708, United States
    Recruiting
  • OHSU
    Portland, Oregon 97239, United States
    • Nizar Chahin, Dr · Contact · chahin@ohsu.edu · 503-494-7772
    • Dr Chahin · Principal investigator
    Recruiting
  • Thomas Jefferson University
    Philadelphia, Pennsylvania 19144, United States
    Recruiting
  • The University of Tennessee Medical Center
    Knoxville, Tennessee 37920, United States
    • Christopher Dr Scheiner · Contact · cscheiner@utmck.edu · 856-521-6174
    • Dr Scheiner · Principal investigator
    Not yet recruiting
  • Vanderbilt Health
    Nashville, Tennessee 37232, United States
    Recruiting
  • Hôpital Raymond Poincaré
    Garches, 92380, France
    • Pr Pascal Laforet · Contact · pascal.laforet@aphp.fr · 01.47.10.77.36
    • Dr Edouard Berling · Principal investigator
    • Dr Claire LEFEUVRE · Sub investigator
    • Dr Alice ROUYER · Sub investigator
    • Pr Guillaume NICOLAS · Sub investigator
    Recruiting
  • CHU Grenoble
    Grenoble, France
    Not yet recruiting
  • Hôpital Salengro
    Lille, France
    Recruiting
  • CHRU Nancy
    Nancy, 54035, France
    • Dr Michaud · Contact · m.michaud@chru-nancy.fr · +33 3 83 85 85 85
    • Dr Michaud · Principal investigator
    • Pauline DUCATEL · Sub investigator
    Recruiting
  • CHU Nantes
    Nantes, France
    Recruiting
  • Pitié-Salpêtrière
    Paris, 75013, France
    • Anthony Behin, Dr · Contact · anthony.behin@aphp.fr · +33 142163774
    • Anthony Behin, Dr · Principal investigator
    • Tanya STOJKOVIC, Dr · Sub investigator
    Recruiting
  • CHU de Strasbourg - Hôpital de Hautepierre
    Strasbourg, 67200, France
    Completed
  • CHU Toulouse
    Toulouse, France
    Recruiting
07

References and documents

Individual participant data

Plan to share: No

No publications or documents are linked to this record.

08

Registry details

Key details

Study ID
NCT05564936
Lead sponsor
Ad scientiam
Responsible party
Sponsor
First posted
Oct 4, 2022
Start date
Jan 24, 2024
Primary completion
Sep 24, 2025 (estimated)
Completion
Sep 24, 2026 (estimated)
Last update
Apr 11, 2025

Study contacts

Pr Laforet
Contact
pascal.laforet@aphp.fr
+33147107752

Oversight

Data monitoring committee
No
FDA-regulated drug
No
FDA-regulated device
Yes
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