CClinicalTrials.gg
Status unknownNCT05188274Updated Jan 12, 2022

A Clinical Study to Evaluate the Safety and Efficacy of T92 in Pediatric Patients With Tourette Syndrome

An interventional study of T92 and Placebo in Tourette Syndrome in Children and Tourette Syndrome in Adolescence, sponsored by Tasly Pharmaceuticals, Inc.. Status unknown at 1 site in United States. Open to participants aged 6 Years to 17 Years. Per ClinicalTrials.gov, last updated 2022-01-12.

Sponsored by Tasly Pharmaceuticals, Inc. · Not applicable, Interventional, and Supportive care

The sponsor has not verified this record recently (last verified Jan 2022), so the status shown — last known as Not yet recruiting — may be out of date.
Phase
Not applicable
Study type
Interventional
Enrollment
150
Allocation
Randomized
Ages
6 Years to 17 Years
Sex
All
01

Study summary

A 12-week clinical study to evaluate the safety and efficacy of T92 in pediatric patients with Tourette Syndrome.

Read the detailed description

This is a multi-center, randomized, double-blind, placebo-controlled, outpatient clinical study designed to evaluate the efficacy and safety of T92 in Tourette Syndrome pediatric patients.

This trial consists of a screening/wash-out period of up to 6 weeks, an 8-week supportive care period and a 4-week follow-up period for all subjects who completed the study. For the first two weeks, the patients will continue to take T92 at half dose and the T92 administration will be stopped from week 3 of the follow-up period.

Subjects will be randomly assigned to receive T92 or matching placebo based on individual body weight. The calculated amount of investigational product (T92 or placebo) will be administrated orally twice daily. Morning dose and evening dose should be administrated at about the same time every day and irrelevant to meals.

02

Conditions studied

  • Tourette Syndrome in Children
  • Tourette Syndrome in Adolescence

Keywords

  • Tourette Syndrome
03

Who can participate

Ages eligible
6 Years to 17 Years
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  1. Male or female children and adolescents aged 6 to 17 years upon screening with a Diagnosis of Tourette Syndrome according to Diagnostic and Statistical Manual of Mental Disorders, Fifth Edition (DSM-V).
  2. TTS ≥ 20 on the YGTSS at screening and baseline.
  3. In the Investigator's opinion the presenting tic symptoms caused impairment in the subject's normal daily routines.
  4. Females of childbearing potential had a negative pregnancy test, practiced acceptable double-barrier methods of contraception (or abstinence), and were not pregnant or lactating.
  5. Written informed assent or consent provided by the subject, and written informed consent provided by the parent(s)/guardians(s), as appropriate per the IRB/EC.
  6. In the opinion of the Investigator, the subject and designated guardian(s) and/or parent(s) must be considered likely to comply with the study protocol and to have a high probability of completing the study.

Exclusion criteria

Exclusion Criteria:

  1. Medical history consistent with another neurologic condition that may have had accompanying abnormal movements (e.g., Huntington's disease, Parkinson's disease, Sydenham's chorea, Wilson's disease, Mental retardation, Traumatic brain injury, Stroke, Restless legs syndrome)
  2. History of schizophrenia, bipolar disorder, or other psychotic disorder; Comorbid conditions such as: Obsessive Compulsive Disorder (OCD) and Attention Deficit Hyperactivity Disorder (ADHD) can be included.
  3. Active major depression disorder.
  4. History of neuroleptic malignant syndrome.
  5. Subjects who have had treatment with:

    1. investigational medication within 3 months of starting study
    2. depot antipsychotics within 3 months of starting study
    3. Antipsychotics with possible effects on TS symptoms: i.e., topiramate within 1 week; levodopa or dopamine agonists within 2 weeks prior to baseline.
    4. VMAT2 inhibitors within 2 weeks prior to baseline.
    5. Atypical antipsychotics within 4 weeks: this class include risperidone (Risperdal), quetiapine (Seroquel), olanzapine (Zyprexa), ziprasidone (Zeldox), paliperidone (Invega), aripiprazole (Abilify) and clozapine (Clozaril).
    6. Selective serotonin reuptake inhibitors unless the dosage has been stable for a minimum of 4 weeks prior to study start and not prescribed to relieve the neurological signs of TS.
  6. Sexually active males or females who would not commit to utilizing 2 of the approved birth control methods or who would not remain abstinent during the trial and for 90 days (males) or 30 days (females) following the last dose of investigational product.
  7. CBIT need to be started at least two months at screening. Could continue on existing therapy or stop it based on PI's opinion.
  8. Significant psychoactive substance use disorder within the past 3 months; or the urine drug screen was positive.
  9. Significant lab abnormality:

    1. Platelets ≤ 75,000/mm3
    2. Hemoglobin ≤ 9 g/dl
    3. Neutrophils, absolute ≤ 1000/mm3
    4. Aspartate transaminase (AST) > 3×ULN (upper limit of normal)
    5. Alanine aminotransferase (ALT) > 3×ULN
    6. Creatinine ≥ 2 mg/dl
  10. History or presence of any clinically important medical condition that, in the judgment of the investigator, is likely to deteriorate, could be detrimental to the subject, or could affect the subject's ability to complete the study.
04

Study design

Phase
Not applicable
Primary purpose
Supportive care
Allocation
Randomized
Intervention model
Parallel assignment
Masking
Quadruple (Participant, Care provider, Investigator, Outcomes assessor)
Enrollment
150 participants (estimated)

Study arms

  • Experimental
    T92 group

    The dose of T92 was calculated based on body weight, orally twice daily. Supportive care duration: 8 weeks

    Dietary Supplement: T92

  • Placebo comparator
    Placebo group

    The dose of placebo was calculated based on body weight, orally twice daily. Supportive care duration: 8 weeks

    Dietary Supplement: Placebo

Interventions

  • Dietary supplementT92

    T92 granules (5g/sachet) will be taken BID for 8 weeks, the dosage will be calculated by individual's body weight.

  • Dietary supplementPlacebo

    The placebo matched to T92 granules will be taken BID for 8 weeks.

05

What researchers measure

Primary outcomes

  1. The mean change from baseline to week 8 in total tic score (TTS) of Yale Global Tic Severity Scale (YGTSS).

    The Yale Global Tic Severity Scale (YGTSS) is a semi-structured clinical interview for assessing the severity of tics in children and adults. The YGTSS enables evaluations of number, frequency, intensity, complexity, and interference of motor and phonic tics, covering the past week. Each domain is scored on a 6-point scale (range 0-5) with a separate rating for "overall impairment" regarding the subject's daily life and activities. YGTSS-TTS is the sum of the total motor tic score plus the total phonic tic score ranging from 0-50. Higher scores indicate greater severity/worse outcome. Changes in TTS after 8 weeks of supportive care duration will be compared between the T92 and placebo groups.

    Time frame: Baseline, Week 8

Secondary outcomes

  1. The change from baseline to Week 8 in total Yale Global Tic Severity Scale (YGTSS) scale YGTSS tic-related impairment (TRI) score at week 8

    The YGTSS ranking of impairment (YGTSS-TRI), with a maximum of 50 points, is based on the impact of the tic disorder on areas of self-esteem, family life, social acceptance, and school scores. Higher scores indicate greater severity/worse outcome.

    Time frame: Baseline, Week 8

  2. Mean change from baseline to TS-CGI severity and improvement at week 8

    The TS-CGI scale is a 7-point Likert scale that allows the clinician to use all available information to assess the impact of tics on the participant's quality of life. Lower scores indicate better quality of life. Mean score was calculated with T92 and placebo group, on week 2, 4, 6, and 8.

    Time frame: Baseline, Week 2, 4, 6 and 8

  3. Clinical response rate, defined as a ≥ 30% reduction from baseline on TTS score at different check points.

    Clinical response defined as a ≥ 30% reduction from baseline on TTS at week 2, 4, 6 and 8. The clinical response rate is the proportion of subjects who achieve clinical response.

    Time frame: Baseline, Week 2, 4, 6 and 8

  4. Evaluation of T92 in reducing severity of the sensations before the emergence of tics by comparing the change in PUTS scores at week 8 from baseline.

    The PUTS is a nine-item self-reported scale that measures the sensations before the emergence of tics, and each item is scored from 1 to 4. The total score (range: 9-36) is obtained by summing all of the nine items. Higher scores indicate greater severity/worse symptoms.

    Time frame: Baseline, Week 4 and 8

  5. Evaluation of T92 in reducing severity of obsessions and compulsion occurring by comparing the change in CY-BOCS scores at week 8 from baseline.

    The CY-BOCS is assessing the severity of obsessions and compulsion occurring over the past week. OCD severity score (range 0-40) including all 10 items rated on a 5-point Likert scale (range 0-4). Higher scores indicate greater severity/worse symptoms.

    Time frame: Baseline, Week 4 and 8

  6. Evaluation of T92 in reducing severity of ADHD symptoms.

    The ADHD-RS-IV is an 18-item scale based on the DSM-IV-TR criteria for ADHD that provides a rating of the severity of symptoms. The first 9 items assess inattentive symptoms and the last 9 items assess hyperactive-impulsive symptoms. Scoring is based on a 4-point Likert-type severity scale: 0 = none, 1 = mild, 2 = moderate, 3 = severe. Higher scores indicate greater severity/worse symptoms.

    Time frame: Baseline, Week 4 and 8

06

Study locations

1 site
  • Yale Child Study Center
    New Haven, Connecticut 06520, United States
07

References and documents

Individual participant data

Plan to share: No

No publications or documents are linked to this record.

08

Registry details

Key details

Study ID
NCT05188274
Lead sponsor
Tasly Pharmaceuticals, Inc.
Responsible party
Sponsor
First posted
Jan 12, 2022
Start date
May 2022 (estimated)
Primary completion
Feb 2024 (estimated)
Completion
Oct 2024 (estimated)
Last update
Jan 12, 2022

Study contacts

Michael H Bloch, MD, PhD
Contact
michael.bloch@yale.edu
203-974-7551
James F Leckman, MD, PhD
Contact
james.leckman@yale.edu
203-785-7971
Michael H Bloch, MD, PhD
principal investigator · Yale University

Oversight

FDA-regulated drug
No
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

Not currently enrolling

This study is status unknown, as verified in Jan 2022. You cannot join it, but the record below documents what was studied.

Follow this study

Get an email when the registry record changes — status, dates, results — or when someone posts here.

Sign in to follow

Discussion

Questions and observations about this study, from anyone following it. Not medical advice, and not a channel to the study team — their contact details are on the registry record.

Sign in to join the discussion. Reading takes no account; posting does. You choose a display name, and a pseudonym is the default.

Nothing here yet. If you are running this trial, taking part in it, or weighing whether to, this is the place to say so.

Start the discussion